Efficacy and Safety Study of STX209 (Arbaclofen) for Social Withdrawal in Adolescents and Adults With Fragile X Syndrome

NCT ID: NCT01282268

Last Updated: 2013-07-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

125 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-05-31

Brief Summary

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To explore the efficacy, safety and tolerability of STX209 (arbaclofen) administered for the treatment of social withdrawal in adolescents and adults with fragile X syndrome (FXS)

Detailed Description

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Conditions

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Fragile X Syndrome

Keywords

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fragile X syndrome autism spectrum disorder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Arbaclofen

Group Type ACTIVE_COMPARATOR

arbaclofen

Intervention Type DRUG

orally disintegrating tablet

Placebo

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type DRUG

orally disintegrating tablet

Interventions

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arbaclofen

orally disintegrating tablet

Intervention Type DRUG

placebo

orally disintegrating tablet

Intervention Type DRUG

Other Intervention Names

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STX209

Eligibility Criteria

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Inclusion Criteria

* Molecular documentation of the full FMR1 mutation
* Current pharmacological treatment regimen has been stable for at least 4 weeks prior to Screening.
* Subjects with a history of seizure disorder must currently be receiving treatment with antiepileptics and must have been seizure free for 6 months, or must be seizure free for 3 years if not currently receiving antiepileptics.
* If the subject is already receiving stable non-pharmacologic educational, behavioral, and/or dietary interventions, participation in these programs must have been continuous during the 2 months prior to Screening

Exclusion Criteria

* Subjects with any condition, including alcohol and drug abuse, which might interfere with the conduct of the study, confound interpretation of the study results, or endanger their own well-being.
* Subjects who plan to initiate or change pharmacologic or non-pharmacologic interventions during the course of the study.
* Subjects who have taken another investigational drug within the last 30 days.
* Subjects who are not able to take oral medications.
Minimum Eligible Age

12 Years

Maximum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Seaside Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Paul Wang, M.D.

Role: STUDY_DIRECTOR

Seaside Therapeutics, Inc.

Locations

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Southwest Autism Research & Resource Center

Phoenix, Arizona, United States

Site Status

Miller Children's Hospital Research Administration

Long Beach, California, United States

Site Status

University of California-Davis, M.I.N.D. Institute

Sacramento, California, United States

Site Status

Psychiatric Centers at San Diego

San Diego, California, United States

Site Status

University of Colorado Denver, Children's Hospital

Aurora, Colorado, United States

Site Status

University of Miami, Mailman Center for Child Development

Miami, Florida, United States

Site Status

Lake Mary Pediatrics

Orange City, Florida, United States

Site Status

Emory University School of Medicine

Decatur, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status

Kennedy Krieger Institute

Baltimore, Maryland, United States

Site Status

University of Massachusetts

Worcester, Massachusetts, United States

Site Status

University of Missouri, Thompson Research Center for Autism & Neurodevelpmental Disorders

Columbia, Missouri, United States

Site Status

Seaver Autism Center, Mount Sinai Medical Center

New York, New York, United States

Site Status

New York State Institute for Basic Research in Developmental Disabilities

Staten Island, New York, United States

Site Status

Duke University Clinical Research Unit

Durham, North Carolina, United States

Site Status

Akron Children's Hospital

Akron, Ohio, United States

Site Status

University of Oklahoma, Physician's Child Study Center

Oklahoma City, Oklahoma, United States

Site Status

Suburban Research Associates/Elwyn Genetics

Media, Pennsylvania, United States

Site Status

Vanderbilt Kennedy Center

Nashville, Tennessee, United States

Site Status

Texas Children's Hospital

Houston, Texas, United States

Site Status

Red Oaks Psychiatry Associates, P.A.

Houston, Texas, United States

Site Status

Road Runner Research

San Antonio, Texas, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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209FX301

Identifier Type: -

Identifier Source: org_study_id