A Study to Evaluate the Efficacy and Safety of DNTH103 in Adults With Chronic Inflammatory Demyelinating Polyneuropathy (CAPTIVATE)

NCT ID: NCT06858579

Last Updated: 2026-01-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

480 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-02-10

Study Completion Date

2030-12-31

Brief Summary

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The purpose of this Phase 3 study is to demonstrate the efficacy of DNTH103 as compared to placebo in participants with chronic inflammatory demyelinating polyneuropathy (CIDP).

Detailed Description

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The study includes the following periods:

* Part A: An open-label period (up to 13 weeks)
* Part B: A randomized, placebo-controlled, double-blind treatment period (up to 52 weeks) for participants who respond to DNTH103 in Part A
* Optional open-label extension (OLE) for eligible participants (up to 104 weeks)
* Safety follow-up (40 weeks)

Conditions

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Chronic Inflammatory Demyelinating Polyneuropathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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DNTH103 (Part A)

DNTH103 intravenous (IV) loading dose on Day 1.

DNTH103 subcutaneous (SC) once every 2 weeks for up to 13 weeks.

Group Type EXPERIMENTAL

DNTH103

Intervention Type DRUG

IV Infusion

DNTH103

Intervention Type DRUG

SC injection

DNTH103 Low Dose (Part B)

DNTH103 SC once every 2 weeks for up to 52 weeks.

Group Type EXPERIMENTAL

DNTH103

Intervention Type DRUG

SC injection

DNTH103 High Dose (Part B)

DNTH103 SC once every 2 weeks for up to 52 weeks.

Group Type EXPERIMENTAL

DNTH103

Intervention Type DRUG

SC injection

Placebo (Part B)

Placebo SC once every 2 weeks for up to 52 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

SC injection

DNTH103 (Optional OLE)

DNTH103 SC once every 2 weeks for up to 104 weeks.

Group Type EXPERIMENTAL

DNTH103

Intervention Type DRUG

SC injection

Interventions

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DNTH103

IV Infusion

Intervention Type DRUG

DNTH103

SC injection

Intervention Type DRUG

Placebo

SC injection

Intervention Type DRUG

Other Intervention Names

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Claseprubart Claseprubart

Eligibility Criteria

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Inclusion Criteria

1. Must have given written informed consent before any study-related activities are carried out.
2. Weight range between 40 kilograms (kg) and 120 kg.
3. Confirmed diagnosis of CIDP or possible CIDP. Participants must have either typical CIDP or one of the following variants: motor or multifocal CIDP. Diagnosis must be confirmed by the Independent CIDP Review Panel.
4. CIDP Disease Activity Status (CDAS) score ≥ 3 at screening.
5. Must be neurologically stable.
6. Must have an INCAT score between 2 and 9 inclusive.
7. Must fulfill one of the following treatment conditions for CIDP:

1. Currently treated with and responded to immunoglobulin (Ig) (intravenous immunoglobulin \[IVIg\] or subcutaneous immunoglobulin \[SCIg\]) alone or Ig (IVIg or SCIg) plus oral corticosteroids, or previously treated with and responded to, but are no longer being treated with (eg, lost access to), a maintenance regimen of Ig (IVIg or SCIg) alone or Ig (IVIg or SCIg) plus oral corticosteroids.
2. Currently treated with and responded to oral corticosteroids alone or oral corticosteroids in combination with azathioprine or mycophenolate mofetil.
3. Refractory participants who have had treatment failure (worsening) or an inadequate response to Ig and/or oral corticosteroids (defined as no clinically meaningful improvement after a period of a minimum of 12 weeks, which may include both active treatment and observation to assess response), or who at any time were unable to tolerate these treatments, experienced adverse effects, or have documented contraindications.
4. Treatment naïve with no history of prior treatment for CIDP.
8. Documented vaccinations against encapsulated bacteria in accordance with local requirements and vaccine availability.
9. Female participants must be of nonchildbearing potential or if of childbearing potential, must agree not to donate ova, not to attempt to become pregnant and, if engaging in sexual intercourse with a male partner, must agree to use a highly effective method of contraception.
10. Male participants must be surgically sterile for at least 90 days prior to Screening or agree not to donate sperm and, if engaging in sexual intercourse with a female partner who could become pregnant, must agree to use an acceptable method of contraception.

Exclusion Criteria

1. Clinical signs or symptoms suggestive of polyneuropathy of causes other than CIDP.
2. Known evidence of central demyelination or known history of myelopathy.
3. History or presence of significant medical/surgical condition including any acute illness or major surgery considered to be clinically significant or that could have a potential impact on safety/efficacy or study procedures.
4. Any other condition, including mental illness or prior therapy that would make the participant unsuitable for this study.
5. Known complement deficiency or history of positive titer for anti-C1 antibodies.
6. Diagnosis of systemic lupus erythematosus (SLE) or family history of SLE (defined as a parent, sibling, or child).
7. Participants with an autoimmune disease affecting joints, muscle or nervous system.
8. Any coexisting or overlapping condition, which may interfere with outcome assessments, such as severe diabetic neuropathy, fibromyalgia, inflammatory arthritis or osteoarthritis affecting the hands and feet.
9. Prior history of N. meningitidis infection.
10. History of active malignancy within 5 years prior to screening, except basal cell carcinoma of the skin, curatively resected squamous cell carcinoma of the skin, cervical carcinoma in situ curatively treated or low-grade prostate adenocarcinoma for which appropriate management is observation alone.
11. Positive test results for active human immunodeficiency virus (HIV-1 or HIV-2), hepatitis B surface antigen (HBsAg), or hepatitis C virus (HCV) antibodies.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Dianthus Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clinical Study Site

Birmingham, Alabama, United States

Site Status RECRUITING

Clinical Study Site

Phoenix, Arizona, United States

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Clinical Study Site

Scottsdale, Arizona, United States

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Clinical Study Site

Los Angeles, California, United States

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San Francisco, California, United States

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San Francisco, California, United States

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Washington D.C., District of Columbia, United States

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Clinical Study Site

Maitland, Florida, United States

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Tampa, Florida, United States

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Honolulu, Hawaii, United States

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Chicago, Illinois, United States

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Edwardsville, Illinois, United States

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Indianapolis, Indiana, United States

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Kansas City, Kansas, United States

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Burlington, Massachusetts, United States

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East Lansing, Michigan, United States

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Omaha, Nebraska, United States

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New York, New York, United States

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New York, New York, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Portland, Oregon, United States

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Dallas, Texas, United States

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Clinical Study Site

Denton, Texas, United States

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Cinical Study Site

Houston, Texas, United States

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Texas Locations

Houston, Texas, United States

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Round Rock, Texas, United States

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Clinical Study Site

Sugar Land, Texas, United States

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Seattle, Washington, United States

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Cinical Study Site

Buenos Aires, Buenos Aires, Argentina

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Cinical Study Site #3

Buenos Aires, , Argentina

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Cinical Study Site #4

Buenos Aires, , Argentina

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Clinical Study Site #2

Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Cinical Study Site #2

San Miguel de Tucumán, , Argentina

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San Miguel de Tucumán, , Argentina

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Randwick, New South Wales, Australia

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Melbourne, Victoria, Australia

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Rio de Janeiro, Rio de Janeiro, Brazil

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Natal, , Brazil

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Salvador, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Hefei, Anhui, China

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Guangzhou, Guangdong, China

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Changsha, Hu'Nan, China

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Changsha, Hu'Nan, China

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Wuhan, Hubei, China

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Chifeng, Inner Mongolia, China

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Suzhou, Jiangsu, China

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Beijing, , China

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Beijing, , China

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Chengdu, , China

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Fujian, , China

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Guangdong, , China

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Guangzhou, , China

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Jilin, , China

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Shanghai, , China

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Shanghai, , China

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Sichuan, , China

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Taiyuan, , China

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Wuhan, , China

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Aarhus, , Denmark

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Copenhagen, , Denmark

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Bordeaux, , France

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Brest, , France

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Bron, , France

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Clermont-Ferrand, , France

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Libourne, , France

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Marseille, , France

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Nice, , France

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Paris, , France

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Paris, , France

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Strasbourg, , France

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Tours, , France

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Tours, , France

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Tbilisi, , Georgia

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Sande, Lower Saxony, Germany

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Aachen, , Germany

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Greifswald, , Germany

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Rüdersdorf, , Germany

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Sande, , Germany

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Bergamo, , Italy

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Bologna, , Italy

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Genova, , Italy

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Gussago, , Italy

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Milan, , Italy

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Pavia, , Italy

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Ponderano, , Italy

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Roma, , Italy

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Clinical Study Site #2

Roma, , Italy

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Roma, , Italy

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Riga, , Latvia

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Riga, , Latvia

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George Town, , Malaysia

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Johor Bahru, , Malaysia

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Kuala Lumpur, , Malaysia

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Kuala Lumpur, , Malaysia

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Kuala Lumpur, , Malaysia

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Utrecht, , Netherlands

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Bydgoszcz, , Poland

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Krakow, , Poland

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Lublin, , Poland

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Lublin, , Poland

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Lublin, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Bucharest, , Romania

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Belgrade, , Serbia

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Belgrade, , Serbia

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Kragujevac, , Serbia

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Niš, , Serbia

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Cinical Study Site

Daegu, , South Korea

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Cinical Study Site

Daejeon, , South Korea

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Cinical Study Site #2

Seoul, , South Korea

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Cinical Study Site #3

Seoul, , South Korea

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Cinical Study Site

Seoul, , South Korea

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Cinical Study Site

Yangsan, , South Korea

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Clinical Study Site

Barcelona, Barcelona, Spain

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Clinical Study Site

Alicante, , Spain

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Clinical Study Site

Barcelona, , Spain

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Cinical Study Site

Barcelona, , Spain

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Clinical Study Site

Bilbao, , Spain

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Clinical Study Site

Oxford, , United Kingdom

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Countries

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United States Argentina Australia Brazil Bulgaria China Denmark France Georgia Germany Italy Latvia Malaysia Netherlands Poland Romania Serbia South Korea Spain United Kingdom

Central Contacts

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Dianthus Clinical Contact Center

Role: CONTACT

929-999-4055

Other Identifiers

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2024-517529-26

Identifier Type: OTHER

Identifier Source: secondary_id

DNTH103-CIDP-301

Identifier Type: -

Identifier Source: org_study_id

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