Ricolinostat in Patients With Painful Diabetic Peripheral Neuropathy

NCT ID: NCT03176472

Last Updated: 2023-09-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

282 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-07

Study Completion Date

2023-04-28

Brief Summary

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This is a randomized, double-blind, 2-arm, parallel group study of up to 274 evaluable patients designed to evaluate the safety and efficacy of the histone deacetylase 6 (HDAC6) inhibitor ricolinostat for painful DPN.

Detailed Description

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The study includes an approximately 12 week randomized, double-blind, placebo controlled Treatment period in which patients will receive either ricolinostat or placebo, followed by an approximately 12 week open label Safety Extension period during which all patients will receive ricolinostat 120 mg daily.

Prior to randomization, patients will be enrolled in a baseline Pain Observation period from Day -14 to Day -1, during which the NRS (average and worst pain) will be recorded daily using an electronic daily diary that will be completed by patients to allow patients to familiarize themselves with the pain rating procedures, and to establish a baseline and confirm eligibility to participate. Patients will also initiate daily dosing during this time to evaluate compliance eligibility for participation. A daily diary will be used by the patient to record the pain assessments and rescue medication use. A follow-up phone contact will be conducted at Day -7 to Day -5 to review diary and dosing compliance.

Following the baseline Pain Observation period, patients who meet entry criteria will be randomized in a 1:1 ratio to receive either ricolinostat or placebo. During the 12-week double-blind, placebo-controlled Treatment period, patients will return for assessments in accordance with the schedule of assessments. At the conclusion of the approximately 12 week open label Safety Extension period, patients will enter a Follow-up safety washout and assessment period, which will incorporate 2 visits at approximately 2 and 4 weeks following the final Safety Extension visit, with assessments performed as outlined in the schedule of assessments.

Conditions

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Painful Diabetic Peripheral Neuropathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Randomized, Double-Blind, Placebo-Controlled, Parallel Group Study
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
double-blind

Study Groups

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ricolinostat

Ricolinostat 120 mg, taken once daily (QD) by mouth; each dose in 12 mL liquid formulation (10 mg ricolinostat per mL)

Group Type EXPERIMENTAL

ricolinostat

Intervention Type DRUG

120 mg per dose in 12 mL liquid formulation

placebo

Placebo, 12 mL of liquid formulation with no active ingredient (i.e., ricolinostat), taken once daily (QD) by mouth

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

12 mL liquid formulation placebo

Interventions

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ricolinostat

120 mg per dose in 12 mL liquid formulation

Intervention Type DRUG

Placebo

12 mL liquid formulation placebo

Intervention Type DRUG

Other Intervention Names

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ACY-1215

Eligibility Criteria

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Inclusion Criteria

* Type 1 or Type 2 diabetes of at least 6 months with optimized and stable glycemic control during the 3 months prior to Screening
* Painful distal symmetric sensorimotor polyneuropathy due to diabetes
* Douleur Neuropathique 4 (DN4) score of ≥4
* Satisfactory diary data during the 14-day Pain Observation period determined by an algorithm that includes diary compliance, overall level of pain and day-to-day variability in pain

Exclusion Criteria

* Pregnant or lactating
* Body Mass Index (BMI) \>40 kg/m2
* Presence of any neuropathy other than DPN and/or significant risk factors for neuropathy other than diabetes
* Other pain conditions that could confound the results of this study, or other chronic pain condition(s) that could affect compliance with pain medication restrictions or confound pain assessments
* Painful DPN patients who have undergone lower limb amputations, are non-ambulatory, or whose walking is so impaired as to require a walker or other assistance for ambulation
* Have met Diagnostic and Statistical Manual of Mental Disorders V (DSM V) criteria for opioid use disorder or alcohol use disorder
* Opioid use at a dose of ≥ 30 morphine milligram equivalents on 3 or more days a week during the month prior to Screening
* Suicidal ideation/behavior as measured by the Columbia-Suicide Severity Rating Scale (C-SSRS)
* The use of marijuana or cannabidiol (CBD) during the 30 days prior to starting study drug
* Chronic use of over-the-counter capsaicin on extremities within 3 months of Screening and/or prescription Qutenza use within 6 months of Screening
* Corrected QT interval at Screening using QTcF of ≥450 msec (male) or ≥460 msec (female)
* Hemoglobin \< 11.5 g/dL (female) or \< 13 g/dL (male), total white blood cell count \< 2500/mm3, neutrophil count \< 1250/mm3, lymphocyte count \< 1000/mm3, or platelet count \< 100,000/mm3
* HIV positive and/or active hepatitis virus (A, B, or C) infection
* Current or previous (≤1 month of Screening) enrollment in a clinical trial involving treatment with an investigational product
* Any known recent exposure within the 14 days prior to initial Screening to coronavirus disease 2019 (COVID-19) or symptoms of COVID-19 infection or other reason to suspect COVID-19 infection as assessed by the Investigator at the time of initial Screening
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Regenacy Pharmaceuticals LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Pinnacle Research Group LLC

Anniston, Alabama, United States

Site Status

Arizona Research Center

Phoenix, Arizona, United States

Site Status

Diabetes/Lipid Management & Research Center

Huntington Beach, California, United States

Site Status

National Research Institute

Huntington Park, California, United States

Site Status

Altman Clinical and Translational Research Institute

La Jolla, California, United States

Site Status

Torrance Clinical Research Institute Inc

Lomita, California, United States

Site Status

Providence Clinical Research

North Hollywood, California, United States

Site Status

Center for Clinical Research Inc

San Francisco, California, United States

Site Status

Diablo Clinical Research Inc

Walnut Creek, California, United States

Site Status

Innovative Research of West Florida Inc

Clearwater, Florida, United States

Site Status

DeLand Clinical Research Unit

Lake Mary, Florida, United States

Site Status

ClinCloud LLC

Maitland, Florida, United States

Site Status

APF Research LLC

Miami, Florida, United States

Site Status

International Research Associates LLC

Miami, Florida, United States

Site Status

Sensible Healthcare LLC

Ocoee, Florida, United States

Site Status

Progressive Medical Research

Port Orange, Florida, United States

Site Status

Meridien Research

Tampa, Florida, United States

Site Status

Metabolic Research Institute Inc

West Palm Beach, Florida, United States

Site Status

Physicians Research Associates, LLC

Lawrenceville, Georgia, United States

Site Status

Rocky Mountain Clinical Research

Idaho Falls, Idaho, United States

Site Status

MediSphere Medical Research Center, LLC

Evansville, Indiana, United States

Site Status

Tandem Clinical Research

Marrero, Louisiana, United States

Site Status

Olive Branch Family Medical Center

Olive Branch, Mississippi, United States

Site Status

Advanced Biomedical Research of America

Las Vegas, Nevada, United States

Site Status

Hassman Research Institute

Berlin, New Jersey, United States

Site Status

NY Scientific

Brooklyn, New York, United States

Site Status

Triad Clinical Trials

Greensboro, North Carolina, United States

Site Status

The Center for Clinical Research

Winston-Salem, North Carolina, United States

Site Status

Coastal Carolina Research Center

North Charleston, South Carolina, United States

Site Status

Palmetto Clinical Research

Summerville, South Carolina, United States

Site Status

FutureSearch Trials of Neurology

Austin, Texas, United States

Site Status

Nerve and Muscle Center of Texas

Houston, Texas, United States

Site Status

Sun Research Institute

San Antonio, Texas, United States

Site Status

Diabetes & Glandular Disease Clinic, P.A.

San Antonio, Texas, United States

Site Status

Wasatch Clinical Research LLC

Salt Lake City, Utah, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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REGY-DN-201

Identifier Type: -

Identifier Source: org_study_id

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