A Study of an FGFR2/3 Inhibitor (CGT4859) in Patients With Cholangiocarcinoma and Other Advanced Solid Tumors

NCT ID: NCT06777316

Last Updated: 2025-07-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

110 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-01-22

Study Completion Date

2027-06-30

Brief Summary

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This is an open-label, phase 1/2 study evaluating the safety, tolerability, pharmacokinetic (what the body does to the drug), pharmacodynamic (what the drug does to the body), and antitumor activity of CGT4859 in adult participants with intrahepatic cholangiocarcinoma (iCCA) or other advanced solid tumors with FGFR2 and/or FGFR3 genetic alternations.

Detailed Description

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Conditions

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Intrahepatic Cholangiocarcinoma (Icc) Cholangiocarcinoma Other Solid Tumors, Adult FGFR2 Gene Fusion/Rearrangement FGFR2 Gene Amplification FGFR2 Gene Short Variants FGFR3 Gene Fusion/Rearrangement FGFR3 Gene Amplification FGFR3 Gene Short Variants FGFR2 Genetic Alterations FGFR3 Genetic Alterations Advanced Solid Tumors

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Phase 1 will evaluate multiple ascending doses until the highest safe dose and the recommended phase 2 dose (RP2D) are determined.

Phase 2 will evaluate the RP2D in 4 cohorts defined by tumor type and prior therapy based on Phase 1 results.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Phase 1: Dose Escalation

Multiple doses of CGT4859 for oral administration

Group Type EXPERIMENTAL

CGT4859

Intervention Type DRUG

CGT4859 is a selective FGFR2/3 inhibitor

Phase 2: Signal Seeking

Oral dose of CGT4859 at the RP2D as determined in Phase 1

Group Type EXPERIMENTAL

CGT4859

Intervention Type DRUG

CGT4859 is a selective FGFR2/3 inhibitor

Interventions

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CGT4859

CGT4859 is a selective FGFR2/3 inhibitor

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Histologically confirmed locally advanced, metastatic, and/or unresectable iCCA or other solid tumor with documented FGFR2/3 alteration in blood and/or tumor.
2. Previously treated with, not appropriate for, or declined standard-of-care first-line treatment.
3. Have measurable disease per RECIST v1.1.
4. Eastern Cooperative Oncology Group (ECOG) performance status of 0-1.
5. Have clinically acceptable local laboratory screening results (clinical chemistry and hematology) within certain limits.
6. Resolution of toxicities from prior therapy to ≤Grade 1 (or baseline), including resolution of clinically significant laboratory abnormalities, before the first dose of study drug. Exceptions are alopecia, hypothyroidism, or type 1 diabetes mellitus controlled with medical intervention, and paronychia controlled with local intervention.

Exclusion Criteria

1. Received chemotherapy or anticancer therapies or radiotherapy within certain timeframes before first dose of study drug.
2. Major surgeries (eg, abdominal laparotomy) within 4 weeks of the first dose of study drug.
3. Clinically significant corneal or retinal disorders or current evidence of retinal detachment.
4. Received more than 2 prior FGFRi therapies
5. Active, symptomatic, or untreated brain metastases unless the participant is clinically stable and off corticosteroids for ≥2 months.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cogent Biosciences, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Mayo Clinic Scottsdale

Scottsdale, Arizona, United States

Site Status RECRUITING

Stanford Cancer Institute

Palo Alto, California, United States

Site Status RECRUITING

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status RECRUITING

Moffitt Cancer Center

Tampa, Florida, United States

Site Status RECRUITING

University of Chicago Medicine Comprehensive Cancer Center

Chicago, Illinois, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

The Christ Hospital

Cincinnati, Ohio, United States

Site Status RECRUITING

Taussig Cancer Center - Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Fox Chase cancer Center

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Tennessee Oncology

Nashville, Tennessee, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Huntsman Cancer Institute - University of Utah

Salt Lake City, Utah, United States

Site Status RECRUITING

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status RECRUITING

Princess Margaret Cancer Centre - UHN

Toronto, Ontario, Canada

Site Status RECRUITING

Countries

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United States Canada

Central Contacts

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Cogent Biosciences, Inc.

Role: CONTACT

617-945-5576

Other Identifiers

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CGT4859-24-101

Identifier Type: -

Identifier Source: org_study_id

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