Study of Futibatinib in Patients With Advanced Cholangiocarcinoma With FGFR2 Fusion or Rearrangement

NCT ID: NCT05727176

Last Updated: 2025-12-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

120 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-07-05

Study Completion Date

2026-12-31

Brief Summary

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This is an open-label, multinational, randomized Phase 2 study confirming the clinical benefit of 20 mg futibatinib and evaluating the safety and efficacy of 16 mg futibatinib in previously treated CCA harboring FGFR2 gene fusions and other rearrangements.

Detailed Description

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This is an open-label, multinational, randomized Phase 2 study confirming the clinical benefit of 20 mg futibatinib and evaluating the safety and efficacy of 16 mg futibatinib in previously treated CCA harboring FGFR2 gene fusions and other rearrangements. Eligible patients will be randomized on a 1:1 basis to the following study arms:

* Patients will receive futibatinib at an oral dose of 16 mg, administered daily (QD) on every day of a 21-day cycle.
* Patients will receive futibatinib at an oral dose of 20 mg, administered daily (QD) on every day of a 21-day cycle.

Patients may continue to receive continuous futibatinib until documentation of progressive disease (PD) per RECIST 1.1, or until other withdrawal criteria are met, whichever comes first.

Conditions

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Advanced Cholangiocarcinoma FGFR2 Fusions Gene Rearrangement

Keywords

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Futibatinib Advanced cholangiocarcinoma cholangiocarcinoma FGFR2 Fusion Rearrangemen TAS-120

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Treatment Arm A

TAS-120 (20mg) tablets, oral; 21-day cycle

Group Type EXPERIMENTAL

TAS-120

Intervention Type DRUG

TAS-120 is an oral FGFR inhibitor

Treatment Arm B

TAS-120 (16mg) tablets, oral; 21-day cycle

Group Type EXPERIMENTAL

TAS-120

Intervention Type DRUG

TAS-120 is an oral FGFR inhibitor

Interventions

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TAS-120

TAS-120 is an oral FGFR inhibitor

Intervention Type DRUG

Other Intervention Names

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Futibatinib

Eligibility Criteria

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Inclusion Criteria

1. Histologically or cytologically confirmed, locally advanced, metastatic, or unresectable intrahepatic of extrahepatic Cholangiocarcinoma.
2. Documented evidence of FGFR2 gene fusions or other FGFR2 rearrangement
3. Received at least one prior systemic gemcitabine and platinum-based regimen for CCA
4. Documentation of radiographic disease progression on the most recent prior therapy
5. Measurable disease
6. performance status 0 or 1
7. Adequate organ function

Exclusion Criteria

1. History or current evidence of calcium and phosphate homeostasis disorder
2. Current evidence of clinically significant retinal disorder
3. Treatment with any of the following within the specified time frame prior to the first dose of futibatinib:

1. Major surgery within the previous 4 weeks (the surgical incision should be fully healed prior to the first dose of futibatinib) and radiotherapy for extended field within 4 weeks or limited field radiotherapy within 2 weeks
2. Patients with locoregional therapy, eg, transarterial chemoembolization (TACE), selective internal radiotherapy (SIRT) or ablation within 4 weeks
3. Any non investigational anticancer therapy within 3 weeks or have not recovered from side effects of such therapy prior to futibatinib. Endocrine therapy is allowed for patients with breast or prostate cancer
4. Targeted therapy or immunotherapy within 3 weeks or within 5 half lives Any investigational agent received within 5 half-lives of the drug or 4 weeks, whichever is shorter.
5. Patients with prior FGFR-directed therapy
4. A serious illness or medical condition(s) including (but not limited to) the following:

1. Known brain metastasis (not including primary brain tumors) unless patient is clinically stable for ≥1 month
2. Known acute systemic infection
3. Myocardial infarction, severe/unstable angina, symptomatic congestive heart failure (New York Heart Association \[NYHA\] Class III or IV New York Heart Association \[NYHA\] Classification) within the previous 2 months; if \>2 months, cardiac function must be within normal limits and the patient must be free of cardiac-related symptoms
4. Significant gastrointestinal disorder(s) that could interfere with the absorption of futibatinib.
5. Other severe acute or chronic medical or psychiatric condition or laboratory abnormality that in the judgment of the Investigator would make the patient inappropriate for entry into this study.
5. Known additional malignancy that is progressing or requires active treatment, with the exception of patients with a prior or concurrent malignancy whose natural history or treatment does not have the potential to interfere with the safety or antitumor assessment of the investigational regimen. Exceptions must be discussed with the Sponsor prior to patient enrollment.
6. Pregnant or lactating female.
7. Known hypersensitivity or severe reaction to futibatinib or its excipients.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Taiho Oncology, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of California San Diego UCSD - Moores Cancer Center

La Jolla, California, United States

Site Status RECRUITING

Tampa General Hospital Cancer Institute

Tampa, Florida, United States

Site Status RECRUITING

Henry Ford Health System

Detroit, Michigan, United States

Site Status RECRUITING

Gabrail Cancer Center Research

Canton, Ohio, United States

Site Status WITHDRAWN

Texas Oncology

Abilene, Texas, United States

Site Status RECRUITING

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, United States

Site Status RECRUITING

Texas Oncology Methodist DFW

Dallas, Texas, United States

Site Status RECRUITING

Texas Onc Methodist (Charlton)

Dallas, Texas, United States

Site Status RECRUITING

Texas Oncology - Northeast

Denton, Texas, United States

Site Status RECRUITING

Center for Oncology and Blood Disorders

Houston, Texas, United States

Site Status WITHDRAWN

Hospital Britanico

Buenos Aires, , Argentina

Site Status RECRUITING

CEMIC

CABA, , Argentina

Site Status RECRUITING

Sanatorio de la Mujer

Rosario, , Argentina

Site Status RECRUITING

St Vincent's Hospital Sydney - The Kinghorn Cancer Centre

Sydney, New South Wales, Australia

Site Status RECRUITING

Alfred Health, Medical Oncology Unit, Second floor William Buckland Radiotherapy Center

Melbourne, Victoria, Australia

Site Status RECRUITING

St John of God Subiaco Hospital

Subiaco, Western Australia, Australia

Site Status RECRUITING

Instituto do Cancer do Estado de Sao Paulo

Cerqueira César, , Brazil

Site Status RECRUITING

IOP - Instituto de Oncologia do Parana

Curitiba, , Brazil

Site Status RECRUITING

Hospital Erasto Gaertner

Curitiba, , Brazil

Site Status RECRUITING

Hospital de Base de Sao Jose do Rio Preto

São José do Rio Preto, , Brazil

Site Status RECRUITING

Fundacao Antonio Prudente - A.C.Camargo Cancer Center

São Paulo, , Brazil

Site Status RECRUITING

Grand River Hospital - Grand River Regional Cancer Centre (GRRCC)

Kitchener, OH, Canada

Site Status RECRUITING

Sunnybrook Health Sciences Center

Toronto, OH, Canada

Site Status RECRUITING

University of Toronto

Toronto, OH, Canada

Site Status RECRUITING

McGill University Health Center

Montreal, Quebec, Canada

Site Status RECRUITING

Guangdong Provincial People's Hospitall

Guangzhou, Guangdong, China

Site Status RECRUITING

Harbin Medical University - Cancer Hospital

Harbin, Heilongjiang, China

Site Status RECRUITING

Jiangsu Provance Hospital

Nanjing, Jiangsu, China

Site Status NOT_YET_RECRUITING

Jilin Cancer Hospital

Changchun, Jilin, China

Site Status RECRUITING

Shandong University - Shandong Cancer Hospital

Jinan, Shandong, China

Site Status RECRUITING

Zhongahan Hospital Fudan unversity

Shanghai, Shanghai Municipality, China

Site Status NOT_YET_RECRUITING

West China Hospital- Sichuan University

Chengdu, Sichuan, China

Site Status RECRUITING

Sir Run Run Shaw Hospital, Zhejiang University

Hangzhou, Zhejiang, China

Site Status RECRUITING

Shanghai Gobroad Cancer Hospital China Pharmaceutical University

Shanghai, , China

Site Status RECRUITING

Tongji University Shanghai East Hospital

Shanghai, , China

Site Status RECRUITING

The University of Hong Kong

Hong Kong Island, , Hong Kong

Site Status RECRUITING

The Chinese University of Hong Kong Prince of Wales Hospital

New Territories, , Hong Kong

Site Status RECRUITING

Policlinico S. Orsola-Malpighi

Bologna, , Italy

Site Status RECRUITING

IRCCS Humanitas Research Hospital

Rozzano, , Italy

Site Status RECRUITING

AOUI Verona - Ospedale Borgo Roma

Verona, , Italy

Site Status RECRUITING

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status RECRUITING

National Cancer Center Hospital East

Kashiwa-Shi, , Japan

Site Status RECRUITING

Nagasaki University Hospital

Nagasaki, , Japan

Site Status RECRUITING

Nagoya University Hospital

Nagoya, , Japan

Site Status RECRUITING

Osaka Metropolitan University Hospital

Osaka-Fu, , Japan

Site Status RECRUITING

Szpital Wojewdzki w Koszalinie im. Mikoaja Kopernika

Koszalin, , Poland

Site Status WITHDRAWN

Centrum Onkologii Ziemi Lubelskiej im. w. Jana z Dukli

Lublin, , Poland

Site Status WITHDRAWN

Europejskie Centrum Zdrowia Otwock Sp. Z.o.o.

Otwock, , Poland

Site Status RECRUITING

Centrum Onkologii-Instytut im. Marii Skłodowskiej - Curie

Warsaw, , Poland

Site Status RECRUITING

Fundação Champalimaud

Lisbon, , Portugal

Site Status RECRUITING

Centro Hospitalar Lisboa Norte CHLN EPE - Hospital de Santa Maria

Lisbon, , Portugal

Site Status RECRUITING

Inje University Haeundae Paik Hospital

Busan, , South Korea

Site Status RECRUITING

Dong-A University Hospital

Busan, , South Korea

Site Status WITHDRAWN

Kyungpook National University Hospital

Daegu, , South Korea

Site Status RECRUITING

Gyeongsang National University Hospital

Jinju, , South Korea

Site Status RECRUITING

CHA Bundang Medical Center

Seongnam, , South Korea

Site Status RECRUITING

Yonsei University Health System - Severance Hospital

Seoul, , South Korea

Site Status RECRUITING

The Catholic University of Korea, St. Mary's Hospital

Seoul, , South Korea

Site Status RECRUITING

Hospital Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Institut Català d'Oncologia de l'Hospitalet de Llobregat - Hospital Duran i Reynals

Barcelona, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status RECRUITING

Clinica Universidad de Navarra, Medical Oncology Service (Mariano Ponz Sarvise)

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Fundación Jimenez Díaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario 12 de octubre

Madrid, , Spain

Site Status RECRUITING

Clinica Universidad de Navarra

Pamplona, , Spain

Site Status RECRUITING

Countries

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Taiwan United States Argentina Australia Brazil Canada China Hong Kong Italy Japan Poland Portugal South Korea Spain

Central Contacts

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Taiho Oncology, INC

Role: CONTACT

Phone: +1 844-878-2446

Email: [email protected]

Facility Contacts

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Susumu Eguchi

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Other Identifiers

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2023-503665-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2022-9400

Identifier Type: OTHER

Identifier Source: secondary_id

TAS-120-205

Identifier Type: -

Identifier Source: org_study_id