A Phase I Study of GC33 in Advanced or Metastatic Liver Cancer (Hepatocellular Carcinoma)

NCT ID: NCT00746317

Last Updated: 2012-10-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

27 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-09-30

Study Completion Date

2012-10-31

Brief Summary

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This phase I trial is studying the safety and best dose of GC33 in patients with advanced or metastatic liver cancer.

Detailed Description

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This is a Phase I open-label dose escalation study of GC33 in patients with advanced or metastatic HCC. This study is designed to evaluate safety, tolerability, pharmacokinetics, and preliminary assessment of anti-tumor activity. Enrollment will proceed until a maximum tolerated dose (MTD) and a recommended Phase II dose has been established.

Conditions

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Advanced or Metastatic HCC

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

Group Type EXPERIMENTAL

GC33

Intervention Type DRUG

IV administration at 4 escalating dose levels.

Interventions

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GC33

IV administration at 4 escalating dose levels.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Signed written Institutional Review Board (IRB)/Ethical Committee (EC) approved informed consent form
* Male or female ≥ 18 years old.
* Life expectancy ≥ 3 months.
* ECOG Performance Status of 0-1.
* Histologically confirmed hepatocellular carcinoma (without fibrolamellar subtype).
* Not a candidate for curative treatments.
* Child-Pugh A or B.
* Hematological, Biochemical and Organ Function:

* AST (SGOT): ≤ 5.0 × ULN
* ALT (SGPT): ≤ 5.0 × ULN
* Total Bilirubin: ≤ 3.0 × ULN
* Platelets: ≥ 50,000/μL
* Absolute Neutrophil Count: ≥ 1,500/μL
* Serum creatinine: ≤ 2.0 × ULN
* PT-INR: ≤ 2.0,
* Ability to provide a tumor tissue sample either by:

* a sample obtained within 3 months prior to informed consent for HCC diagnosis. Resection samples are not acceptable.
* undergo a biopsy to confirm HCC diagnosis
* At least one measurable lesion based on Response Evaluation Criteria In Solid Tumors criteria.

(Extension Phase)

* Signed written Institutional Review Board (IRB)/Ethical Committee (EC) approved informed consent form.
* Male or female ≥ 18 years old.
* Life expectancy ≥ 3 months.
* ECOG Performance Status of 0-1.
* Histologically confirmed hepatocellular carcinoma (without fibrolamellar subtype).
* Not a candidate for curative treatments.
* Child-Pugh A.
* Hematological, Biochemical and Organ Function:

* AST (SGOT): ≤ 5.0 × ULN
* ALT (SGPT): ≤ 5.0 × ULN
* Total Bilirubin: ≤ 3.0 × ULN
* Platelets: ≥ 50,000/μL
* Absolute Neutrophil Count: ≥ 1,500/μL
* Serum creatinine: ≤ 2.0 × ULN
* PT-INR: ≤ 2.0
* IHC confirmed GPC3-positive HCC tumor tissue. Tumor tissue sample may be provided by:

* A formalin fixed paraffin embedded block sample within 12 months prior to informed consent for HCC diagnosis;
* Unstained slides obtained within 3 months prior to informed consent for HCC diagnosis;
* Undergo biopsy to confirm GPC3-positive HCC.
* Resection samples are not acceptable.
* At least one measurable lesion based on Response Evaluation Criteria In Solid Tumors criteria.

Exclusion Criteria

* Child-Pugh C.
* Pregnant or lactating women or women of child-bearing potential and men of childbearing potential not willing to use effective means of contraception.
* Patients known to be positive for Human immunodeficiency virus infection.
* Active infectious diseases requiring treatment except for hepatitis B and C.
* Other malignancies within the last 5 years.
* History of transplantation (organ, bone marrow transplantation,peripheral blood stem cell transplantation, etc.).
* Patients with significant concomitant disease determined by the investigator to be potentially aggravated by the investigational drug.
* Patients with brain metastases, other central nervous system or other psychiatric disease.
* Patients who received major surgery, local therapy for HCC, chemotherapy, radiotherapy, hormone-therapy, immunotherapy, or another investigational drug within 4 weeks prior to Day 1.
* Patients who received the following treatments within 2 weeks prior to Day1:

* Anticoagulant or thrombolytic agents for therapeutic purposes.
* Systemic anti-viral therapy for hepatitis C/cirrhosis.
* Blood transfusion
* History of hypersensitivity to similar agents.
* Patient is unable to comply with the requirements of the protocol and/or follow-up procedures.

(Extension Phase)

* Child-Pugh B or C.
* Pregnant or lactating women or women of child-bearing potential and men of childbearing potential not willing to use effective means of contraception.
* Patients known to be positive for Human immunodeficiency virus infection.
* Active infectious diseases requiring treatment except for hepatitis B and C.
* Other malignancies within the last 5 years.
* History of transplantation (organ, bone marrow transplantation, Peripheral blood stem cell transplantation, etc.).
* Patients with significant concomitant disease determined by the investigator to be potentially aggravated by the investigational drug.
* Patients with brain metastases, other central nervous system or other psychiatric disease.
* Patients who received major surgery, local therapy for HCC, chemotherapy, radiotherapy, hormone-therapy, immunotherapy, or another investigational drug within 4 weeks prior to Day 1.
* Patients who received the following treatments within 2 weeks prior to Day 1:

* Anticoagulations or thrombolytic agents for therapeutic purposes.
* Systemic anti-viral therapy for hepatitis C/cirrhosis.
* Blood transfusion
* History of hypersensitivity to similar agents.
* Patient is unable to comply with the requirements of the protocol and/or follow-up procedures.
* IHC confirmed GPC3-negative HCC tumor tissue.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Chugai Pharmaceutical

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Toshihiko Ohtomo

Role: STUDY_CHAIR

Chugai Pharmaceutical

Locations

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USC/Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Karmanos Cancer Center at the Detroit Medical Center

Detroit, Michigan, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Methodist Hospital

Houston, Texas, United States

Site Status

Swedish Cancer Institute at the Swedish Medical Center

Seattle, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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GC-001US

Identifier Type: -

Identifier Source: org_study_id