A Phase 2 Study of NEU-411 in Companion Diagnostic-Positive Participants With Early Parkinson's Disease

NCT ID: NCT06680830

Last Updated: 2026-01-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

150 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-01-17

Study Completion Date

2027-09-30

Brief Summary

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The goal of this Phase 2 clinical trial is to investigate the efficacy and safety of NEU-411 in men and women aged 40-80 years with early Parkinson's Disease (PD) who have predicted elevations in the activity of the "leucine-rich repeat kinase 2" ("LRRK2" for short) pathway based on their genetic profile. A DNA test will be used to identify the "LRRK2-driven" population with predicted elevation in the LRRK2 pathway.

Participants will:

• Take NEU-411 or placebo every day for 52 weeks

Detailed Description

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NEU-411-PD201 is a Phase 2, randomized, placebo-controlled, proof-of-concept study in participants with early Parkinson's Disease (PD) who have LRRK2-driven PD as measured by an investigational companion diagnostic genetic test (CDx). The study will evaluate the efficacy, safety, pharmacokinetics, and pharmacodynamics of NEU-411, an orally-administered, potent, selective, bioavailable, highly permeable, brain penetrant, small molecule inhibitor of LRRK2 activity as compared to placebo.

After participants are screened for inclusion in the study, approximately 150 participants will be randomized in a 1:1 allocation ratio to NEU-411 30 mg once per day or placebo for a 52-week treatment period. A safety follow-up visit will occur 2 weeks after the last treatment visit.

Conditions

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Parkinson Disease Parkinson Idiopathic Parkinson Disease Early Parkinson Disease (Early PD) Parkinson Disease, Idiopathic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
The Sponsor is also masked.

Study Groups

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NEU-411

Orally-administered NEU-411

Group Type EXPERIMENTAL

NEU-411

Intervention Type DRUG

NEU-411, a potent, selective, orally bioavailable, highly permeable, brain penetrant, small molecule inhibitor of LRRK2 activity

Placebo

Orally-administered matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Orally-administered matched placebo

Interventions

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NEU-411

NEU-411, a potent, selective, orally bioavailable, highly permeable, brain penetrant, small molecule inhibitor of LRRK2 activity

Intervention Type DRUG

Placebo

Orally-administered matched placebo

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Aged 40-80 years at time of screening, inclusive
2. Diagnosis of clinically established or clinically probable Parkinson's Disease (PD)
3. LRRK2-driven PD using the investigational companion diagnostic genetic test (CDx)
4. Modified Hoehn and Yahr (mH\&Y) of 1 to 2.5

Exclusion Criteria

1. Secondary or atypical parkinsonian syndromes
2. Uncontrolled diabetes mellitus with hemoglobin A1c (HbA1c) \>8%
3. Other significant medical conditions (as determined by medical history, examination, or clinical investigations at screening)
Minimum Eligible Age

40 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Qiagen Manchester Limited

UNKNOWN

Sponsor Role collaborator

Roche Diagnostic Ltd.

INDUSTRY

Sponsor Role collaborator

Neuron23 Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Fatta B Nahab, MD, FAAN FANA

Role: PRINCIPAL_INVESTIGATOR

Neuron23 Inc.

Locations

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Banner Sun Health Research Institute

Sun City, Arizona, United States

Site Status RECRUITING

University of Arkansas

Little Rock, Arkansas, United States

Site Status RECRUITING

Neuro-Pain Medical Center

Fresno, California, United States

Site Status RECRUITING

University of California, Irvine

Irvine, California, United States

Site Status RECRUITING

University of California, Los Angeles

Los Angeles, California, United States

Site Status RECRUITING

Esperanza Clinical

Murrieta, California, United States

Site Status RECRUITING

Parkinson's Research Centers of America - Palo Alto

Palo Alto, California, United States

Site Status RECRUITING

University of Colorado - Anschutz Medical Campus

Aurora, Colorado, United States

Site Status RECRUITING

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, United States

Site Status RECRUITING

University of Florida

Gainesville, Florida, United States

Site Status RECRUITING

Neurology One

Orlando, Florida, United States

Site Status RECRUITING

USF Parkinson's & Movement Disorders Clinic

Tampa, Florida, United States

Site Status RECRUITING

Emory University

Atlanta, Georgia, United States

Site Status RECRUITING

Augusta University

Augusta, Georgia, United States

Site Status RECRUITING

Northwestern Medical Group, Department of Neurology

Chicago, Illinois, United States

Site Status RECRUITING

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status RECRUITING

University of Kentucky

Lexington, Kentucky, United States

Site Status RECRUITING

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status RECRUITING

University of Maryland

Baltimore, Maryland, United States

Site Status RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

Quest Research Institute

Farmington Hills, Michigan, United States

Site Status RECRUITING

Struthers Parkinson Center

Golden Valley, Minnesota, United States

Site Status RECRUITING

Cleveland Clinic

Las Vegas, Nevada, United States

Site Status RECRUITING

Northwell Health

Great Neck, New York, United States

Site Status RECRUITING

Icahn School of Medicine at Mount Sinai/Mount Sinai West

New York, New York, United States

Site Status RECRUITING

Columbia University

New York, New York, United States

Site Status RECRUITING

University of Rochester

Rochester, New York, United States

Site Status RECRUITING

University of North Carolina - Chapel Hill

Chapel Hill, North Carolina, United States

Site Status RECRUITING

The Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

The Movement Disorder Clinic of Oklahoma

Tulsa, Oklahoma, United States

Site Status RECRUITING

Oregon Health & Science University (OHSU)

Portland, Oregon, United States

Site Status RECRUITING

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Site Status NOT_YET_RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

Vanderbilt University

Nashville, Tennessee, United States

Site Status RECRUITING

Neurology Consultants of Dallas PA

Dallas, Texas, United States

Site Status NOT_YET_RECRUITING

Baylor College of Medicine

Houston, Texas, United States

Site Status RECRUITING

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status RECRUITING

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status RECRUITING

University of Utah Movement Division

Salt Lake City, Utah, United States

Site Status RECRUITING

University of Virginia

Charlottesville, Virginia, United States

Site Status RECRUITING

EvergreenHealth

Kirkland, Washington, United States

Site Status RECRUITING

Inland Northwest Research

Spokane, Washington, United States

Site Status NOT_YET_RECRUITING

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

IRCCS Ospedale San Raffaele (HSR) - Dipartimento Di Neurologia

Milan, , Italy

Site Status NOT_YET_RECRUITING

Universita Degli Studi Della Campania "Luigi Vanvitelli" - Azienda Ospedaliera Universitaria

Napoli, , Italy

Site Status NOT_YET_RECRUITING

Universita Degli Studi Di Padova - Azienda Ospedaliera Di Padova - Clinica Neurologica

Padua, , Italy

Site Status NOT_YET_RECRUITING

Azienda Ospedaliero Universitaria Pisana - Stabilimento Ospedaliero Di Santa Chiara

Pisa, , Italy

Site Status NOT_YET_RECRUITING

Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) - San Raffaele Pisana

Rome, , Italy

Site Status NOT_YET_RECRUITING

Fondazione Policilinico Universitario A Gemelli IRCCS

Rome, , Italy

Site Status NOT_YET_RECRUITING

Centrum Medyczne Neuromed

Bydgoszcz, , Poland

Site Status NOT_YET_RECRUITING

NZOZ Wielospecjalistyczna Poradnia Lekarska Synapsis Lech Szczechowski

Katowice, , Poland

Site Status NOT_YET_RECRUITING

Pro Life Medica Sp. z o. o. ETA Lublin

Lublin, , Poland

Site Status NOT_YET_RECRUITING

Insula Badania Sp. Z o.o.

Warsaw, , Poland

Site Status NOT_YET_RECRUITING

Policlinica Gipuzkoa - Centro de Investigacion Parkinson (CIP)

San Sebastián, Donostia, Spain

Site Status NOT_YET_RECRUITING

Instituto de Investigacion Sanitaria Biocruces Bizkaia - Hospital Universitario Cruces

Barakaldo, , Spain

Site Status NOT_YET_RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status NOT_YET_RECRUITING

Hospital Clinic de Barcelona (Hospital Clinic i Provincial) - Barnaclinic S.A.

Barcelona, , Spain

Site Status RECRUITING

Universidad Autonoma de Madrid (UAM) - Hospital Universitario de La Princesa

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario HM Puerta del Sur

Móstoles, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio (HUVR) - Instituto de Biomedicina de Sevilla (IBIS)

Seville, , Spain

Site Status NOT_YET_RECRUITING

St George's Hospital, University of London

London, England, United Kingdom

Site Status RECRUITING

University College London Hospitals NHS Foundation Trust

London, England, United Kingdom

Site Status NOT_YET_RECRUITING

Clinical Aging Research Unit, Newcastle University

Newcastle upon Tyne, England, United Kingdom

Site Status RECRUITING

Ninewells Hospital and Medical School - NHS Tayside

Dundee, Scotland, United Kingdom

Site Status RECRUITING

Countries

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United States Italy Poland Spain United Kingdom

Central Contacts

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Fatta B Nahab, MD, FAAN, FANA

Role: CONTACT

650-228-2527

Facility Contacts

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Serena Lowery

Role: primary

623-832-0080

Erin Hatcher

Role: primary

501-214-2178

Mirian Payo

Role: primary

559-437-9700 ext. 305

Rene Anguiano

Role: primary

949-824-6407

Diane Yang

Role: primary

310-206-3356

Esperanza Clinical

Role: primary

951-417-4466

Leeana Bade

Role: primary

650-394-6690

Emily Forbes, DO

Role: primary

303-724-4644

Karla Arias

Role: primary

561-392-1818 ext. 2

Camille Swartz

Role: primary

352-733-2429

Carem Acosta

Role: primary

407-674-1648

Erica Botting

Role: primary

813-974-8026

Brian Sperin

Role: primary

Buff Farrow

Role: primary

706-721-0619

Camryn Butze

Role: primary

312-503-6824

Emily Jackson

Role: primary

913-588-0859

Corisa Logan

Role: primary

859-218-5076

Anna Leonard-Leumas

Role: primary

504-842-0148

Victoria Davis

Role: primary

410-328-4526

Alexandra Gottlieb

Role: primary

617-667-9890

Nancy Virdi

Role: primary

248-957-8944 ext. 1103

Carrie Weaver

Role: primary

952-993-5903

Liliana Dumitrescu

Role: primary

702-483-6000

Noureddin Elayan

Role: primary

516-325-7000

Ricardo Renvill

Role: primary

212-844-6055

Columbia Movement Disorders Research

Role: primary

347-882-4315

Amy Chesire

Role: primary

585-341-7500

Jessica Ferrall

Role: primary

919-962-8852

Katherine Ambrogi

Role: primary

614-688-6685

Elise Gibson

Role: primary

918-392-4530

Emily Leonard

Role: primary

503-367-4719

Brian Urbani

Role: primary

215-955-2635

Robin Bulgarino

Role: primary

843-792-1115

Haley Kling

Role: primary

615-208-3974

Christina Howell

Role: primary

214-750-9977 ext. 293

Aneesch Martin

Role: primary

713-798-2606

Brittany Duncan

Role: primary

713-486-3134

Koni Lopez

Role: primary

512-218-1222 ext. 214

Kendra Fowler

Role: primary

801-581-7828

Lauren Miller

Role: primary

434-982-6599

Gowri Rajendran

Role: primary

425-899-5370

Michael Dauer

Role: primary

509-960-2818 ext. 6

Shelby Schold

Role: primary

414-955-0698

Daniela Capilupo

Role: primary

+39 0226434815

Teresa Del Santo

Role: primary

+39 3494026479

Angelo Antonini

Role: primary

+39 0498213607

Pierangela Riani

Role: primary

+39 050992567

Miriam Casali

Role: primary

+39 0652252311

Flavia Torlizzi

Role: primary

+39 0630155633

Beata Lisewska

Role: primary

+48 696268565

Katarzyna Smilowska

Role: primary

+48 600282870

Dominika Tomaka, MD

Role: primary

+48 691485946

Marta Jethon

Role: primary

+48 501035250

Gurutz Linazasoro, MD

Role: primary

+34 943002812

Naiara Azcue

Role: primary

+34 944881576

Jorge Hernandez Vara, MD

Role: primary

+34 934893000 ext. 4884

Alicia Garrido, Pla

Role: primary

+34 932275785

Lydia Lopez Manzanares

Role: primary

+34 915202405

Patricia Vicente

Role: primary

+34 912673100 ext. 7988

Pablo Mir, MD

Role: primary

+34 955923039

Francesca Morgante, MD

Role: primary

+44 20 8725 5403

Ellie Clook

Role: primary

+44 20 3448 4531

Nicola Pavese, MD, PhD, FRCP, FEAN

Role: primary

+44 0191 2081264

Justine Hudson

Role: primary

+44 1382423086

Other Identifiers

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NEU-411-PD201

Identifier Type: -

Identifier Source: org_study_id

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