Study to Evaluate DNL201 in Subjects With Parkinson's Disease

NCT ID: NCT03710707

Last Updated: 2020-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

29 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-04

Study Completion Date

2019-12-06

Brief Summary

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The purpose of this study is to evaluate the safety, tolerability, pharmacokinetics, and pharmacodynamics of multiple oral doses of DNL201 in subjects with Parkinson's disease.

Detailed Description

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Conditions

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Parkinson Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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DNL201 low dose

Group Type EXPERIMENTAL

DNL201

Intervention Type DRUG

Oral repeating dose

DNL201 high dose

Group Type EXPERIMENTAL

DNL201

Intervention Type DRUG

Oral repeating dose

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral repeating dose

Interventions

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DNL201

Oral repeating dose

Intervention Type DRUG

Placebo

Oral repeating dose

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Body mass index (BMI) between 18 and 35.0 kg/m2, inclusive
* Clinical diagnosis of Parkinson's disease meeting UK Brain Bank criteria and H\&Y Stage I, II, or III.
* sPD subgroup without a LRRK2 mutation; PD LRRK2 subgroup with LRRK2 mutation
* Screening dopamine transporter (DAT) SPECT scan with a DAT deficit consistent with Parkinson's disease
* Able to hold Parkinson's disease medications 8 hours (overnight) prior to specific study assessments

Exclusion Criteria

* Any history of clinically significant asthma, chronic obstructive pulmonary disease, or emphysema within 5 years of screening, or other clinically significant pulmonary disease within 6 months of screening
* Abnormal Vitals including Respiratory Rate, Body Temperature, and Blood Pressure
* Pulmonary Function Tests (PFTs) (FVC \<60% predicted, FEV1 \<50% predicted, FEV1:FVC ratio \<0.6, DLCO \<70% predicted)
* Clinically significant neurologic disorder other than Parkinson's disease, including history of stroke, cognitive impairment, seizure within 5 years of screening, or head trauma with loss of consciousness within 6 months of screening
* Montreal Cognitive Assessment (MoCA) score of \<24 at screening
Minimum Eligible Age

30 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Denali Therapeutics Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clinical Site(s)

Long Beach, California, United States

Site Status

Clinical Site(s)

Aurora, Colorado, United States

Site Status

Clinical Site(s)

Miami, Florida, United States

Site Status

Clinical Site(s)

Orlando, Florida, United States

Site Status

Clinical Site(s)

Farmington Hills, Michigan, United States

Site Status

Clinical Site(s)

Philadelphia, Pennsylvania, United States

Site Status

Clinical Site(s)

Spokane, Washington, United States

Site Status

Countries

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United States

References

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Maloney MT, Wang X, Ghosh R, Andrews SV, Maciuca R, Masoud ST, Agam M, Caprioli RM, Astarita G, Bondar VV, Chen J, Chiu CL, Davis SS, Ho AC, Nguyen HN, Propson NE, Reyzer ML, Davis OB, Deen MC, Zhu S, Di Paolo G, Vocadlo DJ, Estrada AA, de Vicente J, Lewcock JW, Arguello A, Suh JH, Huntwork-Rodriguez S, Henry AG. LRRK2 kinase activity regulates Parkinson's disease-relevant lipids at the lysosome. Mol Neurodegener. 2025 Aug 6;20(1):89. doi: 10.1186/s13024-025-00880-7.

Reference Type DERIVED
PMID: 40770658 (View on PubMed)

Joshi D, Kulkarni M, Parekh P, Shah S, Greig NH, Acharya S. Targeting protein kinases in Parkinson's disease: the emerging role of phytoconstituents. Nutr Neurosci. 2025 Jul 18:1-32. doi: 10.1080/1028415X.2025.2531356. Online ahead of print.

Reference Type DERIVED
PMID: 40680102 (View on PubMed)

Other Identifiers

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DNLI-B-0002

Identifier Type: -

Identifier Source: org_study_id

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