A Clinical Study of NLY01 in Patient's With Early Parkinson's Disease

NCT ID: NCT04154072

Last Updated: 2024-09-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

255 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-02-27

Study Completion Date

2023-02-14

Brief Summary

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This is a phase 2 study designed to assess the safety, tolerability and efficacy of NLY01 in subjects with early untreated Parkinson's disease (PD). Evidence suggests NLY01, a pegylated form of exenatide, may be beneficial in PD and is being developed as a potential treatment for neurodegenerative disorders.

Detailed Description

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Conditions

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Parkinson Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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NLY01 (2.5 mg)

NLY01 2.5 mg injection

Group Type ACTIVE_COMPARATOR

NLY01

Intervention Type DRUG

exenatide and polyethylene glycol (PEG)

NLY01 (5.0 mg)

NLY01 5.0 mg injection

Group Type ACTIVE_COMPARATOR

NLY01

Intervention Type DRUG

exenatide and polyethylene glycol (PEG)

Vehicle

inactive drug, injection

Group Type PLACEBO_COMPARATOR

Vehicle

Intervention Type DRUG

Saline (Sodium Chloride)

Interventions

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NLY01

exenatide and polyethylene glycol (PEG)

Intervention Type DRUG

Vehicle

Saline (Sodium Chloride)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients who are diagnosed with Parkinson's disease according to UK Parkinson's Disease Society Brain Bank Clinical Diagnostic criteria or Movement Disorder Society Research Criteria
* Patients with Parkinson's disease according to protocol specified scale assessments
* DaTscan consistent with diagnosis of Parkinson's Disease
* Men or women 30 to 80 years of age

Exclusion Criteria

* Diagnosis of secondary or atypical parkinsonism
* Prior use of dopaminergic treatment or MAO-B inhibitors for more than 28 days
* Medical or recreational use of marijuana or THC-containing compounds within 3 months of screening visit
* Pregnant or planning to become pregnant
* Metabolic, surgical, psychiatric or laboratory abnormality that would interfere with study compliance or safety in the judgment of the investigator
Minimum Eligible Age

30 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Neuraly, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Dan Lee

Role: STUDY_DIRECTOR

Neuraly, Inc.

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

St. Joseph's Hospital and Medical Center - Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

Movement Disorders Center

Scottsdale, Arizona, United States

Site Status

Mayo Clinic Arizona, Mayo Clinic Scottsdale

Scottsdale, Arizona, United States

Site Status

Banner Sun Health Research Institute

Sun City, Arizona, United States

Site Status

University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

Site Status

University of California, Irvine

Irvine, California, United States

Site Status

Keck School of Medicine of USC/University of Southern California

Los Angeles, California, United States

Site Status

University of California, Los Angeles, Center for Neurotherapeutics

Los Angeles, California, United States

Site Status

SC3 Research

Pasadena, California, United States

Site Status

University of California Davis Health

Sacramento, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

University of Colorado

Denver, Colorado, United States

Site Status

Rocky Mountain Movement Disorder Center

Englewood, Colorado, United States

Site Status

Institute for Neurodegenerative Disorders

New Haven, Connecticut, United States

Site Status

Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Parkinson's Disease and Movement Disorder Center

Boca Raton, Florida, United States

Site Status

Nova Clinical Research

Bradenton, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Infinity Clinical Research

Hollywood, Florida, United States

Site Status

Mayo Clinic Florida

Jacksonville, Florida, United States

Site Status

Visionary Investigators Network

Miami, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Renstar Medical Research

Ocala, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Charter Research

Winter Park, Florida, United States

Site Status

Augusta University

Augusta, Georgia, United States

Site Status

NeuroStudies

Decatur, Georgia, United States

Site Status

Northwestern Medical Group Neurology Clinic

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

SIU Medicine

Springfield, Illinois, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Maryland, Neurology Ambulatory Center, Maryland Parkinson's Disease and Movement Disorder Center

Baltimore, Maryland, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital Clinical Trials Pharmacy

Boston, Massachusetts, United States

Site Status

Boston University Medical Center

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

University of Michigan Hospital

Ann Arbor, Michigan, United States

Site Status

Quest Research Institute

Farmington Hills, Michigan, United States

Site Status

Henry Ford West Bloomfield Hospital

West Bloomfield, Michigan, United States

Site Status

Struthers Parkinson's Center

Golden Valley, Minnesota, United States

Site Status

University of Minnesota Delaware Clinical Research Unit

Minneapolis, Minnesota, United States

Site Status

Neurology Specialists of Monmouth County

West Long Branch, New Jersey, United States

Site Status

NYU Langone Medical Center, The Marlene and Paolo Fresco Institute for Parkinson's and Movement Disorders

New York, New York, United States

Site Status

Neurological Institute, Columbia University Medical Center

New York, New York, United States

Site Status

UNC CTRC

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Raleigh Neurology

Raleigh, North Carolina, United States

Site Status

Wake Forest Baptist Health Sciences

Winston-Salem, North Carolina, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

Site Status

University of Toledo, Gardner-McMaster Parkinson Center

Toledo, Ohio, United States

Site Status

The Movement Disorder Clinic of Oklahoma

Tulsa, Oklahoma, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Booth Gardner Parkinson's Care Center

Kirkland, Washington, United States

Site Status

Froedtert Hospital

Milwaukee, Wisconsin, United States

Site Status

Toronto Western Hospital

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

References

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McGarry A, Rosanbalm S, Leinonen M, Olanow CW, To D, Bell A, Lee D, Chang J, Dubow J, Dhall R, Burdick D, Parashos S, Feuerstein J, Quinn J, Pahwa R, Afshari M, Ramirez-Zamora A, Chou K, Tarakad A, Luca C, Klos K, Bordelon Y, St Hiliare MH, Shprecher D, Lee S, Dawson TM, Roschke V, Kieburtz K. Safety, tolerability, and efficacy of NLY01 in early untreated Parkinson's disease: a randomised, double-blind, placebo-controlled trial. Lancet Neurol. 2024 Jan;23(1):37-45. doi: 10.1016/S1474-4422(23)00378-2.

Reference Type DERIVED
PMID: 38101901 (View on PubMed)

Other Identifiers

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NLY01-PD-1

Identifier Type: -

Identifier Source: org_study_id

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