A Study To Assess Adverse Events and Effectiveness of Upadacitinib Oral Tablets in Adult and Adolescent Participants With Vitiligo

NCT ID: NCT06118411

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

614 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-19

Study Completion Date

2028-02-29

Brief Summary

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Vitiligo is a common chronic autoimmune disease that causes the body's immune system to attack its own pigment producing skin cells. This study is to evaluate how safe and effective upadacitinib is in participants with non-segmental vitiligo (NSV). Adverse effects and change in disease activity will be assessed.

Upadacitinib is an approved drug for various immune-mediated inflammatory diseases and is currently being investigated for the treatment of NSV. There will be 2 replicate studies running at the same time (Study 1 and Study 2 with periods A and B) and an optional exploratory Narrow-Band Ultraviolet B (NB-UVB) phototherapy study (Study 3). In Period A, participants are placed in 1 of 2 groups called treatment arms. Each group receives a different treatment. There is a 1 in 3 chance that participants will receive placebo and 2 in 3 chance participants will receive upadacitinib. In Period B, all participants will receive upadacitinib. Approximately 270 adult and adolescent participants with NSV will be enrolled in each main study ((Study 1 and Study 2, 540 subjects total) at approximately 90 sites worldwide with an option for adult participants who completed Period A of either study and did not achieve T-VASI 90 at week 48 while on study drug, to enter Study 3.

In Studies 1 and 2: Period A, participants will receive oral tablets of upadacitinib or placebo once a day for 48 weeks. In Period B, participants will receive oral tablets of upadacitinib 15 mg once a day for 112 weeks. Participants will be followed up for 30 days. Study 3 participants will receive upadacitinib monotherapy or upadacitinib with NB-UBV phototherapy for at least 24 weeks followed by upadacitinib alone.

There may be higher treatment burden for participants in this trial compared to their standard of care. Participants will attend regular visits during the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects and completing questionnaires.

Detailed Description

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Conditions

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Vitiligo

Keywords

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Vitiligo Non-Segmented Vitiligo Viti-Up Upadacitinib

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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(Optional) Study 3:

Participants will receive 15 mg upadacitinib once daily for 112 weeks and NB-UVB for up to 28 weeks

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

NB-UVB (narrow-band ultraviolet B) Phototherapy

Intervention Type OTHER

NB-UVB phototherapy is a commonly used treatment modality in participants with vitiligo and can be administered in an office setting or at home 2 times per week

Study 1, Period A: Group 1

Participants will receive upadacitinib 15 mg once daily for 48 weeks.

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

Study 1, Period A: Group 2

Participants will receive placebo once daily for 48 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral Tablets

Study 2, Period A: Group 1

Participants will receive upadacitinib 15 mg once daily for 48 weeks.

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

Study 2, Period A: Group 2

Participants will receive placebo once daily for 48 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral Tablets

Study 1, Period B: Group 1 Open-Label Extension Period

Participants that were randomized to receive upadacitinib in Period A Group 1, will continue to receive upadacitinib 15 mg once daily for 112 weeks in Period B.

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

Study 1, Period B: Group 2 Open-Label Extension Period

Participants that were randomized to receive placebo in Period A Group 2, will receive upadacitinib 15 mg once daily for 112 weeks in Period B.

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

Study 2, Period B: Group 1 Open-Label Extension Period

Participants that were randomized to receive upadacitinib in Period A Group 1, will continue to receive upadacitinib 15 mg once daily for 112 weeks in Period B.

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

Study 2, Period B: Group 2 Open-Label Extension Period

Participants that were randomized to receive placebo in Period A Group 2, will receive upadacitinib 15 mg once daily for 112 weeks in Period B.

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

(Optional) Study 3, Period B: Open Label Upadacitinib

Open Label Upadacitinib Participants will receive upadacitinib 15 mg once daily for 112 weeks

Group Type EXPERIMENTAL

Upadacitinib

Intervention Type DRUG

Oral Tablets

NB-UVB (narrow-band ultraviolet B) Phototherapy

Intervention Type OTHER

NB-UVB phototherapy is a commonly used treatment modality in participants with vitiligo and can be administered in an office setting or at home 2 times per week

Interventions

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Upadacitinib

Oral Tablets

Intervention Type DRUG

Placebo

Oral Tablets

Intervention Type DRUG

NB-UVB (narrow-band ultraviolet B) Phototherapy

NB-UVB phototherapy is a commonly used treatment modality in participants with vitiligo and can be administered in an office setting or at home 2 times per week

Intervention Type OTHER

Other Intervention Names

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ABT-494 Rinvoq

Eligibility Criteria

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Inclusion Criteria

* Documented clinical diagnosis of non-segmented vitiligo (NSV).
* At Screening and Baseline Visits, participants must satisfy at least 1 of the following criteria:

* \>= 0.5 F-VASI and 5 \<= T-VASI \< 50 AND have failed at least 1 topical corticosteroid and/or at least 1 topical calcineurin inhibitor for vitiligo; or
* \>= 0.5 F-VASI and 5 \<= T-VASI \< 50 AND have a sign of actively progressing vitiligo; or
* \>= 0.5 F-VASI and 10 \<= T-VASI \< 50.

Exclusion Criteria

* Segmental or localized vitiligo.
* History of active skin disease other than vitiligo that could interfere with the assessment of vitiligo.
* \>33% leukotrichia in areas of vitiligo on the face or \> 33% leukotrichia in areas of vitiligo on the body (including the face).
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Advanced Research Associates - Glendale /ID# 259915

Glendale, Arizona, United States

Site Status

Alliance Dermatology and Mohs Center /ID# 259926

Phoenix, Arizona, United States

Site Status

Private Practice - Dr. Tooraj Raoof /ID# 260055

Encino, California, United States

Site Status

University of California Irvine /ID# 260080

Irvine, California, United States

Site Status

Vitiligo & Pigmentation Institute of Southern California /ID# 259970

Los Angeles, California, United States

Site Status

Dermatology Research Associates /ID# 260056

Los Angeles, California, United States

Site Status

Duplicate_Stanford University /ID# 260081

Redwood City, California, United States

Site Status

Integrative Skin Science and Research /ID# 260060

Sacramento, California, United States

Site Status

University of California Davis Health /ID# 260062

Sacramento, California, United States

Site Status

Clinical Trials Research Institute /ID# 259910

Thousand Oaks, California, United States

Site Status

Skin Care Research Boca Raton /ID# 260094

Boca Raton, Florida, United States

Site Status

Apex Clinical Trials /ID# 260096

Brandon, Florida, United States

Site Status

Florida Academic Dermatology Center /ID# 259919

Coral Gables, Florida, United States

Site Status

Direct Helpers Research Center /ID# 259932

Hialeah, Florida, United States

Site Status

Skin Care Research - Hollywood /ID# 260101

Hollywood, Florida, United States

Site Status

Encore Medical Research /ID# 259963

Hollywood, Florida, United States

Site Status

GSI Clinical Research, LLC /ID# 259918

Margate, Florida, United States

Site Status

Life Clinical Trials /ID# 260097

Margate, Florida, United States

Site Status

Savin Medical Group, LLC /ID# 259968

Miami Lakes, Florida, United States

Site Status

Advanced Clinical Research Institute /ID# 260058

Tampa, Florida, United States

Site Status

Encore Medical Research - Weston /ID# 260542

Weston, Florida, United States

Site Status

Cleaver Medical Group Dermatology /ID# 259925

Dawsonville, Georgia, United States

Site Status

DeNova Research /ID# 260611

Chicago, Illinois, United States

Site Status

Indiana University Health University Hospital /ID# 259974

Indianapolis, Indiana, United States

Site Status

Dawes Fretzin, LLC /ID# 260068

Indianapolis, Indiana, United States

Site Status

Tufts Medical Center /ID# 260088

Boston, Massachusetts, United States

Site Status

UMass Memorial Medical Center /ID# 259921

Worcester, Massachusetts, United States

Site Status

Oakland Hills Dermatology /ID# 260602

Auburn Hills, Michigan, United States

Site Status

Great Lakes Research Group - Bay City /ID# 260600

Bay City, Michigan, United States

Site Status

Hamzavi Dermatology - Canton /ID# 260545

Canton, Michigan, United States

Site Status

Clarkston Dermatology /ID# 260069

Clarkston, Michigan, United States

Site Status

Henry Ford Medical Center - New Center One /ID# 260059

Detroit, Michigan, United States

Site Status

Minnesota Clinical Study Center /ID# 260154

New Brighton, Minnesota, United States

Site Status

Vivida Dermatology- Flamingo /ID# 260609

Las Vegas, Nevada, United States

Site Status

Schweiger Dermatology, P.C. /ID# 260152

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai /ID# 259909

New York, New York, United States

Site Status

DermResearchCenter of New York, Inc. /ID# 259906

Stony Brook, New York, United States

Site Status

ClinOhio Research Services /ID# 260300

Columbus, Ohio, United States

Site Status

Oregon Medical Research Center /ID# 259911

Portland, Oregon, United States

Site Status

Oregon Dermatology and Research Center /ID# 259917

Portland, Oregon, United States

Site Status

Medical University of South Carolina /ID# 259916

Charleston, South Carolina, United States

Site Status

Bellaire Dermatology Associates /ID# 260044

Bellaire, Texas, United States

Site Status

Dermatology Treatment and Research Center /ID# 260078

Dallas, Texas, United States

Site Status

Innovative Dermatology - Plano /ID# 260628

Plano, Texas, United States

Site Status

Dermatology Clinical Research Center of San Antonio /ID# 260047

San Antonio, Texas, United States

Site Status

Progressive Clinical Research /ID# 260070

San Antonio, Texas, United States

Site Status

Buenos Aires Skin /ID# 259885

Ciudad Autonoma de Buenos Aire, Buenos Aires F.D., Argentina

Site Status

Instituto de Neumonologia y Dermatologia /ID# 259888

Ciudad Autonoma de Buenos Aire, Buenos Aires F.D., Argentina

Site Status

Psoriahue Med Interdisciplinar /ID# 259890

Ciudad Autonoma de Buenos Aire, Buenos Aires F.D., Argentina

Site Status

Instituto De Investigaciones Clínicas Córdoba /ID# 260371

Córdoba, Córdoba Province, Argentina

Site Status

Sanatorio 9 de Julio /ID# 260245

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Centro de Investigacion y Prevencion Cardiovascular (CIPREC) /ID# 259889

Buenos Aires, , Argentina

Site Status

Cliniques Universitaires UCL Saint-Luc /ID# 259429

Brussels, Brussels Capital, Belgium

Site Status

Grand Hôpital de Charleroi - Les Viviers /ID# 259437

Charleroi, Hainaut, Belgium

Site Status

UZ Gent /ID# 259430

Ghent, Oost-Vlaanderen, Belgium

Site Status

CHU de Liege /ID# 259427

Liège, , Belgium

Site Status

Ambulatory for Specialized Medical Care-IPSMC-skin and venereal diseases /ID# 259955

Sofiya, Sofia, Bulgaria

Site Status

Diagnostic Consultative Centre (Dcc) - Foкus 5 /ID# 259956

Sofiya, Sofia, Bulgaria

Site Status

Diagnosis - Consult Centre 20 - Sofia /ID# 259953

Sofiya, Sofia, Bulgaria

Site Status

Medical Center Cordis /ID# 259954

Pleven, , Bulgaria

Site Status

Dermatology Research Institute - Blackfoot Trail /ID# 261175

Calgary, Alberta, Canada

Site Status

Dr. Chih-ho Hong Medical Inc. /ID# 260239

Surrey, British Columbia, Canada

Site Status

Wiseman Dermatology Research /ID# 260236

Winnipeg, Manitoba, Canada

Site Status

Brunswick Dermatology Center /ID# 260237

Fredericton, New Brunswick, Canada

Site Status

LEADER Research /ID# 260407

Hamilton, Ontario, Canada

Site Status

Private Practice - Dr. Kim Papp Clinical Research /ID# 260406

Waterloo, Ontario, Canada

Site Status

Centre de Recherche dermatologique du Quebec Metropolitain /ID# 260241

Québec, Quebec, Canada

Site Status

Dre Angelique Gagne-Henley M.D. inc. /ID# 260238

Saint-Jérôme, Quebec, Canada

Site Status

Beijing Tongren Hospital Affiliated To Capital Medical University /ID# 260919

Beijing, Beijing Municipality, China

Site Status

Dermatology Hospital of Southern Medical University /ID# 260136

Guangzhou, Guangdong, China

Site Status

The Second Affiliated Hospital of Guangzhou Medical University /ID# 259929

Guangzhou, Guangdong, China

Site Status

Renmin Hospital of Wuhan University /ID# 260477

Wuhan, Hubei, China

Site Status

Second Affiliated Hospital of Xian Jiaotong University /ID# 260011

Xi'an, Shaanxi, China

Site Status

The First Affiliated Hospital of Xi'an Jiaotong University /ID# 260340

Xi'an, Shaanxi, China

Site Status

Shandong Dermatological Hospital /ID# 260338

Jinan, Shandong, China

Site Status

Huashan Hospital, Fudan University /ID# 259823

Shanghai, Shanghai Municipality, China

Site Status

Chengdu Second Municipal People's Hospital /ID# 260423

Chengdu, Sichuan, China

Site Status

West China Hospital, Sichuan University /ID# 260624

Chengdu, Sichuan, China

Site Status

Tianjin Medical University General Hospital /ID# 259812

Tianjin, Tianjin Municipality, China

Site Status

First Affiliated Hospital of Kunming Medical University /ID# 260017

Kunming, Yunnan, China

Site Status

Hangzhou Third People'S Hospital /ID# 261005

Hangzhou, Zhejiang, China

Site Status

Sir Run Run Shaw Hospital Zhejiang University School of Medicine /ID# 260626

Hangzhou, Zhejiang, China

Site Status

The First Affiliated Hospital of Wenzhou Medical University /ID# 259822

Wenzhou, Zhejiang, China

Site Status

Chu de Nice-Hopital L'Archet Ii /Id# 259442

Nice, Alpes-Maritimes, France

Site Status

Centre Hospitalier Universitaire de Bordeaux - Groupe Hospitalier Saint-Andre /ID# 259443

Bordeaux, Gironde, France

Site Status

CHU Toulouse - Hopital Larrey /ID# 259445

Toulouse, Haute-Garonne, France

Site Status

Hopitaux Universitaires Henri Mondor - Hopital Henri Mondor /ID# 259446

Créteil, Paris, France

Site Status

HCL - Hopital Edouard Herriot /ID# 259444

Lyon, Rhone, France

Site Status

Universitaetsklinikum Erlangen /ID# 260153

Erlangen, Bavaria, Germany

Site Status

Klinikum rechts der Isar /ID# 260291

Munich, Bavaria, Germany

Site Status

Dermatologie Mahlow /ID# 260148

Blankenfelde-Mahlow, Brandenburg, Germany

Site Status

MVZ Dermatologisches Zentrum Bonn GmbH /ID# 260287

Bonn, Hesse, Germany

Site Status

Universitaetsklinikum Frankfurt /ID# 260288

Frankfurt am Main, Hesse, Germany

Site Status

Fachklinik Bad Bentheim /ID# 260293

Bad Bentheim, Lower Saxony, Germany

Site Status

Universitaetsklinikum Muenster /ID# 260147

Münster, North Rhine-Westphalia, Germany

Site Status

Universitaetsmedizin Mainz /ID# 260151

Mainz, Rhineland-Palatinate, Germany

Site Status

Universitaetsklinikum Carl Gustav Carus Dresden /ID# 260289

Dresden, Saxony, Germany

Site Status

Private Practice - Dr. Abdou Zarzour /ID# 260290

Halle, Saxony-Anhalt, Germany

Site Status

Charite Universitaetsmedizin Berlin - Campus Mitte /ID# 260294

Berlin, , Germany

Site Status

DERMA-B Egeszsegugyi es Szolgaltato - Debrecen - Gyepusor Utca /ID# 260072

Debrecen, , Hungary

Site Status

Hadassah Medical Center-Hebrew University /ID# 259849

Jerusalem, Jerusalem, Israel

Site Status

The Chaim Sheba Medical Center /ID# 259851

Ramat Gan, Tel Aviv, Israel

Site Status

Tel Aviv Sourasky Medical Center /ID# 259850

Tel Aviv, Tel Aviv, Israel

Site Status

Rambam Health Care Campus /ID# 259852

Haifa, , Israel

Site Status

Rabin Medical Center /ID# 260420

Petah Tikva, , Israel

Site Status

IRCCS Istituti Fisioterapici Ospitalieri-Istituto Dermatologico San Gallicano /ID# 259771

Rome, Roma, Italy

Site Status

ASST degli Spedali Civili di Brescia /ID# 259772

Brescia, , Italy

Site Status

Nagoya City University Hospital /ID# 260551

Nagoya, Aichi-ken, Japan

Site Status

Dermatology and Ophthalmology Kume Clinic /ID# 260555

Sakai-shi, Osaka, Japan

Site Status

The University of Osaka Hospital /ID# 261285

Suita-shi, Osaka, Japan

Site Status

Nippon Medical School Hospital /ID# 260550

Bunkyo-ku, Tokyo, Japan

Site Status

Tokyo Medical University Hospital /ID# 260552

Shinjuku-ku, Tokyo, Japan

Site Status

Yamagata University Hospital /ID# 260553

Yamagata, Yamagata, Japan

Site Status

Yamanashi Prefectural Central Hospital /ID# 260554

Kofu, Yamanashi, Japan

Site Status

Bravis Ziekenhuis /ID# 259501

Bergen op Zoom, North Brabant, Netherlands

Site Status

Amphia Ziekenhuis /ID# 259696

Breda, North Brabant, Netherlands

Site Status

Amsterdam UMC, locatie AMC /ID# 259676

Amsterdam, North Holland, Netherlands

Site Status

Dermodent Centrum Medyczne Aldona Czajkowska Rafał Czajkowski /ID# 259690

Osielsko, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

Specjalistyczny Gabinet Dermatologiczny Aplikacyjno Badawczy /ID# 260016

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Malopolskie Centrum Kliniczne /ID# 259686

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Krakowskie Centrum Medyczne /ID# 261424

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Klinika Osipowicz & Turkowski sp.z.o.o /ID# 259761

Warsaw, Masovian Voivodeship, Poland

Site Status

Klinika Ambroziak Dermatologia /ID# 260018

Warsaw, Masovian Voivodeship, Poland

Site Status

Royalderm Agnieszka Nawrocka /ID# 259691

Warsaw, Masovian Voivodeship, Poland

Site Status

Osteo Medic s.c. Artur Racewicz Jerzy Supronik /ID# 259753

Bialystok, Podlaskie Voivodeship, Poland

Site Status

Centrum Medyczne Angelius Provita /ID# 259752

Katowice, Silesian Voivodeship, Poland

Site Status

Twoja Przychodnia SCM /ID# 259757

Szczecin, West Pomeranian Voivodeship, Poland

Site Status

Unidade Local de Saude de Coimbra, EPE /ID# 259793

Coimbra, , Portugal

Site Status

Unidade Local de Saude da Regiao de Leiria, EPE /ID# 259789

Leiria, , Portugal

Site Status

Hospital CUF Descobertas /ID# 259788

Lisbon, , Portugal

Site Status

Unidade Local de Saude de Santo Antonio, E.P.E. /ID# 259791

Porto, , Portugal

Site Status

Santa Cruz Behavioral (SCB) Research Center /ID# 260100

Bayamón, , Puerto Rico

Site Status

Dr. Samuel Sanchez PSC /ID# 260090

Caguas, , Puerto Rico

Site Status

Mindful Medical Research /ID# 260092

San Juan, , Puerto Rico

Site Status

Derma therapy spol /ID# 260838

Bratislava, Bratislava Region, Slovakia

Site Status

Fakultna nemocnica Trnava /ID# 260164

Trnava, , Slovakia

Site Status

Chungnam National University Hospital /ID# 260917

Daejeon, Daejeon Gwang Yeogsi, South Korea

Site Status

Soon Chun Hyang University Hospital Bucheon /ID# 260836

Bucheon-si, Gyeonggido, South Korea

Site Status

The Catholic University Of Korea St. Vincent's Hospital /ID# 260880

Suwon, Gyeonggido, South Korea

Site Status

Ajou University Hospital /ID# 260916

Suwon, Gyeonggido, South Korea

Site Status

Kyung Hee University Hospital at Gangdong /ID# 260879

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Hospital Universitario Germans Trias i Pujol /ID# 259371

Badalona, Barcelona, Spain

Site Status

Hospital Universitario de Getafe /ID# 259376

Getafe, Madrid, Spain

Site Status

Hospital Universitario Quironsalud Madrid /ID# 259377

Pozuelo de Alarcón, Madrid, Spain

Site Status

Hospital Universitario Clinico San Cecilio /ID# 259374

Granada, , Spain

Site Status

Grupo Pedro Jaen /ID# 259375

Madrid, , Spain

Site Status

Consorci Hospital General Universitario de Valencia /ID# 259372

Valencia, , Spain

Site Status

Hospital Clinico Universitario Lozano Blesa /ID# 259373

Zaragoza, , Spain

Site Status

Countries

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United States Argentina Belgium Bulgaria Canada China France Germany Hungary Israel Italy Japan Netherlands Poland Portugal Puerto Rico Slovakia South Korea Spain

Related Links

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Other Identifiers

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2023-506195-27-00

Identifier Type: OTHER

Identifier Source: secondary_id

M19-044

Identifier Type: -

Identifier Source: org_study_id