Trastuzumab Deruxtecan Versus Standard Neoadjuvant Treatment for HER2-positive Breast Cancer

NCT ID: NCT05900206

Last Updated: 2025-09-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

370 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-10-26

Study Completion Date

2032-04-30

Brief Summary

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The goal of this clinical trial is to compare trastuzumab deruxtecan (T-DXd) to standard preoperative treatment in patients with non-metastatic HER2-positive breast cancer. The main questions it aims to answer are:

* is T-DXd more effective than standard preoperative treatment?
* are there markers in the tumor or blood of patients with HER2-positive breast cancer that can help us predict response to treatment?

Participants will be divided into two groups, where one group will be treated with three courses of T-DXd and the other group will be treated with three courses standard of care treatment. Thereafter, further treatment will be decided by the tumor's molecular subtype.

Detailed Description

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Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Parallel, two arms for cycles 1-3. Further treatment (cycles 4-6) decided by molecular intrinsic subtype.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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T-DXd (cycles 1-3)

Trastuzumab Deruxtecan, administered every three weeks for three courses. Further treatment is decided by the intrinsic molecular (PAM50) subtype of the tumor.

Group Type EXPERIMENTAL

Trastuzumab deruxtecan

Intervention Type DRUG

Experimental drug. Provided in 100mg vials. IV infusion.

Standard treatment (TCHP or PCHP; cycles 1-3)

TCHP (Docetaxel, Carboplatin, Trastuzumab, Pertuzumab) or PCHP (Paclitaxel, Carboplatin, Trastuzumab, Pertuzumab), administered every three weeks for three courses. Further treatment is decided by the intrinsic molecular (PAM50) subtype of the tumor.

Group Type ACTIVE_COMPARATOR

Docetaxel

Intervention Type DRUG

Active comparator. IV infusion.

Paclitaxel

Intervention Type DRUG

Active comparator. IV infusion.

Carboplatin

Intervention Type DRUG

Active comparator. IV infusion.

Trastuzumab

Intervention Type DRUG

Active comparator. IV infusion.

Pertuzumab

Intervention Type DRUG

Active comparator. IV infusion.

ER-positive and Luminal (cycles 4-6)

Ribociclib, letrozole, trastuzumab, pertuzumab

Group Type OTHER

Ribociclib

Intervention Type DRUG

Experimental drug. Tablets.

Letrozole

Intervention Type DRUG

Experimental drug. Tablets.

ER-negative and Luminal, or Basal-like, or Normal-like (cycles 4-6)

Epirubicin and Cyclophosphamide in case of no complete radiologic response after the initial three courses. In case of complete radiologic response, treatment from cycles 1-3 (T-DXd or TCHP/PCHP) will continue instead for three more courses.

Group Type OTHER

Epirubicin

Intervention Type DRUG

Active comparator. IV infusion.

Cyclophosphamide

Intervention Type DRUG

Active comparator. IV infusion.

HER2-enriched (cycles 4-6)

The same treatment with T-DXd or TCHP/PCHP administered every three weeks for three more courses will continue from cycles 1-3

Group Type OTHER

Trastuzumab deruxtecan

Intervention Type DRUG

Experimental drug. Provided in 100mg vials. IV infusion.

Docetaxel

Intervention Type DRUG

Active comparator. IV infusion.

Paclitaxel

Intervention Type DRUG

Active comparator. IV infusion.

Carboplatin

Intervention Type DRUG

Active comparator. IV infusion.

Trastuzumab

Intervention Type DRUG

Active comparator. IV infusion.

Pertuzumab

Intervention Type DRUG

Active comparator. IV infusion.

Interventions

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Trastuzumab deruxtecan

Experimental drug. Provided in 100mg vials. IV infusion.

Intervention Type DRUG

Docetaxel

Active comparator. IV infusion.

Intervention Type DRUG

Paclitaxel

Active comparator. IV infusion.

Intervention Type DRUG

Carboplatin

Active comparator. IV infusion.

Intervention Type DRUG

Trastuzumab

Active comparator. IV infusion.

Intervention Type DRUG

Pertuzumab

Active comparator. IV infusion.

Intervention Type DRUG

Ribociclib

Experimental drug. Tablets.

Intervention Type DRUG

Letrozole

Experimental drug. Tablets.

Intervention Type DRUG

Epirubicin

Active comparator. IV infusion.

Intervention Type DRUG

Cyclophosphamide

Active comparator. IV infusion.

Intervention Type DRUG

Other Intervention Names

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T-DXd, Enhertu Herceptin PErjeta Kisqali

Eligibility Criteria

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Inclusion Criteria

1. Women or men 18 years or older
2. Before patient registration/randomization, written informed consent must be given according to ICH/GCP, and national/local regulations
3. Histologically confirmed breast cancer with an invasive component measuring ≥ 20 mm and/or with morphologically confirmed spread to regional lymph nodes (stage cT2-cT4 with any cN, or cN1-cN3 with any cT).
4. Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1 at the time of randomization (see Appendix B).
5. Known estrogen-receptor and/or progesterone receptor status, as assessed locally by IHC. The cut-off for positivity for ER/PR for this study is at least 10% of cell nuclei staining for ER or PR, respectively.
6. Known HER2-positive breast cancer defined as an IHC status of 3+. If IHC is 2+, a positive in situ hybridization (FISH, CISH, or SISH) test is required by local laboratory testing. ISH positivity is defined as a ratio of ≥ 2 for the number of HER2 gene copies to the number of signals for chromosome 17 copies.
7. Left Ventricular Ejection Fraction (LVEF) ≥ 50%
8. Adequate bone-marrow, hepatic and renal function defined as laboratory tests within 7 days prior to enrolment:

i. Hematology:
1. Absolute granulocytes \> 1.5 x 109/L
2. Platelets \> 100 x 109/L
3. Hb \> 90 gr/L ii. Biochemistry

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1. Bilirubin ≤ upper limit of normal (ULN)
2. Serum creatinine ≤ 1.5 x ULN
3. Aspartate aminotransferase (AST) and alanine aminotransferase (ALT) ≤ 1.5 x ULN
4. Albumin ≥ 30 gr/L iii. Coagulation:

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1. INR/PT ≤ 1.5 x ULN, unless the subject is receiving anticoagulant therapy and INR/PT is within intended therapeutic range
2. aPTT ≤ 1.5 x ULN, unless the subject is receiving anticoagulant therapy and aPTT is within intended therapeutic range
9. Availability of tumor and blood samples as described in the protocol
10. Negative serum pregnancy test for women of childbearing potential or for patients who have experienced menopause onset \<12 months prior to randomization.
11. Patients of childbearing potential must be willing to use one highly effective contraception or two effective forms of nonhormonal contraception. See also 5.6 Precautions.
12. Participants must be able to communicate with the investigator and comply with the requirements of the study procedures

Exclusion Criteria

1. Participation in other interventional trials
2. Presence of distant metastases, including node metastases in the contralateral thoracic region or in the mediastinum
3. Other malignancy diagnosed during the past five years, except adequately controlled limited basal cell carcinoma or squamous-cell carcinoma of the skin, in situ melanoma or carcinoma in situ of the cervix.
4. History of invasive breast cancer
5. History of DCIS, except for patients treated exclusively with mastectomy \>5 years prior to diagnosis of current breast cancer
6. Active cardiac disease or a history of cardiac dysfunction including any of the following:

1. History of unstable angina pectoris, myocardial infarction or recent (\<6 months) cardiovascular event including stroke and pericarditis
2. History of documented congestive heart failure (New York Heart Association functional classification II-IV)
3. Documented cardiomyopathy
4. QTc \> 450 msec as measured by Fridericia's formula, family or personal history of long or short QT syndrome, Brugada syndrome or known history of QTc prolongation or Torsade de Pointes.
5. Uncontrolled hypertension
6. Symptomatic or uncontrolled arrhythmia, including atrial fibrillation.
7. Patients with ER-positive BC being treated with drugs recognized as strong inhibitors or inducers of the isoenzyme CYP3A (see table 5) which cannot be discontinued at least 7 days prior to planned treatment with ribociclib.
8. Concomitant medication(s) with a known risk to prolong the QT interval and/or known to cause Torsades de Pointes that cannot be discontinued or replaced by safe alternative medication
9. Pregnant or breastfeeding female patients, or patients who are planning to become pregnant
10. History of (non-infectious) Interstitial Lung Disease (ILD) / pneumonitis that required steroids, has current ILD/pneumonitis, or where suspected ILD/pneumonitis cannot be ruled out by imaging at screening.
11. Lung-specific intercurrent clinically significant illnesses including, but not limited to, any underlying pulmonary disorder (e.g. pulmonary emboli within three months of the study enrollment, severe asthma, severe COPD, restrictive lung disease, pleural effusion etc.)
12. Any autoimmune, connective tissue or inflammatory disorders (e.g. Rheumatoid arthritis, Sjogren's, sarcoidosis etc.) where there is documented, or a suspicion of pulmonary involvement at the time of screening. Full details of the disorder should be recorded in the eCRF for patients who are included in the study.
13. Prior pneumonectomy
14. History of positive testing for HIV or known AIDS
15. Acute or chronic infection with hepatitis B or C virus
16. Any impairment of gastrointestinal (GI) function or GI disease that may significantly alter the absorption of the study drugs (e.g., uncontrolled ulcerative diseases, uncontrolled nausea, vomiting, diarrhea, malabsorption syndrome, or small bowel resection).
17. Receipt of live, attenuated vaccine within 30 days prior to the first dose of trastuzumab deruxtecan. Note: Patients, if enrolled, should not receive live vaccine during the study and up to 30 days after the last dose of study drug.
18. Any psychological, including substance abuse, familial, sociological or geographical condition potentially hampering compliance with the study protocol and follow-up schedule; those conditions should be discussed with the patient before registration in the trial.
19. Allergic reactions or hypersensitivity to the study drugs or other monoclonal antibodies
20. Administration of other experimental drugs, either concomitantly or during the past 30 days before treatment initiation.
21. Pre-treatment axillary surgery
22. Recent major surgery (within 4 weeks from start of study treatment) or anticipated need for major surgery during the study.
23. A pleural effusion, ascites or pericardial effusion that requires drainage, peritoneal shunt, or Cell-free and Concentrated Ascites Reinfusion Therapy (CART).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Karolinska University Hospital

OTHER

Sponsor Role lead

Responsible Party

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Theodoros Foukakis

Associate Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Theodoros Foukakis, MD/PhD

Role: PRINCIPAL_INVESTIGATOR

Karolinska University Hospital

Alexios Matikas, MD/PhD

Role: PRINCIPAL_INVESTIGATOR

Karolinska University Hospital

Locations

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Skåne University Hospital

Malmo, , Sweden

Site Status NOT_YET_RECRUITING

Örebro University Hospital

Örebro, , Sweden

Site Status NOT_YET_RECRUITING

Sankt Gorans Hospital

Stockholm, , Sweden

Site Status NOT_YET_RECRUITING

Stockholm Southern Hospital

Stockholm, , Sweden

Site Status NOT_YET_RECRUITING

Karolinska University Hospital

Stockholm, , Sweden

Site Status RECRUITING

Norrlands University Hospital

Umeå, , Sweden

Site Status NOT_YET_RECRUITING

Uppsala University Hospital

Uppsala, , Sweden

Site Status NOT_YET_RECRUITING

Countries

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Sweden

Central Contacts

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Mats Hellström, BSc

Role: CONTACT

(0046)0812370000

Facility Contacts

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Fredrika Killander, MD/PhD

Role: primary

(0046)046177428

Antonios Valachis, MD-PhD

Role: primary

(0046)0735617691

Luisa Edman Kessler, MD/PhD

Role: primary

+46736160284

Elin Barnekow, MD

Role: primary

(0046)0736565798

Alexios Matikas, MD/PhD

Role: primary

+46767823322

Anne Andersson, MD/PhD

Role: primary

(0046)0907857887

Henrik Lindman, MD/PhD

Role: primary

(0046)0706884878

References

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Matikas A, Naume B, Wildiers H, Sonke G, Dieci MV, Karakatsanis A, Andersson A, Barnekow E, Kessler LE, Einbeigi Z, Killander F, Linderholm B, Schiza A, Valachis A, Nearchou A, Engebraaten O, Porojnicu A, Soland MH, Mannsaker B, Raj SX, Blix ES, Nordstrand CS, Lambertini M, Vernieri C, Punie K, Sotiriou C, Bergh J, Villacampa G, Zouzos A, Hellstrom M, Hartman J, Foukakis T. Randomised trial of trastuzumab deruxtecan and biology-driven selection of neoadjuvant treatment for HER2-positive breast cancer: a study protocol of ARIADNE. BMJ Open. 2025 Aug 27;15(8):e102626. doi: 10.1136/bmjopen-2025-102626.

Reference Type DERIVED
PMID: 40866060 (View on PubMed)

Other Identifiers

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ARIADNE

Identifier Type: -

Identifier Source: org_study_id

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