A Study of AC Followed by a Combination of Paclitaxel Plus Trastuzumab or Lapatinib or Both Given Before Surgery to Patients With Operable HER2 Positive Invasive Breast Cancer

NCT ID: NCT00486668

Last Updated: 2016-06-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

529 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-07-31

Study Completion Date

2017-03-31

Brief Summary

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The primary purpose of this study is to determine whether breast cancer tumors respond (as measured by pathologic complete response: the absence of microscopic evidence of invasive tumor cells in the breast) to combined chemotherapy of AC(doxorubicin and cyclophosphamide) followed by paclitaxel plus trastuzumab or lapatinib or both given before surgery to patients with HER2-positive breast cancer. Trastuzumab will also be given to all patients after surgery. The study will also evaluate the toxic effects of the chemotherapy combination, including effects on the heart, and will determine survival and progression-free survival 5 years after treatment. Also, the study will look at whether there are gene expression profiles in the tumor tissue that can predict pathologic complete response.

Detailed Description

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Women with breast cancers that overexpress HER2 are at greater risk for disease progression and death than women whose tumors do not overexpress HER2. Trastuzumab, a recombinant humanized monoclonal antibody against the extracellular domain of the HER2 protein blocks downstream signaling of HER2 and substantially improves the efficacy of chemotherapy in women with metastatic and early-stage HER2-positive breast cancers. Because resistance to trastuzumab eventually results in progressive disease in the metastatic setting and contributes to recurrence following adjuvant trastuzumab-based therapy, it is important to develop agents other than trastuzumab that target HER2 signaling through different mechanisms of action. Lapatinib is an oral, small molecule, dual tyrosine kinase inhibitor of HER2 and EGFR. Lapatinib has shown a lack of cross-resistance with trastuzumab in preclinical studies and activity in women with HER2-positive, metastatic breast cancer that has progressed during trastuzumab treatment. Trastuzumab blocks the downstream signaling of HER2 by binding to the extracellular domain of the receptor. Lapatinib binds to the intracellular domains of HER2 and EGFR and prevents activation of downstream signaling pathways. Because of this different mechanism of action, lapatinib may be effective in trastuzumab-resistant disease. The study will also provide important safety information on trastuzumab and lapatinib combinations immediately following anthracycline exposure, and also provide an initial direct comparison of cardiac effects of trastuzumab and lapatinib when incorporated into a standard sequential AC followed by weekly paclitaxel (neo)adjuvant regimen.

Availability of a second agent that can interrupt HER2-signaling pathways through completely different mechanisms than those of trastuzumab offers the potential for further improvement in the management of patients with HER2-overexpressing breast cancer in both the adjuvant and metastatic setting. Co-administration of both trastuzumab and lapatinib with chemotherapy may be important in improving outcomes in subsets of HER2-positive breast cancers. However, use of two inhibitors of the HER2 pathway will increase costs and may increase toxicity, so it will be important to identify the subsets of patients who would benefit from the dual therapy. Inhibition of HER2 with a single agent clearly is sufficient for many patients as evidenced by the results of the trastuzumab trials. Therefore, co-administration to unselected populations of women with HER2-positive breast cancers would not represent an optimal approach. Given the activity of lapatinib, it is likely that it will also be sufficiently active in inhibiting HER2-pathway activation in some patients to allow for its use as the sole inhibitor of the HER2 pathway. Different populations may also derive greater benefit from one of the HER2-blocking agents relative to the other. Identification of potential predictive factors for pathologic complete response to the combination or to either agent administered alone in neoadjuvant trials would provide important information for adjuvant trials designed to definitively address these important issues.

This study will compare 3 combined chemotherapy regimens: AC followed by paclitaxel plus trastuzumab and lapatinib, AC followed by paclitaxel plus lapatinib, and AC followed by paclitaxel plus trastuzumab given before surgery to patients with HER2-positive breast cancer.

Conditions

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Invasive Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group 1: AC then paclitaxel + trastuzumab

AC followed by paclitaxel plus trastuzumab

Group Type ACTIVE_COMPARATOR

doxorubicin

Intervention Type DRUG

60 mg/m2 IV every 21 days for cycles 1-4

cyclophosphamide

Intervention Type DRUG

600 mg/m2 IV every 21 days for cycles 1-4

paclitaxel

Intervention Type DRUG

80 mg/m2 IV on days 1, 8, and 15 every 28 days for cycles 5-8

trastuzumab

Intervention Type DRUG

First dose: 4 mg/kg IV, subsequent doses: 2 mg/kg IV weekly beginning on day 1 of the first paclitaxel cycle until 1-7 days before surgery

Group 2: AC then paclitaxel + lapatinib

AC followed by paclitaxel plus lapatinib

Group Type EXPERIMENTAL

doxorubicin

Intervention Type DRUG

60 mg/m2 IV every 21 days for cycles 1-4

cyclophosphamide

Intervention Type DRUG

600 mg/m2 IV every 21 days for cycles 1-4

paclitaxel

Intervention Type DRUG

80 mg/m2 IV on days 1, 8, and 15 every 28 days for cycles 5-8

lapatinib

Intervention Type DRUG

Group 2: 1250 mg PO daily beginning on day 1 of the first paclitaxel cycle until 1 day before surgery. Group 3: 750 mg PO daily beginning on day 1 of the first paclitaxel cycle until 1 day before surgery.

Group 3: AC then paclitaxel + trastuzumab + lapatinib

AC followed by paclitaxel plus trastuzumab plus lapatinib

Group Type EXPERIMENTAL

doxorubicin

Intervention Type DRUG

60 mg/m2 IV every 21 days for cycles 1-4

cyclophosphamide

Intervention Type DRUG

600 mg/m2 IV every 21 days for cycles 1-4

paclitaxel

Intervention Type DRUG

80 mg/m2 IV on days 1, 8, and 15 every 28 days for cycles 5-8

trastuzumab

Intervention Type DRUG

First dose: 4 mg/kg IV, subsequent doses: 2 mg/kg IV weekly beginning on day 1 of the first paclitaxel cycle until 1-7 days before surgery

lapatinib

Intervention Type DRUG

Group 2: 1250 mg PO daily beginning on day 1 of the first paclitaxel cycle until 1 day before surgery. Group 3: 750 mg PO daily beginning on day 1 of the first paclitaxel cycle until 1 day before surgery.

Interventions

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doxorubicin

60 mg/m2 IV every 21 days for cycles 1-4

Intervention Type DRUG

cyclophosphamide

600 mg/m2 IV every 21 days for cycles 1-4

Intervention Type DRUG

paclitaxel

80 mg/m2 IV on days 1, 8, and 15 every 28 days for cycles 5-8

Intervention Type DRUG

trastuzumab

First dose: 4 mg/kg IV, subsequent doses: 2 mg/kg IV weekly beginning on day 1 of the first paclitaxel cycle until 1-7 days before surgery

Intervention Type DRUG

lapatinib

Group 2: 1250 mg PO daily beginning on day 1 of the first paclitaxel cycle until 1 day before surgery. Group 3: 750 mg PO daily beginning on day 1 of the first paclitaxel cycle until 1 day before surgery.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Female
* 18 years or older
* ECOG performance status of 0 or 1
* Primary breast tumor palpable and measures greater than or equal to 2.0 cm by physical exam
* Diagnosis of invasive adenocarcinoma made by core needle biopsy
* Breast cancer determined to be HER2-positive
* LVEF assessment by MUGA scan or ECG within 3 months prior to randomization
* Blood counts must meet the following criteria:

* ANC greater than or equal to 1200/mm3
* Platelet count greater than or equal to 100,000/mm3
* Hemoglobin greater than or equal to 10 g/dL
* Serum creatinine less than or equal to ULN for the lab
* Adequate hepatic function by these criteria:

* Total bilirubin less than or equal to the ULN for the lab unless the patient has a bilirubin elevation greater than ULN to 1.5 x ULN resulting from Gilbert's disease or similar syndrome due to slow conjugation of bilirubin; and
* Alkaline phosphatase less than or equal to 2.5 x ULN; and
* AST less than or equal to 1.5 x ULN for the lab.
* If skeletal pain present or alkaline phosphatase greater than ULN (but less than or equal to 2.5 x ULN), bone scan or PET scan must not demonstrate metastatic disease
* If AST or alkaline phosphatase greater than ULN , liver imaging (CT, MRI or PET scan) must not demonstrate definitive metastatic disease and the requirements in criterion for hepatic function must be met
* Able to swallow oral medications

Exclusion Criteria

* FNA alone to diagnose the primary tumor
* Excisional biopsy or lumpectomy was performed prior to randomization
* Surgical axillary staging procedure prior to randomization. Exceptions: 1) FNA or core biopsy of an axillary node for any patient, and 2) although not recommended, a pre-neoadjuvant therapy SN biopsy for patients with clinically negative axillary nodes.
* Tumors clinically staged as T4
* Ipsilateral cN2b or cN3 disease (Patients with cN1 or cN2a disease are eligible)
* Definitive clinical or radiologic evidence of metastatic disease
* Synchronous bilateral invasive breast cancer
* Requirement for chronic use of any of the medications or substances specified in the protocol
* Treatment including RT, chemotherapy, and/or targeted therapy for the currently diagnosed breast cancer prior to randomization
* Any sex hormonal therapy, e.g., birth control pills, ovarian hormone replacement therapy, etc. (These patients are eligible if therapy is discontinued prior to randomization)
* Continued therapy with any hormonal agent such as raloxifene, tamoxifen, or other SERM. (Patients are eligible only if these medications are discontinued prior to randomization)
* Prior history of breast cancer, including DCIS (Patients with a history of LCIS are eligible)
* Prior therapy with anthracyclines, taxanes, trastuzumab, or lapatinib for any malignancy
* Other malignancies unless the patient is considered to be disease-free for 5 or more years prior to randomization and is deemed by her physician to be at low risk for recurrence. Patients with the following cancers are eligible if diagnosed and treated within the past 5 years: carcinoma in situ of the cervix, carcinoma in situ of the colon, melanoma in situ, and basal cell and squamous cell carcinoma of the skin.
* Cardiac disease that would preclude the use of the drugs included in the B-41 treatment regimens. This includes but is not confined to:

* Active cardiac disease:

* angina pectoris requiring the use of anti-anginal medication;
* ventricular arrhythmias except for benign premature ventricular contractions controlled by medication;
* conduction abnormality requiring a pacemaker;
* supraventricular and nodal arrhythmias requiring a pacemaker or not controlled with medication; and
* clinically significant valvular disease.
* History of cardiac disease:

* myocardial infarction;
* congestive heart failure; or
* cardiomyopathy.
* Uncontrolled hypertension, defined as blood pressure greater than 150/90 mm/Hg on antihypertensive therapy
* History of or current symptomatic interstitial pneumonitis or pulmonary fibrosis or definitive evidence of interstitial pneumonitis or pulmonary fibrosis described on CT or chest x-ray in asymptomatic patients
* Sensory/motor neuropathy greater than or equal to grade 2, as defined by the NCI's CTCAE v3.0
* Malabsorption syndrome, ulcerative colitis, resection of the stomach or small bowel, or other disease significantly affecting gastrointestinal function
* Other non-malignant systemic disease that would preclude treatment with any of the treatment regimens or would prevent required follow-up
* Conditions that would prohibit administration of corticosteroids
* Administration of any investigational agents within 30 days before randomization
* Pregnancy or lactation
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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GlaxoSmithKline

INDUSTRY

Sponsor Role collaborator

NSABP Foundation Inc

NETWORK

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Norman Wolmark, MD

Role: PRINCIPAL_INVESTIGATOR

NSABP Foundation Inc

Locations

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MBCCOP, Gulf Coast

Mobile, Alabama, United States

Site Status

Scripps Cancer Center-San Diego

La Jolla, California, United States

Site Status

University of California, Irvine Medical Center

Long Beach, California, United States

Site Status

Pacific Shores Medical Group

Long Beach, California, United States

Site Status

St. Joseph Hospital

Orange, California, United States

Site Status

Desert Regional Medical Center Comprehensive Cancer Center

Palm Springs, California, United States

Site Status

Stanford University Medical Center

Palo Alto, California, United States

Site Status

Sutter Medical Center

Sacramento, California, United States

Site Status

Kaiser Permanente-San Diego

San Diego, California, United States

Site Status

Santa Rosa Memorial Hospital

Santa Rosa, California, United States

Site Status

Kaiser Permanente-Vallejo

Vallejo, California, United States

Site Status

University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status

Memorial Hospital

Colorado Springs, Colorado, United States

Site Status

Kaiser Permanente-Franklin

Denver, Colorado, United States

Site Status

CCOP-Colorado Cancer Research Prog. Inc.(Administrative Only)

Denver, Colorado, United States

Site Status

Kaiser Permanente Rock Creek

Lafayette, Colorado, United States

Site Status

Hartford Hospital

Hartford, Connecticut, United States

Site Status

Eastern Connecticut Hematology & Oncology Associates

Norwich, Connecticut, United States

Site Status

Sibley Memorial Hospital

Washington D.C., District of Columbia, United States

Site Status

MD Anderson Cancer Center

Orlando, Florida, United States

Site Status

Phoebe Putney Memorial Hospital

Albany, Georgia, United States

Site Status

MBCCOP, Medical College of Georgia Research Institute

Augusta, Georgia, United States

Site Status

University of Hawaii

Honolulu, Hawaii, United States

Site Status

Kaiser Permanente Hawaii - Moanalua Med Center

Honolulu, Hawaii, United States

Site Status

Kootenai Cancer Center

Coeur d'Alene, Idaho, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Decatur Memorial Hospital

Decatur, Illinois, United States

Site Status

Cancer Institute at Alexian Brothers Hospital Network

Elk Grove, Illinois, United States

Site Status

Edward Hospital

Naperville, Illinois, United States

Site Status

Edward Cancer Center Plainfield

Plainfield, Illinois, United States

Site Status

CCOP, Central Illinois

Springfield, Illinois, United States

Site Status

CCOP, Carle Cancer Center

Urbana, Illinois, United States

Site Status

St. Vincent Hospital and Health Care Center

Indianapolis, Indiana, United States

Site Status

CCOP, Northern Indiana Cancer Research Consortium

South Bend, Indiana, United States

Site Status

CCOP, Des Moines, IA

Des Moines, Iowa, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

CCOP, Sioux Community Cancer consortium

Sioux City, Iowa, United States

Site Status

CCOP, Wichita KS

Wichita, Kansas, United States

Site Status

University of Kentucky Medical Center

Lexington, Kentucky, United States

Site Status

NortonHealtcare Inc.

Louisville, Kentucky, United States

Site Status

CCOP, Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status

Greater Baltimore Medical Center

Baltimore, Maryland, United States

Site Status

Franklin Square Hospital Center

Baltimore, Maryland, United States

Site Status

Boston Medical Center

Boston, Massachusetts, United States

Site Status

CCOP, Michigan Cancer Research Consortium

Ann Arbor, Michigan, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

CCOP, Grand Rapids Clnical Oncology Program

Grand Rapids, Michigan, United States

Site Status

CCOP, Kalamazoo, MI

Kalamazoo, Michigan, United States

Site Status

Michigan State University - Breslin Cancer Center

Lansing, Michigan, United States

Site Status

CCOP, William Beaumont Hospital

Royal Oak, Michigan, United States

Site Status

Providence Hospital - Southfield

Southfield, Michigan, United States

Site Status

Hennepin County Medical Center

Minneapolis, Minnesota, United States

Site Status

CCOP, Metro-Minnesota

Minneapolis, Minnesota, United States

Site Status

University of Missouri-Ellis Fischel

Columbia, Missouri, United States

Site Status

CCOP, Kansas City (Administrative Only)

Kansas City, Missouri, United States

Site Status

CCOP, Ozark Health Ventures LLC

Springfield, Missouri, United States

Site Status

Saint Louis UniversityHealth Sciences Center

St Louis, Missouri, United States

Site Status

CCOP, Heartland Cancer Research

St Louis, Missouri, United States

Site Status

CCOP, Montana Cancer Consortium

Billings, Montana, United States

Site Status

CCOP, Missouri Valley Consortium

Omaha, Nebraska, United States

Site Status

Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

Site Status

Newark Beth Israel Medical Center

Newark, New Jersey, United States

Site Status

New York Oncology Hematology PC-Albany

Albany, New York, United States

Site Status

Cancer Center at Glens Falls Hospital

Glens Falls, New York, United States

Site Status

CCOP, Hematology-Oncology Associates of CNY

Syracuse, New York, United States

Site Status

Alamance Regional Medical Center

Burlington, North Carolina, United States

Site Status

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

CCOP, Southeast Cancer Control Consortium

Charlotte, North Carolina, United States

Site Status

Alamance Regional Medical Center - Off site Clinic

Mebane, North Carolina, United States

Site Status

Wake Forest University School of Medicine

Winston-Salem, North Carolina, United States

Site Status

Akron City Hospital

Akron, Ohio, United States

Site Status

Aultman Hospital

Canton, Ohio, United States

Site Status

Case Western Reserve/University Hospitals-Ireland Cancer Cntr.

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

CCOP, Columbus, OH

Columbus, Ohio, United States

Site Status

CCOP, Dayton, OH

Dayton, Ohio, United States

Site Status

CCOP, Oklahoma

Tulsa, Oklahoma, United States

Site Status

Lehigh Valley Hospital

Allentown, Pennsylvania, United States

Site Status

Geisinger Clinic

Danville, Pennsylvania, United States

Site Status

Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Albert Einstein Healthcare Network

Philadelphia, Pennsylvania, United States

Site Status

Allegheny General Hospital/Allegheny-Singer Research Institute

Pittsburgh, Pennsylvania, United States

Site Status

NSABP Foundation, Inc.

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Western Pennsylvania Hospital

Pittsburgh, Pennsylvania, United States

Site Status

Mercy Hospital

Scranton, Pennsylvania, United States

Site Status

Reading Hospital & Medical Center

West Reading, Pennsylvania, United States

Site Status

CCOP, Main Line Health

Wynnewood, Pennsylvania, United States

Site Status

CCOP, Upstate Carolina

Spartanburg, South Carolina, United States

Site Status

Sanford Cancer Center

Souix Falls, South Dakota, United States

Site Status

Thompson Cancer Survival Center-Dowell Springs

Knoxville, Tennessee, United States

Site Status

Joe Arrington Cancer Research & Treatment Center

Lubbock, Texas, United States

Site Status

University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

MBCCOP, Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Puget Sound Oncology Consortium

Seattle, Washington, United States

Site Status

CCOP, Virginia Mason

Seattle, Washington, United States

Site Status

CCOP, Northwest

Tacoma, Washington, United States

Site Status

West Virginia University Hospitals Inc.

Morgantown, West Virginia, United States

Site Status

Camden-Clark Memorial Hospital

Parkersburg, West Virginia, United States

Site Status

Wheeling Hospital

Wheeling, West Virginia, United States

Site Status

CCOP, Marshfield Clinic

Marshfield, Wisconsin, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Odette Cancer Centre

Toronto, Ontario, Canada

Site Status

Royal Victoria Hospital

Montreal, Quebec, Canada

Site Status

Jewish General Hospital

Montreal, Quebec, Canada

Site Status

St. Mary's Hospital Center

Montreal, Quebec, Canada

Site Status

University of Montreal Hospital Group

Montreal, Quebec, Canada

Site Status

Centre Hospitalier Affilie Universitaire De Quebec, Hospital du St-Sacrement

Québec, Quebec, Canada

Site Status

MBCCOP, San Juan, Puerto Rico

San Juan, , Puerto Rico

Site Status

Countries

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United States Canada Puerto Rico

References

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Robidoux A, Tang G, Rastogi P, Geyer CE Jr, Azar CA, Atkins JN, Fehrenbacher L, Bear HD, Baez-Diaz L, Sarwar S, Margolese RG, Farrar WB, Brufsky AM, Shibata HR, Bandos H, Paik S, Costantino JP, Swain SM, Mamounas EP, Wolmark N. Lapatinib as a component of neoadjuvant therapy for HER2-positive operable breast cancer (NSABP protocol B-41): an open-label, randomised phase 3 trial. Lancet Oncol. 2013 Nov;14(12):1183-92. doi: 10.1016/S1470-2045(13)70411-X. Epub 2013 Oct 4.

Reference Type BACKGROUND
PMID: 24095300 (View on PubMed)

Rastogi P, Tang G, Hassan S, Geyer CE Jr, Azar CA, Magrinat GC, Suga JM, Bear HD, Baez-Diaz L, Sarwar S, Boileau JF, Brufsky AM, Shibata HR, Bandos H, Paik S, Yothers G, Swain SM, Mamounas EP, Wolmark N. Long-term outcomes of dual vs single HER2-directed neoadjuvant therapy in NSABP B-41. Breast Cancer Res Treat. 2023 Jun;199(2):243-252. doi: 10.1007/s10549-023-06881-8. Epub 2023 Mar 22.

Reference Type DERIVED
PMID: 36944848 (View on PubMed)

Other Identifiers

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NSABP B-41

Identifier Type: -

Identifier Source: org_study_id

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