Trastuzumab Deruxtecan (DS-8201a) Versus Investigator's Choice for HER2-low Breast Cancer That Has Spread or Cannot be Surgically Removed [DESTINY-Breast04]

NCT ID: NCT03734029

Last Updated: 2025-10-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

557 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-27

Study Completion Date

2026-08-01

Brief Summary

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This study will compare DS-8201a to physician choice standard treatment.

Participants must have HER2-low breast cancer that has been treated before.

Participants' cancer:

* Cannot be removed by an operation
* Has spread to other parts of the body

Detailed Description

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This is a randomized, 2-arm, Phase 3, open-label, multicenter study to compare the safety and efficacy of trastuzumab deruxtecan versus the physician's choice (2:1) in HER2-low, unresectable and/or metastatic breast cancer participants.

The Sponsor proposes to define a new HER2-low population in this trial including tumors with IHC 1+ and IHC 2+/ISH- HER2 expression.

Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Parallel model, randomized at a 2:1 ratio
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Trastuzumab deruxtecan

HER2-low, unresectable, and/or metastatic breast cancer participants previously treated with chemotherapy randomized to DS8201a

Group Type EXPERIMENTAL

Trastuzumab deruxtecan (DS-8201a)

Intervention Type DRUG

DS-8201a is a lyophilized powder reconstituted into a sterile aqueous solution (100 mg/5 mL) to be administered intravenously

Physician's Choice

HER2-low, unresectable, and/or metastatic breast cancer participants previously treated with chemotherapy randomized to Physician's choice from the following options:

* Capecitabine
* Eribulin
* Gemcitabine
* Paclitaxel
* Nab-paclitaxel

Group Type ACTIVE_COMPARATOR

Capecitabine

Intervention Type DRUG

Administered according to label, as one option for Physician's Choice (determined before randomization)

Eribulin

Intervention Type DRUG

Administered according to label, as one option for Physician's Choice (determined before randomization)

Gemcitabine

Intervention Type DRUG

Administered according to label, as one option for Physician's Choice (determined before randomization)

Paclitaxel

Intervention Type DRUG

Administered according to label, as one option for Physician's Choice (determined before randomization)

Nab-paclitaxel

Intervention Type DRUG

Administered according to label, as one option for Physician's Choice (determined before randomization)

Interventions

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Trastuzumab deruxtecan (DS-8201a)

DS-8201a is a lyophilized powder reconstituted into a sterile aqueous solution (100 mg/5 mL) to be administered intravenously

Intervention Type DRUG

Capecitabine

Administered according to label, as one option for Physician's Choice (determined before randomization)

Intervention Type DRUG

Eribulin

Administered according to label, as one option for Physician's Choice (determined before randomization)

Intervention Type DRUG

Gemcitabine

Administered according to label, as one option for Physician's Choice (determined before randomization)

Intervention Type DRUG

Paclitaxel

Administered according to label, as one option for Physician's Choice (determined before randomization)

Intervention Type DRUG

Nab-paclitaxel

Administered according to label, as one option for Physician's Choice (determined before randomization)

Intervention Type DRUG

Other Intervention Names

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DS-8201a

Eligibility Criteria

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Inclusion Criteria

* Is the age of majority in their country
* Has pathologically documented breast cancer that:

1. Is unresectable or metastatic
2. Has low-HER2 expression defined as IHC 2+/ISH- or IHC 1+ (ISH- or untested)
3. Is HR-positive or HR-negative
4. Has progressed on, and would no longer benefit from, endocrine therapy
5. Has been treated with 1 to 2 prior lines of chemotherapy/adjuvant in the recurrent or metastatic setting
6. Was never previously HER2-positive (ICH 3+ or ISH+) on prior pathology testing (per American Society of Clinical Oncology-College of American Pathologists \[ASCO-CAP\] guidelines)
* Has documented radiologic progression (during or after most recent treatment)
* Has adequate archival tumor samples available or is wiling to provide fresh biopsies prior to randomization for:

1. assessment of HER2 status
2. assessment of post-treatment status
* Has at least 1 measurable lesion per Response Evaluation Criteria In Solid Tumors 1.1
* Has protocol-defined adequate cardiac, bone marrow, renal, hepatic and blood clotting functions
* Male and female participants of reproductive/childbearing potential, agrees to follow instructions for method(s) of contraception and agrees to avoid preserving ova or sperm for at least 4.5 months after treatment (or longer, per locally approved labels)

Exclusion Criteria

* Is ineligible for all options in the physician's choice arm
* Has breast cancer ever assessed with high-HER2 expression
* Has previously been treated with any anti-HER2 therapy, including an antibody drug conjugate
* Has uncontrolled or significant cardiovascular disease
* Has spinal cord compression or clinically active central nervous system metastases
* Has history of (noninfectious) interstitial lung disease (ILD)/pneumonitis that required steroids, has current ILD/pneumonitis, or suspected ILD/pneumonitis that cannot be ruled out by imaging at screening
* Has any medical history or condition that per protocol or in the opinion of the investigator is inappropriate for the study
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Daiichi Sankyo Co., Ltd.

INDUSTRY

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role collaborator

Daiichi Sankyo

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Global Clinical Leader

Role: STUDY_DIRECTOR

Daiichi Sankyo

Locations

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Ironwood Cancer & Research Centers - Chandler II

Chandler, Arizona, United States

Site Status

Banner MD Anderson Cancer Center

Gilbert, Arizona, United States

Site Status

Cancer Treatment Centers of America at Western Regional Medical Center

Goodyear, Arizona, United States

Site Status

UCLA School of Medicine

Los Angeles, California, United States

Site Status

Stanford Cancer Institute

Palo Alto, California, United States

Site Status

Cancer Care Associates Medical Group, Inc. TORI

Redondo Beach, California, United States

Site Status

University of California at San Francisco (PARENT)

San Francisco, California, United States

Site Status

Eastern Connecticut Hematology/Oncology Assoc.

Norwich, Connecticut, United States

Site Status

Christiana Care Health Services, Inc.

Newark, Delaware, United States

Site Status

Sylvester Comprehensive Cancer Center - Deerfield Beach

Boca Raton, Florida, United States

Site Status

Florida Cancer Specialists (South Region)

Fort Myers, Florida, United States

Site Status

Memorial Healthcare System MRH Cancer Center

Hollywood, Florida, United States

Site Status

Orlando Health, Inc.

Orlando, Florida, United States

Site Status

Moffitt Cancer Center -Tampa

Tampa, Florida, United States

Site Status

Cancer Treatment Centers of America-Georgia

Newnan, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Cancer Treatment Centers of America

Zion, Illinois, United States

Site Status

Cancer Center of Kansas

Wichita, Kansas, United States

Site Status

Touro Infirmary

New Orleans, Louisiana, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, United States

Site Status

Saint Barnabas Medical Center

Livingston, New Jersey, United States

Site Status

New York University Medical Center

New York, New York, United States

Site Status

Memorial Sloan Kettering Hospital

New York, New York, United States

Site Status

Weill Cornell Medicine Breast Center

New York, New York, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center Health System

Pittsburgh, Pennsylvania, United States

Site Status

St Francis Hospital

Greenville, South Carolina, United States

Site Status

Brig Center for Cancer Care and Survivorship

Knoxville, Tennessee, United States

Site Status

Baptist Cancer Center

Memphis, Tennessee, United States

Site Status

Tennessee Oncology - Skyline Satellite

Nashville, Tennessee, United States

Site Status

BloomTrials Clinical Research, LLC

Dallas, Texas, United States

Site Status

The Methodist Hospital Research Institute

Houston, Texas, United States

Site Status

University of Texas M. D. Anderson Cancer Center - Investigational Cancer Therapeutics

Houston, Texas, United States

Site Status

Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status

Medizinische Universität Innsbruck

Innsbruck, , Austria

Site Status

Kepler Universitätsklinikum

Linz, , Austria

Site Status

LKH - Universitätsklinikum der PMU Salzburg

Salzburg, , Austria

Site Status

AKH - Medizinische Universität Wien (4305)

Vienna, , Austria

Site Status

Klinikum Wels-Grieskirchen GmbH

Wels, , Austria

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Brussel

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

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Grand Hôpital de Charleroi

Loverval, , Belgium

Site Status

CHU UCL Namur

Namur, , Belgium

Site Status

Centre Hospitalier Wallonie picarde - Site IMC

Tournai, , Belgium

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Tom Baker Cancer Center

Calgary, Alberta, Canada

Site Status

Toronto Sunnybrook Hospital

Toronto, Ontario, Canada

Site Status

McGill University - Dept. Oncology Clinical Research Program

Montreal, Quebec, Canada

Site Status

Anhui Provincial Hospital

Hefei, Anhui, China

Site Status

Cancer Hospital Chinese Academy of Medical Sciences

Beijing, Beijing Municipality, China

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Chinese PLA General Hospital

Beijing, Beijing Municipality, China

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Fuzhou General Hospital of Nanjing Military Area Command of Chinese PLA

Fuzhou, Fujian, China

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Sun Yat-sen Memorial hospital, Sun Yat-sen University

Guangzhou, Guangdong, China

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Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, China

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Hubei Cancer Hospital

Wuhan, Hubei, China

Site Status

The Affiliated Drum Tower Hospital of Nanjing University

Nanjing, Jiangsu, China

Site Status

The First Hospital of Jilin University

Changchun, Jilin, China

Site Status

Jilin Cancer Hospital

Changchun, Jilin, China

Site Status

Liaoning Cancer Hospital & Institute

Shenyang, Liaoning, China

Site Status

General Hospital of Ningxia Medical University

Yinchuan, Ningxia Hui, China

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Linyi Cancer Hospital

Linyi, Shandong, China

Site Status

Shanghai General Hospital

Shanghai, Shanghai Municipality, China

Site Status

Fudan University Shanghai Cancer Center

Shanghai, Shanghai Municipality, China

Site Status

West China Hospital, Sichuan University

Chengdu, Sichuan, China

Site Status

Sir Run Run Shaw Hospital, Zhejiang University, School of Medicine

Hangzhou, Zhejiang, China

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Zhejiang Cancer Hospital

Hangzhou, Zhejiang, China

Site Status

Institut Paoli Calmettes

Marseille, Bouches-du-Rhône, France

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Centre François Baclesse

Caen, Calvados, France

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CARIO - Centre Armoricain de Radiothérapie, Imagerie médicale et Oncologie

Plérin, Cotes d'Armor, France

Site Status

CHU Brest - Hôpital Morvan

Brest, Finistere, France

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Institut Bergonié

Bordeaux, Gironde, France

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Clinique Clementville

Montpellier, Herault, France

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Institut Régional du Cancer de Montpellier

Montpellier, Herault, France

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CRLCC Eugene Marquis

Rennes, Ille Et Vilaine, France

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ICO - Site René Gauducheau

Saint-Herblain, Loire Atlantique, France

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Centre Hospitalier Emile Roux

Le Puy-en-Velay, Loiret, France

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ICO - Site Paul Papin

Angers, Maine Et Loire, France

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Centre Hospitalier Valenciennes

Valenciennes, Nord, France

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Hôpital Saint-Louis - Paris

Paris, Paris, France

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Clinique Victor Hugo - Centre Jean Bernard

Le Mans, Sarthe, France

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Institut Sainte Catherine

Avignon, Vaculuse, France

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Hôpital d'Instruction des Armees Begin*

Saint-Mandé, Val De Marne, France

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Institut Gustave Roussy

Villejuif, Val De Marne, France

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Institut Curie - site de Paris

Paris, , France

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Hopital Tenon

Paris, , France

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Universitaetsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Klinikum der Universitaet Muenchen - Campus Grosshardern

Munich, Bavaria, Germany

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General Hospital of Athens "Alexandra"

Athens, , Greece

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General Oncology Hospital of Kifissia " Agioi Anargyroi"

Athens, , Greece

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Athens Medical Center

Athens, , Greece

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University General Hospital of Heraklion

Heraklion, , Greece

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University General Hospital of Larissa

Larissa, , Greece

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Bioclinic Thessaloniki

Thessaloniki, , Greece

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Euromedica General Clinic Thessaloniki

Thessaloniki, , Greece

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General Hospital Papageorgiou

Thessaloniki, , Greece

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Interbalkan Hospital of Thessaloniki

Thessaloniki, , Greece

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Del-pesti Centrumkorhaz - Orszagos Hematologiai es Infektologiai Intezet

Budapest, , Hungary

Site Status

Orszagos Onkologiai Intezet

Budapest, , Hungary

Site Status

Debreceni Egyetem

Debrecen, , Hungary

Site Status

Bekes Megyei Kozponti Korhaz Pandy Kalman Tagkorhaza

Gyula, , Hungary

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SzSzB Megyei Korhazak es Egyetemi Oktatokorhaz

Nyíregyháza, , Hungary

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Jasz-Nagykun-Szolnok Megyei Hetenyi Geza Korhaz-Rendelointezet

Szolnok, , Hungary

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Rambam Health Care Center

Haifa, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Hadassah University Hospital - Ein Kerem

Jerusalem, , Israel

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Rabin Medical Center-Beilinson Campus

Petah Tikva, , Israel

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Chaim Sheba Medical Center

Ramat Gan, , Israel

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Kaplan Medical Center

Rehovot, , Israel

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Ziv Medical Center

Safed, , Israel

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Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

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Azienda Ospedaliera Card. G. Panico

Tricase, Lecce, Italy

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Azienda Socio Sanitaria Territoriale di Monza (Presidio San Gerardo)

Monza, Milano, Italy

Site Status

Istituto Clinico Humanitas

Rozzano, Milano, Italy

Site Status

Ospedale Sacro Cuore Don Calabria

Negrar, Verona, Italy

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Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status

Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia (Presidio Spedali Civili)

Brescia, , Italy

Site Status

Azienda Ospedaliera Univ. Policlinico Gaspare Rodolico

Catania, , Italy

Site Status

Azienda Ospedaliero Universitaria Mater Domini-Campus Universitario

Catanzaro, , Italy

Site Status

IEO Istituto Europeo di Oncologia

Milan, , Italy

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Istituto Nazionale Tumori Fondazione G. Pascale

Napoli, , Italy

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Ospedale degli Infermi

Rimini, , Italy

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Azienda Ospedaliera Universitaria Policlinico Tor Vergata

Roma, , Italy

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Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

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Aichi Cancer Center Hospital

Nagoya, Aichi-ken, Japan

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National Cancer Center Hospital East

Kashiwa-shi, Chiba, Japan

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NHO Shikoku Cancer Center

Matsuyama, Ehime, Japan

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NHO Kyushu Cancer Center

Fukuoka, Fukuoka, Japan

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Fukushima Medical University Hospital

Fukushima, Fukushima, Japan

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Hiroshima City Hiroshima Citizens Hospital

Hiroshima, Hiroshima, Japan

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NHO Hokkaido Cancer Center

Sapporo, Hokkaido, Japan

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Hyogo College of Medicine Hospital

Nishinomiya-shi, Hyōgo, Japan

Site Status

Hakuaikai Sagara Hospital

Kagoshima, Kagoshima-ken, Japan

Site Status

Tokai University Hospital

Isehara, Kanagawa, Japan

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Kanagawa Cancer Center

Yokohama, Kanagawa, Japan

Site Status

NHO Osaka National Hospital

Osaka, Osaka, Japan

Site Status

Kindai University Hospital

Onohigashi, Osakasayama-shi, Japan

Site Status

Saitama Cancer Center

Kitaadachi-gun, Saitama, Japan

Site Status

Shizuoka Cancer Center

Sunto-gun, Shizuoka, Japan

Site Status

Cancer Institute Hospital of JFCR

Kōtoku, Tokyo-To, Japan

Site Status

Toranomon Hospital

Minatoku, Tokyo-To, Japan

Site Status

Showa University Hospital

Shinagawa-Ku, Tokyo-To, Japan

Site Status

Hospital de Braga

Braga, , Portugal

Site Status

Centro Hospitalar do Alto do Ave, EPE

Guimarães, , Portugal

Site Status

Fundação Champalimaud

Lisbon, , Portugal

Site Status

Centro Hospitalar de Lisboa Norte, E.P.E. - Hospital de Santa Maria

Lisbon, , Portugal

Site Status

Unidade Local de Saúde de Matosinhos, EPE (Hospital Pedro Hispano)

Matosinhos Municipality, , Portugal

Site Status

Centro Hospitalar do Porto, E.P.E. - Hospital de Santo António

Porto, , Portugal

Site Status

Instituto Português de Oncologia do Porto Francisco Gentil, EPE

Porto, , Portugal

Site Status

Centro Hospitalar de Entre o Douro e Vouga, E.P.E - Hospital de São Sebastião

Santa Maria da Feira, , Portugal

Site Status

Centro Hospitalar Vila Nova de Gaia/Espinho, E.P.E

Vila Nova de Gaia, , Portugal

Site Status

Centro Hospitalar de Trás-os-Montes e Alto Douro, EPE

Vila Real, , Portugal

Site Status

FSBSI "Russian Oncological Scientific Center n.a. N.N. Blokhin"

Moscow, , Russia

Site Status

SBIH of Moscow City "Moscow City Oncology Hospital №62" of Moscow Healthcare Departement

Moscow, , Russia

Site Status

SBIH of Yaroslavl Region "Regional Clinical Oncological Hospital"

Yaroslavl, , Russia

Site Status

National Cancer Center

Goyang-si, Gyeonggi-do, South Korea

Site Status

Inha University Hospital

Incheon, Gyeonggi-do, South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Ajou University Hospital

Suwon, Gyeonggi-do, South Korea

Site Status

Chungbuk National University Hospital

Cheongju-si, North Chungcheong, South Korea

Site Status

Kyungpook National University Chilgok Hospital

Daegu, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

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Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

ICO l'Hospitalet - Hospital Duran i Reynals

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Universitario Donostia

San Sebastián, Guipuzcoa, Spain

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Complejo Hospitalario Universitario A Coruña

A Coruña, La Coruña, Spain

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Hospital Universitario de Canarias

San Cristóbal de La Laguna, Tenerife, Spain

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Hospital de Basurto

Bilbao, Vizcaya, Spain

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Hospital del Mar

Barcelona, , Spain

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Hospital Quironsalud Barcelona

Barcelona, , Spain

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Hospital Universitari Vall d'Hebron

Barcelona, , Spain

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Hospital Clinic de Barcelona

Barcelona, , Spain

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MD Anderson Cancer Centre

Madrid, , Spain

Site Status

Hospital Ruber Internacional

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

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Hospital Universitario Clinico San Carlos

Madrid, , Spain

Site Status

Hospital Clinico Universitario Virgen de la Victoria

Málaga, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Instituto Valenciano de Oncologia IVO

Valencia, , Spain

Site Status

Hospital General Universitario de Valencia

Valencia, , Spain

Site Status

Karolinska universitetssjukhuset - Solna

Solna, , Sweden

Site Status

Länssjukhuset Sundsvall-Härnösand

Sundsvall, , Sweden

Site Status

Akademiska Sjukhuset

Uppsala, , Sweden

Site Status

Hirslanden Medical Center

Aarau, , Switzerland

Site Status

Universitaetsspital Basel

Basel, , Switzerland

Site Status

Kantonsspital Graubuenden

Chur, , Switzerland

Site Status

Centre Hospitalier Universitaire Vaudois

Lausanne, , Switzerland

Site Status

Kantonsspital St. Gallen

Sankt Gallen, , Switzerland

Site Status

Kantonsspital Winterthur

Winterthur, , Switzerland

Site Status

Universitaetsspital Zuerich

Zurich, , Switzerland

Site Status

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Royal Cornwall Hospital

Truro, Cornwall, United Kingdom

Site Status

Queen Mary University of London

London, Greater London, United Kingdom

Site Status

University College London Hospitals

London, Greater London, United Kingdom

Site Status

Royal Free Hospital

London, Greater London, United Kingdom

Site Status

Western General Hospital

Edinburgh, Lothian Region, United Kingdom

Site Status

Nottingham University Hospitals City Campus

Nottingham, Nottinghamshire, United Kingdom

Site Status

Royal Surrey County Hospital

Guildford, Surrey, United Kingdom

Site Status

Countries

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United States Austria Belgium Canada China France Germany Greece Hungary Israel Italy Japan Portugal Russia South Korea Spain Sweden Switzerland Taiwan United Kingdom

References

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Modi S, Jacot W, Yamashita T, Sohn J, Vidal M, Tokunaga E, Tsurutani J, Ueno NT, Prat A, Chae YS, Lee KS, Niikura N, Park YH, Xu B, Wang X, Gil-Gil M, Li W, Pierga JY, Im SA, Moore HCF, Rugo HS, Yerushalmi R, Zagouri F, Gombos A, Kim SB, Liu Q, Luo T, Saura C, Schmid P, Sun T, Gambhire D, Yung L, Wang Y, Singh J, Vitazka P, Meinhardt G, Harbeck N, Cameron DA; DESTINY-Breast04 Trial Investigators. Trastuzumab Deruxtecan in Previously Treated HER2-Low Advanced Breast Cancer. N Engl J Med. 2022 Jul 7;387(1):9-20. doi: 10.1056/NEJMoa2203690. Epub 2022 Jun 5.

Reference Type RESULT
PMID: 35665782 (View on PubMed)

Modi S, Jacot W, Iwata H, Park YH, Vidal Losada M, Li W, Tsurutani J, Ueno NT, Zaman K, Prat A, Papazisis K, Rugo HS, Yamashita T, Harbeck N, Im SA, De Laurentiis M, Pierga JY, Wang X, Gombos A, Tokunaga E, Orbegoso Aguilar C, Yung L, Xiao F, Cheng Y, Cameron D. Trastuzumab deruxtecan in HER2-low metastatic breast cancer: long-term survival analysis of the randomized, phase 3 DESTINY-Breast04 trial. Nat Med. 2025 Oct 8. doi: 10.1038/s41591-025-03981-4. Online ahead of print.

Reference Type DERIVED
PMID: 41062831 (View on PubMed)

Ueno NT, Cottone F, Dunton K, Jacot W, Yamashita T, Sohn J, Tokunaga E, Prat A, Tsurutani J, Park YH, Rugo HS, Xu B, Cardoso F, Mitri Z, Mahtani R, Aguilar CO, Xiao F, Harbeck N, Cameron DA, Modi S. Patient-reported outcomes from DESTINY-Breast04: trastuzumab deruxtecan versus physician's choice of chemotherapy in patients with HER2-low mBC. Oncologist. 2025 May 8;30(5):oyaf048. doi: 10.1093/oncolo/oyaf048.

Reference Type DERIVED
PMID: 40349139 (View on PubMed)

Yamashita T, Sohn JH, Tokunaga E, Niikura N, Park YH, Lee KS, Chae YS, Xu B, Wang X, Im SA, Li W, Lu YS, Aguilar CO, Nishijima S, Nishiyama Y, Sugihara M, Modi S, Tsurutani J. Trastuzumab deruxtecan versus treatment of physician's choice in previously treated Asian patients with HER2-low unresectable/metastatic breast cancer: subgroup analysis of the DESTINY-Breast04 study. Breast Cancer. 2024 Sep;31(5):858-868. doi: 10.1007/s12282-024-01600-7. Epub 2024 Jun 17.

Reference Type DERIVED
PMID: 38884900 (View on PubMed)

Ma R, Shi Y, Yan R, Yin S, Bu H, Huang J. Efficacy and safety of trastuzumab deruxtecan in treating human epidermal growth factor receptor 2-low/positive advanced breast cancer:A meta-analysis of randomized controlled trials. Crit Rev Oncol Hematol. 2024 Apr;196:104305. doi: 10.1016/j.critrevonc.2024.104305. Epub 2024 Mar 3.

Reference Type DERIVED
PMID: 38442809 (View on PubMed)

Jhaveri K, Eli LD, Wildiers H, Hurvitz SA, Guerrero-Zotano A, Unni N, Brufsky A, Park H, Waisman J, Yang ES, Spanggaard I, Reid S, Burkard ME, Vinayak S, Prat A, Arnedos M, Bidard FC, Loi S, Crown J, Bhave M, Piha-Paul SA, Suga JM, Chia S, Saura C, Garcia-Saenz JA, Gambardella V, de Miguel MJ, Gal-Yam EN, Rapael A, Stemmer SM, Ma C, Hanker AB, Ye D, Goldman JW, Bose R, Peterson L, Bell JSK, Frazier A, DiPrimeo D, Wong A, Arteaga CL, Solit DB. Neratinib + fulvestrant + trastuzumab for HR-positive, HER2-negative, HER2-mutant metastatic breast cancer: outcomes and biomarker analysis from the SUMMIT trial. Ann Oncol. 2023 Oct;34(10):885-898. doi: 10.1016/j.annonc.2023.08.003. Epub 2023 Aug 18.

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Rugo HS, Crossno CL, Gesthalter YB, Kelley K, Moore HB, Rimawi MF, Westbrook KE, Buys SS. Real-World Perspectives and Practices for Pneumonitis/Interstitial Lung Disease Associated With Trastuzumab Deruxtecan Use in Human Epidermal Growth Factor Receptor 2-Expressing Metastatic Breast Cancer. JCO Oncol Pract. 2023 Aug;19(8):539-546. doi: 10.1200/OP.22.00480. Epub 2023 May 19.

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Narayan P, Dilawari A, Osgood C, Feng Z, Bloomquist E, Pierce WF, Jafri S, Kalavar S, Kondratovich M, Jha P, Ghosh S, Tang S, Pazdur R, Beaver JA, Amiri-Kordestani L. US Food and Drug Administration Approval Summary: Fam-Trastuzumab Deruxtecan-nxki for Human Epidermal Growth Factor Receptor 2-Low Unresectable or Metastatic Breast Cancer. J Clin Oncol. 2023 Apr 10;41(11):2108-2116. doi: 10.1200/JCO.22.02447. Epub 2023 Feb 13.

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Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2018-003069-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

184223

Identifier Type: REGISTRY

Identifier Source: secondary_id

DESTINY-B04

Identifier Type: OTHER

Identifier Source: secondary_id

DS8201-A-U303

Identifier Type: -

Identifier Source: org_study_id

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