A Phase 3B Study to Evaluate Bone Mineral Density With Long-Term Use of Relugolix Combination Tablet in Women With Uterine Fibroids or Endometriosis

NCT ID: NCT05862272

Last Updated: 2025-08-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1000 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-08-14

Study Completion Date

2030-09-30

Brief Summary

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The purpose of this clinical trial to characterize changes in bone mineral density during continuous treatment with relugolix combination tablet for up to 48 months (4 years) and 1 year of post-treatment follow-up in premenopausal women with heavy menstrual bleeding associated with uterine leiomyomas (fibroids) or with moderate-to-severe pain associated with endometriosis.

Detailed Description

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A prospective, single-arm, open-label, Phase 3B study to assess the effect of continuous 48 months (4 years) of treatment with relugolix combination tablet (relugolix 40 mg/estradiol \[E2\] 1 mg/norethindrone acetate \[NETA\] 0.5 mg) on bone mineral density in premenopausal women with heavy menstrual bleeding associated with uterine leiomyomas (fibroids) and premenopausal women with moderate to severe pain associated with endometriosis.

Approximately 1000 women (500 with heavy menstrual bleeding associated with uterine fibroids and 500 with moderate to severe pain associated with endometriosis) will receive relugolix combination tablet, during which time BMD will be assessed by dual-energy X-ray absorptiometry every 6 months.

A subset of participants will be eligible to enter this study following completion of 1 year of treatment with relugolix combination therapy in MVT-601-050 (NCT04756037; SERENE) and will complete 3 years of treatment under this protocol.

Upon completion of 48 months (4 years) of treatment or after early termination of treatment, participants will enter a 1-year post-treatment follow-up period during which time bone mineral density will be assessed at Month 6 and Month 12 following treatment cessation.

Conditions

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Uterine Fibroids Endometriosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Relugolix Combination Tablet

Participants will receive relugolix combination therapy orally once daily for 48 months.

Group Type EXPERIMENTAL

Relugolix Combination Tablet

Intervention Type DRUG

A fixed-dose combination tablet containing relugolix 40 mg, estradiol (E2) 1 mg, and norethindrone acetate (NETA) 0.5 mg.

Interventions

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Relugolix Combination Tablet

A fixed-dose combination tablet containing relugolix 40 mg, estradiol (E2) 1 mg, and norethindrone acetate (NETA) 0.5 mg.

Intervention Type DRUG

Other Intervention Names

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TAK-385 T-1331285 RVT-601 MVT-601 MVT-601A MYFEMBREE

Eligibility Criteria

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Inclusion Criteria

* Is a premenopausal woman, 18 to 50 years of age (inclusive);
* A diagnosis of uterine fibroids confirmed by imaging or review of medical records and reports heavy menstrual bleeding negatively affecting quality of life. or
* A diagnosis of endometriosis that is associated with moderate to severe pain.;
* If at risk of pregnancy is willing to avoid pregnancy for 4 years (the duration of the treatment period) using nonhormonal methods of contraception.
* Has a negative serum pregnancy test at the screening visit and a negative urine pregnancy test at the allocation visit (or Month 12 if entering from MVT-601-050 \[NCT04756037; SERENE\]);
* In good physical and mental health based on medical, surgical, and gynecological history as well as physical, gynecological, and breast examinations, clinical laboratory test results, and vital sign measurements;
* Has a body mass index ≥ 18 kg/m\^2.

Exclusion Criteria

* Has a weight or body habitus that exceeds the limit of the DXA scanner or has a condition that precludes an adequate DXA measurement at the lumbar spine or proximal femur
* Has a DXA result demonstrating the following criteria at any anatomic site (lumbar spine, total hip, femoral neck):

1. For patients entering de novo a Z-score ≤ -1.5 or T-score ≤ -2.0 (if ≥ 40 years of age)
2. For patients entering from MVT-601-050 (NCT04756037; SERENE) a 12-month on-treatment DXA demonstrating Z-score ≤ -2.0, T-score ≤ -2.5 (if ≥ 40 years of age), or BMD loss ≥ 8% compared with pre-treatment baseline;
* Screening 25-OH vitamin D level \< 12 ng/mL (patients with 25-OH vitamin D deficiency with levels ≥ 12 to \< 20 ng/mL are permitted if supplementing with vitamin D or if vitamin D supplementation is started in the screening period);
* Has a history of or currently has Cushing's Syndrome, Rheumatoid Arthritis, metabolic bone disease, uncorrected hyperparathyroidism, Paget's disease of the bone, collagen vascular disease, Marfan's syndrome, Ehlers-Danlos syndrome (if confirmed on genetic testing or meets definitive criteria for hypermobility type), chronic kidney disease (CKD) stage 3 or greater with glomerular filtration rate (GFR) \< 60 mL/min/m2 using Modification of Diet in Renal Disease (MDRD) method, hyperprolactinemia, known pituitary adenoma, hyperthyroidism, anorexia nervosa, bulimia (within the last year), abnormal bone mineral metabolism (eg, hypophosphatemia). Patients whose hyperparathyroidism or hyperthyroidism has been successfully treated or whose hyperprolactinemia has been successfully treated are allowed;
* History of low trauma (fragility) fracture.
* Past history of use or current use of medication used to treat bone loss other than calcium and vitamin D preparations;
* Prior use of depot-medroxyprogesterone acetate for a treatment period \> 2 years (if treatment occurred within the past 5 years) or prior use of GnRH agonist or antagonist for \> 12 months total (unless directly entering from MVT-601-050 \[NCT04756037; SERENE\]);
* Malabsorptive disease (including, but not limited to, inflammatory bowel disease and gastric bypass surgery);
* Current breast cancer, history of breast cancer or other hormone-sensitive malignancy, at increased risk for hormone-sensitive malignancy, or taking an aromatase inhibitor for breast cancer treatment or prevention
* History of organ transplantation or history of bone marrow
* BIRADS ≥ 3 Mammogram at entry (or within the past 6 months).
* Has a known human immunodeficiency virus (HIV) infection or at high risk of contracting HIV
* Has a current psychiatric disorder that would, in the investigator or medical monitor's opinion, impair the ability of the patient to participate in the study or would impair interpretation of their data.
* Is currently using a hormonal intrauterine device or contraceptive implant, hormonal contraceptive, or other prohibited medication and is unwilling to discontinue this hormonal contraception
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Sumitomo Pharma Switzerland GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Myovant Medical Director

Role: STUDY_DIRECTOR

Myovant Sciences GmbH

Locations

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Mobile

Mobile, Alabama, United States

Site Status RECRUITING

Chandler

Chandler, Arizona, United States

Site Status RECRUITING

Mesa

Mesa, Arizona, United States

Site Status RECRUITING

Peoria

Peoria, Arizona, United States

Site Status RECRUITING

Phoenix

Phoenix, Arizona, United States

Site Status RECRUITING

Tucson

Tucson, Arizona, United States

Site Status RECRUITING

Burbank

Burbank, California, United States

Site Status RECRUITING

Canoga Park

Canoga Park, California, United States

Site Status RECRUITING

Encinitas

Encinitas, California, United States

Site Status RECRUITING

Inglewood

Inglewood, California, United States

Site Status RECRUITING

Lomita

Lomita, California, United States

Site Status RECRUITING

Long Beach

Long Beach, California, United States

Site Status RECRUITING

Los Angeles

Los Angeles, California, United States

Site Status RECRUITING

Sacramento

Sacramento, California, United States

Site Status RECRUITING

San Fernando

San Fernando, California, United States

Site Status RECRUITING

Stanford

Stanford, California, United States

Site Status RECRUITING

Valley Village

Valley Village, California, United States

Site Status RECRUITING

Aurora

Aurora, Colorado, United States

Site Status RECRUITING

Greenwood Village

Greenwood Village, Colorado, United States

Site Status RECRUITING

Lakewood

Lakewood, Colorado, United States

Site Status RECRUITING

Washington

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Aventura

Aventura, Florida, United States

Site Status RECRUITING

Deland

DeLand, Florida, United States

Site Status RECRUITING

Hialeah

Hialeah, Florida, United States

Site Status RECRUITING

Kissimmee

Kissimmee, Florida, United States

Site Status RECRUITING

Lake Worth

Lake Worth, Florida, United States

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Margate

Margate, Florida, United States

Site Status RECRUITING

Miami

Miami, Florida, United States

Site Status RECRUITING

Miami

Miami, Florida, United States

Site Status RECRUITING

Miami

Miami, Florida, United States

Site Status RECRUITING

Miami Beach

Miami Beach, Florida, United States

Site Status RECRUITING

Miami Springs

Miami Springs, Florida, United States

Site Status RECRUITING

New Port Richey

New Port Richey, Florida, United States

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New Port Richey

New Port Richey, Florida, United States

Site Status RECRUITING

Orlando

Orlando, Florida, United States

Site Status RECRUITING

Orlando

Orlando, Florida, United States

Site Status RECRUITING

Panama City

Panama City, Florida, United States

Site Status RECRUITING

Sarasota

Sarasota, Florida, United States

Site Status RECRUITING

Tamarac

Tamarac, Florida, United States

Site Status RECRUITING

Tampa

Tampa, Florida, United States

Site Status RECRUITING

Venice

Venice, Florida, United States

Site Status RECRUITING

West Palm Beach

West Palm Beach, Florida, United States

Site Status RECRUITING

Atlanta

Atlanta, Georgia, United States

Site Status RECRUITING

Atlanta

Atlanta, Georgia, United States

Site Status RECRUITING

College Park

College Park, Georgia, United States

Site Status RECRUITING

Fayetteville

Fayetteville, Georgia, United States

Site Status RECRUITING

Norcross

Norcross, Georgia, United States

Site Status RECRUITING

Idaho Falls

Idaho Falls, Idaho, United States

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Idaho Falls

Idaho Falls, Idaho, United States

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Meridian

Meridian, Idaho, United States

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Chicago

Chicago, Illinois, United States

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Chicago

Chicago, Illinois, United States

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Schaumburg

Schaumburg, Illinois, United States

Site Status RECRUITING

Lenexa

Lenexa, Kansas, United States

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Wichita

Wichita, Kansas, United States

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Covington

Covington, Louisiana, United States

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Marrero

Marrero, Louisiana, United States

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Metairie

Metairie, Louisiana, United States

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New Orleans

New Orleans, Louisiana, United States

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New Orleans

New Orleans, Louisiana, United States

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Slidell

Slidell, Louisiana, United States

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Baltimore

Baltimore, Maryland, United States

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Laurel

Laurel, Maryland, United States

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Towson

Towson, Maryland, United States

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Bay City

Bay City, Michigan, United States

Site Status RECRUITING

Dearborn Heights

Dearborn Heights, Michigan, United States

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Detroit

Detroit, Michigan, United States

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Ridgeland

Ridgeland, Mississippi, United States

Site Status RECRUITING

Saint Louis

St Louis, Missouri, United States

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St Louis

St Louis, Missouri, United States

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Grand Island

Grand Island, Nebraska, United States

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Norfolk

Norfolk, Nebraska, United States

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Las Vegas

Las Vegas, Nevada, United States

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North Las Vegas

North Las Vegas, Nevada, United States

Site Status RECRUITING

West New York

West New York, New Jersey, United States

Site Status RECRUITING

Durham

Durham, North Carolina, United States

Site Status RECRUITING

New Bern

New Bern, North Carolina, United States

Site Status RECRUITING

Raleigh

Raleigh, North Carolina, United States

Site Status RECRUITING

Raleigh

Raleigh, North Carolina, United States

Site Status RECRUITING

Winston Salem

Winston-Salem, North Carolina, United States

Site Status RECRUITING

Cincinnati

Cincinnati, Ohio, United States

Site Status RECRUITING

Cleveland

Cleveland, Ohio, United States

Site Status RECRUITING

Columbus

Columbus, Ohio, United States

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Columbus

Columbus, Ohio, United States

Site Status RECRUITING

Dublin

Dublin, Ohio, United States

Site Status RECRUITING

Englewood

Englewood, Ohio, United States

Site Status RECRUITING

Middletown

Middletown, Ohio, United States

Site Status RECRUITING

Erie

Erie, Pennsylvania, United States

Site Status RECRUITING

Philadelphia

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Philadelphia

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Bluffton

Bluffton, South Carolina, United States

Site Status RECRUITING

Greenville

Greenville, South Carolina, United States

Site Status RECRUITING

Summerville

Summerville, South Carolina, United States

Site Status RECRUITING

West Columbia

West Columbia, South Carolina, United States

Site Status RECRUITING

Chattanooga

Chattanooga, Tennessee, United States

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Jackson

Jackson, Tennessee, United States

Site Status RECRUITING

Memphis

Memphis, Tennessee, United States

Site Status RECRUITING

Memphis

Memphis, Tennessee, United States

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Arlington

Arlington, Texas, United States

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Dallas

Dallas, Texas, United States

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Dallas

Dallas, Texas, United States

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Fort Worth

Fort Worth, Texas, United States

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Galveston

Galveston, Texas, United States

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Houston

Houston, Texas, United States

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Houston

Houston, Texas, United States

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Houston

Houston, Texas, United States

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Houston

Houston, Texas, United States

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League City

League City, Texas, United States

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Pearland

Pearland, Texas, United States

Site Status RECRUITING

San Antonio

San Antonio, Texas, United States

Site Status RECRUITING

San Antonio

San Antonio, Texas, United States

Site Status RECRUITING

Sugar Land

Sugar Land, Texas, United States

Site Status RECRUITING

Sugar Land

Sugar Land, Texas, United States

Site Status RECRUITING

Webster

Webster, Texas, United States

Site Status RECRUITING

Pleasant Grove

Pleasant Grove, Utah, United States

Site Status RECRUITING

Salt Lake City

Salt Lake City, Utah, United States

Site Status RECRUITING

Annandale

Annandale, Virginia, United States

Site Status RECRUITING

Newport News

Newport News, Virginia, United States

Site Status RECRUITING

Virginia Beach

Virginia Beach, Virginia, United States

Site Status RECRUITING

Seattle

Seattle, Washington, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Clinical Trials at Myovant

Role: CONTACT

650-278-8743

Other Identifiers

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MVT-601A-006

Identifier Type: -

Identifier Source: org_study_id

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