A Study to Evaluate Safety and Efficacy of Elagolix in Participants With Endometriosis With Associated Moderate to Severe Pain

NCT ID: NCT03343067

Last Updated: 2019-11-27

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

11 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-27

Study Completion Date

2018-10-23

Brief Summary

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This is a Phase 3, dose-escalation study designed to evaluate the safety and efficacy of both elagolix alone and elagolix plus estradiol/norethindrone acetate (E2/NETA) over 24 months in the management of endometriosis with associated moderate to severe pain in premenopausal women.

Detailed Description

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Conditions

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Endometriosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Arm A

Day 1 Through Month 3 (Open-Label): Open-Label elagolix 150 mg QD

Month 4 Through Month 24 (Double-Blind): Efficacy responders to elagolix 150 mg QD at Month 3 and continue treatment through Month 24

Group Type EXPERIMENTAL

elagolix

Intervention Type DRUG

Tablets

Arm C

Day 1 Through Month 3 (Open-Label): Open-Label elagolix 150 mg QD

Month 4 Through Month 24 (Double-Blind): Incomplete efficacy responders to elagolix 150 mg QD at Month 3 and randomized to elagolix 200 mg BID plus E2/NETA 1/0.5 mg QD treatment group and continue treatment through Month 24.

Group Type EXPERIMENTAL

elagolix

Intervention Type DRUG

Tablets

estradiol/norethindrone acetate (E2/NETA)

Intervention Type DRUG

Capsules

Arm D

Day 1 Through Month 3 (Open-Label): Open-Label elagolix 150 mg QD

Month 4 Through Month 6 (Double-Blind): Incomplete efficacy responders to elagolix 150 mg QD at Month 3 and randomized to elagolix 150 mg QD treatment group

Month 7 Through Month 24 (Double-Blind): Incomplete efficacy responders to elagolix 150 mg QD at Month 6 and assigned to elagolix 200 mg BID plus E2/NETA 1/0.5 mg QD treatment group and continue treatment through Month 24.

Group Type EXPERIMENTAL

elagolix

Intervention Type DRUG

Tablets

estradiol/norethindrone acetate (E2/NETA)

Intervention Type DRUG

Capsules

Arm B

Day 1 Through Month 3 (Open-Label): Open-Label elagolix 150 mg QD

Month 4 Through Month 6 (Double-Blind): Incomplete efficacy responders to elagolix 150 mg QD at Month 3 and randomized to elagolix 150 mg QD treatment group

Month 7 Through Month 24 (Double-Blind): Efficacy responders to elagolix 150 mg QD at Month 6 and continue treatment through Month 24.

Group Type EXPERIMENTAL

elagolix

Intervention Type DRUG

Tablets

Interventions

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elagolix

Tablets

Intervention Type DRUG

estradiol/norethindrone acetate (E2/NETA)

Capsules

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participant is a premenopausal female 18 to 49 years of age (inclusive) at the time of Screening.
* Participant has a documented surgical diagnosis (e.g., laparoscopy or laparotomy) of endometriosis established by visualization or histology within 10 years prior to entry into Washout or Screening,
* Participant must agree to use only those rescue analgesics permitted by the protocol during the Screening and Treatment Periods for her endometriosis-associated pain.
* Participant must have the following documented in the e-Diary during the last 35 days prior to Study Day 1:

1. At least 2 days of "moderate" or "severe" DYS, AND either,
2. At least 2 days of "moderate" or "severe" NMPP and an average NMPP score of at least 1.0, OR
3. At least 4 days of "moderate" or "severe" NMPP and an average NMPP score of at least 0.5.

Exclusion Criteria

* Participant has chronic pelvic pain that is not caused by endometriosis that requires chronic analgesic therapy, which would interfere with the assessment of endometriosis-associated pain.
* Participant is using any systemic corticosteroids for over 14 days within 3 months prior to Screening or is likely to require treatment with systemic corticosteroids during the course of the study. Over-the-counter and prescription topical, inhaled or intranasal corticosteroids are allowed.
* Participant has a history of major depression or post-traumatic stress disorder (PTSD) within 2 years prior to screening or other major psychiatric disorder at any time
* Participant has a history of suicide attempts or answered "yes" to questions 4 or 5 on the suicidal ideation portion of the Columbia-Suicide Severity Rating Scale (C-SSRS) at Screening or prior to study drug dosing on Day 1.
* Participant has any condition that would interfere with obtaining adequate dual energy x-ray absorptiometry (DXA) measurements
* Screening DXA results of the lumbar spine (L1 - L4), femoral neck or total hip bone mineral density (BMD) corresponding to less than 2 or more standard deviations below normal (Z-score \< -2.0 for participants \< 40 years of age, T-score for participants \>= 40 years of age).
* Participant has either

1. a newly diagnosed, clinically significant medical condition that requires therapeutic intervention (e.g., new onset hypertension) that has not been stabilized 30 days prior to enrollment on Day 1 OR
2. a clinically significant medical condition that is anticipated to required intervention during the course of study participation (e.g., anticipated major elective surgery) OR
3. an unstable medical condition that makes the participant an unsuitable candidate for the study in the opinion of the Investigator
* Participant has any conditions contraindicated with use of E2/NETA
Minimum Eligible Age

18 Years

Maximum Eligible Age

49 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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AbbVie Inc.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Pinnacle Research Group /ID# 202016

Anniston, Alabama, United States

Site Status

Noble Clinical Research /ID# 170628

Tucson, Arizona, United States

Site Status

Lynn Institute of the Ozarks /ID# 165052

Little Rock, Arkansas, United States

Site Status

SC Clinical Research /ID# 165049

Garden Grove, California, United States

Site Status

Marvel Clinical Research /ID# 169633

Huntington Beach, California, United States

Site Status

Health care Affiliates Medical Group /ID# 165048

Santa Ana, California, United States

Site Status

Western States Clinical Res /ID# 169809

Wheat Ridge, Colorado, United States

Site Status

Nova Clinical Research, LLC /ID# 202227

Bradenton, Florida, United States

Site Status

Midland Florida Clinical Research Center /ID# 201327

DeLand, Florida, United States

Site Status

Southeastern Integrated Med /ID# 203109

Gainesville, Florida, United States

Site Status

Care Partners Clinical Researc /ID# 168395

Jacksonville, Florida, United States

Site Status

LCC Medical Research Institute /ID# 168888

Miami, Florida, United States

Site Status

A Premier Clinical Research of Florida, LLC /ID# 201887

Orange City, Florida, United States

Site Status

GCP Clinical Research, LLC /ID# 169774

Tampa, Florida, United States

Site Status

Triple O Research Institute /ID# 201128

West Palm Beach, Florida, United States

Site Status

Bingham Memorial Hospital /ID# 170110

Blackfoot, Idaho, United States

Site Status

Leavitt Womens Healthcare /ID# 169495

Idaho Falls, Idaho, United States

Site Status

Quad Clinical Research, LLC /ID# 168294

Chicago, Illinois, United States

Site Status

Quad Clinical Research, LLC /ID# 170629

Chicago, Illinois, United States

Site Status

Women's Health Care, PC /ID# 165033

Newburgh, Indiana, United States

Site Status

Delricht Research /ID# 200219

New Orleans, Louisiana, United States

Site Status

Quad Clinical Research, LLC /ID# 200180

St Louis, Missouri, United States

Site Status

Montana Health Research Inst /ID# 170624

Billings, Montana, United States

Site Status

Excel Clinical Research /ID# 170620

Las Vegas, Nevada, United States

Site Status

Northwell health system /ID# 200162

Manhasset, New York, United States

Site Status

Radiant Research, Inc /ID# 200045

Akron, Ohio, United States

Site Status

Central Ohio Clinical Research /ID# 170750

Columbus, Ohio, United States

Site Status

Optimed Research /ID# 167642

Columbus, Ohio, United States

Site Status

VitaLink Research /ID# 168401

Greenville, South Carolina, United States

Site Status

VitaLink Research /ID# 170625

Greenville, South Carolina, United States

Site Status

Fusion Clinical Research of Spartanburg /ID# 200010

Spartanburg, South Carolina, United States

Site Status

Centex Studies, Inc /ID# 169897

Houston, Texas, United States

Site Status

America's Adv. Wellness Center /ID# 170005

Houston, Texas, United States

Site Status

ClinRx Research, LLC /ID# 201189

Plano, Texas, United States

Site Status

Progressive Clinical Research /ID# 205565

San Antonio, Texas, United States

Site Status

Eastern Virginia Med School /ID# 165016

Norfolk, Virginia, United States

Site Status

Seattle Reproductive Medicine /ID# 171079

Seattle, Washington, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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M16-383

Identifier Type: -

Identifier Source: org_study_id

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