Study of the Safety and Contraceptive Efficacy of Relugolix Combination Therapy in Women With Uterine Fibroids or Endometriosis Who Are at Risk for Pregnancy

NCT ID: NCT04756037

Last Updated: 2026-01-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1020 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-18

Study Completion Date

2026-02-28

Brief Summary

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The purpose of this study is to assess the contraceptive efficacy of relugolix combination therapy.

Detailed Description

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This is a single-arm, open-label, phase 3 study to assess the contraceptive efficacy of relugolix combination therapy (relugolix 40 milligrams \[mg\], estradiol \[E2\] 1 mg, and norethindrone acetate \[NETA\] 0.5 mg).

Conditions

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Contraception

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Relugolix/E2/NETA

Participants will receive relugolix combination therapy for 1 year (13 consecutive 28-day treatment cycles).

Group Type EXPERIMENTAL

Relugolix Combination Therapy

Intervention Type DRUG

Participants will receive orally 1 fixed-dose combination tablet (relugolix 40 mg/E2 1 mg/NETA 0.5 mg) once daily.

Interventions

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Relugolix Combination Therapy

Participants will receive orally 1 fixed-dose combination tablet (relugolix 40 mg/E2 1 mg/NETA 0.5 mg) once daily.

Intervention Type DRUG

Other Intervention Names

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Myfembree

Eligibility Criteria

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Inclusion Criteria

1. Is a premenopausal woman, 18 to 50 years of age.
2. Is at risk of pregnancy (that is, having heterosexual intercourse at least once per month) and is seeking contraception.
3. Has normal, regular menstrual cycles that are between 21 and 35 days in duration.
4. Has a diagnosis of uterine fibroids or endometriosis meeting either of the following criteria:

1. Diagnosis of uterine fibroids by confirmation of ultrasound performed in the last 2 years and patient report of heavy menstrual bleeding affecting quality of life.
2. Diagnosis of endometriosis and has had surgical or direct visualization (laparoscopy or laparotomy) and/or histopathologic confirmation of endometriosis, and the patient reports moderate, severe, or very severe pain during the most recent menses and/or during nonmenstrual portion of the cycle in the prior month
5. Is willing to use the study intervention as the sole method of contraception for 13 consecutive 28-day treatment cycles and does not intend to use any other form of contraception (for example, condoms).

Exclusion Criteria

1. Is pregnant, or breastfeeding, or has breastfed in the last year.
2. Has a known history of infertility or sub-fertility.
3. Has presence or history of a venous thromboembolic event (for example, deep vein thrombosis, pulmonary embolism), an arterial thrombotic or thromboembolic event (for example, myocardial infarction, stroke, or peripheral arterial), or a transient ischemic attack, angina pectoris, or claudication.
4. Has a higher risk of arterial, venous thrombotic, or thromboembolic disorders.
5. Has a history of migraine with aura or focal neurological symptoms.
6. Has uncontrolled hypertension, diabetes with inadequate control, or multiple cardiovascular risk factors.
7. Has a history of clinically significant ventricular arrhythmias.
8. Has clinically significant liver disease, including active viral hepatitis or cirrhosis.
9. Has a history of pancreatitis associated with severe hypertriglyceridemia.
10. Has known human immunodeficiency virus (HIV) infection or high risk of contracting HIV.
11. Has a hepatic hemangioma or has a history of cholestasis with prior estrogen use or during pregnancy.
12. Has a serious contraindication to pregnancy (for example, a medical condition or use of chronic medication such as isotretinoin or thalidomide).
13. History of suicidal ideation or behavior, or confirmed "yes" to any question (with exception of non-suicidal self-injurious behavior, unless deemed as an unacceptable risk by the investigator) on the C-SSRS.
14. Has a bone mineral density Z-score ≤ -2.0 at lumbar spine, femoral neck, or total hip during the screening period.
15. Has a history of or currently has osteoporosis, or other metabolic bone disease, collagen vascular disease, chronic kidney disease (CKD) stage 3 or greater with glomerular filtration rate (GFR) \< 60 mL/min/m2 using Modification of Diet in Renal Disease (MDRD) method, hyperparathyroidism, hyperprolactinemia, known pituitary adenoma, hyperthyroidism, anorexia nervosa, abnormal bone mineral metabolism (eg, hypophosphatemia), or low traumatic (fragility) fracture.
16. Has used chronic glucocorticoids that are oral, parenteral, inhaled (prednisone equivalents of ≥ 2.5 mg daily for ≥ 3 months) in 12 months prior to the study.
17. Has known BRCA mutation or other mutation associated with increased risk of breast cancer.
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Sumitomo Pharma Switzerland GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Mobile

Mobile, Alabama, United States

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Chandler

Chandler, Arizona, United States

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Mesa

Mesa, Arizona, United States

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Peoria

Peoria, Arizona, United States

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Phoenix

Phoenix, Arizona, United States

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Burbank

Burbank, California, United States

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Canoga Park

Canoga Park, California, United States

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Encinitas

Encinitas, California, United States

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Gardena

Gardena, California, United States

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Lancaster

Lancaster, California, United States

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Long Beach

Long Beach, California, United States

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Long Beach

Long Beach, California, United States

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Palo Alto

Palo Alto, California, United States

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Sacramento

Sacramento, California, United States

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San Diego

San Diego, California, United States

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San Fernando

San Fernando, California, United States

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Valley Village

Valley Village, California, United States

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West Covina

West Covina, California, United States

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Aurora

Aurora, Colorado, United States

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Greenwood Village

Greenwood Village, Colorado, United States

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Washington

Washington D.C., District of Columbia, United States

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Washington

Washington D.C., District of Columbia, United States

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Aventura

Aventura, Florida, United States

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Boynton Beach

Boynton Beach, Florida, United States

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Davie

Davie, Florida, United States

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Deland

DeLand, Florida, United States

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Hialeah

Hialeah, Florida, United States

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Jacksonville

Jacksonville, Florida, United States

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Kissimmee

Kissimmee, Florida, United States

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Lake Worth

Lake Worth, Florida, United States

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Loxahatchee

Loxahatchee Groves, Florida, United States

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Margate

Margate, Florida, United States

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Miami

Miami, Florida, United States

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Miami

Miami, Florida, United States

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Miami

Miami, Florida, United States

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Miami

Miami, Florida, United States

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New Port Richey

New Port Richey, Florida, United States

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Orlando

Orlando, Florida, United States

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Orlando

Orlando, Florida, United States

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Panama City

Panama City, Florida, United States

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Sarasota

Sarasota, Florida, United States

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Atlanta

Atlanta, Georgia, United States

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Atlanta

Atlanta, Georgia, United States

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College Park

College Park, Georgia, United States

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Columbus

Columbus, Georgia, United States

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Norcross

Norcross, Georgia, United States

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Sandy Springs

Sandy Springs, Georgia, United States

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Savannah

Savannah, Georgia, United States

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Smyrna

Smyrna, Georgia, United States

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Meridian

Meridian, Idaho, United States

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Nampa

Nampa, Idaho, United States

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Chicago

Chicago, Illinois, United States

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Chicago

Chicago, Illinois, United States

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Brownsburg

Brownsburg, Indiana, United States

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Mishawaka

Mishawaka, Indiana, United States

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Shawnee

Shawnee, Kansas, United States

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Covington

Covington, Louisiana, United States

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Marrero

Marrero, Louisiana, United States

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Metairie

Metairie, Louisiana, United States

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New Orleans

New Orleans, Louisiana, United States

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Shreveport

Shreveport, Louisiana, United States

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Baltimore

Baltimore, Maryland, United States

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Towson

Towson, Maryland, United States

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Dearborn Heights

Dearborn Heights, Michigan, United States

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Detroit

Detroit, Michigan, United States

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Saginaw

Saginaw, Michigan, United States

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Jackson

Jackson, Mississippi, United States

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Saint Louis

St Louis, Missouri, United States

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Saint Louis

St Louis, Missouri, United States

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Las Vegas

Las Vegas, Nevada, United States

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Las Vegas

Las Vegas, Nevada, United States

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North Las Vegas

North Las Vegas, Nevada, United States

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Cherry Hill

Cherry Hill, New Jersey, United States

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Albuquerque

Albuquerque, New Mexico, United States

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New York

New York, New York, United States

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Durham

Durham, North Carolina, United States

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New Bern

New Bern, North Carolina, United States

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Raleigh

Raleigh, North Carolina, United States

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Raleigh

Raleigh, North Carolina, United States

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Winston-Salem

Winston-Salem, North Carolina, United States

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Minot

Minot, North Dakota, United States

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Columbus

Columbus, Ohio, United States

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Columbus

Columbus, Ohio, United States

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Columbus

Columbus, Ohio, United States

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Fairfield

Fairfield, Ohio, United States

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Franklin

Franklin, Ohio, United States

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Portland

Portland, Oregon, United States

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Philadelphia

Philadelphia, Pennsylvania, United States

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Philadelphia

Philadelphia, Pennsylvania, United States

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Myrtle Beach

Myrtle Beach, South Carolina, United States

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Summerville

Summerville, South Carolina, United States

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Chattanooga

Chattanooga, Tennessee, United States

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Memphis

Memphis, Tennessee, United States

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Austin

Austin, Texas, United States

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Beaumont

Beaumont, Texas, United States

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Dallas

Dallas, Texas, United States

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Fort Worth

Fort Worth, Texas, United States

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Houston

Houston, Texas, United States

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Houston

Houston, Texas, United States

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Houston

Houston, Texas, United States

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League City

League City, Texas, United States

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Pearland

Pearland, Texas, United States

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San Antonio

San Antonio, Texas, United States

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San Antonio

San Antonio, Texas, United States

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Salt Lake City

Salt Lake City, Utah, United States

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Annandale

Annandale, Virginia, United States

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Norfolk

Norfolk, Virginia, United States

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Bellevue

Bellevue, Washington, United States

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Seattle

Seattle, Washington, United States

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Cidra

Cidra, , Puerto Rico

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San Juan

San Juan, , Puerto Rico

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San Juan

San Juan, , Puerto Rico

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Countries

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United States Puerto Rico

References

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Neblett MF 2nd, Stewart EA. Oral Gonadotropin-Releasing Hormone Antagonists for the Treatment of Uterine Leiomyomas. Obstet Gynecol. 2023 May 1;141(5):901-910. doi: 10.1097/AOG.0000000000005145. Epub 2023 Apr 5.

Reference Type DERIVED
PMID: 37103532 (View on PubMed)

Other Identifiers

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MVT-601-050

Identifier Type: -

Identifier Source: org_study_id

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