A Study Evaluating the Efficacy and Safety of Vixarelimab in Participants With Idiopathic Pulmonary Fibrosis and in Participants With Systemic Sclerosis-Associated Interstitial Lung Disease

NCT ID: NCT05785624

Last Updated: 2026-01-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

286 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-05-26

Study Completion Date

2026-01-09

Brief Summary

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The main purpose of the study is to evaluate the efficacy of vixarelimab compared with placebo on lung function in participants with idiopathic pulmonary fibrosis (IPF) and in participants with systemic sclerosis-associated interstitial lung disease (SSc-ILD). Participants who complete 52-weeks of treatment in the Double-blind Treatment (DBT) period can choose to enroll in the optional Open-label Extension (OLE) period to receive treatment with vixarelimab for another 52 weeks.

Cohort 1 has completed enrollment and has been closed for further enrollment. Cohort 2 is enrolling participants.

Detailed Description

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Conditions

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Idiopathic Pulmonary Fibrosis Systemic Sclerosis With Lung Involvement

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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DBT: Cohort 1: Vixarelimab

Participants with IPF will receive vixarelimab, subcutaneously (SC), once every two weeks (Q2W) for 52 weeks in the DBT period. This cohort has completed enrollment and has been closed.

Group Type EXPERIMENTAL

Vixarelimab

Intervention Type DRUG

Vixarelimab will be administered as per the schedule specified in the respective arms.

DBT: Cohort 1: Placebo

Participants with IPF will receive vixarelimab matching placebo, SC, Q2W for 52 weeks in the DBT period. This cohort has completed enrollment and has been closed.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered as per the schedule specified in the respective arms.

DBT: Cohort 2: Vixarelimab

Participants with SSC-ILD will receive vixarelimab, SC, Q2W for 52 weeks in the DBT period.

Group Type EXPERIMENTAL

Vixarelimab

Intervention Type DRUG

Vixarelimab will be administered as per the schedule specified in the respective arms.

DBT: Cohort 2: Placebo

Participants with SSC-ILD will receive vixarelimab matching placebo, SC, Q2W for 52 weeks in the DBT period.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered as per the schedule specified in the respective arms.

OLE Period: Cohort 1: Vixarelimab

Participants with IPF who complete 52 weeks of treatment in the DBT period can choose to enroll in the OLE period to receive vixarelimab, SC, Q2W for 52 weeks.

Group Type EXPERIMENTAL

Vixarelimab

Intervention Type DRUG

Vixarelimab will be administered as per the schedule specified in the respective arms.

OLE Period: Cohort 2: Vixarelimab

Participants with SSC-ILD who complete 52 weeks of treatment in the DBT period can choose to enroll in the OLE period to receive vixarelimab, SC, Q2W for 52 weeks.

Group Type EXPERIMENTAL

Vixarelimab

Intervention Type DRUG

Vixarelimab will be administered as per the schedule specified in the respective arms.

Interventions

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Vixarelimab

Vixarelimab will be administered as per the schedule specified in the respective arms.

Intervention Type DRUG

Placebo

Placebo will be administered as per the schedule specified in the respective arms.

Intervention Type DRUG

Other Intervention Names

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RO7622888 KPL-716

Eligibility Criteria

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Inclusion Criteria

* FVC ≥45% predicted during screening as determined by the over-reader
* Forced expiratory volume in 1 second (FEV1)/FVC ratio \>0.70 during screening as determined by the over-reader
* DLco ≥30% and ≤90% of predicted during screening (Hgb corrected) as determined by the over-reader
* Minimum 6-MWT distance of 150 m with maximum use of 6 liters per minute (L/min) at sea-level and up to 8 L/min at altitude (\> 5000 feet \[1524 m\] above sea level) of supplemental oxygen while maintaining oxygen saturation of \>83% during the 6MWT during screening
* Participant and investigator consideration of all medicinal treatment options and/or possibly lung transplantation prior to consideration of participation in the study


* Age 40-85 years
* Documented diagnosis of IPF or IPF (likely)
* HRCT pattern consistent with the diagnosis of IPF, confirmed by central review of chest HRCT and central review of any available lung biopsy
* For participants receiving pirfenidone or nintedanib treatment for IPF: treatment for ≥3 months with a stable dose for ≥4 weeks prior to screening and during screening, with plans to continue treatment during the study period


* Age 18-85 years
* Diagnosis of SSc as defined using the American College of Rheumatology/European Alliance of Associations for Rheumatology (EULAR) criteria
* HRCT demonstrating ≥10% extent of fibrosis, confirmed by central review of Chest HRCT
* Evidence of progression of pulmonary fibrosis
* For participants receiving tocilizumab treatment for SSc-ILD: treatment for ≥3 months with a stable dose for ≥4 weeks prior to screening and during screening, with no contraindications according to local prescribing information, and no intention to change or modify their treatment regimen for the duration of the study
* For participants receiving nintedanib treatment for SSc-ILD: treatment for ≥ 3 months with a stable dose for ≥ 4 weeks prior to screening and during screening, with no contraindications according to local prescribing information, and no intention to change or modify their treatment regimen for the duration of the study
* Availability of skin for biopsy preferably on proximal forearms having Modified Rodnan Skin Score (mRSS) ≥2 at the biopsy location


* Completion of 52 weeks of treatment in the double-blinded treatment period
* Investigator determination of a favorable benefit-risk for the individual participant, i.e., the expectation of reasonable likelihood for therapeutic benefit and tolerability of the study drug after evaluation of the preceding 52 weeks of double-blinded treatment

Exclusion Criteria

* Percentage of predicted FVC value showing improvement in the 6-month period prior to screening and including screening value
* Known post-bronchodilator response in FEV1 and/or FVC (defined as an increase in percent predicted values by ≥ 10)
* Resting oxygen saturation of \<89% using up to 4 L/min of supplemental oxygen at sea level and up to 6 L/min at altitude (5000 feet \[1524 m\] above sea level) during screening
* History of lung transplant
* Previous treatment with vixarelimab
* Acute respiratory or systemic bacterial, viral, or fungal infection either during screening or prior to screening not successfully resolved by 4 weeks prior to screening visit
* Presence of pulmonary hypertension requiring treatment
* History of malignancy within the 5 years prior to screening
* Positive hepatitis C virus (HCV) antibody test result accompanied by a positive HCV ribonucleic acid (RNA) test at screening
* Known immunodeficiency
* Known evidence of active or untreated latent tuberculosis


* Evidence of other known causes of ILD
* Emphysema present on ≥50% of the HRCT, or the extent of emphysema is greater than the extent of fibrosis, according to central review of the HRCT


* Evidence of other known causes of ILD
* Rheumatic autoimmune disease other than SSc
* Receiving pirfenidone treatment within 4 weeks prior to screening
* Receipt of nintedanib in combination with tocilizumab


* Significant non-compliance in the double-blinded treatment period, per investigator's judgment
* Any new clinically significant pulmonary disease other than IPF or SSc-ILD since enrolling in the double-blinded treatment period
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Banner University Medicine Lung Institute

Phoenix, Arizona, United States

Site Status

Southern Arizona VA Health Care System NAVREF PPDS

Tucson, Arizona, United States

Site Status

University of California, San Francisco-Fresno

Fresno, California, United States

Site Status

University of Southern California Keck School of Medicine

Los Angeles, California, United States

Site Status

UCLA Rheumatology

Los Angeles, California, United States

Site Status

University of California, San Francisco Medical Center

San Francisco, California, United States

Site Status

The Lundquist Institute for BioMedical Innovation at Harbor-UCLA Medical Cente

Torrance, California, United States

Site Status

Renstar Medical Research

Ocala, Florida, United States

Site Status

Coastal Pulmonary and Critical Care PLC

St. Petersburg, Florida, United States

Site Status

Weston Hospital

Weston, Florida, United States

Site Status

Piedmont Pulmonary and Sleep Medicine Buckhead

Atlanta, Georgia, United States

Site Status

Emory Clinic

Atlanta, Georgia, United States

Site Status

GenHarp Clinical Solutions

Evergreen Park, Illinois, United States

Site Status

Northwestern Medicine - Northwestern Medicine Glen

Glenview, Illinois, United States

Site Status

IU Health Ball Memorial Physicians Pulmonary and Critical Care Medicine

Muncie, Indiana, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Michigan Hospital

Ann Arbor, Michigan, United States

Site Status

Hannibal Regional Healthcare System HRMG Hannibal

Hannibal, Missouri, United States

Site Status

Pulmonix LLC

Greensboro, North Carolina, United States

Site Status

Southeastern Research Center

Winston-Salem, North Carolina, United States

Site Status

The University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status

Baylor Scott and White Health - Advanced Lung Disease Specialists - Dallas

Dallas, Texas, United States

Site Status

IntraCare Health Center ? Prestige

Dallas, Texas, United States

Site Status

El Paso Pulmonary Association Elligo PPDS

El Paso, Texas, United States

Site Status

McGovern Medical School

Houston, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

University of Utah - PPDS

Salt Lake City, Utah, United States

Site Status

Centro Médico Dra de Salvo

Buenos Aires, , Argentina

Site Status

Consultorios Médicos Dr. Doreski

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Instituto Ave Pulmo

Mar del Plata, , Argentina

Site Status

Fundacion Scherbovsky

Mendoza, , Argentina

Site Status

INSARES

Mendoza, Mendoza City, , Argentina

Site Status

Instituto Medico Rio Cuarto

Río Cuarto, , Argentina

Site Status

Instituto Medico de la Fundacion Estudios Clinicos

Rosario, , Argentina

Site Status

Instituto De Patologias Respiratorias

San Miguel de Tucumán, , Argentina

Site Status

Centro de Investigaciones Medicas Tucuman

San Miguel de Tucumán, , Argentina

Site Status

Centro de Investigaciones Reumatologicas

San Miguel de Tucumán, , Argentina

Site Status

Instituto Del Buen Aire

Santa Fe, , Argentina

Site Status

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status

St Vincent's Hospital Sydney

Darlinghurst, New South Wales, Australia

Site Status

Monash Health Monash Medical Centre

Clayton, Victoria, Australia

Site Status

AZORG Campus Aalst-Moorselbaan

Aalst, , Belgium

Site Status

CHU de Liège

Liège, , Belgium

Site Status

L2 Ip - Instituto de Pesquisas Clinicas Ltda - ME

Brasília, Federal District, Brazil

Site Status

Hospital Brasilia

Brasília, Federal District, Brazil

Site Status

Hospital de Clinicas de Porto Alegre HCPA PPDS

Pôrto Alegre, Pará, Brazil

Site Status

Hospital Dia do Pulmao

Blumenau, Santa Catarina, Brazil

Site Status

Kelowna Allergy and Respiratory Health Clinic

Kelowna, British Columbia, Canada

Site Status

Dynamic Drug Advancement Ltd.

Ajax, Ontario, Canada

Site Status

Dr Anil Dhar Professional Medicine Corporation

Windsor, Ontario, Canada

Site Status

CEC SpA

Ñuñoa, , Chile

Site Status

Enroll SpA - PPDS

Providencia, , Chile

Site Status

Centro de Investigacion del Maule

Talca, , Chile

Site Status

Hopital Avicenne

Bobigny, , France

Site Status

Hopital Louis Pradel

Bron, , France

Site Status

Hopital Nord AP-HM

Marseille, , France

Site Status

Hôpital Arnaud de Villeneuve

Montpellier, , France

Site Status

Hopital Pasteur 2

Nice, , France

Site Status

Groupe Hospitalier Bichat Claude Bernard

Paris, , France

Site Status

CHU de Reims

Reims, , France

Site Status

Evangelische Lungenklinik Berlin

Berlin, , Germany

Site Status

Universitaetsklinikum Duesseldorf

Düsseldorf, , Germany

Site Status

Ruhrlandklinik

Essen, , Germany

Site Status

University General Hospital of Heraklion

Heraklion, , Greece

Site Status

University General Hospital of Larissa

Larissa, , Greece

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Barzilai Medical Center

Ashkelon, , Israel

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Shamir Medical Center Assaf Harofeh

Beer Jacob, , Israel

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Lady Davis Carmel Medical Center

Haifa, , Israel

Site Status

Hadassah Medical Center

Jerusalem, , Israel

Site Status

Rabin Medical Center

Petah Tikva, , Israel

Site Status

The Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Kaplan Medical Center

Rehovot, , Israel

Site Status

Tel Aviv Sourasky Medical Center PPDS

Tel Aviv, , Israel

Site Status

Azienda Ospedaliera Universitaria Senese

Siena, Abruzzo, Italy

Site Status

Presidio Ospedaliero GB Morgagni L Pierantoni

Forlì, Emilia-Romagna, Italy

Site Status

Arcispedale Santa Maria Nuova

Reggio Emilia, Emilia-Romagna, Italy

Site Status

Fondazione Policlinico Universitario A Gemelli

Rome, Lazio, Italy

Site Status

Ospedale S. Giuseppe Multimedica

Milan, Lombardy, Italy

Site Status

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Turin, Piedmont, Italy

Site Status

Azienda Ospedaliera Universitaria "Policlinico - Vittorio Emanuele" (Presidio Gaspare Rodolico)

Catania, Sicily, Italy

Site Status

Azienda Ospedaliero Universitaria Ospedali Riuniti di Ancona-Umberto I G.M. Lancisi G. Salesi

Ancona, The Marches, Italy

Site Status

Azienda Ospedaliera Universitaria Careggi

Florence, Tuscany, Italy

Site Status

CICUM San Miguel

Americana, Jalisco, Mexico

Site Status

Bioclinica - Centro Integral En Reumatologia Sociedad Anónima de Capital Variable - PPDS

Guadalajara, Jalisco, Mexico

Site Status

Hospital Universitario Dr. Jose Eleuterio Gonzalez

Monterrey, Nuevo León, Mexico

Site Status

Christchurch Hospital

Christchurch, , New Zealand

Site Status

Dunedin Hospital

Dunedin, , New Zealand

Site Status

Waikato Hospital

Hamilton, , New Zealand

Site Status

SPZOZ Uniwersytecki Szpital Kliniczny nr 1 im. Norberta Barlickiego Uniwersytetu Medycznego w Lodzi

Lodz, , Poland

Site Status

EMED Centrum Uslug Medycznych Ewa Smialek

Rzeszów, , Poland

Site Status

PULMAG Grzegorz Gasior Marzena Kociolek Spolka Cywilna

Sosnowiec, , Poland

Site Status

Wojskowy Instytut Medyczny Panstwowy Instytut Badawczy

Warsaw, , Poland

Site Status

Dr JM Engelbrecht Trial site

Cape Town, , South Africa

Site Status

University of Cape Town Lung Institute UCTLI

Cape Town, , South Africa

Site Status

St Augustines Hospital

Durban, , South Africa

Site Status

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status

The Catholic University of Korea Eunpyeong St. Mary's Hospital

Seoul, , South Korea

Site Status

Hanyang University Medical Center

Seoul, , South Korea

Site Status

Asan Medical Center - PPDS

Seoul, , South Korea

Site Status

Samsung Medical Center - PPDS

Seoul, , South Korea

Site Status

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

CHUS H Clinico U de Santiago

Santiago de Compostela, LA Coruna, Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Hospital Clinico San Carlos

Madrid, , Spain

Site Status

Hospital Universitario Virgen de la Victoria

Málaga, , Spain

Site Status

Hospital Universitario Son Espases

Palma de Mallorca, , Spain

Site Status

Far East Memorial Hospital

New Taipei City, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Countries

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United States Argentina Australia Belgium Brazil Canada Chile France Germany Greece Israel Italy Mexico New Zealand Poland South Africa South Korea Spain Taiwan

Other Identifiers

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2022-502828-42

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2022-502828-42-00

Identifier Type: CTIS

Identifier Source: secondary_id

GB44496

Identifier Type: -

Identifier Source: org_study_id

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