A Phase 3 Study to Evaluate the Long-term Safety, Tolerability and Efficacy of Efgartigimod PH20 SC in Adult Participants With Bullous Pemphigoid

NCT ID: NCT05681481

Last Updated: 2025-04-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

64 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-22

Study Completion Date

2025-03-20

Brief Summary

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The purpose of this study is to evaluate the safety of efgartigimod PH20 SC over a longer period of time in adult participants with moderate-to-severe bullous pemphigoid (BP) who have completed ARGX-113-2009 study. The study will also evaluate the efficacy of efgartigimod PH20 SC.

Eligible participants can roll over from the main study (ARGX-113-2009) to this open-label extension study (ARGX-113-2010). The study consists of a treatment period of up to 48 weeks in which participants receive efgartigimod PH20 SC. After the first 5 visits, the participants will visit the study centers at least once every 4 weeks. The participants who are not receiving efgartigimod PH20 SC (after the main study or currently on the study), will enter an observation period with study visits at least once every 8 weeks. If the participant relapses, they can re-enter the treatment period where they will receive efgartigimod PH20 SC. The treatment and observation period is followed by a follow-up period of 8 weeks. Oral or topical corticosterioids can be administered at the investigator's indiscretion

Detailed Description

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Conditions

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Bullous Pemphigoid

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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efgartigimod PH20 SC

participants receiving efgartigimod PH20 SC on top of Prednisone

Group Type EXPERIMENTAL

efgartigimod PH20 SC

Intervention Type BIOLOGICAL

Subcutaneous injection of efgartigimod coformulated with rHuPH20, a permeation enhancer

Prednisone

Intervention Type DRUG

Oral Prednisone

Interventions

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efgartigimod PH20 SC

Subcutaneous injection of efgartigimod coformulated with rHuPH20, a permeation enhancer

Intervention Type BIOLOGICAL

Prednisone

Oral Prednisone

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Has completed the week 36 visit of ARGX-113-2009
* Is capable of providing signed informed consent and complying with protocol requirements
* Agrees to use contraceptive measures consistent with local regulations and the following: Women of childbearing potential must have a negative urine pregnancy test at baseline before receiving the study drug and must use one of the contraception methods described in the protocol from signing the ICF until the last dose of the study drug

Exclusion Criteria

* Clinically significant disease, recent major surgery (within 3 months of baseline), or intends to have surgery during the study; or any other medical condition that, in the investigator's opinion would confound the results of the study or put the participant at undue risk
* Known hypersensitivity to the study drug or 1 of its excipients
* Permanently discontinued IMP in ARGX-113-2009 due to an adverse event (AE) considered related to the study drug and for whom the benefit/risk balance is not considered positive
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Medical Dermatology Specialists

Phoenix, Arizona, United States

Site Status

First OC Dermatology

Fountain Valley, California, United States

Site Status

Miami Dermatology and Laser Institute

Miami, Florida, United States

Site Status

University of Michigan Hospital

Ann Arbor, Michigan, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Wright State Physicians

Fairborn, Ohio, United States

Site Status

Premier Specialists

Kogarah, , Australia

Site Status

Diagnostic and Consulting Center Aleksandrovska EOOD

Sofia, , Bulgaria

Site Status

West China Hospital of Sichuan University

Chengdu, , China

Site Status

The First Affiliated Hospital of Chongqing Medical University

Chongqing, , China

Site Status

Ruijin Hospital Shanghai Jiaotong University School of Medicine

Shanghai, , China

Site Status

Poliklinika Solmed

Zagreb, , Croatia

Site Status

Fakultni nemocnice Bulovka

Prague, , Czechia

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitätsklinikum Carl Gustav Carus an der TU Dresden

Dresden, , Germany

Site Status

Universitatsklinikum Dusseldorf

Düsseldorf, , Germany

Site Status

Universitatsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status

LMU Klinikum der Universität

München, , Germany

Site Status

Universitätsklinikum Würzburg

Würzburg, , Germany

Site Status

Hospital of Venereal and Skin Diseases A.Syggros

Athens, , Greece

Site Status

Hospital Of Skin And Venereal Diseases of Thessaloniki

Thessaloniki, , Greece

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Sheba Medical Center - PPDS

Ramat Gan, , Israel

Site Status

Azienda Ospedaliero Universitaria Policlinico Vittorio Emanuele

Catania, , Italy

Site Status

Azienda USL Toscana Centro - Ospidale Piero Palagi

Florence, , Italy

Site Status

Azienda Sanitaria Di Firenze

Florence, , Italy

Site Status

Ospedale Policlinico San Martino

Genova, , Italy

Site Status

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Fondazione IRCCS Policlinico San Matteo di Pavia

Pavia, , Italy

Site Status

IDI IRCCS - Istituto Dermopatico dell'Immacolata

Roma, , Italy

Site Status

Fondazione Policlinico Universitario A. Gemelli

Rome, , Italy

Site Status

Hokkaido University Hospital

Sapporo, , Japan

Site Status

Universitair Medisch Centrum Groningen

Groningen, , Netherlands

Site Status

University Clinical Center of Serbia - PPDS

Belgrade, , Serbia

Site Status

Univerzitna nemocnica Bratislava

Bratislava, , Slovakia

Site Status

Fakultna nemocnica Trnava

Trnava, , Slovakia

Site Status

Hospital Universitario Clínico San Cecilio

Granada, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario Doctor Peset

Valencia, , Spain

Site Status

Guy's and St Thomas' NHS Foundation Trust

London, , United Kingdom

Site Status

Countries

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United States Australia Bulgaria China Croatia Czechia Germany Greece Hungary Israel Italy Japan Netherlands Serbia Slovakia Spain United Kingdom

Other Identifiers

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2024-515832-59-00

Identifier Type: CTIS

Identifier Source: secondary_id

ARGX-113-2010

Identifier Type: -

Identifier Source: org_study_id

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