A Study to Evaluate the Efficacy and Safety of Dupilumab in Adult Patients With Bullous Pemphigoid

NCT ID: NCT04206553

Last Updated: 2025-10-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

106 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-10-28

Study Completion Date

2025-01-05

Brief Summary

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The main purpose of this study is to investigate whether dupilumab is effective and safe for the treatment of bullous pemphigoid. Dupilumab is a type of drug called a "monoclonal antibody". An antibody is a special kind of protein that the immune (defense) system normally makes to fight bacteria and viruses. Bullous pemphigoid is an autoimmune subepidermal blistering disease, predominately affecting the elderly (typical onset after age 60).

The study is looking at several other research questions, including:

* Side effects that may be experienced by people taking dupilumab
* How dupilumab works in the body and affects the body
* How dupilumab affects quality of life
* How much dupilumab is present in the blood
* To see if dupilumab works to wean the patient off oral corticosteroids

Detailed Description

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Conditions

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Bullous Pemphigoid

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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dupilumab

Group Type EXPERIMENTAL

dupilumab

Intervention Type DRUG

Loading dose administered subcutaneous (SC), followed by SC once every 2 weeks (Q2W) dosing.

Oral corticosteroids (OCS)

Intervention Type DRUG

Prednisone or prednisolone per standard of care to obtain control of disease activity.

Matching placebo

Group Type EXPERIMENTAL

Matching Placebo

Intervention Type DRUG

Matching dupilumab without active substance

Oral corticosteroids (OCS)

Intervention Type DRUG

Prednisone or prednisolone per standard of care to obtain control of disease activity.

Interventions

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dupilumab

Loading dose administered subcutaneous (SC), followed by SC once every 2 weeks (Q2W) dosing.

Intervention Type DRUG

Matching Placebo

Matching dupilumab without active substance

Intervention Type DRUG

Oral corticosteroids (OCS)

Prednisone or prednisolone per standard of care to obtain control of disease activity.

Intervention Type DRUG

Other Intervention Names

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Dupixent® REGN668 SAR231893

Eligibility Criteria

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Inclusion Criteria

* Patients must have characteristic clinical features of bullous pemphigoid (BP) (eg, urticarial or eczematous or erythematous plaques, bullae, pruritus) at the screening and baseline visits.
* Study participants are required to have a confirmed diagnosis of BP based on histopathology, immunopathology, and serology at the baseline visit, as defined in the protocol.
* Bullous Pemphigoid Disease Area Index (BPDAI) activity score ≥24 at baseline and screening visits.
* Baseline peak pruritus NRS score for maximum itch intensity ≥4
* Karnofsky performance status score ≥50% at the screening visit.

Exclusion Criteria

* Forms of pemphigoid other than classic BP (eg, Brunsting-Perry cicatricial pemphigoid, anti-p200 pemphigoid, epidermolysis bullosa acquisita, or BP with concomitant pemphigus vulgaris)
* Patients who are receiving treatments known to cause or exacerbate BP (eg, angiotensin converting enzyme inhibitors, penicillamine, furosemide, phenacetin, dipeptidyl peptidase 4 inhibitor) who have not been on a stable dose of these medications for at least 4 weeks prior to the screening visit
* Have ever received treatment with an IL-4 or IL-13 antagonist such as dupilumab, tralokinumab, or lebrikizumab.
* Treatment with systemic corticosteroids within 7 days before the baseline visit
* Treatment with topical corticosteroids of medium potency or higher, topical calcineurin inhibitor, or topical crisaborole within 7 days before the baseline visit
* Treatment with non-steroidal immunosuppressive/immunomodulating drug(s) (eg, mycophenolate mofetil, azathioprine, or methotrexate) within 4 weeks before the baseline visit.
* Treatment with BP-directed biologics as follows:
* Any cell-depleting agents including but not limited to rituximab: within 12 months before the baseline visit, or until lymphocyte and CD 19+ lymphocyte count returns to normal, whichever is longer
* Other biologics (such as IL-5 inhibitors benralizumab or mepolizumab): within 5 half-lives (if known) or 16 weeks prior to the baseline visit, whichever is longer
* Intravenous immunoglobulin within 16 weeks prior to the baseline visit
Minimum Eligible Age

18 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sanofi

INDUSTRY

Sponsor Role collaborator

Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trial Management

Role: STUDY_DIRECTOR

Regeneron Pharmaceuticals

Locations

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Regeneron study Site

Birmingham, Alabama, United States

Site Status

Regeneron Study Site

Scottsdale, Arizona, United States

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Regeneron Study Site

Redwood City, California, United States

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Farmington, Connecticut, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Iowa City, Iowa, United States

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Boston, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Chapel Hill, North Carolina, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Providence, Rhode Island, United States

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Murray, Utah, United States

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Charlottesville, Virginia, United States

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Kogarah, New South Wales, Australia

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Box Hill, Victoria, Australia

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Bobigny, , France

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Bordeaux, , France

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Lille, , France

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Nice, , France

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Paris, , France

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Rouen, , France

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Münster, North Rhine-Westphal, Germany

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Mainz, Rhineland-Palatinate, Germany

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Regeneron Study Site 2

Dresden, Saxony, Germany

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Lübeck, Schleswig-Holstein, Germany

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Berlin, , Germany

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Buxtehude, , Germany

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Erlangen, , Germany

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Freiburg im Breisgau, , Germany

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Regeneron Study site'

Magdeburg, , Germany

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Marburg, , Germany

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Munich, , Germany

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Stuttgart, , Germany

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Afula, , Israel

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Petah Tikva, , Israel

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Tel Aviv, , Israel

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Kurume, Hukuoka, Japan

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Hirosaki, , Japan

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Ichinomiya, , Japan

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Osaka, , Japan

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Sapporo, , Japan

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Tokyo, , Japan

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Krakow, Lesser Poland Voivodeship, Poland

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Regeneron Study site'

Ossy, , Poland

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Regeneron Study site'

Wroclaw, , Poland

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Regeneron Study Site

Badalona, Barcelona, Spain

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Madrid, , Spain

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Madrid, , Spain

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Regeneron study Site

Pamplona, , Spain

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Regeneron study Site

Taipei, Zhongzheng District, Taiwan

Site Status

Regeneron study Site

Taoyuan, , Taiwan

Site Status

Countries

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United States Australia France Germany Israel Japan Poland Spain Taiwan

References

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Murrell DF, Joly P, Werth VP, Ujiie H, Worm M, Mangold AR, Avetisova E, Maloney J, Laws E, Mortensen E, Dubost-Brama A, Shabbir A. Study Design of a Phase 2/3 Randomized Controlled Trial of Dupilumab in Adults with Bullous Pemphigoid: LIBERTY-BP ADEPT. Adv Ther. 2024 Jul;41(7):2991-3002. doi: 10.1007/s12325-024-02810-3. Epub 2024 Mar 5.

Reference Type DERIVED
PMID: 38443648 (View on PubMed)

Other Identifiers

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2019-003520-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2024-510745-34-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

R668-BP-1902

Identifier Type: -

Identifier Source: org_study_id

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