A Study to Evaluate the Efficacy and Safety of Ruxolitinib Cream in Participants With Prurigo Nodularis (PN)

NCT ID: NCT05764161

Last Updated: 2025-12-18

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

190 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-06-12

Study Completion Date

2025-11-04

Brief Summary

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The purpose of this study is to evaluate the safety and tolerability of Ruxolitinib cream in participants with Prurigo Nodularis (PN).

Detailed Description

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The study comprises of a 12 week double-blind, vehicle-controlled (DBVC) treatment period, followed by a 40 week open label extension period, and 30 day safety follow-up period During the double blind period, all PN-affected areas identified at baseline will be treated, and during the open label period, only active PN-affected areas will be treated.

Conditions

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Prurigo Nodularis

Keywords

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PN INCB18424-320 INCB18424 Prurigo Prurigo Nodularis Skin Diseases Dermatitis ruxolitinib

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ruxolitinib 1.5% Cream

Participants apply ruxolitinib 1.5% cream topically to the affected areas as a thin film BID for 12 weeks during the DBVC period. Participants who have completed the treatment during DBVC period will enter the open label extension (OLE) period for up to 40 weeks.

Group Type EXPERIMENTAL

Ruxolitinib Cream

Intervention Type DRUG

Ruxolitinib cream 1.5% twice daily (BID) during the continuous and open label treatment period.

Vehicle Cream

Participants apply ruxolitinib matching vehicle cream topically to the affected areas as a thin film twice daily (BID) for 12 weeks during the DBVC period. Participants who have completed the treatment during DBVC period will enter the open label extension (OLE) period for up to 40 weeks.

Group Type PLACEBO_COMPARATOR

Vehicle Cream

Intervention Type DRUG

Ruxolitinib matching vehicle cream 1.5% twice daily (BID) during the vehicle-controlled period.

Interventions

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Ruxolitinib Cream

Ruxolitinib cream 1.5% twice daily (BID) during the continuous and open label treatment period.

Intervention Type DRUG

Vehicle Cream

Ruxolitinib matching vehicle cream 1.5% twice daily (BID) during the vehicle-controlled period.

Intervention Type DRUG

Other Intervention Names

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Opzelura INCB018424 phosphate cream

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of PN ≥ 3 months before screening.
* ≥ 6 pruriginous lesions on ≥ 2 different body areas (such as right and left leg) at screening and baseline having a treatment area \<20% BSA.
* IGA-CPG-S score of ≥ 2 at screening and baseline.
* Baseline PN-related WI-NRS score ≥ 7.
* Willingness to avoid pregnancy or fathering children.

Exclusion Criteria

* Chronic pruritus due to a condition other than PN
* Total estimated BSA treatment area (excluding the scalp) \> 20%.
* Neuropathic and psychogenic pruritus
* Active atopic dermatitis lesions within 3 months of screening and baseline.
* Uncontrolled thyroid function
* Concurrent skin or other serious or unstable medical conditions which may interfere with the evaluation of PN such as immunocompromised status, acute/chronic infections, active malignancy, history of TB, history of DVT/VTE, etc Protocol defined abnormal laboratory results.
* Use of any protocol-defined prohibited medication unless a washout is completed or use of medication known to cause itching.
* Psoralen and ultraviolet A or ultraviolet B therapy within 4 weeks before baseline or Ultraviolet light therapy or prolonged exposure to natural or artificial sources of ultraviolet radiation (within 2 weeks before baseline
* Pregnant or lactating, or considering pregnancy.
* History of alcoholism or drug addiction within 1 year
* Known allergy or reaction to any of the components of the study drug.
* Committed to a mental health institution by virtue of an order issued either by the judicial or the administrative authorities.
* Employees of the sponsor or investigator or otherwise dependents of them.
* The following participants are excluded in France:

1. Vulnerable populations according to article L.1121-6 of the French Public Health Code.
2. Adults under legal protection or who are unable to express their consent per article L.1121-8 of the French Public Health Code.
3. Individuals not affiliated with the social security system.
Minimum Eligible Age

18 Years

Maximum Eligible Age

99 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama At Birmingham

Birmingham, Alabama, United States

Site Status

Northwest Arkansas Clinical Trials Center

Arkansas City, Arkansas, United States

Site Status

Dermatology Research Associates

Los Angeles, California, United States

Site Status

Clinical Science Institute Clinical Research Specialists Inc

Santa Monica, California, United States

Site Status

Cura Clinical Research

Sherman Oaks, California, United States

Site Status

Ars - Maitland Clinical Research Unit

Orlando, Florida, United States

Site Status

Marietta Dermatology the Skin Cancer Center Marietta

Marietta, Georgia, United States

Site Status

The South Bend Clinic Main Campus

South Bend, Indiana, United States

Site Status

Axon Clinical Research

Baltimore, Maryland, United States

Site Status

Activmed Practices Research, Llc Beverly

Beverly, Massachusetts, United States

Site Status

Oakview Dermatology

Athens, Ohio, United States

Site Status

Aventiv Research Inc-Dublin

Dublin, Ohio, United States

Site Status

Wright State Physicians, Inc.

Fairborn, Ohio, United States

Site Status

University of Pittsburgh Medical Center Upmc Dermatology Clinic Oakland Falk Medical Building

Pittsburgh, Pennsylvania, United States

Site Status

Dermdox Center For Dermatology

Sugarloaf, Pennsylvania, United States

Site Status

Dermresearch, Inc.

Austin, Texas, United States

Site Status

Premier Specialists Pty Ltd

Kogarah, New South Wales, Australia

Site Status

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status

Holdsworth House Medical Practice

Sydney, New South Wales, Australia

Site Status

Westmead Hospital

Sydney, New South Wales, Australia

Site Status

Veracity Clinical Research

Woolloongabba, Queensland, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Paratus Clinical Research, Woden

Phillip, , Australia

Site Status

Landeskrankenhaus Universitatsklinikum Graz

Graz, , Austria

Site Status

Ordensklinikum Linz Gmbh Elisabethinen

Linz, , Austria

Site Status

Sozialmedizinisches Zentrum Ost-Donauspital

Vienna, , Austria

Site Status

Medical Center Medconsult Pleven Ood

Pleven, , Bulgaria

Site Status

Medical Center- Prolet Ltd

Rousse, , Bulgaria

Site Status

Medical Center Unimed Eood

Sevlievo, , Bulgaria

Site Status

Dcc 'Alexandrovska', Eood

Sofia, , Bulgaria

Site Status

Medical Center Hera Eood

Sofia, , Bulgaria

Site Status

Umhat Prof. Dr. Stoyan Kirkovich Ad

Stara Zagora, , Bulgaria

Site Status

Kingsway Clinical Research

Etobicoke, Ontario, Canada

Site Status

Lynderm Research Inc

Markham, Ontario, Canada

Site Status

North York Research Inc.

North YORK, Ontario, Canada

Site Status

Skin Centre For Dermatology

Peterborough, Ontario, Canada

Site Status

Diex Recherche Quebec Inc.

Québec, Quebec, Canada

Site Status

Herlev Og Gentofte Hospital

Hellerup, , Denmark

Site Status

Sjaellands Universitetshospital

Roskilde, , Denmark

Site Status

Bordeaux Chu Hopital Saint - Andre

Bordeaux, , France

Site Status

Chu Dijon-Bourgogne

Dijon, , France

Site Status

Hopital Edouard Herrio

Lyon, , France

Site Status

Chu de Nice - Hospital L Archet

Nice, , France

Site Status

Centre Hospitalier Universitaire de Poitiers

Poitiers, , France

Site Status

Chu Amiens - Hopital Sud

Salouël, , France

Site Status

Klinikum Bielefeld Rosenhohe Dermatologie

Bielefeld, , Germany

Site Status

Universitatsklinikum Frankfurt

Frankfurt am Main, , Germany

Site Status

Universitatsmedizin Goettingen

Göttingen, , Germany

Site Status

Dermatologische Gemeinschaftspraxis Mahlow

Mahlow, , Germany

Site Status

Universitatsklinikum Munster

Münster, , Germany

Site Status

Fondazione Irccs Ca Granda Ospedale Maggiore

Milan, , Italy

Site Status

Universita Degli Studi Della Campania Luigi Vanvitelli

Napoli, , Italy

Site Status

Azienda Ospedaliera Di Perugia - Ospedale Santa Maria Della Misericordia

Perugia, , Italy

Site Status

Azienda Ospedaliero Universitaria Pisana - Ospedale S. Chiara

Pisa, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico Tor Vergata

Rome, , Italy

Site Status

Diamond Clinic Specjalistyczne Poradnie Lekarskie

Krakow, , Poland

Site Status

Dermoklinika Centrum Medyczne S.C., M. Kierstan, J. Narbutt, A. Lesiak

Lodz, , Poland

Site Status

Luxderm Specjalistyczny Gabinet Dermatologiczny

Lublin, , Poland

Site Status

Centrum Badawcze Panaceum Agnieszka Brzezicka, Magdalena Lenkiewicz Sp. Z O.O.

Malbork, , Poland

Site Status

Solumed Centrum Medyczne

Poznan, , Poland

Site Status

Dermaceum Centrum Badan Klinicznych

Wroclaw, , Poland

Site Status

Dermmedica Sp. Z O.O.

Wroclaw, , Poland

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea Seoul St. Mary'S Hospital

Seoul, , South Korea

Site Status

Korea University Guro Hospital

Seoul, , South Korea

Site Status

Ajou University Hospital

Suwon, , South Korea

Site Status

Ceim Hospital Universitari Germans Trias I Pujol

Badalona, , Spain

Site Status

Hospital Universitario de Gran Canaria Doctor Negrin

Las Palmas de Gran Canaria, , Spain

Site Status

Hospital Universitario Ramon Y Cajal

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Clinica Gaias Santiago

Santiago de Compostela, , Spain

Site Status

Dermatology & Skin Care Clinic

Buochs, , Switzerland

Site Status

Centre Hospitalier Universitaire Vaudois (Chuv)

Lausanne, , Switzerland

Site Status

Universitatsspital Zurich

Zurich-flughafen, , Switzerland

Site Status

Countries

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United States Australia Austria Bulgaria Canada Denmark France Germany Italy Poland South Korea Spain Switzerland

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2022-502461-23-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

INCB18424-320

Identifier Type: -

Identifier Source: org_study_id