A Study to Evaluate the Safety and Efficacy of Ruxolitinib Cream in Participants With Prurigo Nodularis (PN)

NCT ID: NCT05755438

Last Updated: 2025-11-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

204 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-10

Study Completion Date

2025-08-13

Brief Summary

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The purpose of this study is to evaluate the safety and tolerability of Ruxolitinib cream in participants with Prurigo Nodularis (PN).

Detailed Description

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The study comprises of a 12 week double-blind, vehicle-controlled (DBVC) treatment period, followed by a 40 week open label extension period, and 30 day safety follow-up period During the double blind period, all PN-affected areas identified at baseline will be treated, and during the open label period, only active PN-affected areas will be treated.

Conditions

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Prurigo

Keywords

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Prurigo Prurigo Nodularis PN Skin Diseases Dermatitis Eczematous ruxolitinib INCB 18424

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Vehicle Cream BID

Participants apply ruxolitinib matching vehicle cream topically to the affected areas as a thin film twice daily (BID) for 12 weeks during the DBVC period. Participants who have completed the treatment during DBVC period will apply ruxolitinib 1.5% cream topically during the open label extension (OLE) period for up to 40 weeks.

Group Type PLACEBO_COMPARATOR

Vehicle Cream

Intervention Type DRUG

Ruxolitinib matching vehicle cream 1.5% twice daily (BID) during the vehicle controlled period (DBVC).

Ruxolitinib 1.5% Cream

Participants apply ruxolitinib 1.5% cream topically to the affected areas as a thin film BID for 12 weeks during the DBVC period. Participants who have completed the treatment during DBVC period will apply ruxolitinib 1.5% cream the open label extension (OLE) period for up to 40 weeks.

Group Type EXPERIMENTAL

Ruxolitinib Cream

Intervention Type DRUG

Ruxolitinib cream 1.5% twice daily (BID) during the vehicle controlled (DBVC)and open label treatment period (OLE).

Interventions

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Ruxolitinib Cream

Ruxolitinib cream 1.5% twice daily (BID) during the vehicle controlled (DBVC)and open label treatment period (OLE).

Intervention Type DRUG

Vehicle Cream

Ruxolitinib matching vehicle cream 1.5% twice daily (BID) during the vehicle controlled period (DBVC).

Intervention Type DRUG

Other Intervention Names

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INCB018424 phosphate cream

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of PN ≥ 3 months before screening.
* ≥ 6 pruriginous lesions on ≥ 2 different body areas (such as right and left leg) at screening and baseline having a treatment area \<20% BSA.
* IGA-CPG-S score of ≥ 2 at screening and baseline.
* Baseline PN-related WI-NRS score ≥ 7.
* Willingness to avoid pregnancy or fathering children.

Exclusion Criteria

* Chronic pruritus due to a condition other than PN
* Total estimated BSA treatment area (excluding the scalp) \> 20%.
* Neuropathic and psychogenic pruritus
* Active atopic dermatitis lesions within 3 months of screening and baseline.
* Uncontrolled thyroid function
* Concurrent skin or other serious or unstable medical conditions which may interfere with the evaluation of PN such as immunocompromised status, acute/chronic infections, active malignancy, history of TB, history of DVT/VTE, etc Protocol defined abnormal laboratory results.
* Use of any protocol-defined prohibited medication unless a washout is completed or use of medication known to cause itching.
* Psoralen and ultraviolet A or ultraviolet B therapy within 4 weeks before baseline or Ultraviolet light therapy or prolonged exposure to natural or artificial sources of ultraviolet radiation (within 2 weeks before baseline
* Pregnant or lactating, or considering pregnancy.
* History of alcoholism or drug addiction within 1 year
* Known allergy or reaction to any of the components of the study drug.
* Committed to a mental health institution by virtue of an order issued either by the judicial or the administrative authorities.
* Employees of the sponsor or investigator or otherwise dependents of them.
* The following participants are excluded in France:

1. Vulnerable populations according to article L.1121-6 of the French Public Health Code.
2. Adults under legal protection or who are unable to express their consent per article L.1121-8 of the French Public Health Code.
3. Individuals not affiliated with the social security system.
Minimum Eligible Age

18 Years

Maximum Eligible Age

99 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Haq Nawaz, md

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Medical Dermatology Specialists Phoenix

Phoenix, Arizona, United States

Site Status

Johnson Dermatology

Fort Smith, Arkansas, United States

Site Status

First Oc Dermatology

Fountain Valley, California, United States

Site Status

Dermatology Associates Pc

Rockville, Maryland, United States

Site Status

Clarkston Medical Group

Clarkston, Michigan, United States

Site Status

Revival Research Institute, Llc Troy

Troy, Michigan, United States

Site Status

Medisearch Clinical Trials

Saint Joseph, Missouri, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

UC Health, Llc

Cincinnati, Ohio, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Central Sooner Research

Norman, Oklahoma, United States

Site Status

Dermatology Associates of Plymouth Meeting

Plymouth Meeting, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

International Clinical Research Tennessee Llc

Murfreesboro, Tennessee, United States

Site Status

North Texas Center For Clinical Research Ntccr

Frisco, Texas, United States

Site Status

Austin Institute For Clinical Research Aicr Pflugerville

Pflugerville, Texas, United States

Site Status

Center For Clinical Studies

Webster, Texas, United States

Site Status

Premier Clinical Research

Spokane, Washington, United States

Site Status

Conexa Investigacion Clinica S.A.

Buenos Aires, , Argentina

Site Status

Cedic Centro de Investigaciones Clinicas

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Buenos Aires Skin

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Psoriahue-Medicina Interdisciplinar

Ciudad Autonoma Buenos Aires, , Argentina

Site Status

Centro de Investigaciones Medicas Mar Del Plata

Mar del Plata, , Argentina

Site Status

Fundacion Scherbovsky

Mendoza, , Argentina

Site Status

Instituto de Especialidades de La Salud Rosario

Rosario, , Argentina

Site Status

Centro de Investigaciones Medicas Tucuman

San Miguel de Tucumán, , Argentina

Site Status

Ulb Hospital Erasme

Brussels, , Belgium

Site Status

Cliniques Universitaires Ucl Saint-Luc

Brussels, , Belgium

Site Status

Az Sint-Lucas

Ghent, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Universitair Ziekenhuis (Uz) Leuven

Leuven, , Belgium

Site Status

Centre Hospitalier Universitaire de Liege - Sart Tilman

Liège, , Belgium

Site Status

Chu Ucl Namur de Saint Elisabeth

Namur, , Belgium

Site Status

Beacon Dermatology

Calgary, Alberta, Canada

Site Status

Simcomed Health Ltd

Barrie, Ontario, Canada

Site Status

Dermeffects

London, Ontario, Canada

Site Status

Research Toronto

Toronto, Ontario, Canada

Site Status

Centre de Recherche Saint-Louis

Québec, Quebec, Canada

Site Status

Centro Medico Skinmed

Las Condes, , Chile

Site Status

Ciec - Centro Internacional de Estudios Cli-Nicos

Santiago, , Chile

Site Status

Clinical Research Chile Spa.

Valdivia, , Chile

Site Status

Hospital Prive D'Antony

Antony, , France

Site Status

Hospital Morvan

Brest, , France

Site Status

Centre Hospitalier Universitaire de Nantes (Chu de Nantes) - Hotel-Dieu

Nantes, , France

Site Status

University Hospital of Saint Etienne

Saint-Etienne, , France

Site Status

University Medical Center Rwth Aachen

Aachen, , Germany

Site Status

Fachklinik Bad Bentheim Dermatologie

Bad Bentheim, , Germany

Site Status

Universitaetsklinikum Carl Gustav Carus Tu Dresden

Dresden, , Germany

Site Status

Universitatsklinikum Schleswig Holstein

Kiel, , Germany

Site Status

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

Mainz, , Germany

Site Status

Universitats-Hautklink Tubingen

Tübingen, , Germany

Site Status

Hautarztpraxis Dr. Med. Matthias Hoffmann

Witten, , Germany

Site Status

Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia (Presidio Spedali Civili)

Brescia, , Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico G.Rodolico San Marco

Catania, , Italy

Site Status

Asl 1 Avezzano L'Aquila Sulmona- Ospedale Regionale San Salvatore

Coppito, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico 'Federico Ii'

Napoli, , Italy

Site Status

Fondazione Policlinico Universitario Agostino Gemelli Irccs

Roma, , Italy

Site Status

Ospedali Riuniti Di Ancona

Torrette, , Italy

Site Status

Amsterdam University Medical Centre

Amsterdam, , Netherlands

Site Status

Bravis Ziekenhuis

Bergen op Zoom, , Netherlands

Site Status

Pratia McM Krakow

Krakow, , Poland

Site Status

ETG LODZ

Lodz, , Poland

Site Status

Kliniczny Szpital Wojewodzki Nr 1

Rzeszów, , Poland

Site Status

Clinical Research Group Sp. Z.O.O

Warsaw, , Poland

Site Status

High-Med Przychodnia Specjalistycza

Warsaw, , Poland

Site Status

Centralny Szpital Kliniczny Mswia

Warsaw, , Poland

Site Status

Hospital General Unviersitario de Alicante

Alicante, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital de Manises

Manises, , Spain

Site Status

Hospital Universitario Quironsalud Madrid

Pozuelo de Alarcón, , Spain

Site Status

Complejo Hospitalario Universitario de Santiago

Santiago de Compostela, , Spain

Site Status

Countries

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Brazil United States Argentina Belgium Canada Chile France Germany Italy Netherlands Poland Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2022-501621-20-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

INCB 18424-319

Identifier Type: -

Identifier Source: org_study_id