Study to Compare Axicabtagene Ciloleucel With Standard of Care Therapy as First-line Treatment in Participants With High-risk Large B-cell Lymphoma

NCT ID: NCT05605899

Last Updated: 2025-10-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

300 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-02-10

Study Completion Date

2031-03-31

Brief Summary

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The goal of this clinical study is to compare the study drug, axicabtagene ciloleucel, versus standard of care (SOC) in first-line therapy in participants with high-risk large B-cell lymphoma.

Detailed Description

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Five years after randomization, participants who have received axicabtagene ciloleucel will transition to a separate long-term follow-up study (study KT-US-982-5968) to complete the remainder of the 15-year follow-up assessments.

Conditions

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High-risk Large B-cell Lymphoma (LBCL)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Axicabtagene Ciloleucel

Participants will receive cyclophosphamide 500 mg/m\^2/day intravenously (IV) and fludarabine 30 mg/m\^2/day IV lymphodepletion chemotherapy for 3 days followed by axicabtagene ciloleucel administered as a single IV infusion at a target dose of 2 x 10\^6 anti-cluster of differentiation (CD)19 chimeric antigen receptor (CAR) transduced autologous T cells/kg on Day 0.

Group Type EXPERIMENTAL

Axicabtagene Ciloleucel

Intervention Type BIOLOGICAL

A single infusion of chimeric antigen receptor (CAR)-transduced autologous T cells

Cyclophosphamide

Intervention Type DRUG

Administered intravenously

Fludarabine

Intervention Type DRUG

Administered intravenously

Standard of Care Therapy

Participants will receive the investigator's choice of one of the following therapies/dosing schedules:

* Rituximab plus cyclophosphamide, doxorubicin, vincristine, and prednisone (R-CHOP) for a total of 6 cycles (21-day cycle)

* Rituximab 375 mg/m\^2 on Day 1
* Cyclophosphamide 750 mg/m\^2 on Day 1
* Doxorubicin 50 mg/m\^2 on Day 1
* Vincristine 1.4 mg/m\^2 (maximum 2 mg) on Day 1
* Prednisone 40 mg/m\^2 on Day 1 through Day 5
* Dose-adjusted etoposide, prednisone, vincristine, cyclophosphamide, doxorubicin, and rituximab (DA-EPOCH-R) for a total of 6 cycles (21-day cycle)

* Rituximab 375 mg/m\^2 on Day 1
* Etoposide 50 mg/m\^2 on Days 1 to 4
* Doxorubicin 10 mg/m\^2 on Days 1 to 4
* Vincristine 0.4 mg/m\^2 on Days 1 to 4
* Cyclophosphamide 750 mg/m\^2 on Day 5
* Prednisone 60 mg/m\^2 twice daily on Days 1 to 5

Group Type ACTIVE_COMPARATOR

Cyclophosphamide

Intervention Type DRUG

Administered intravenously

Etoposide

Intervention Type DRUG

Administered intravenously

Rituximab

Intervention Type DRUG

Administered intravenously

Doxorubicin

Intervention Type DRUG

Administered intravenously

Vincristine

Intervention Type DRUG

Administered intravenously

Prednisone

Intervention Type DRUG

Administered orally

Interventions

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Axicabtagene Ciloleucel

A single infusion of chimeric antigen receptor (CAR)-transduced autologous T cells

Intervention Type BIOLOGICAL

Cyclophosphamide

Administered intravenously

Intervention Type DRUG

Fludarabine

Administered intravenously

Intervention Type DRUG

Etoposide

Administered intravenously

Intervention Type DRUG

Rituximab

Administered intravenously

Intervention Type DRUG

Doxorubicin

Administered intravenously

Intervention Type DRUG

Vincristine

Administered intravenously

Intervention Type DRUG

Prednisone

Administered orally

Intervention Type DRUG

Other Intervention Names

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Yescarta® Axi-cel

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed large B cell lymphoma (LBCL) based on 2016 World Health Organization (WHO) classification by local pathology lab assessment, including of the following:

* Diffuse large B-cell lymphoma (DLBCL), not otherwise specified (NOS)
* High-grade B-cell lymphoma (HGBL)
* Note: Transformed DLBCL from follicular lymphoma or from marginal zone lymphoma is eligible if no prior treatment with anthracycline-containing regimen.
* High-risk disease defined as an International Prognostic Index (IPI) score of 4 or 5 at initial diagnosis.
* Have received only 1 cycle of rituximab plus chemotherapy (R-chemotherapy).
* Adequate bone marrow, renal, hepatic, pulmonary, and cardiac function.
* Females of childbearing potential must have a negative serum or urine pregnancy test.

Exclusion Criteria

* The following WHO 2016 subcategories by local assessment:

* T-cell/histiocyte-rich LBCL
* Primary DLBCL of the central nervous system (CNS)
* Primary mediastinal (thymic) LBCL
* B-cell lymphoma, unclassifiable, with features intermediate between DLBCL and classical Hodgkin lymphoma
* Burkitt lymphoma
* History of Richter's transformation of chronic lymphocytic leukemia
* Presence of detectable cerebrospinal fluid (CSF)-malignant cells, brain metastases, or a history of CNS involvement of lymphoma.
* Presence of cardiac lymphoma involvement.
* Any prior treatment for LBCL other than the 1 cycle of R-chemotherapy.
* History of severe immediate hypersensitivity reaction to any of the agents used in this study.
* Presence of CNS disorder. History of stroke, transient ischemic attack, or posterior reversible encephalopathy syndrome (PRES) within 12 months prior to enrollment.
* History of acute or chronic active hepatitis B or C infection.
* Positive for human immunodeficiency virus (HIV) unless taking appropriate anti-HIV medications, with an undetectable viral load by PCR and with a cluster of differentiation 4 (CD4) count \> 200 cells/uL.
* Medical conditions or residual toxicities from prior therapies likely to interfere with assessment of safety or efficacy of study treatment. Please refer to protocol for further details.
* History of clinically significant cardiac disease within 12 months before enrollment.
* History of any medical condition requiring maintenance systemic immunosuppression/systemic disease modifying agents within the last 2 years.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kite, A Gilead Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kite Study Director

Role: STUDY_DIRECTOR

Kite, A Gilead Company

Locations

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University of Alabama Hospital

Birmingham, Alabama, United States

Site Status RECRUITING

Banner MD Anderson Cancer Center

Gilbert, Arizona, United States

Site Status RECRUITING

Mayo Clinic

Phoenix, Arizona, United States

Site Status RECRUITING

UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status RECRUITING

University of California Los Angeles (UCLA)

Los Angeles, California, United States

Site Status RECRUITING

Stanford Cancer Institute

Palo Alto, California, United States

Site Status RECRUITING

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status RECRUITING

Moffitt Cancer Center

Tampa, Florida, United States

Site Status RECRUITING

Georgia Cancer Center at Augusta University

Augusta, Georgia, United States

Site Status RECRUITING

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status RECRUITING

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status RECRUITING

University of Iowa

Iowa City, Iowa, United States

Site Status RECRUITING

The University of Kansas Hospital

Westwood, Kansas, United States

Site Status RECRUITING

Norton Cancer Institute, St. Matthews Campus

Shelbyville, Kentucky, United States

Site Status RECRUITING

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status RECRUITING

University of MD Greenebaum Comprehensive Cancer Center

Baltimore, Maryland, United States

Site Status RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

University of Michigan

Ann Arbor, Michigan, United States

Site Status RECRUITING

Mayo Clinic Cancer Center Outpatient Pharmacy

Rochester, Minnesota, United States

Site Status RECRUITING

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status RECRUITING

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status RECRUITING

Weill Cornell Medical College - NewYork Presbyterian Hospital

New York, New York, United States

Site Status RECRUITING

Columbia University Medical Center

New York, New York, United States

Site Status RECRUITING

University of Rochester Medical Center

Rochester, New York, United States

Site Status RECRUITING

Montefiore Medical Center

The Bronx, New York, United States

Site Status RECRUITING

Novant Health Cancer Institute- Hematology

Charlotte, North Carolina, United States

Site Status RECRUITING

Oncology Hematology Care Clinical Trials, LLC

Cincinnati, Ohio, United States

Site Status RECRUITING

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status WITHDRAWN

Prisma Health Cancer Institute

Greenville, South Carolina, United States

Site Status RECRUITING

Avera Cancer Institute

Sioux Falls, South Dakota, United States

Site Status WITHDRAWN

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status RECRUITING

Henry-Joyce Cancer Center

Nashville, Tennessee, United States

Site Status RECRUITING

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status RECRUITING

The University of Texas, MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Intermountain LDS Hospital/Blood and Marrow Transplant/ Acute Leukemia Program

Salt Lake City, Utah, United States

Site Status RECRUITING

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status RECRUITING

Fred Hutchinson Cancer Center

Seattle, Washington, United States

Site Status WITHDRAWN

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status RECRUITING

Royal Brisbane and Women's Hospital

South Brisbane, Queensland, Australia

Site Status RECRUITING

Peter MacCallum Cancer Center

Melbourne, Victoria, Australia

Site Status RECRUITING

Medizinische Universität Innsbruck

Innsbruck, , Austria

Site Status RECRUITING

Zuniklinikum Salzburg, Landeskrankenhaus, Universitatsklinik fur Innere Medizin III der PMU

Salzburg, , Austria

Site Status RECRUITING

Universitätsklinikum St. Pölten

Sankt Pölten, , Austria

Site Status RECRUITING

Medizinische Universität Wien (AKH Wien, Medical University Vienna and General Hospital Vienna)

Vienna, , Austria

Site Status RECRUITING

Jewish General Hospital

Montreal, , Canada

Site Status RECRUITING

The Ottowa Hospital- General Campus

Ottawa, , Canada

Site Status RECRUITING

Princess Margaret Cancer Centre

Toronto, , Canada

Site Status RECRUITING

CHU Bordeaux-Hopital Haut-Leveque

Bordeaux, , France

Site Status RECRUITING

Centre Leon Berard

Cedex Lyon 08, , France

Site Status RECRUITING

CHU Dijon

Dijon, , France

Site Status RECRUITING

Hopital Claude Huriez CHU Lille, Service Maladies du sang

Lille, , France

Site Status RECRUITING

Hopital Saint Eloi

Montpellier, , France

Site Status RECRUITING

Centre Hospitalier Universitaire de Nice

Nice, , France

Site Status RECRUITING

Hopital Henri MONDOR, APHP

Paris, , France

Site Status RECRUITING

CHU Pontchaillou

Rennes, , France

Site Status RECRUITING

Centre Hospitalier Universitaire(CHU) de Toulouse

Toulouse, , France

Site Status RECRUITING

Helios Klinikum Berlin-Buch

Berlin, , Germany

Site Status RECRUITING

Charite Universitaetsmedizin Berlin

Berlin, , Germany

Site Status RECRUITING

Universitätsklinikum bonn, medizinische klinik III

Bonn, , Germany

Site Status RECRUITING

Uniklinikum Duesseldorf, Klinik fuer Haematologie, Onkologie und klinische Immunologie

Düsseldorf, , Germany

Site Status RECRUITING

Universitätsklinik Erlangen

Erlangen, , Germany

Site Status RECRUITING

IRCCS Azienda Ospedaliero-Universitaria di Bologna

Bologna, , Italy

Site Status RECRUITING

ASST Degli Spedali Civili di Brescia

Brescia, , Italy

Site Status RECRUITING

Ospedale San Raffaele

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliera di Perugia - Ospedale S. Maria della Misericordia

Perugia, , Italy

Site Status RECRUITING

Grande Ospedale Metropolitano Bianchi Melacrino Morelli

Reggio Calabria, , Italy

Site Status RECRUITING

Universita Cattolica del Sacro Cuore

Rome, , Italy

Site Status RECRUITING

IRCCS Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

University Hospital, Kyoto Prefectural University of Medicine

Kyoto, , Japan

Site Status RECRUITING

Tohoku University Hospital

Miyagi, , Japan

Site Status RECRUITING

Osaka University Hospital

Osaka, , Japan

Site Status RECRUITING

Juntendo University Hospital

Tokyo, , Japan

Site Status RECRUITING

Tokyo Metropolitan Komagome Hospital

Tokyo, , Japan

Site Status RECRUITING

Academisch Medisch Centrum

Amsterdam, , Netherlands

Site Status RECRUITING

University Medical Center Groningen

Groningen, , Netherlands

Site Status RECRUITING

Leiden University Medical Center

Leiden, , Netherlands

Site Status RECRUITING

Maastricht Universitair Medisch Centrum

Maastricht, , Netherlands

Site Status RECRUITING

Universitair Medisch Centrum Utrecht

Utrecht, , Netherlands

Site Status RECRUITING

Centro Hospitalar Universitario Lisboa Norte, E.P.E. - Hospital de Santa Maria

Lisbon, , Portugal

Site Status RECRUITING

Instituto Portugues de Oncologia de Lisboa Francisco Gentil - E.P.E.

Lisbon, , Portugal

Site Status RECRUITING

Instituto Portugues de Oncologia do Porto Francisco Gentil, E.P.E.

Porto, , Portugal

Site Status RECRUITING

Institut Catala d'Oncologia

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari Vall D'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario de Salamanca

Salamanca, , Spain

Site Status RECRUITING

Hospital Universitario Marqués de Valdecilla

Santander, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Clínico Universitario de Valencia

Valencia, , Spain

Site Status RECRUITING

Addenbrookes Hospital (Cambridge University Hospitals NHS Foundation Trust)

Birmingham, , United Kingdom

Site Status RECRUITING

University Hospitals Southampton

Southampton, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Austria Canada France Germany Italy Japan Netherlands Portugal Spain United Kingdom

Central Contacts

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Medical Information

Role: CONTACT

844-454-5483(1-844-454-KITE)

Related Links

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Other Identifiers

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2022-501489-24-00

Identifier Type: OTHER

Identifier Source: secondary_id

KT-US-484-0136

Identifier Type: -

Identifier Source: org_study_id

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