Assess the Safety, Pharmacokinetics, Pharmacodynamics and Clinical Activity of RXC007 in Idiopathic Pulmonary Fibrosis

NCT ID: NCT05570058

Last Updated: 2024-08-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-09-08

Study Completion Date

2025-01-09

Brief Summary

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The purpose of the study is to assess the safety and tolerability of RXC007 when given for 12 weeks (84 days), alone and in combination with nintedanib or pirfenidone.

Detailed Description

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The purpose of this study is to investigate the study drug RXC007.

The main objectives of this study are as follows:

* To determine the safety and tolerability (degree to which side effects of a drug can be tolerated) of RXC007 when it is administered as twice daily doses over a period of up to 12 weeks (84 days).
* To investigate the concentration of RXC007 (how much drug is in your blood), how this changes over a period of time and to evaluate whether there are differences in the concentration between different dose strengths of RXC007.
* To investigate the effect of RXC007 on the body (known as pharmacodynamics) by analysing the levels of certain biomarkers in the body and to assess the effect of RXC007 on markers associated with Idiopathic Pulmonary Fibrosis (IPF). Biomarkers are markers within the body such as a molecule or compound made by cells in the body, which can be measured and used to identify a particular disease.

Conditions

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IPF Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Cohort 1

12:4 (RXC007 : Placebo) Dose level 1: 12 weeks (84 days) dosing

Group Type EXPERIMENTAL

RXC007

Intervention Type DRUG

RXC007 will be administered in the form of oral capsules at 3 potential dose levels: 20 mg, 50mg and 70 mg in 5 cohorts. 12 patients of cohorts 1, 2 and the Expansion cohort will receive RXC007. The Dosage regimen is BID or QD.

Placebo

Intervention Type DRUG

The placebo will be administered in the form of oral capsules at each dose level to 4 of the 16 participants within cohorts 1, 2 and the Expansion cohort. The Dosage regimen is BID or QD

Cohort 2

12:4 (RXC007 : Placebo) Dose level 2: 12 weeks (84 days) dosing

Group Type EXPERIMENTAL

RXC007

Intervention Type DRUG

RXC007 will be administered in the form of oral capsules at 3 potential dose levels: 20 mg, 50mg and 70 mg in 5 cohorts. 12 patients of cohorts 1, 2 and the Expansion cohort will receive RXC007. The Dosage regimen is BID or QD.

Placebo

Intervention Type DRUG

The placebo will be administered in the form of oral capsules at each dose level to 4 of the 16 participants within cohorts 1, 2 and the Expansion cohort. The Dosage regimen is BID or QD

Expansion Cohort

12:4 (RXC007 : Placebo) Dose level 3: 12 weeks (84 days) dosing

Group Type EXPERIMENTAL

RXC007

Intervention Type DRUG

RXC007 will be administered in the form of oral capsules at 3 potential dose levels: 20 mg, 50mg and 70 mg in 5 cohorts. 12 patients of cohorts 1, 2 and the Expansion cohort will receive RXC007. The Dosage regimen is BID or QD.

Placebo

Intervention Type DRUG

The placebo will be administered in the form of oral capsules at each dose level to 4 of the 16 participants within cohorts 1, 2 and the Expansion cohort. The Dosage regimen is BID or QD

Interventions

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RXC007

RXC007 will be administered in the form of oral capsules at 3 potential dose levels: 20 mg, 50mg and 70 mg in 5 cohorts. 12 patients of cohorts 1, 2 and the Expansion cohort will receive RXC007. The Dosage regimen is BID or QD.

Intervention Type DRUG

Placebo

The placebo will be administered in the form of oral capsules at each dose level to 4 of the 16 participants within cohorts 1, 2 and the Expansion cohort. The Dosage regimen is BID or QD

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Aged ≥40 to 80 years at the time of signing the informed consent.
* Diagnosis of IPF within 5 years of Screening based on the modified ATS/ERS/JRS/ALAT IPF guidelines for diagnosis and management of IPF (Raghu et al, 2018) and confirmed on independent central imaging review.
* Combination of HRCT pattern, as assessed by central reviewers, consistent with diagnosis of IPF (see the modified ATS/ERS/JRS/ALAT IPF guidelines \[Raghu et al, 2018\]).
* FVC % predicted ≥50% predicted of normal at Screening, with no clinically significant deterioration between the Screening Visit and randomisation, as determined by the Investigator.
* DLco (Hb-adjusted) at screening ≥30%.
* In the main study, participants receiving treatment for IPF with nintedanib or pirfenidone are allowed if on treatment for at least 3 months and on a stable dose for at least 4 weeks prior to Screening and during Screening.
* In patients who are not on any treatment for IPF but have previously received nintedanib or pirfenidone, there needs to be a washout period ≥4 weeks prior to Screening.
* No clinically significant abnormalities, in the opinion of the investigator, in vital signs (e.g., blood pressure, pulse rate, respiration rate, oral temperature) within 28 days before first dose of IMP.

Exclusion Criteria

* Currently receiving or planning to initiate treatment for IPF with agents not approved for that indication.
* FEV1/FVC ratio \<0.7 at Screening, pre-bronchodilator use.
* Lower respiratory tract infection requiring antibiotics within 4 weeks of Screening or during Screening.

4\. The extent of emphysema in the lungs exceeds fibrosis, based on central review of HRCT scans.
* Need for continuous oxygen supplementation, defined as \>15 hours/day.
* Acute IPF exacerbation within 6 months of Screening or during Screening.
* Clinical diagnosis of any connective-tissue disease (including, but not limited to, scleroderma, polymyositis/dermatomyositis, systemic lupus erythematosus, and rheumatoid arthritis) or a diagnosis of interstitial pneumonia with autoimmune features as determined by the Investigator applying the recent ERS/ATS research statement \[Fischer et al 2015\]. Note: Serological testing is not needed if not clinically indicated.
* Disease other than IPF with a life expectancy of less than 12 weeks.


* Participants with any contra-indication to bronchoscopy and alveolar lavage including tracheal stenosis, pulmonary hypertension, severe hypoxia, or hypercapnia.
* Patients in the sub study are not permitted to receive nintedanib or pirfenidone within 3 weeks of randomisation and throughout the Treatment period. (Note: background IPF treatment should not be stopped for the purpose of eligibility)
Minimum Eligible Age

40 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Simbec-Orion Group

INDUSTRY

Sponsor Role collaborator

Redx Pharma Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Philip Molyneaux, MD

Role: PRINCIPAL_INVESTIGATOR

Royal Brompton & Harefield NHS Foundation Trust

Toby Maher, MD

Role: PRINCIPAL_INVESTIGATOR

University of Southern California, USA

Locations

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Medical University of Vienna

Vienna, , Austria

Site Status

E PNE UZ Leuven

Leuven, , Belgium

Site Status

CHU De Liège

Liège, , Belgium

Site Status

Pneumologicka klinika 1.LF UK a

Prague, , Czechia

Site Status

Azienda Ospedaliero-Universitaria "Ospedali-Riuniti" di Ancona

Ancona, , Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico ''G.Rodolico-San Marco''

Catania, , Italy

Site Status

Colonello D'avanzo Hospital

Foggia, , Italy

Site Status

PO Vito Fazzi

Lecce, , Italy

Site Status

Ospedale S. Giuseppe Milano

Milan, , Italy

Site Status

Azienda Ospedaliera Universitaria of Modena

Modena, , Italy

Site Status

Fondazione Policlinico Universitario A. Gemelli

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria Integrata Verona

Verona, , Italy

Site Status

University Clinical Centre in Gdansk

Gdansk, , Poland

Site Status

Barlicki University Hospital

Lodz, , Poland

Site Status

Institute of Tuberculosis and Lung Diseases in Warsaw

Warsaw, , Poland

Site Status

Policlinica Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario Clínic de Barcelona

Barcelona, , Spain

Site Status

L'Hospital Universitari de Bellvitge

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, , Spain

Site Status

Hospital Universitario Marqués de Valdecilla

Santander, , Spain

Site Status

Hospital Clínico Universitario de Santiago de Compostela

Santiago de Compostela, , Spain

Site Status

University Hospital of Geneve

Geneva, , Switzerland

Site Status

Belfast City Hospital

Belfast, , United Kingdom

Site Status

Queen Elizabeth Hospital

Birmingham, , United Kingdom

Site Status

Royal Papworth Hospital NHSFT

Cambridge, , United Kingdom

Site Status

Royal Infirmary of Edinburgh

Edinburgh, , United Kingdom

Site Status

Guy's Hospital

London, , United Kingdom

Site Status

Royal Brompton Hospital

London, , United Kingdom

Site Status

Altnagelvin Area Hospital

Londonderry, , United Kingdom

Site Status

Churchill Hospital, Oxford University Hospitals NHS Trust

Oxford, , United Kingdom

Site Status

Countries

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Austria Belgium Czechia Italy Poland Spain Switzerland United Kingdom

Other Identifiers

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RXC007/0002

Identifier Type: -

Identifier Source: org_study_id

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