LYT-100 in Patients With Idiopathic Pulmonary Fibrosis (IPF)

NCT ID: NCT05321420

Last Updated: 2025-10-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-22

Study Completion Date

2025-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study a randomized, double-blind, four arm study to evaluate the safety and efficacy of LYT-100 compared to pirfenidone or placebo in adults with Idiopathic Pulmonary Fibrosis.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study is a randomized, double-blind, being conducted at centers globally to evaluate the safety and efficacy of LYT-100 compared to pirfenidone or placebo in 240 treatment naïve adult patients with IPF ≥ 40 years in age. Patients will be randomized in a ratio of 1:1:1:1 to receive treatment of LYT-100, pirfenidone, or placebo to be taken daily for up to 183 days (26 week treatment period) with the primary outcome of Rate of decline in Forced Vital Capacity (FVC; in mL) over 26 weeks. Secondary endpoints, including spirometry, inflammatory biomarkers, and patient-reported outcomes will also be evaluated.

After completion of the double-blind period of the study, patients may participate in a long-term extension to evaluate tolerability and long-term safety. Patients receiving LYT-100 in the double-blind period will continue the dose throughout the long-term extension. Patients receiving pirfenidone or placebo in the double-blind period will be re-randomized in a 1:1 ratio to receive LYT-100 550mg or 825mg TID dose throughout the long-term extension.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Idiopathic Pulmonary Fibrosis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Placebo

Placebo oral administration

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

placebo

pirfenidone 801 mg TID

pirfenidone 801 mg TID oral administration

Group Type ACTIVE_COMPARATOR

Pirfenidone

Intervention Type DRUG

pirfenidone 801 mg TID

LYT-100 550 mg TID

LYT-100 (Deupirfenidone) 550 mg TID oral administration

Group Type EXPERIMENTAL

Deupirfenidone

Intervention Type DRUG

Deupirfenidone

LYT-100 825 mg TID

LYT-100 (Deupirfenidone) 825 mg TID oral administration

Group Type EXPERIMENTAL

Deupirfenidone

Intervention Type DRUG

Deupirfenidone

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Placebo

placebo

Intervention Type DRUG

Pirfenidone

pirfenidone 801 mg TID

Intervention Type DRUG

Deupirfenidone

Deupirfenidone

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Treatment naïve patients or those with \<6 months of exposure to nintedanib with physician diagnosed IPF based on ATS/ERS/JRS/ALAT 2018 guidelines
* Idiopathic Pulmonary Fibrosis on HRCT, performed within 12 months of Visit 1 as confirmed by central readers
* DLCO corrected for Hemoglobin (Hb) \[visit 1\] ≥ 30% and ≤90% of predicted of normal
* FVC ≥ 45% of predicted normal

Exclusion Criteria

* Primary obstructive airway physiology (pre-bronchodilator FEV1/FVC \< 0.7 at Visit 1)
* Known explanation for interstitial lung disease, including but not limited to radiation, sarcoidosis, hypersensitivity pneumonitis, bronchiolitis obliterans organizing pneumonia, human immunodeficiency virus (HIV), viral hepatitis, and cancer
* Diagnosis of any connective tissue disease, including but not limited to scleroderma/systemic sclerosis, polymyositis/dermatomyositis, systemic lupus erythematosus, and rheumatoid arthritis
* Major extrapulmonary physiological restriction (e.g., chest wall abnormality, large pleural effusion)
* Cardiovascular diseases, any of the following:

* Uncontrolled hypertension, within 3 months of Visit 1
* Myocardial infarction within 6 months of Visit 1
* Unstable cardiac angina within 6 months of Visit 1
* Prior hospitalization for confirmed COVID-19, acute exacerbation of IPF or any lower respiratory tract infection within 3-months of Visit 1
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

PureTech

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Camilla Graham, MD

Role: STUDY_DIRECTOR

PureTech

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama Birmingham

Birmingham, Alabama, United States

Site Status

Science 37

Los Angeles, California, United States

Site Status

NewportNativeMD, Inc.

Newport Beach, California, United States

Site Status

Paradigm Clinical Research Centers, Inc.

Redding, California, United States

Site Status

Los Angeles Biomedical Research Institute at Harbor UCLA Medical Center

Torrance, California, United States

Site Status

University of Connecticut Health Center

Farmington, Connecticut, United States

Site Status

Accel Research Sites Network

DeLand, Florida, United States

Site Status

Harmony Medical Research Institute, Inc

Hialeah, Florida, United States

Site Status

Piedmont Healthcare, Inc.

Atlanta, Georgia, United States

Site Status

Clinical Research Investments

Decatur, Georgia, United States

Site Status

Indiana University School of Medicine

Indianapolis, Indiana, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Pulmonix

Greensboro, North Carolina, United States

Site Status

Southeastern Research Center

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Temple University

Philadelphia, Pennsylvania, United States

Site Status

Clinical Trials Center of Middle Tennessee

Franklin, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor Scott & White Research Institute

Dallas, Texas, United States

Site Status

Renovatio Clinical - The Woodlands Research Center

The Woodlands, Texas, United States

Site Status

Pulmonary Associates of Richmond

Richmond, Virginia, United States

Site Status

TPMG Clinical Research

Williamsburg, Virginia, United States

Site Status

Instituto Médico de la Fundación de Estudios Clinicos / Fundación Estudios

Rosario, Santa Fe Province, Argentina

Site Status

Aprillus Asistencia e Investigación

Buenos Aires, , Argentina

Site Status

CEMER Centro Medico de Enfermedades Respiratorias

Buenos Aires, , Argentina

Site Status

Instituto de Medicina Respiratoria - IMER

Córdoba, , Argentina

Site Status

Respira Salud Clinica Integral

Godoy Cruz, , Argentina

Site Status

Instituto Ave Pulmo - Fundacion Enfisema

Mar del Plata, , Argentina

Site Status

Polo de Salud Vistalba

Mendoza, , Argentina

Site Status

CIMRO- Centro de Investigación Médica Respiratoria Oncológica

Mendoza, , Argentina

Site Status

INSARES - Instituto de Salud Respiratoria

Mendoza, , Argentina

Site Status

Centro Médico Dharma

Mendoza, , Argentina

Site Status

Instituto de Enfermedades Respiratorias e Investigación Clínica

San Juan Bautista, , Argentina

Site Status

Investigaciones en Patologías Respiratorias

San Miguel de Tucumán, , Argentina

Site Status

Instituto del Buen Aire

Santa Fe, , Argentina

Site Status

Clinica Central S.A.

Villa Regina, , Argentina

Site Status

Clinica Maule

Maule, , Chile

Site Status

Centro de Estudios Clinicos

Santiago, , Chile

Site Status

Clinica Universidad de Los Andes

Santiago, , Chile

Site Status

Centro Respiratorio Integral

Valparaíso, , Chile

Site Status

Fundacion Cardiomet CEQUIN

Armenia, , Colombia

Site Status

Instituto Neumologico del Oriente S.A.

Bucaramanga, , Colombia

Site Status

Centro de Investigaciones Clinicas S.A.S

Cali, , Colombia

Site Status

National Ceneter for Tuberculosis and Lung Diseases JSC

Tbilisi, , Georgia

Site Status

Tbilisi State Medical University and Ingorokva High Medical Technology University Clinic LLC

Tbilisi, , Georgia

Site Status

Emergency Cardiology Center by Academician G. Chapidze LLC

Tbilisi, , Georgia

Site Status

LTD Aversi Clinic

Tbilisi, , Georgia

Site Status

LTD The First Medical Center

Tbilisi, , Georgia

Site Status

University Hospital Alexandroupolis

Alexandroupoli, , Greece

Site Status

"Sotiria" Chest Diseases Hospital of Athens

Athens, , Greece

Site Status

University General Hospital "Attikon"

Athens, , Greece

Site Status

Athens Medical Center

Athens, , Greece

Site Status

University General Hospital of Patras

Pátrai, , Greece

Site Status

General Hospital of Thessaloniki "G. Papanikolaou"

Thessaloniki, , Greece

Site Status

Rhythm Heart Institute Vadodara

Vadodara, Gujarat, India

Site Status

Sparsh Super Specialty Hospital

Bengaluru, Karnataka, India

Site Status

Mgm Medical College And Hospital, Aurangabad

Aurangabad, Maharashtra, India

Site Status

Government Medical College and Hospital Aurangabad

Aurangabad, Maharashtra, India

Site Status

Oriion Citicare Super Specialty Hospital

Aurangabad, Maharashtra, India

Site Status

Getwell Hospital and Research Institute

Nagpur, Maharashtra, India

Site Status

Govt. General and Chest Hospital

Hyderabad, Telangana, India

Site Status

Apollo Spectra Hospital

Kanpur, Uttar Pradesh, India

Site Status

Nil Ratan Sircar Medical College And Hospital, Kolkata

Kolkata, West Bengal, India

Site Status

BHS Lakeview Heart

Belagāve, , India

Site Status

Hospital Sultanah Bahiyah

Alor Star, Kedah, Malaysia

Site Status

Hospital Pulau Pinang

George Town, , Malaysia

Site Status

Hospital Serdang

Kajang, , Malaysia

Site Status

Institut Perubatan Respiratori

Kuala Lumpur, , Malaysia

Site Status

University Malaya Medical Centre

Kuala Lumpur, , Malaysia

Site Status

Hospital Tengku Ampuan Afzan

Kuantan, , Malaysia

Site Status

Hospital Universitario Dr. José Eleuterio González

Monterrey, Nuevo León, Mexico

Site Status

Integral Health Medical Unit

San Nicolás de los Garza, Nuevo León, Mexico

Site Status

CALPULAB

Calpulalpan, , Mexico

Site Status

Oaxaca Site Management Organization

Oaxaca City, , Mexico

Site Status

ONCARE Group

San Pedro Garza García, , Mexico

Site Status

St. Luke's Medical Center - Global City

City of Taguig, , Philippines

Site Status

Philippine General Hospital

Manila, , Philippines

Site Status

Lung Center of the Philippines

Quezon City, , Philippines

Site Status

S.C. Netconsult SRL

Iași, , Romania

Site Status

S.C. Lavinia Davidescu Clinic SRL

Oradea, , Romania

Site Status

"Dr. Victor Babes" Clinical Hospital of Infectious Diseases and Pneumophtisiology

Timișoara, , Romania

Site Status

Durban Lung Centre

Durban, , South Africa

Site Status

WITS Clinical Research

Johannesburg, , South Africa

Site Status

Ahmed Kathrada Lenmed Private Hospital

Johannesburg, , South Africa

Site Status

Netcare Milpark Hospital

Parktown, , South Africa

Site Status

Ryexo Clinical Research

Pretoria, , South Africa

Site Status

The Catholic University Of Korea Bucheon St. Mary's Hospital

Bucheon-si, Gyeonggi-do, South Korea

Site Status

Hanyang University - Myongji Hospital

Goyang-si, Gyeonggi-do, South Korea

Site Status

InJe University Haeundae Paik Hospital

Busan, , South Korea

Site Status

Keimyung University - Dongsan Medical Center

Daegu, , South Korea

Site Status

Chonnam National University Hospital

Gwangju, , South Korea

Site Status

CHA Bundang Medical Center

Gyeonggi-do, , South Korea

Site Status

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status

Kyung Hee University Hospital

Seoul, , South Korea

Site Status

Hanyang University Seoul Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea, Yeouido St.Mary's Hospital

Seoul, , South Korea

Site Status

Ulsan University Hospital

Ulsan, , South Korea

Site Status

Siriraj Hospital

Bangkok, , Thailand

Site Status

Khon Kaen University

Khon Kaen, , Thailand

Site Status

Central Chest Institute Of Thailand

Nonthaburi, , Thailand

Site Status

Songklanagarind Hospital

Songkhla, , Thailand

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Chile Colombia Georgia Greece India Malaysia Mexico Philippines Romania South Africa South Korea Thailand

Related Links

Access external resources that provide additional context or updates about the study.

http://www.elevateipf.com

Recruiting website for patients in the United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

LYT-100-2022-204

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.