Management of Progressive Disease in Idiopathic Pulmonary Fibrosis

NCT ID: NCT03939520

Last Updated: 2024-12-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE4

Total Enrollment

378 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-06-11

Study Completion Date

2026-01-31

Brief Summary

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Idiopathic pulmonary fibrosis (IPF) is a prototype of chronic, progressive, and fibrotic lung disease. It has been considered rare, with an incidence estimated to 11.5 cases per 100 000 individuals per year. Increasing rates of hospital admissions and deaths due to IPF suggest an increasing burden of disease. The median survival time from diagnosis is 2-4 years.

Recently two disease-modifying therapies, pirfenidone and nintedanib, have been approved worldwide. Both drugs reduce the disease progression as measured by progressive decline in forced vital capacity (FVC), with a reduction of overall mortality showed by meta-analysis of phase III pirfenidone trials.

However, progression of disease continues to occur despite the currently available drug therapy. Many patients die from progressive, chronic hypoxemic respiratory failure, or less frequently from acute exacerbation of pulmonary fibrosis. In these patients, no data are available to guide management between continuation of the prescribed antifibrotic drug, to switch to the other available antifibrotic drug, or to combine the available drugs.

The combination of nintedanib and pirfenidone is not recommended outside clinical trials. However, although both antifibrotic drugs were developed and approved as monotherapy, two recent trials have suggested the feasibility and safety of combining them over a 12-24 weeks period. These results encourage further studies of combination treatment with pirfenidone and nintedanib in patients with IPF. Such study is timely, as there is a risk that clinicians facing the continued worsening of disease in patients receiving one of the available drugs may prescribe both drugs combined outside clinical trials, potentially exposing patients to a currently unknown risk.

This study will evaluate the efficacy and tolerance of the combination pirfenidone and nintedanib as compared to a "switch monotherapy": i.e. switching from the current to the other of the two existing drugs prescribed as monotherapy, in patients who present chronic worsening IPF despite receiving either pirfenidone or nintedanib and as to a "control group": i.e.treatment still be on as before randomization (pirfenidone or nintedanib).

Detailed Description

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Conditions

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Progressive Idiopathic Pulmonary Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Combined therapy

Group Type EXPERIMENTAL

pirfenidone and nintedanib

Intervention Type DRUG

The experimental group will receive pirfenidone 2403 mg per day (at least 1602 mg) in combination with nintedanib 300 mg per day (at least 200 mg) during 24 weeks.

Switch monotherapy

Group Type ACTIVE_COMPARATOR

pirfenidone or nintedanib

Intervention Type DRUG

The second intervention group will switch from one monotherapy during 24 weeks: with pirfenidone 2403 mg per day (at least 1602 mg) or nintedanib 300 mg per day (at least 200 mg) to the other monotherapy (nintedanib in patients who received pirfenidone as first line therapy before inclusion and conversely).

Control group

Group Type OTHER

pirfenidone or nintedanib

Intervention Type DRUG

The control group will keep on the same monotherapy during 24 weeks: with pirfenidone 2403 mg per day (at least 1602 mg) or nintedanib 300 mg per day (at least 200 mg) to the other monotherapy (nintedanib in patients who received pirfenidone as first line therapy before inclusion and conversely).

Interventions

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pirfenidone and nintedanib

The experimental group will receive pirfenidone 2403 mg per day (at least 1602 mg) in combination with nintedanib 300 mg per day (at least 200 mg) during 24 weeks.

Intervention Type DRUG

pirfenidone or nintedanib

The second intervention group will switch from one monotherapy during 24 weeks: with pirfenidone 2403 mg per day (at least 1602 mg) or nintedanib 300 mg per day (at least 200 mg) to the other monotherapy (nintedanib in patients who received pirfenidone as first line therapy before inclusion and conversely).

Intervention Type DRUG

pirfenidone or nintedanib

The control group will keep on the same monotherapy during 24 weeks: with pirfenidone 2403 mg per day (at least 1602 mg) or nintedanib 300 mg per day (at least 200 mg) to the other monotherapy (nintedanib in patients who received pirfenidone as first line therapy before inclusion and conversely).

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patient aged ≥ 50 years.
* Patient with Idiopathic Pulmonary Fibrosis satisfying the ATS/ERS/JRS/ALAT diagnostic criteria (29) diagnosed.

In the absence of a surgical lung biopsy, high-resolution computed tomography (HRCT) must be "consistent with Usual Interstitial Pneumonia (UIP)" defined as meeting either criteria A, B, and C, or criteria A and C, or criteria B and C below:

A. Definite honeycomb lung destruction with basal and peripheral predominance. B. Presence of reticular abnormality and traction bronchiectasis consistent with fibrosis, with basal and peripheral predominance.

C. Atypical features are absent, specifically nodules and consolidation. Ground glass opacity, if present, is less extensive than reticular opacity pattern.

* \- Patient who fulfill at least 1 of the 4 criteria for IPF progression in the 12 months (+/- one six months) before screening, despite antifibrotic treatment in clinical practice (if yes check the option(s)). These criteria are: 0 Relative decline in FVC ≥10% predicted 0 Relative decline in FVC ≥5-\<10% predicted and worsened respiratory symptoms 0 Relative decline in FVC ≥5-\<10% predicted and increased extent of fibrotic changes on chest imaging 0 Worsened respiratory symptoms and increased extent of fibrotic changes on chest imaging
* Patient must have been on a stable dose of pirfenidone or nintedanib prescribed as first-line therapy for at least 6 months, with good tolerance of 1602 to 2403 mg per day of pirfenidone or 200 to 300 mg per day of nintedanib.
* Patient who has a FVC ≥ 45% of predicted.
* Patient who has a forced expiratory volume in 1 second (FEV1)/FVC ratio \> 0.70.
* Patient who has a life expectancy of at least 9 months.
* Patient who has provided his written informed consent to participate in the study.
* Patient affiliated to a social insurance regimen.

Exclusion Criteria

* Patients under judicial protection.
* Female patient who is pregnant or lactating, or is of child bearing potential (defined as a sexually mature woman not surgically sterilized or not post-menopausal for at least 24 consecutive months if ≤ 55 years or 12 months if \> 55 years) and who did not agree to use highly effective methods of birth control throughout the study.
* Patient who is currently on both pirfenidone and nintedanib.
* Patient who has already received pirfenidone and nintedanib either concomitantly or successively.
* Patient who has a contra-indication to pirfenidone or nintedanib.
* Patient who has emphysema \> 15% on HRCT or the extent of emphysema is greater than the extent of fibrosis according to reported results from the most recent HRCT.
* Patient who had acute exacerbation of idiopathic pulmonary fibrosis within the previous 3 months.
* Patient who has a history of cigarette smoking within the previous 3 months.
* Patient who has received experimental therapy for IPF within 4 weeks before baseline.
* Patient who is receiving systemic corticosteroids equivalent to prednisone \> 15 mg/day or equivalent within 2 weeks before baseline.
* Patient who received Immuno-suppressants (e.g. methotrexate, azathioprine, cyclophosphamide, cyclosporine, sirolimus, everolimus or other immunosuppressants) within 4 weeks before baseline.
* Patient who has a history of a malignancy within the previous 5 years, with the exception of basal cell skin neoplasms. In addition, a malignant diagnosis or condition first occurring prior to 5 years must be considered cured, inactive, and not under current treatment.
* Patient who, in the Investigator's opinion, is not able to perform home spirometry in accordance with the protocol.
* Patient who has any concurrent condition other than IPF that, in the Investigator's opinion, is unstable and/or would impact the likelihood of survival for the study duration or the subject's ability to complete the study as designed, or may influence any of the safety or efficacy assessments included in the study.
* Patient who has baseline resting oxygen saturation of \< 88% on room air or supplemental oxygen.
* Patient who had lung transplantation or who is on a lung transplant list and the investigator anticipates the patient will not be able to complete the study prior to transplant.
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hospices Civils de Lyon

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Vincent COTTIN, Pr

Role: PRINCIPAL_INVESTIGATOR

Hospices Civils de Lyon

Locations

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CHU d'Angers

Angers, , France

Site Status RECRUITING

Centre Hospitalier de la côte Basque

Bayonne, , France

Site Status NOT_YET_RECRUITING

CHRU de Besançon - Hôpital Jean Minjoz

Besançon, , France

Site Status NOT_YET_RECRUITING

AP - HP - Hôpital Avicenne

Bobigny, , France

Site Status RECRUITING

CHRU Hôpital Cavale Blanche

Brest, , France

Site Status RECRUITING

Hôpital Pneumologique et Cardiovasculaire Louis Pradel

Bron, , France

Site Status RECRUITING

CHU de Caen - Hôpital de la Côte de Nacre

Caen, , France

Site Status RECRUITING

CHU Dijon Bourgogne - Hôpital François Mitterrand

Dijon, , France

Site Status RECRUITING

CHRU de Lille - Hôpital Albert Calmette

Lille, , France

Site Status RECRUITING

CHU de Marseille - Hôpital Nord

Marseille, , France

Site Status RECRUITING

CHRU de Montpellier - Hôpital Arnaud de Villeneuve

Montpellier, , France

Site Status RECRUITING

CHU - Hôpital G.R. Laennec

Nantes, , France

Site Status RECRUITING

CHU de Nice, Hôpital Pasteur

Nice, , France

Site Status RECRUITING

APHP - Hôpital Xavier Bichat-Claude Bernard

Paris, , France

Site Status RECRUITING

Groupe Hospitalier Paris Saint Joseph

Paris, , France

Site Status RECRUITING

Ch de Cornouaille

Quimper, , France

Site Status NOT_YET_RECRUITING

CHU Rennes - Hôpital Pontchaillou

Rennes, , France

Site Status RECRUITING

CHU de Toulouse - Hôpital Larrey

Toulouse, , France

Site Status RECRUITING

CHRU, Tours - Hôpital Bretonneau

Tours, , France

Site Status RECRUITING

CHU Nancy - Hôpital Brabois

Vandœuvre-lès-Nancy, , France

Site Status RECRUITING

Hôpital Robert Schuman

Vantoux, , France

Site Status RECRUITING

Countries

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France

Central Contacts

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Vincent COTTIN, Pr

Role: CONTACT

4 27 85 77 00 ext. +33

Yvonne Varillon

Role: CONTACT

472356964 ext. +33

Facility Contacts

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Frédéric GAGNADOUX

Role: primary

Pierre RIGAUD

Role: primary

Mathilde DUPREZ

Role: primary

Hilario NUNES

Role: primary

Aude BARNIER

Role: primary

Vincent Cottin, Pr

Role: primary

Emmanuel BERGOT

Role: primary

Philippe BONNIAUD

Role: primary

Lidwine WEMEAU-STERVINOU

Role: primary

Martine REYNAUD-GAUBERT

Role: primary

Anne-Sophie GAMEZ

Role: primary

Stéphanie DIROU

Role: primary

Charles-Hugo MARQUETTE

Role: primary

Bruno CRESTANI

Role: primary

Jean-Marc NACCACHE

Role: primary

Nicolas BIZIEN, Dr

Role: primary

Stéphane JOUNEAU

Role: primary

Grégoire PRÉVOT

Role: primary

Laurent PLANTIER

Role: primary

Anne GUILLAUMOT

Role: primary

Benoit GODBERT

Role: primary

Other Identifiers

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2019-004326-19

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

69HCL19_0029

Identifier Type: -

Identifier Source: org_study_id