Study to Evaluate EP547 in Subjects With Cholestatic Pruritus Due to Primary Biliary Cholangitis or Primary Sclerosing Cholangitis

NCT ID: NCT05525520

Last Updated: 2025-07-31

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

62 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-10-06

Study Completion Date

2024-09-05

Brief Summary

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This phase 2 trial will evaluate the effects of EP547 in subjects with cholestatic pruritus due to Primary Biliary Cholangitis (PBC) or Primary Sclerosing Cholangitis (PSC)

Detailed Description

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Conditions

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Pruritus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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EP547 100 mg

Group Type EXPERIMENTAL

EP547

Intervention Type DRUG

Once daily

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Once daily

Interventions

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EP547

Once daily

Intervention Type DRUG

Placebo

Once daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age 18 to 80 years
* Documented primary biliary cholangitis (PBC) or primary sclerosing cholangitis (PSC)
* Presence of consistent moderate to severe pruritus
* Use of anti-pruritic and anti-cholestatic (including UDCA and obeticholic acid) medication allowed if meeting additional criteria
* Individuals with concomitant inflammatory bowel disease must meet additional relevant criteria

Exclusion Criteria

* Pruritus associated with an etiology other than PBC or PSC
* Prior or planned liver transplantation
* Evidence of compensated or decompensated cirrhosis
* Alternative causes of liver disease
* Presence of documented secondary sclerosing cholangitis
* Current evidence of clinically significant high-grade strictures or presence of biliary stent
* History of significant small bowel resection or short bowel syndrome
* Has exclusionary laboratory or biochemical results at Screening
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Escient Pharmaceuticals, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama Birmingham Hospital

Birmingham, Alabama, United States

Site Status

Dignity Health Center for Clinical Research at St. Joseph Hospital

Phoenix, Arizona, United States

Site Status

Southern California Research Center

Coronado, California, United States

Site Status

Science 37

Culver City, California, United States

Site Status

California Liver Research Institute

Pasadena, California, United States

Site Status

University of Miami - Schiff Center for Liver Diseases

Miami, Florida, United States

Site Status

University of Iowa Hospitals & Clinics

Iowa City, Iowa, United States

Site Status

Tulane University Health Sciences Center

New Orleans, Louisiana, United States

Site Status

Ochsner Medical Center

New Orleans, Louisiana, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

NYU Grossman School of Medicine Gastroenterology and Hepatology

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Gastro Health Research

Cincinnati, Ohio, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

UPMC Center for Liver Disease

Pittsburgh, Pennsylvania, United States

Site Status

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, United States

Site Status

Liver Associates of Texas, PA

Houston, Texas, United States

Site Status

Gastro Health & Nutrition

Katy, Texas, United States

Site Status

Digestive & Liver Disease Specialists

Norfolk, Virginia, United States

Site Status

Bon Secours Liver Institute of Virginia

Richmond, Virginia, United States

Site Status

UZ Antwerpen

Antwerp, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

(G.I.R.I.) GI Research Institute

Vancouver, British Columbia, Canada

Site Status

Toronto Centre for Liver Disease Toronto General Hospital

Toronto, Ontario, Canada

Site Status

Centre hospitalier de l'Université de Montréal (CHUM)

Montreal, Quebeck, Canada

Site Status

APHP Avicenne

Bobigny, , France

Site Status

CHU Grenoble- Alpes- Site Nord

Grenoble, , France

Site Status

CHU de Lille

Lille, , France

Site Status

Saint Antoine Hospital

Paris, , France

Site Status

Hospital Rangueil

Toulouse, , France

Site Status

Paul Brousse Hospital

Villejuif, , France

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Rambam Medical Center- Keriat Eliezer Family Health Center

Haifa, , Israel

Site Status

Hadassah Medical Center (Ein-Karem)

Jerusalem, , Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Academic Medical Center- University of Amsterdam

Amsterdam, , Netherlands

Site Status

Hospital General Universitario Alicante

Alicante, , Spain

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Hospital de Montecelo

Pontevedra, , Spain

Site Status

Campus Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

La Fe University and Polytechnic Hospital

Valencia, , Spain

Site Status

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status

University Hospitals Birmingham NHS Foundation Trust

Birmingham, , United Kingdom

Site Status

Glasgow Royal Infirmary

Glasgow, , United Kingdom

Site Status

King's College Hospital NHS Foundation Trust

London, , United Kingdom

Site Status

Institute of Cellular Medicine, Newcastle University

Newcastle, , United Kingdom

Site Status

Norfolk and Norwich University Hospitals NHS Foundation Trust

Norwich, , United Kingdom

Site Status

University of Nottingham - Nottingham Digestive Diseases Centre Biomedical Research Unit

Nottingham, , United Kingdom

Site Status

University Hospitals Plymouth NHS Trust - Derriford Hospital

Plymouth, , United Kingdom

Site Status

Countries

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United States Belgium Canada France Israel Netherlands Spain United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2021-002526-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

EP-547-201

Identifier Type: -

Identifier Source: org_study_id

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