Study to Evaluate the Effects of Two Doses of Seladelpar (MBX-8025) in Subjects With Primary Biliary Cirrhosis (PBC)

NCT ID: NCT02609048

Last Updated: 2025-02-25

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

41 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-11-04

Study Completion Date

2016-07-01

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The primary objective of this study is to evaluate the effect of seladelpar (MBX-8025) on alkaline phosphatase (AP) levels in participants with primary biliary cirrhosis (PBC).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Primary:

To evaluate the effect of MBX-8025 on Alkaline Phosphatase (AP) levels

Secondary:

To evaluate the safety and tolerability of MBX-8025 in subjects with Primary Biliary Cirrhosis (PBC) To evaluate the effects of MBX-8025 on Primary Biliary Cirrhosis (PBC) response criteria To evaluate the effects of MBX-8025 on other markers of liver function, lipids, pruritus and Quality of Life (QoL)

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Primary Biliary Cirrhosis (PBC)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Placebo Dose

Participants received 2 placebo-to-match (PTM) seladelpar capsules, orally, once daily for 12 weeks.

Group Type PLACEBO_COMPARATOR

Placebo Comparator

Intervention Type DRUG

Placebo Capsule

Seladelpar 50 mg Dose

Participants received seladelpar 50 mg capsule (1 x 50 mg capsule) and a PTM seladelpar capsule, orally, once daily for 12 weeks.

Group Type EXPERIMENTAL

Placebo Comparator

Intervention Type DRUG

Placebo Capsule

Experimental: Seladelpar 50 mg

Intervention Type DRUG

Seladelpar 50 mg capsule

Seladelpar 200 mg Dose

Participants received seladelpar 200 mg capsules (2 x 100 mg capsules), orally, once daily for 12 weeks.

Group Type EXPERIMENTAL

Experimental: Seladelpar / MBX-8025 200 mg

Intervention Type DRUG

Seladelpar 100 mg capsules

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Placebo Comparator

Placebo Capsule

Intervention Type DRUG

Experimental: Seladelpar 50 mg

Seladelpar 50 mg capsule

Intervention Type DRUG

Experimental: Seladelpar / MBX-8025 200 mg

Seladelpar 100 mg capsules

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Placebo MBX-8025 Livdelzi® MBX-8025 Livdelzi®

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Must have given written informed consent (signed and dated) and any authorizations required by local law
2. 18 to 75 years old (inclusive)
3. Male or female with a diagnosis of PBC, by at least two of the following criteria:

* History of AP above upper limit of normal (ULN) for at least six months
* Positive Anti-Mitochondrial Antibodies (AMA) titers (\>1/40 on immunofluorescence or M2 positive by enzyme linked immunosorbent assay (ELISA) or positive PBC-specific antinuclear antibodies
* Documented liver biopsy result consistent with PBC
4. On a stable and recommended dose of UDCA for the past twelve months
5. AP ≥ 1.67 × ULN
6. For females of reproductive potential, use of at least one barrier contraceptive and a second effective birth control method during the study and for at least two weeks after the last dose. For male subjects, use of appropriate contraception (e.g., condoms), so their female partners of reproductive potential do not become pregnant during the study and for at least two weeks after the last dose

Exclusion Criteria

1. A medical condition, other than PBC, that in the investigator's opinion would preclude full participation in the study or confound its results (e.g., cancer on active treatment)
2. Aspartate Aminotransferase (AST) or Alanine Aminotransferase (ALT) \> 3 × ULN
3. Total bilirubin \> 2 × ULN
4. Auto-immune hepatitis
5. Primary sclerosing cholangitis
6. Known history of alpha-1-Antitrypsin deficiency
7. Known history of chronic viral hepatitis
8. Creatine kinase above ULN
9. Serum creatinine above ULN
10. For females, pregnancy or breast-feeding
11. Use of colchicine, methotrexate, azathioprine, or systemic steroids in the two months preceding screening
12. Current use of fibrates, including fenofibrates, or simvastatin
13. Use of an experimental treatment for PBC
14. Use of experimental or unapproved immunosuppressant
15. Any other condition(s) that would compromise the safety of the subject or compromise the quality of the clinical study, as judged by the Investigator
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Pol F Boudes, M.D.

Role: STUDY_CHAIR

Gilead Sciences

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Mayo Clinic of Arizona

Phoenix, Arizona, United States

Site Status

University of California, Davis Medical Center

Sacramento, California, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

University of Miami, Center for Liver Diseases

Miami, Florida, United States

Site Status

Norman Gitlin, MD

Atlanta, Georgia, United States

Site Status

Digestive Helathcare of Georgia

Atlanta, Georgia, United States

Site Status

Indiana University Hospital - Clinical Research Center

Indianapolis, Indiana, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Gastroenterology Associates of Western Michigan, PLC, d.b.a. West Michigan Clinical Research

Wyoming, Michigan, United States

Site Status

Kansas City Gastroenterology and Hepatology

Kansas City, Missouri, United States

Site Status

St. Louis University School of Medicine

St Louis, Missouri, United States

Site Status

University of Nebraska Medical Center / The Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

North Shore-Long Island Jewish Health System / Division of Gastroenterology

Manhasset, New York, United States

Site Status

NYU Langone Medical Center

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai - The Mount Sinai Medical Center

New York, New York, United States

Site Status

Consultants for Clinical Research

Cincinnati, Ohio, United States

Site Status

CHI St. Luke's Health Baylor College of Medicine Medical Center - Advanced Liver Therapies

Houston, Texas, United States

Site Status

Pinnacle Clinical Research

Live Oak, Texas, United States

Site Status

American Research Corporation at Texas Liver Institute

San Antonio, Texas, United States

Site Status

Bon Secours St. Mary's Hospital of Richmond

Newport News, Virginia, United States

Site Status

Digestive and Liver Disease Specialists

Norfolk, Virginia, United States

Site Status

University of Calgary Liver Unit (Heritage Medical Research Clinic)

Calgary, Alberta, Canada

Site Status

Toronto General Hospital

Toronto, Ontario, Canada

Site Status

Charite Universitatsmedizin Berlin - Campus Mitte

Berlin, , Germany

Site Status

Leber- und Studienzentrum am Checkpoint

Berlin, , Germany

Site Status

Universitatsklinikum Bonn

Bonn, , Germany

Site Status

Universitatsklinikum Carl Gustav Carus an der TU Dresden

Dresden, , Germany

Site Status

University Hospital Erlangen

Erlangen, , Germany

Site Status

Universitatsklinikum Essen, Zentrum fur Innere Medizin

Essen, , Germany

Site Status

Ifi-Studien und Projekte GmbH, A.d. Asklepios Klinik St. Georg

Hamburg, , Germany

Site Status

Universitatsklinikum Hamburg-Eppendorf MARTINISTRASSE 52

Hamburg, , Germany

Site Status

Med. Hochschule Hannover, Klinik fur Gastroenterologie

Hanover, , Germany

Site Status

Medizinische Universitatsklinik

Heidelberg, , Germany

Site Status

Gastroenterologische Gemeinschaftspraxis Herne

Herne, , Germany

Site Status

UKSH, Campus Kiel, Klinik fur Allgemeine Innere Medizin 1

Kiel, , Germany

Site Status

UKSH, Campus Kiel

Kiel, , Germany

Site Status

Universitatsklinikum Leipzig AOR

Leipzig, , Germany

Site Status

Universitatsmedizin der Johannes Gutenberg - Universitat Mainz

Mainz, , Germany

Site Status

Wojewodzki Szpital Obserwacyjno-Zakazny im. Tadeusza w Bydgoszczy

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

SPZOZ Szpital Uniwersytecki w Krakowie

Krakow, Malopolski, Poland

Site Status

Centrum Onkologii-Instytut Im. Marii Sklodowskiej-Curie

Warsaw, Masovian Voivodeship, Poland

Site Status

SP CSK im. Prof. K. Gibinskiego SUM w Katowicach

Katowice, Silesian Voivodeship, Poland

Site Status

ID Clinic Arkadiusz Pisula

Mysłowice, Silesian Voivodeship, Poland

Site Status

Derriford Hospital

Plymouth, England, United Kingdom

Site Status

University Hospital Birmingham NHS Foundation Trust

Birmingham, , United Kingdom

Site Status

Addenbrooke Hospital

Cambridge, , United Kingdom

Site Status

Hull and East Yorkshire NHS Trust

Hull, , United Kingdom

Site Status

The Newcastle upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, , United Kingdom

Site Status

Nottingham University Hospitals NHS Trust

Nottingham, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada Germany Poland United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Jones D, Boudes PF, Swain MG, Bowlus CL, Galambos MR, Bacon BR, Doerffel Y, Gitlin N, Gordon SC, Odin JA, Sheridan D, Worns MA, Clark V, Corless L, Hartmann H, Jonas ME, Kremer AE, Mells GF, Buggisch P, Freilich BL, Levy C, Vierling JM, Bernstein DE, Hartleb M, Janczewska E, Rochling F, Shah H, Shiffman ML, Smith JH, Choi YJ, Steinberg A, Varga M, Chera H, Martin R, McWherter CA, Hirschfield GM. Seladelpar (MBX-8025), a selective PPAR-delta agonist, in patients with primary biliary cholangitis with an inadequate response to ursodeoxycholic acid: a double-blind, randomised, placebo-controlled, phase 2, proof-of-concept study. Lancet Gastroenterol Hepatol. 2017 Oct;2(10):716-726. doi: 10.1016/S2468-1253(17)30246-7. Epub 2017 Aug 14.

Reference Type DERIVED
PMID: 28818518 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2015-002698-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CB8025-21528

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.