Study of INT 747 in Combination With URSO in Patients With Primay Biliary Cirrhosis (PBC)

NCT ID: NCT00550862

Last Updated: 2024-02-06

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

165 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-10-31

Study Completion Date

2010-12-31

Brief Summary

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The primary hypothesis is that INT-747 will cause a reduction in alkaline phosphatase levels in Primary Biliary Cirrhosis patients, over a 12 week treatment period, as compared to placebo.

Detailed Description

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None provided

Conditions

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Liver Cirrhosis, Biliary

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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INT-747 10 mg

INT-747 10 mg once daily in combination with URSO for 12 weeks.

Group Type EXPERIMENTAL

INT-747

Intervention Type DRUG

Once a day (QD) by mouth (PO)

Ursodeoxycholic Acid (URSO)

Intervention Type DRUG

Stable dose for at least 6 months prior to screening. Dose as prescribed by physician.

INT-747 25 mg

INT-747 25 mg once daily in combination with URSO for 12 weeks.

Group Type EXPERIMENTAL

INT-747

Intervention Type DRUG

Once a day (QD) by mouth (PO)

Ursodeoxycholic Acid (URSO)

Intervention Type DRUG

Stable dose for at least 6 months prior to screening. Dose as prescribed by physician.

INT-747 50 mg

INT-747 50 mg once daily in combination with URSO for 12 weeks.

Group Type EXPERIMENTAL

INT-747

Intervention Type DRUG

Once a day (QD) by mouth (PO)

Ursodeoxycholic Acid (URSO)

Intervention Type DRUG

Stable dose for at least 6 months prior to screening. Dose as prescribed by physician.

Placebo

Placebo once daily in combination with URSO for 12 weeks.

Group Type PLACEBO_COMPARATOR

INT-747

Intervention Type DRUG

Once a day (QD) by mouth (PO)

Ursodeoxycholic Acid (URSO)

Intervention Type DRUG

Stable dose for at least 6 months prior to screening. Dose as prescribed by physician.

Placebo

Intervention Type DRUG

Placebo

Interventions

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INT-747

Once a day (QD) by mouth (PO)

Intervention Type DRUG

Ursodeoxycholic Acid (URSO)

Stable dose for at least 6 months prior to screening. Dose as prescribed by physician.

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Other Intervention Names

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Obeticholic acid (OCA), 6-ECDCA URSO, UDCA

Eligibility Criteria

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Inclusion Criteria

* Male or female age 18 to 70 years.
* Stable dose of ursodeoxycholic acid (URSO, UDCA) for at least 6 months prior to screening.
* Female patients must be postmenopausal, surgically sterile, or prepared to use 2 methods of contraception with all sexual partners during the study and for 14 days after the end of dosing.
* Male patients must be prepared to use 2 methods of contraception with all sexual partners during the study and for 14 days after the end of the dosing.
* Proven or likely PBC, as demonstrated by the patient presenting with at least 2 of the following 3 diagnostic factors:

1. History of increased AP levels for at least 6 months prior to Day 0
2. Positive AMA titer (\>1:40 titer on immunofluorescence or M2 positive by ELISA) or PBC-specific antinuclear antibodies (antinuclear dot and nuclear rim positive)
3. Liver biopsy consistent with PBC.
* Screening AP value between 1.5 and 10 × ULN.

Exclusion Criteria

* Administration of the following drugs at any time during the 3 months prior to screening for the study: colchicine, methotrexate, azathioprine, or systemic corticosteroids.
* Screening conjugated (direct) bilirubin \>2 × ULN.
* Screening ALT or AST \>5 × ULN.
* Screening serum creatinine \>1.5 mg/dL (133 mol/L).
* History or presence of hepatic decompensation (e.g., variceal bleeds, encephalopathy, or poorly controlled ascites).
* History or presence of other concomitant liver diseases including hepatitis due to hepatitis B or C virus (HCV, HBV) infection, primary sclerosing cholangitis (PSC), alcoholic liver disease, definite autoimmune liver disease or biopsy proven nonalcoholic steatohepatitis (NASH).
* Pregnancy.
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Intercept Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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David A Shapiro, MD

Role: STUDY_DIRECTOR

Intercept Pharmaceuticals - Chief Medical Officer

Locations

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U Florida Hepatology

Gainesville, Florida, United States

Site Status

University of Miami - Center for Liver Diseases

Miami, Florida, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Henry Ford Health Center Columbus

Novi, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Beth Israel Medical Center

New York, New York, United States

Site Status

Mt. Sinai School of Medicine

New York, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

McGuire DVAMC

Richmond, Virginia, United States

Site Status

Virginia Mason Medical Center

Seattle, Washington, United States

Site Status

Karls-Franzens University

Graz, , Austria

Site Status

University of Calgary

Calgary, Alberta, Canada

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

University of Manitoba

Winnipeg, Manitoba, Canada

Site Status

University of Toronto Western Hospital

Toronto, Ontario, Canada

Site Status

Centre de Recherche du CHUM / University of Montreal

Montreal, Quebec, Canada

Site Status

Hopital de l'Hotel Dieu

Lyon, , France

Site Status

Johann Wolfgang Goethe University

Frankfurt, , Germany

Site Status

University Medical Centre Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Medical School of Hannover

Hanover, , Germany

Site Status

University of Munich

Munich, , Germany

Site Status

AMC University of Amsterdam

Amsterdam, , Netherlands

Site Status

Erasmus Medical Centre

Rotterdam, , Netherlands

Site Status

Hospital Clinic i Provincial

Barcelona, , Spain

Site Status

Queen Elizabeth Medical Center

Edgbaston, Birmingham, United Kingdom

Site Status

Royal Free Hospital

Hampstead, London, United Kingdom

Site Status

John Radcliffe Hospital

Headington, Oxford, United Kingdom

Site Status

Royal Infirmary

Edinburgh, , United Kingdom

Site Status

University Upon Tyne/Newcastle

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Austria Canada France Germany Netherlands Spain United Kingdom

References

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Hirschfield GM, Mason A, Luketic V, Lindor K, Gordon SC, Mayo M, Kowdley KV, Vincent C, Bodhenheimer HC Jr, Pares A, Trauner M, Marschall HU, Adorini L, Sciacca C, Beecher-Jones T, Castelloe E, Bohm O, Shapiro D. Efficacy of obeticholic acid in patients with primary biliary cirrhosis and inadequate response to ursodeoxycholic acid. Gastroenterology. 2015 Apr;148(4):751-61.e8. doi: 10.1053/j.gastro.2014.12.005. Epub 2014 Dec 11.

Reference Type DERIVED
PMID: 25500425 (View on PubMed)

Other Identifiers

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747-202

Identifier Type: -

Identifier Source: org_study_id

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