Study of OCA in Combination With BZF Evaluating Efficacy, Safety, and Tolerability in Participants With PBC

NCT ID: NCT04594694

Last Updated: 2025-11-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

75 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-02

Study Completion Date

2025-10-14

Brief Summary

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Study to evaluate the efficacy, safety, and tolerability of investigational drug obeticholic acid (OCA) in combination with the investigational drug bezafibrate (BZF) in participants with Primary Biliary Cholangitis (PBC).

Detailed Description

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Conditions

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Primary Biliary Cholangitis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Treatment A: BZF 200 milligrams (mg) Immediate release (IR)

Participants will receive Bezafibrate (BZF) 200 mg IR + OCA Placebo + BZF 400 mg Placebo

Group Type ACTIVE_COMPARATOR

Bezafibrate 200 MG

Intervention Type DRUG

200 mg IR tablet of Bezafibrate once daily for the remainder of the study

OCA Placebo

Intervention Type DRUG

One tablet daily for the remainder of the study

Bezafibrate 400 mg Placebo

Intervention Type DRUG

One tablet daily for the remainder of the study

Treatment B: BZF 400 mg SR

Participants will receive BZF 400 mg SR + OCA Placebo + BZF 200 mg Placebo

Group Type ACTIVE_COMPARATOR

OCA Placebo

Intervention Type DRUG

One tablet daily for the remainder of the study

Bezafibrate 200 mg Placebo

Intervention Type DRUG

One tablet daily for the remainder of the study

Bezafibrate 400 MG

Intervention Type DRUG

400 mg SR tablet of Bezafibrate once daily for the remainder of the study

Treatment C: OCA 5 mg to 10 mg + BZF 200 mg IR

Participants will receive OCA 5 mg to 10 mg + BZF 200 mg IR + BZF 400 mg Placebo

Group Type EXPERIMENTAL

Obeticholic acid

Intervention Type DRUG

5 mg tablet of OCA once daily titrating up to a maximum of 10 mg OCA once daily

Bezafibrate 200 MG

Intervention Type DRUG

200 mg IR tablet of Bezafibrate once daily for the remainder of the study

Bezafibrate 400 mg Placebo

Intervention Type DRUG

One tablet daily for the remainder of the study

Treatment D: OCA 5 mg to 10 mg + BZF 400 mg SR

Participants will receive OCA 5 mg to 10 mg + BZF 400 mg SR + BZF 200 mg Placebo

Group Type EXPERIMENTAL

Obeticholic acid

Intervention Type DRUG

5 mg tablet of OCA once daily titrating up to a maximum of 10 mg OCA once daily

Bezafibrate 200 mg Placebo

Intervention Type DRUG

One tablet daily for the remainder of the study

Bezafibrate 400 MG

Intervention Type DRUG

400 mg SR tablet of Bezafibrate once daily for the remainder of the study

Long-term safety extension (LTSE) phase: OCA + BZF

Participants will continue the original treatment assignment allocated during the DB Period. The OCA and BZF dose may be optimized based on safety and efficacy during the DB period.

Group Type EXPERIMENTAL

OCA

Intervention Type DRUG

OCA one tablet will be administered.

Bezafibrate

Intervention Type DRUG

Bezafibrate one tablet will be administered.

Interventions

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Obeticholic acid

5 mg tablet of OCA once daily titrating up to a maximum of 10 mg OCA once daily

Intervention Type DRUG

Bezafibrate 200 MG

200 mg IR tablet of Bezafibrate once daily for the remainder of the study

Intervention Type DRUG

OCA Placebo

One tablet daily for the remainder of the study

Intervention Type DRUG

Bezafibrate 200 mg Placebo

One tablet daily for the remainder of the study

Intervention Type DRUG

Bezafibrate 400 MG

400 mg SR tablet of Bezafibrate once daily for the remainder of the study

Intervention Type DRUG

Bezafibrate 400 mg Placebo

One tablet daily for the remainder of the study

Intervention Type DRUG

OCA

OCA one tablet will be administered.

Intervention Type DRUG

Bezafibrate

Bezafibrate one tablet will be administered.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* A definite or probable diagnosis of PBC
* Qualifying ALP and/or bilirubin liver biochemistry values
* Taking Ursodeoxycholic Acid (UDCA) for at least 12 months or no UDCA for 3 months before Day 1

Exclusion Criteria

* History or presence of other concomitant liver diseases
* Clinical complications of PBC
* History or presence of hepatic decompensating events
* Current or history of gallbladder disease
* If female, known pregnancy, or has a positive urine pregnancy test (confirmed by a positive serum pregnancy test), or lactating
* Treatment with commercially available OCA or other farnesoid X receptor (FXR) agonists, or participation in a previous study involving OCA within 3 months before Screening.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Intercept Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Lynda Szczech

Role: STUDY_DIRECTOR

Intercept Pharmaceuticals, Inc.

Locations

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Flinders Medical Centre

Bedford Park, Perth, Australia

Site Status

Royal Adelaide Hospital

Adelaide, , Australia

Site Status

UZ Gasthuisberg

Leuven, , Belgium

Site Status

Clinical Hospital Dubrava

Zagreb, , Croatia

Site Status

Zagreb University Hospital Center

Zagreb, , Croatia

Site Status

Hepato-Gastroenterologie HK, s.r.o.

Hradec Králové, , Czechia

Site Status

Artroscan s.r.o., Gastroenterologicka ambulance

Ostrava, , Czechia

Site Status

Research Site s.r.o.

Pilsen, , Czechia

Site Status

Tartu University Hospital

Tartu, , Estonia

Site Status

Hôpital Henri Mondor

Créteil, , France

Site Status

Centre Hospitalier Universitaire Grenoble

Grenoble, , France

Site Status

CHRU de Lille

Lille, , France

Site Status

Groupe Hospitalier Pitié Salpêtrière - Assistance publique - Hôpitaux de Paris

Paris, , France

Site Status

CHU Paris Est - Hopital Saint Antoine

Paris, , France

Site Status

Universitatsklinikum Hamburg-Eppendorf UKE

Hamburg, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Department of Medicine and Research Laboratory of Internal Medicine, University Hospital of Larissa

Larissa, , Greece

Site Status

Budai Hepatologiai Centrum (BHC)

Budapest, , Hungary

Site Status

DEOEC II. sz. Belgyógyászati Klinika

Debrecen, , Hungary

Site Status

Hadassah Ein-Karem Medical Center - Liver unit

Jerusalem, , Israel

Site Status

Tel Aviv Surasky Medical Center

Tel Aviv, , Israel

Site Status

Hospital of Lithuanian University of Health Sciences, Kauno Klinikos

Kaunas, , Lithuania

Site Status

Vlinius University

Vilnius, , Lithuania

Site Status

Academisch Medisch Centrum

Amsterdam, , Netherlands

Site Status

Universitetet i Oslo - Akershus Universitetssykehus (AHUS)

Loerenskog, , Norway

Site Status

Narodowy Instytut Onkologii, Klinika Gastroenterologii Onkologicznej

Warsaw, , Poland

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Kyungpook National University Hospital

Daegu, , South Korea

Site Status

Fundacio Clinic Per La Recerca Biomedica

Barcelona, , Spain

Site Status

Consorcio Hospital General Universitario

Valencia, , Spain

Site Status

Hull University Teaching Hospitals NHS Trust

Hull, , United Kingdom

Site Status

Institute of Cellular Medicine, Newcastle University

Newcastle upon Tyne, , United Kingdom

Site Status

John Radcliffe Hospital

Oxford, , United Kingdom

Site Status

Countries

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Australia Belgium Croatia Czechia Estonia France Germany Greece Hungary Israel Lithuania Netherlands Norway Poland South Korea Spain United Kingdom

References

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Lindor KD, Gershwin ME, Poupon R, Kaplan M, Bergasa NV, Heathcote EJ; American Association for Study of Liver Diseases. Primary biliary cirrhosis. Hepatology. 2009 Jul;50(1):291-308. doi: 10.1002/hep.22906. No abstract available.

Reference Type BACKGROUND
PMID: 19554543 (View on PubMed)

European Association for the Study of the Liver. EASL Clinical Practice Guidelines: management of cholestatic liver diseases. J Hepatol. 2009 Aug;51(2):237-67. doi: 10.1016/j.jhep.2009.04.009. Epub 2009 Jun 6. No abstract available.

Reference Type BACKGROUND
PMID: 19501929 (View on PubMed)

Other Identifiers

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747-213

Identifier Type: -

Identifier Source: org_study_id

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