Study of Seladelpar in Participants With Primary Biliary Cholangitis (PBC)

NCT ID: NCT03301506

Last Updated: 2025-12-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

500 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-12

Study Completion Date

2028-11-30

Brief Summary

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An Open Label Long-Term Study to Evaluate the Safety and Tolerability of Seladelpar in Subjects with Primary Biliary Cholangitis (PBC)

Detailed Description

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Primary:

To evaluate the long-term safety and tolerability of seladelpar

Secondary:

* To evaluate the long-term efficacy of seladelpar
* To evaluate the effect of seladelpar on patient-reported outcomes (pruritus)

Conditions

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Primary Biliary Cirrhosis

Keywords

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PBC Primary Biliary Cholangitis (PBC)

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Seladelpar 5 mg Capsules

Group Type EXPERIMENTAL

Seladelpar 5 mg Capsule

Intervention Type DRUG

Participants will be assigned to a treatment group if tolerability issues noted in the previous study.

Seladelpar 10 mg Capsule

Group Type EXPERIMENTAL

Seladelpar 10 mg Capsule

Intervention Type DRUG

Participants will be assigned to a treatment group unless there are tolerability issues.

Interventions

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Seladelpar 5 mg Capsule

Participants will be assigned to a treatment group if tolerability issues noted in the previous study.

Intervention Type DRUG

Seladelpar 10 mg Capsule

Participants will be assigned to a treatment group unless there are tolerability issues.

Intervention Type DRUG

Other Intervention Names

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MBX-8025 Livdelzi® MBX-8025 Livdelzi®

Eligibility Criteria

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Inclusion Criteria

1. Must have given written informed consent (signed and dated)
2. Participated in a PBC study with seladelpar
3. Females of reproductive potential must use at least one barrier contraceptive and a second effective birth control method during the study and for at least 90 days after the last dose. Male individuals who are sexually active with female partners of reproductive potential must use barrier contraception and their female partners must use a second effective birth control method during the study and for at least 90 days after the last dose

Exclusion Criteria

1. Treatment-related adverse event (AE) leading to study drug discontinuation in a previous PBC study with seladelpar
2. A medical condition, other than PBC, that in the Investigator's opinion would preclude full participation in the study or confound its results (eg, cancer, any active infection)
3. AST or ALT above 3 × the upper limit of normal (ULN)
4. Total bilirubin above 2 × ULN
5. MELD score ≥ 12. For individuals on anticoagulation medication, evaluation of the baseline INR, in concert with any current dose adjustments in anti-coagulant medications, will be taken into account when calculating this score. This will be done in consultation with the medical monitor.
6. Evidence of advanced PBC as defined by the Rotterdam criteria: albumin below 1× the lower limit of normal (LLN) AND total bilirubin above 1 × ULN)
7. eGFR ≤45 mL/min/1.73 m2 (calculated by MDRD formula)
8. Auto-immune hepatitis
9. Primary sclerosing cholangitis
10. Known history of alpha-1-antitrypsin deficiency
11. Known history of chronic viral hepatitis
12. For females, pregnancy or breast-feeding
13. Use of colchicine, methotrexate, azathioprine, or long-term use of systemic steroids (eg prednisone, prednisolone, budesonide) (\>2 weeks) within 2 months prior to Screening
14. Current use of fibrates or use of fibrates within 3 months prior to Screening
15. Current use of obeticholic acid or use of obeticholic acid within 3 months prior to Screening
16. Use of an experimental or unapproved treatment for PBC within 3 months prior to Screening
17. History of malignancy diagnosed or treated, actively or within 2 years, or active evaluation for malignancy; localized treatment of squamous or non-invasive basal cell skin cancers and cervical carcinoma in-situ is allowed if appropriately treated prior to Screening
18. Treatment with any other investigational therapy or medical device within 30 days or within 5 half-lives, whatever is longer, prior to Screening
19. Any other condition(s) that would compromise the safety of the individual or compromise the quality of the clinical study, as judged by the Investigator
20. Immunosuppressant therapies (eg, cyclosporine, tacrolimus, anti-TNF or other immunosuppressive biologics)
21. Other medications that effect liver or GI functions such as absorption of medications or the roux-en-y gastric bypass procedure may be prohibited and should be discussed with the medical monitor on a case-by-case basis
22. Positive for:

1. Hepatitis B, defined as the presence of hepatitis B surface antigen
2. Hepatitis C, defined as the presence of hepatitis C virus ribonucleic acid (RNA)
3. Human immunodeficiency virus (HIV) antibody
23. Active COVID-19 infection during screening
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Arkansas Diagnostic Center

Little Rock, Arkansas, United States

Site Status

Stanford University School of Medicine

Palo Alto, California, United States

Site Status

California Liver Research Institute

Pasadena, California, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

Site Status

California Pacific Medical Center

San Francisco, California, United States

Site Status

University of Colorado - Denver - PPDS

Aurora, Colorado, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Covenant Research Fort Myers

Fort Myers, Florida, United States

Site Status

Florida Digestive Health Specialist

Lakewood Rch, Florida, United States

Site Status

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status

Covenant Research, LLC

Sarasota, Florida, United States

Site Status

Digestive Healthcare of Georgia PC

Atlanta, Georgia, United States

Site Status

University of Chicago Hospitals

Chicago, Illinois, United States

Site Status

East Jefferson General Hospital

New Orleans, Louisiana, United States

Site Status

Mercy Medical Center (Baltimore)

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center - 330 Brookline Ave

Boston, Massachusetts, United States

Site Status

Henry Ford Health System

Novi, Michigan, United States

Site Status

MNGI Digestive Health PA-Plymouth

Minneapolis, Minnesota, United States

Site Status

Southern Therapy and Advanced Research LLC

Jackson, Mississippi, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

NYU Langone Medical Center

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

University of Rochester Medical Center - PPDS

Rochester, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Northeast Clinical Research Center, LLC

Bethlehem, Pennsylvania, United States

Site Status

Penn State Health Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Galen Medical Group

Chattanooga, Tennessee, United States

Site Status

Gastro One-8110 Walnut Run Rd

Cordova, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Liver Institute at Methodist Dallas

Dallas, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

The Texas Liver Institute - 607 Camden St

San Antonio, Texas, United States

Site Status

Pinnacle Clinical Research, PLLC

San Antonio, Texas, United States

Site Status

Maryview Hospital Inc., d/b/a Bon Secours Liver Institute of Hampton Roads

Newport News, Virginia, United States

Site Status

Bon Secours Richmond Community Hospital, Inc. d/b/a Bon Secours Liver Institute of Richmond

Richmond, Virginia, United States

Site Status

Liver Institute Northwest, PLLC

Seattle, Washington, United States

Site Status

CINME S.A. - Centro de Investigaciones Metabólicas-Viamonte 2278

Balvanera, , Argentina

Site Status

Hospital Italiano de Buenos Aires

Buenos Aires, , Argentina

Site Status

DIM Clínica Privada

El Palomar, , Argentina

Site Status

Hospital Italiano de La Plata

La Plata, , Argentina

Site Status

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

Klinikum Wels-Grieskirchen GmbH - Standort Wels

Wels, , Austria

Site Status

UZ Gent

Ghent, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

University of Calgary Medicine

Calgary, , Canada

Site Status

Toronto General Hospital

Toronto, , Canada

Site Status

Centro Clinico Mediterraneo

La Serena, , Chile

Site Status

Fakultni nemocnice Ostrava

Ostrava, , Czechia

Site Status

Hospices Civils de Lyon - Hôpital de La Croix Rousse

Lyon, , France

Site Status

AP-HP - Hôpital Saint Antoine

Paris, , France

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitatsklinkum Erlangen-Ulmenweg 18

Erlangen, , Germany

Site Status

ifi-Institute for Interdisciplinary Medicine

Hamburg, , Germany

Site Status

Gastroenterologische Gemeinschaftspraxis Herne

Herne, , Germany

Site Status

Gastroenterologisch Hepatologisches Zentrum Kiel - Preetzer Chaussee 134

Kiel, , Germany

Site Status

Universitätsklinikum Tübingen

Tübingen, , Germany

Site Status

University General Hospital of Larissa

Larissa, , Greece

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Somogy Varmegyei Kaposi Mor Oktato Korhaz

Kaposvár, , Hungary

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Hadassah Medical Center- Ein Kerem - PPDS

Jerusalem, , Israel

Site Status

The Chaim Sheba Medical Center - PPDS

Tel Aviv, , Israel

Site Status

Tel Aviv Sourasky Medical Center Ichilov - PPDS

Tel Aviv, , Israel

Site Status

Azienda Ospedaliero-Universitaria di Modena - Ospedale Civile di Baggiovara

Modena, , Italy

Site Status

Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone-Palermo-Piazza Delle Cliniche 2

Palermo, , Italy

Site Status

Fondazione IRCCS San Gerardo dei Tintori

Rozzano, , Italy

Site Status

Consultorio de la Doctora Maria Sarai Gonzalez Huezo

Metepec, , Mexico

Site Status

Consultorio Medico - Distrito Federal

Roma Norte, , Mexico

Site Status

Radboud Universitair Medisch Centrum

Nijmegen, , Netherlands

Site Status

Christchurch Hospital

Christchurch, , New Zealand

Site Status

Dunedin Hospital

Dunedin, , New Zealand

Site Status

Uniwersyteckie Centrum Kliniczne Im. Prof. K. Gibinskiego Slaskiego Uniwersytetu Medycznego w Katowi

Katowice, , Poland

Site Status

ID Clinic Arkadiusz Pisula

Mysłowice, , Poland

Site Status

Fundeni Clinical Institute

Bucharest, , Romania

Site Status

Soon Chun Hyang University Hospital Bucheon

Bucheon-si, , South Korea

Site Status

Inje University Busan Paik Hospital

Busan, , South Korea

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Kyungpook National University Hospital

Daegu, , South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Songpa-Gu, , South Korea

Site Status

Hospital Universitario Germans Trias i Pujol

Badalona, , Spain

Site Status

Hospital Universitario Vall d'Hebron - PPDS

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario La Paz - PPDS

Horcajo de la Sierra, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario Virgen de la Victoria

Málaga, , Spain

Site Status

Hospital Universitario Marques de Valdecilla

Santander, , Spain

Site Status

Universitätsspital Zürich

Zurich, , Switzerland

Site Status

Gazi University Faculty of Medicine

Ankara, , Turkey (Türkiye)

Site Status

Ege Universitesi Tip Fakultesi Hastanesi

Bornova, , Turkey (Türkiye)

Site Status

Ankara Bilkent City Hospital

Çankaya, , Turkey (Türkiye)

Site Status

Marmara University Pendik Training and Research Hospital

Maltepe, , Turkey (Türkiye)

Site Status

Bezmialem Vakif Universitesi Tip Fakultesi Hastanesi

Topkapı, , Turkey (Türkiye)

Site Status

Queen Elizabeth Hospital Birmingham

Birmingham, , United Kingdom

Site Status

Hull Royal Infirmary

Hull, , United Kingdom

Site Status

Barts Health NHS Trust, Royal London Hospital, Ambrose King Centre

London, , United Kingdom

Site Status

King's College Hospital

London, , United Kingdom

Site Status

The Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, , United Kingdom

Site Status

Queen's Medical Centre

Nottingham, , United Kingdom

Site Status

Derriford Hospital

Plymouth, , United Kingdom

Site Status

Queen Alexandra Hospital

Portsmouth, , United Kingdom

Site Status

Countries

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Russia United States Argentina Australia Austria Belgium Canada Chile Czechia France Germany Greece Hungary Israel Italy Mexico Netherlands New Zealand Poland Romania South Korea Spain Switzerland Turkey (Türkiye) United Kingdom

References

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Levy C, Trivedi PJ, Kowdley KV, Gordon SC, Bowlus CL, Londono MC, Hirschfield GM, Gulamhusein A, Lawitz EJ, Vierling JM, Mayo MJ, Jacobson IM, Kremer AE, Corpechot C, Jones D, Buggisch P, Zhuo S, Proehl S, Heusner C, McWherter CA, Crittenden DB; ASSURE Investigators. Long-Term Efficacy and Safety of Selective PPARdelta Agonist Seladelpar in Primary Biliary Cholangitis: ASSURE Interim Study Results. Am J Gastroenterol. 2025 Jun 24. doi: 10.14309/ajg.0000000000003603. Online ahead of print.

Reference Type DERIVED
PMID: 40553148 (View on PubMed)

Mayo MJ, Vierling JM, Bowlus CL, Levy C, Hirschfield GM, Neff GW, Galambos MR, Gordon SC, Borg BB, Harrison SA, Thuluvath PJ, Goel A, Shiffman ML, Swain MG, Jones DEJ, Trivedi P, Kremer AE, Aspinall RJ, Sheridan DA, Dorffel Y, Yang K, Choi YJ, McWherter CA. Open-label, clinical trial extension: Two-year safety and efficacy results of seladelpar in patients with primary biliary cholangitis. Aliment Pharmacol Ther. 2024 Jan;59(2):186-200. doi: 10.1111/apt.17755. Epub 2023 Oct 30.

Reference Type DERIVED
PMID: 37904314 (View on PubMed)

Related Links

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Other Identifiers

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2020-005198-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2024-511753-22-00

Identifier Type: CTIS

Identifier Source: secondary_id

CB8025-31731-RE

Identifier Type: -

Identifier Source: org_study_id