Pharmacogenetics of Liver Toxicity in Patients With Multiple Sclerosis Treated With Fingolimod

NCT ID: NCT05516303

Last Updated: 2022-08-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Total Enrollment

65 participants

Study Classification

OBSERVATIONAL

Study Start Date

2022-06-07

Study Completion Date

2022-10-31

Brief Summary

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To investigate whether polymorphic differences can be identified between Multiple Sclerosis patients developing elevated liver enzymes (defined as ALT, AST, GGT or bilirubinemia levels five above the upper normal limit on at least one) compared to those not developing elevated liver enzymes after exposure to fingolimod for multiple sclerosis.

Detailed Description

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PURPOSE: To investigate whether polymorphic differences can be identified between Multiple sclerosis (MS) patients treated by fingolimod who had liver enzymes elevation compared to those who do not.

OBJECTIVE: To determine whether elevated liver enzyme tests (ALT, AST, GGT or bilirubinemia above the upper limit of normal) in MS patients treated with fingolimod is associated with genetic polymorphisms.

METHOD OF RECRUITMENT:

Patients will be identified through a clinic database and chart reviews. A phone call will be made to determine interest. Upon a follow-up neurological consultation, consent into study will be sought.

PROCEDURES:

Blood samples will be collected for genetic analyses, fingolimod and fingolimod-phosphate quantification and a questionnaire will be administered

Conditions

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Multiple Sclerosis

Study Design

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Observational Model Type

CASE_CONTROL

Study Time Perspective

RETROSPECTIVE

Study Groups

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Case

MS patients treated with fingolimod who experienced liver enzymes elevation

Genetic polymorphism

Intervention Type GENETIC

One blood tube will be taken for genetic testing

Measurement of fingolimod and fingolimod-phosphate concentrations

Intervention Type DIAGNOSTIC_TEST

Measurement of fingolimod and fingolimod-phosphate concentrations before usual drug administration time

Control

MS patients treated with fingolimod not experiencing elevated liver enzymes

Genetic polymorphism

Intervention Type GENETIC

One blood tube will be taken for genetic testing

Measurement of fingolimod and fingolimod-phosphate concentrations

Intervention Type DIAGNOSTIC_TEST

Measurement of fingolimod and fingolimod-phosphate concentrations before usual drug administration time

Interventions

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Genetic polymorphism

One blood tube will be taken for genetic testing

Intervention Type GENETIC

Measurement of fingolimod and fingolimod-phosphate concentrations

Measurement of fingolimod and fingolimod-phosphate concentrations before usual drug administration time

Intervention Type DIAGNOSTIC_TEST

Eligibility Criteria

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Inclusion Criteria

* Adults (\> 18 years)
* Have a definite Multiple Sclerosis with a relapsing-remitting course (McDonald criteria)
* Treated with fingolimod
* Have given consent and signed an informed consent form

Exclusion Criteria

* an elevated liver test result on baseline before starting fingolimod treatment
* presence of a viral, hereditary or auto-immune liver pathology
* Time of fingolimod exposure lower than three months
* Woman currently pregnant or breastfeeding
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University Hospital, Caen

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilles Defer, MD

Role: PRINCIPAL_INVESTIGATOR

University Hospital, Caen

Locations

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Caen University Hospital

Caen, , France

Site Status RECRUITING

Countries

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France

Central Contacts

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Sophie Nguyen, MSc

Role: CONTACT

+33(0)231065127

Facility Contacts

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Sophie Nguyen, Msc

Role: primary

Other Identifiers

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22-0041

Identifier Type: -

Identifier Source: org_study_id

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