A Study of EP0031 in Patients With Advanced RET-altered Malignancies

NCT ID: NCT05443126

Last Updated: 2026-02-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

265 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-09-30

Study Completion Date

2027-06-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The aim of this study is to assess the safety, side effects and effectiveness of EP0031 in patients with advanced RET-altered malignancies (NSCLC)

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

EP0031 is being investigated in this modular, interventional Phase I/II dose escalation and dose expansion study to investigate the optimal dose in adult patients with advanced RET-altered malignancies. Currently there are no approved RET-targeted treatments for patients who progress on first-generation SRIs. However, it is proposed that EP0031 can overcome resistance mechanisms to first generation SRIs, as EP0031 is a potent and selective RET inhibitor with broad activity against common RET fusions and mutations. Phase I (dose escalation and optimization) has completed and a RP2D has been selected for Phase II.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Advanced Solid Tumor NSCLC

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

RET fusion-positive NSCLC (prior 1st gen SRI)

EP0031 capsules at the recommended phII dose, taken once daily until progressive disease (PD), unacceptable toxicity or patient withdrawal

Group Type EXPERIMENTAL

EP0031

Intervention Type DRUG

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

RET mutation-positive MTC (prior 1st gen SRI)

EP0031 capsules at the recommended phII dose, taken once daily until progressive disease (PD), unacceptable toxicity or patient withdrawal

Group Type EXPERIMENTAL

EP0031

Intervention Type DRUG

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

Other RET-altered solid tumours (prior 1st gen SRI)

EP0031 capsules at the recommended phII dose, taken once daily until progressive disease (PD), unacceptable toxicity or patient withdrawal

Group Type EXPERIMENTAL

EP0031

Intervention Type DRUG

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

RET fusion-positive NSCLC (no prior SRI therapy)

EP0031 capsules at the recommended phII dose, taken once daily until progressive disease (PD), unacceptable toxicity or patient withdrawal

Group Type EXPERIMENTAL

EP0031

Intervention Type DRUG

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

RET mutation-positive MTC (no prior SRI therapy)

EP0031 capsules at the recommended phII dose, taken once daily until progressive disease (PD), unacceptable toxicity or patient withdrawal

Group Type EXPERIMENTAL

EP0031

Intervention Type DRUG

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

Other RET-altered solid tumours (no prior SRI therapy)

EP0031 capsules at the recommended phII dose, taken once daily until progressive disease (PD), unacceptable toxicity or patient withdrawal

Group Type EXPERIMENTAL

EP0031

Intervention Type DRUG

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

EP0031

EP0031 is a potent next-generation selective RET-inhibitor (SRI)

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

Applicable to all patients:

1. Must be ≥18 years of age, with documented RET-altered cancers
2. Patients should be well informed and consented about alternative treatment options including approved RET-targeted therapies
3. ECOG performance status of 0 or 1 and life expectancy \>3 months at screening
4. Ability to understand and provide written informed consent and able to participate in all required evaluations and procedures
5. Additional cohort specific criteria apply

Exclusion Criteria

Patients with any of the following will not be included in the study:

1. Any known major driver gene alterations other than RET.
2. Spinal cord compression or brain metastases. Patients with stable brain metastases can be enrolled.
3. Active infection requiring systemic antibiotic, antifungal, or antiviral medication
4. Severe or uncontrolled medical condition or psychiatric condition
5. Chronic glomerulonephritis or renal transplant
6. Patients with active hepatitis B infection or active hepatitis C
7. Patients with active HIV infection. Patients living with HIV may be eligible if they have adequate CD4+ T-cell count and no history of AIDS-defining opportunistic infections in the past 12 months
8. Receipt of any strong inhibitor or inducer of CYP3A4
9. Impaired hepatic or renal function, inadequate bone marrow reserve or organ function
10. Any clinically important abnormalities in rhythm, conduction, or morphology on resting ECG or any factor that increases the risk of QTc prolongation or of arrhythmic events , or congestive heart failure Grade II-IV according to the New York Heart Association, myocardial infarction, or unstable angina within the previous 6 months
11. Uncontrolled hypertension
12. Corneal ulceration at screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Ellipses Pharma

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status RECRUITING

Stanford University

Stanford, California, United States

Site Status RECRUITING

Georgetown University

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Florida Cancer Specialist

Fort Myers, Florida, United States

Site Status RECRUITING

RUSH University Medical Center

Chicago, Illinois, United States

Site Status TERMINATED

Northwestern University

Evanston, Illinois, United States

Site Status RECRUITING

University of Kentucky

Lexington, Kentucky, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Karmanos

Detroit, Michigan, United States

Site Status TERMINATED

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

NYU Langone Health

New York, New York, United States

Site Status RECRUITING

Providence Portland Medical Centre

Portland, Oregon, United States

Site Status RECRUITING

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Sarah Cannon

Nashville, Tennessee, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status RECRUITING

Washington University

Seattle, Washington, United States

Site Status RECRUITING

Seattle Cancer Care / Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status RECRUITING

Assistance publique - Hôpitaux de Marseille

Marseille, Bouches-du-Rhône, France

Site Status RECRUITING

Center Bergonié

Bordeaux, Gironde, France

Site Status RECRUITING

Institut Gustave-Roussy

Villejuif, Paris, France

Site Status RECRUITING

Centre François Baclesse

Caen, , France

Site Status RECRUITING

Centre Léon Bérard

Lyon, , France

Site Status RECRUITING

Charité Comprehensive Cancer Center

Berlin, , Germany

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

Site Status RECRUITING

Hospital Universitario de A Coruña

A Coruña, , Spain

Site Status RECRUITING

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Insular de Gran Canaria

Las Palmas de Gran Canaria, , Spain

Site Status RECRUITING

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status RECRUITING

University Hospital October 12

Madrid, , Spain

Site Status RECRUITING

Hospital Madrid Sanchinarro

Madrid, , Spain

Site Status RECRUITING

Hospital Virgen de la Victoria de Malaga

Málaga, , Spain

Site Status RECRUITING

Tawam Hospital

Al Ain City, Abu Dhabi Emirate, United Arab Emirates

Site Status RECRUITING

Sheik Shakhbout Medical City (SSMC)

Abu Dhabi, , United Arab Emirates

Site Status RECRUITING

Cleveland Clinic Abu Dhabi (CCAD)

Abu Dhabi, , United Arab Emirates

Site Status RECRUITING

University College London Hospital

London, , United Kingdom

Site Status RECRUITING

Guy's Hospital

London, , United Kingdom

Site Status RECRUITING

The Royal Marsden NHS Foundation Trust

London, , United Kingdom

Site Status RECRUITING

The Christie NHS Foundation Trust - Christie Hospital

Manchester, , United Kingdom

Site Status RECRUITING

Sheffield Teaching Hospitals NHS Foundation Trust

Sheffield, , United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States France Germany Italy Spain United Arab Emirates United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Clinical Trials Team

Role: CONTACT

+44 20 3743 0992

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Andrew Gianoukakis, MD

Role: primary

Emmanuel Ugwu

Role: primary

Stephen Liu, MD

Role: primary

Judy Wang, MD

Role: primary

Jyoti Patel

Role: primary

Susanne Arnold

Role: primary

Lori Wirth, MD

Role: primary

Alex Drilon, MD

Role: primary

Salman Punekar, MD

Role: primary

Matthew H Taylor, MD

Role: primary

Marcia Brose, M.D

Role: primary

Nurse Navigator Hotline

Role: primary

(844) 482-4812

Yasir Elamin, MD

Role: primary

Alexander Spira, MD

Role: primary

Daniel Morgensztern, MD

Role: primary

Rebecca Wood

Role: primary

206-606-6970

Pascale Tomasini, Dr

Role: primary

Role: backup

Antoine Italiano, Dr

Role: primary

Role: backup

Benjamin Besse, Prof

Role: primary

Role: primary

Role: primary

Elena Garralda

Role: primary

Pilar Garrido Lopez

Role: primary

Irene Moreno

Role: primary

Selvaraj Giridharan, Dr

Role: primary

Hassan Shahryar Sheik, Dr

Role: primary

Christos Leftheriotis

Role: primary

Martin Forster

Role: primary

Debashi Starker

Role: primary

Sanjay Popat, Dr.

Role: primary

Matthew Krebs

Role: primary

Jonathan Wadsley

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

EP0031-101

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Study of AS1411 in Advanced Solid Tumours
NCT00881244 COMPLETED PHASE1