Extracellular Vesicle Treatment for Acute Respiratory Distress Syndrome (ARDS) (EXTINGUISH ARDS)

NCT ID: NCT05354141

Last Updated: 2024-11-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

970 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-01

Study Completion Date

2025-08-31

Brief Summary

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To evaluate the safety and efficacy of intravenous (IV) administration of bone marrow mesenchymal stem cell derived extracellular vesicles (EVs), ExoFlo, versus placebo for the treatment of hospitalized patients with moderate-to-severe Acute Respiratory Distress Syndrome (ARDS).

Detailed Description

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This is a Phase III, multicenter, randomized, double-blinded, placebo-controlled trial for the treatment of moderate-to-severe Acute Respiratory Distress Syndrome (ARDS).

Conditions

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Acute Respiratory Distress Syndrome ARDS

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Multicenter, randomized, double-blinded, placebo-controlled trial
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
Double-Blinded

Study Groups

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Placebo

Normal saline 100 mL

Group Type PLACEBO_COMPARATOR

Intravenous normal saline

Intervention Type OTHER

Placebo

Experimental Dose

Normal saline 85 mL and ExoFlo 15 mL

Group Type EXPERIMENTAL

ExoFlo

Intervention Type BIOLOGICAL

Intravenous administration of bone marrow mesenchymal stem cell derived extracellular vesicles

Interventions

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ExoFlo

Intravenous administration of bone marrow mesenchymal stem cell derived extracellular vesicles

Intervention Type BIOLOGICAL

Intravenous normal saline

Placebo

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. Men and women aged 18-75 years of age
2. Presence of the following criteria for moderate to severe ARDS as defined by the Berlin Criteria within 24 hours of the first infustion:

1. Onset within 7 days of known clinical insult or requiring increasing respiratory rate, increasing oxygen flows, or increased work of breathing, and
2. Bilateral lung opacities not fully explained by pleural effusions, atelectasis, or nodules, and
3. PaO2/FiO2 (P/F ratio) ≤ 200 mm Hg, and
4. Invasive or noninvasive ventilation with a minimum PEEP 5 cm H2O or minimum of continuous positive airway pressure (CPAP) 5 cm H2O, or High Flow Nasal Oxygen at ≥ 30 L/min, and
5. Respiratory failure not fully explained by cardiac failure or fluid overload.

Exclusion Criteria

1. Lack of signed and dated informed consent form (either by the individual or by the individual's healthcare proxy).
2. Stated unwillingness to comply with all study procedures and availability for the duration of the study
3. Vulnerable populations such as pregnant patients, children, individuals with severe physical or mental disabilities who cannot provide meaningful consent.
4. Active malignancy requiring treatment within the last two years, with the exception of non-melanoma skin cancers.
5. Major physical trauma in the last 2 days, including motor vehicle accidents, assaults, mechanical falls with sequelae of significant bleeding or craniofacial bruising, and surgeries, such that not one or more injury may be undiagnosed at time of screening.
6. Duration of mechanical ventilation exceeds 3 days or 72 hours from diagnosis of ARDS.
7. ALT or AST \> 8 x Upper Limit of Normal (ULN).
8. Documented history of cirrhosis.
9. DNR order, as in electing not to receive chest compressions, cardiac defibrillation, cardiac drugs, or intubation.
10. Moribund-expected survival \< 24 hours.
11. Severe metabolic disturbances at randomization (e.g., ketoacidosis, pH \< 7.2)
12. Patient currently connected to Extracorporeal Membrane Oxygenation at initiation of screening.
13. If the candidate, either a male or female of reproductive potential, is unwilling to two methods of highly effective birth control contraception such as condoms with oral contraceptive pill or choose to remain abstinent if already practicing abstinence during the screening period. The required duration of usage of double method OR maintenance of abstinence must include the time from the beginning of the screening period until Day 61, day of withdrawal or early termination
14. Use of investigational COVID-19 agents or any other investigational agents within 30 days prior to the first dose.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Direct Biologics, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bill Arana

Role: STUDY_DIRECTOR

Direct Biologics, LLC

Locations

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Direct Biologics Investigational Site

Birmingham, Alabama, United States

Site Status RECRUITING

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Chandler, Arizona, United States

Site Status RECRUITING

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Phoenix, Arizona, United States

Site Status RECRUITING

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Little Rock, Arkansas, United States

Site Status RECRUITING

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Davis, California, United States

Site Status RECRUITING

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Fullerton, California, United States

Site Status RECRUITING

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Irvine, California, United States

Site Status RECRUITING

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Orange, California, United States

Site Status RECRUITING

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Sacramento, California, United States

Site Status RECRUITING

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San Francisco, California, United States

Site Status RECRUITING

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Washington D.C., District of Columbia, United States

Site Status RECRUITING

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Jacksonville, Florida, United States

Site Status RECRUITING

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Boise, Idaho, United States

Site Status RECRUITING

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Iowa City, Iowa, United States

Site Status RECRUITING

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Wichita, Kansas, United States

Site Status RECRUITING

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Silver Spring, Maryland, United States

Site Status RECRUITING

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Boston, Massachusetts, United States

Site Status RECRUITING

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Burlington, Massachusetts, United States

Site Status RECRUITING

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Springfield, Massachusetts, United States

Site Status RECRUITING

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Ann Arbor, Michigan, United States

Site Status RECRUITING

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Detroit, Michigan, United States

Site Status RECRUITING

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Jackson, Mississippi, United States

Site Status RECRUITING

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Flushing, New York, United States

Site Status RECRUITING

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Queens, New York, United States

Site Status RECRUITING

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The Bronx, New York, United States

Site Status RECRUITING

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Durham, North Carolina, United States

Site Status RECRUITING

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Winston-Salem, North Carolina, United States

Site Status RECRUITING

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Cincinnati, Ohio, United States

Site Status RECRUITING

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Cleveland, Ohio, United States

Site Status RECRUITING

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Portland, Oregon, United States

Site Status RECRUITING

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Charleston, South Carolina, United States

Site Status RECRUITING

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Knoxville, Tennessee, United States

Site Status RECRUITING

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Nashville, Tennessee, United States

Site Status RECRUITING

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Dallas, Texas, United States

Site Status RECRUITING

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Fort Worth, Texas, United States

Site Status RECRUITING

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Houston, Texas, United States

Site Status RECRUITING

Direct Biologics Investigational Site

Murray, Utah, United States

Site Status RECRUITING

Direct Biologics Investigational Site

Salt Lake City, Utah, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Bill Arana

Role: CONTACT

1-800-791-1021

Related Links

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https://directbiologics.com/

Direct Biologics, LLC

Other Identifiers

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DB-EF-PHASEIII-0001

Identifier Type: -

Identifier Source: org_study_id

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