Umbilical Cord Lining Stem Cells (ULSC) in Patients With COVID-19 ARDS

NCT ID: NCT04494386

Last Updated: 2024-04-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

17 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-23

Study Completion Date

2023-05-12

Brief Summary

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ULSC-CV-01 is a clinical trial that comprises both Phase 1 and Phase 2a, which will be conducted sequentially. This trial will evaluate the safety and potential efficacy of allogeneic Umbilical Cord Lining Stem Cells (ULSC), which are a type of umbilical cord tissue derived mesenchymal stem cells (MSC), with intravenous (IV) administration in hospitalized patients with acute respiratory distress syndrome (ARDS) due to COVID-19.

Detailed Description

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The Phase 1, open-label, non-controlled trial in this study will investigate the safety of intravenous (IV) infusion of ULSC in a total of 20 patients with COVID-19-related ARDS that will include patients that are not intubated and not on a ventilator (NV) and patients that are intubated and on a ventilator (V) for respiratory support. Separate cohorts of each group (NV and V) will receive either a single dose (one infusion) or repeat dose (two infusions separated by 48-hour interval).

The Phase 2a randomized and placebo-controlled trial in this study will investigate the potential efficacy of IV infusion of ULSC in a total of 40 patients with COVID-19-related ARDS that will all be EITHER NV or V; the determination of that eligibility criterion and the ULSC dosing regimen will be based on Phase 1 data of safety and tolerability. Phase 2a will evaluate EITHER single dose (one infusion) or repeat dose (two infusions separated by 48-hour interval). The randomization will be 3:1 with 30 patients receiving investigational product (ULSC) and 10 patients receiving placebo (carrier control).

Conditions

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Covid19 Corona Virus Infection SARS-CoV Infection ARDS Coronavirus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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ULSC in Phase 1 Open Label

Intravenous (IV) infusion of ULSC in 20 patients with COVID-19 ARDS:

In Phase 1, two separate cohorts per group will receive either a single dose (one infusion) or repeat dose regimen (two infusions separated by 48-hour interval). The first cohort enrolled will receive the single dose; the next cohort enrolled will be administered the repeat dose regimen.

Group Type EXPERIMENTAL

Umbilical Cord Lining Stem Cells (ULSC)

Intervention Type BIOLOGICAL

IV infusion of allogeneic ULSC (100 million cells per dose) in sterile saline for injection

ULSC in Phase 2a Randomized

Intravenous (IV) infusion of ULSC in 30 patients with COVID-19 ARDS:

In Phase 2a, 30 patients assigned ULSC will receive either a single dose (one infusion) or repeat dose regimen (two infusions separated by 48-hour interval). The ULSC dosing regimen will be chosen based on Phase 1 data of safety and tolerability.

Group Type EXPERIMENTAL

Umbilical Cord Lining Stem Cells (ULSC)

Intervention Type BIOLOGICAL

IV infusion of allogeneic ULSC (100 million cells per dose) in sterile saline for injection

Placebo in Phase 2a Randomized

Intravenous (IV) infusion of carrier control in 10 patients with COVID-19 ARDS:

In Phase 2a, 10 patients assigned Placebo will receive either single dose (one infusion) or repeat dose (two infusions separated by 48-hour interval) of carrier control; the dosing regimen will correspond to that of the experimental arm.

Group Type PLACEBO_COMPARATOR

Placebo (carrier control)

Intervention Type OTHER

IV infusion of carrier control consisting of sterile saline for injection

Interventions

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Umbilical Cord Lining Stem Cells (ULSC)

IV infusion of allogeneic ULSC (100 million cells per dose) in sterile saline for injection

Intervention Type BIOLOGICAL

Placebo (carrier control)

IV infusion of carrier control consisting of sterile saline for injection

Intervention Type OTHER

Other Intervention Names

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Umbilical Cord Lining Stem Cells (ULSC), type of mesenchymal stem cells (MSC) derived from single donor umbilical cord tissue for allogeneic use

Eligibility Criteria

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Inclusion Criteria

1. Adult, male or female, age ≥18 years old
2. Diagnosis of the presence of the COVID-19 agent with confirmation of COVID-19 by standard reverse transcriptase polymerase chain reaction (RT-PCR) or equivalent test.
3. Patient with diagnosis of COVID-related ARDS, classified as either:

* Not requiring mechanical ventilation (NV) or
* Requiring mechanical ventilation (V).

According to Berlin Definition of Acute Respiratory Distress Syndrome (ARDS), patients will be categorized based on degrees of hypoxemia \[arterial partial pressure of oxygen (PaO2)/oxygen concentration (FiO2)\]:
* Mild ARDS: 200 mm Hg \< PaO2/FIO2 ≤ 300 mm Hg
* Moderate ARDS: 100 mm Hg \< PaO2/FIO2 ≤ 200 mm Hg
* Severe ARDS: PaO2/FIO2 ≤ 100 mm Hg
4. Patient who has exhibited deterioration in condition during the past 72 hours prior to the informed consent.
5. Patient receiving standard of care in-hospital therapy, including appropriate critical oxygenation, fluid, and hemodynamic support as indicated clinically.
6. Patient or responsible family member or surrogate signs informed consent.

Exclusion Criteria

1. Hypersensitivity to study product components. History of hypersensitivity to dimethyl sulfoxide (DMSO).
2. Active cancer or prior diagnosis of cancer within the past year; however, patients with basal and squamous cell cancer of skin will not be excluded.
3. Organ transplant recipient.
4. Chronic renal failure being treated by renal replacement therapy (dialysis) before development of COVID-19.
5. Any other condition that, in the judgment of the Investigator or Sponsor, would be a contraindication to enrollment, study product administration, or follow-up.
6. Pregnancy or lactation; a negative pregnancy test between screening and day 1 (before administration of treatment) will be required of women with childbearing potential, and they will be advised of the requirement to use an effective means of contraception. A woman is considered to be of childbearing potential unless she is postmenopausal and without menses for 12 months or without a uterus and/or both ovaries.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Restem, LLC.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Miami Baptist Hospital

Miami, Florida, United States

Site Status

Sanford Research

Sioux Falls, South Dakota, United States

Site Status

Countries

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United States

Other Identifiers

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ULSC-CV-01

Identifier Type: -

Identifier Source: org_study_id

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