A Study to Evaluate the Safety and Tolerability, Pharmacokinetics, and Antiviral Activity of Maribavir for the Treatment of Cytomegalovirus (CMV) Infection in Children and Adolescents Who Have Received a Hematopoietic Stem Cell Transplant (HSCT) or a Solid Organ Transplant (SOT)

NCT ID: NCT05319353

Last Updated: 2025-07-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

80 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-11-13

Study Completion Date

2027-01-18

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The main aim of this study is to find out the safety, tolerability and pharmacokinetics (PK) of maribavir for the treatment of CMV infection in children and teenagers after HSCT or SOT and to identify the optimal dose of maribavir using a 200 milligrams (mg) tablet formulation or powder for oral suspension.

The participants will be treated with maribavir for 8 weeks.

Participants need to visit their doctor during 12-week follow-up period.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Cytomegalovirus (CMV)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Three dosing cohorts based on participant's age.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Cohort 1: Maribavir 400, 200 or 100 mg

Participants with greater than or equal to (\>=) 12 to less than (\<) 18 years of age will receive maribavir 400 milligrams (mg) (2\*200 mg tablets or powder for oral suspension) twice daily (BID) based on body weight \>= 25 kilogram (kg); or 200 mg tablet or powder for oral suspension BID based on body weight 14 to \< 25 kg; or 100 mg powder for oral suspension BID based on body weight 10 to \< 14 kg for up to 8 weeks treatment period (Day 1/Week 0 to Day 56/Week 8).

Group Type EXPERIMENTAL

Maribavir

Intervention Type DRUG

Participants will receive maribavir.

Cohort 2: Maribavir 400, 200 or 100 mg

Participants with \>= 6 to \< 12 years of age will receive maribavir 400 mg (2\*200 mg tablets or powder for oral suspension) BID based on body weight \>= 25 kg; or 200 mg tablet or powder for oral suspension BID based on body weight 14 to \< 25 kg; or 100 mg powder for oral suspension BID based on body weight 10 to \< 14 kg orally for up to 8 weeks treatment period (Day 1/Week 0 to Day 56/Week 8).

Group Type EXPERIMENTAL

Maribavir

Intervention Type DRUG

Participants will receive maribavir.

Cohort 3: Maribavir 400, 200, 100 or 50 mg

Participants with 0 to \< 6 years of age will receive maribavir 400 mg (2\*200 mg tablets or powder for oral suspension) BID based on body weight \>= 25 kg; or 200 mg tablet or powder for oral suspension BID based on body weight 14 to \< 25 kg; or 100 mg powder for oral suspension BID based on body weight 10 to \< 14 kg; or 50 mg powder for oral suspension BID based on body weight 7 to \< 10 kg; or 50 mg powder for oral suspension once daily (QD) based on body weight 5 to \<7 kg for up to 8 weeks treatment period (Day 1/Week 0 to Day 56/Week 8).

Group Type EXPERIMENTAL

Maribavir

Intervention Type DRUG

Participants will receive maribavir.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Maribavir

Participants will receive maribavir.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

TAK-620

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Parent/both parents or legally authorized representative (LAR) must provide signature of informed consent and there must be documentation of assent by the participant, as age appropriate, before completing any study-related procedures.
* Be a male or female child or adolescent \< 18 years of age at the time of consent. For participants in Cohort 3 only (0 to \<6 years) must have a gestational age of at least 39 weeks and a minimum weight of 5 kg.
* Be a recipient of an SOT or an HSCT that is functioning at the time of screening.
* Have a documented CMV infection which may be a first episode of post-transplant CMV viremia (primary or reactivation) or refractory to other anti-CMV treatments, with a CMV DNA screening value of \>= 1365 International Units per milliliter (IU/mL) in whole blood or \>= 455 IU/mL in plasma in 2 consecutive assessments separated by at least 1 day, as determined by local laboratory quantitative polymerase chain reaction (qPCR) or comparable quantitative nucleic acid amplification test (qNAAT) results. Quantitative assays must be standardized to the World Health Organization (WHO) CMV International Standard. Both samples must be taken within 14 days of first dose of study drug, with the second sample obtained within 5 days prior to first dose of study drug. The same laboratory and same sample type (whole blood or plasma) must be used for both assessments. If documented and verified values are available in medical history that fulfill this criterion entirely, they may be used instead.
* Have all the following results as part of screening laboratory assessments:
* Absolute neutrophil count \>= 500 per cubic millimeter (/mm\^3) (0.5 × 10\^9 per liter \[/L\])
* Platelet count \>= 15,000/mm\^3 (15 × 10\^9/L)
* Hemoglobin \>= 8 grams per deciliter (g/dL) (\>=80 grams per liter \[g/L\]).
* Have an estimated glomerular filtration rate (creatinine-based Bedside Schwartz equation) \>= 30 milliliters per minute (mL/min) /1.73 meter square (m\^2).
* Be a female of nonchildbearing potential. If a female of childbearing potential, have a negative serum human chorionic gonadotropin (hCG) or beta-human chorionic gonadotropin (β-hCG) pregnancy test at screening. Males, or nonpregnant, nonlactating females who are sexually active must agree to comply with the applicable contraceptive requirements of this protocol during the study treatment administration period and for 90 days after the last dose of study treatment.
* Have life expectancy of \>= 8 weeks.
* Be willing and have an understanding and ability to fully comply with the study procedures and restrictions defined in the protocol. For younger children, the parent/both parents or LAR must meet this criterion.
* Participants must have a confirmed negative human immunodeficiency virus (HIV) test result within 3 months of first dose of study drug or, if unavailable, be tested by a local laboratory during the screening period.

Exclusion Criteria

* Have CMV tissue invasive disease involving the central nervous system (CNS) or retina as assessed by the investigator at the time of screening.
* Have uncontrolled other type of infection as assessed by the investigator on the date of enrollment.
* Have a history of clinically relevant alcohol or drug abuse that may interfere with treatment compliance or assessments with the protocol as determined by the investigator.
* Be receiving valganciclovir, ganciclovir, cidofovir, foscarnet, leflunomide, letermovir, or artesunate when study treatment is initiated, or anticipated to require one of these agents during the 8-week treatment period.
* Have a known hypersensitivity to maribavir or to any excipients.
* Have severe vomiting, diarrhea, or other severe gastrointestinal (GI) illness within 24 hours prior to the first dose of study treatment or a GI absorption abnormality that would preclude administration of oral medication.
* Require mechanical ventilation or vasopressors for hemodynamic support at baseline (Visit 2/Day 1/Week 0).
* Be pregnant (or expecting to conceive) or nursing.
* Have previously completed, discontinued, or have been withdrawn from this study.
* Have received any investigational agent or device within 30 days before initiation of study treatment (includes CMV specific T-cells) or plan to receive an investigational agent or device during the study.

Previously approved agents under investigation for additional indications are not exclusionary.

* Have previously received maribavir or CMV vaccine at any time.
* Have any clinically significant medical or surgical condition that, in the investigator's opinion, could interfere with interpretation of study results, contraindicate the administration of the study treatment, or compromise the safety or well-being of the participant.
* Have severe liver disease (Child-Pugh score of \>= 10).
* Have serum aspartate aminotransferase greater than (\>) 5 times upper limit of normal (ULN) at screening, or serum alanine aminotransferase \> 5 times ULN at screening, or total bilirubin \>= 3.0 times ULN at screening (except for documented Gilbert's syndrome), as analyzed by local laboratory.
* Have positive results for HIV.
* Have active malignancy with the exception of nonmelanoma skin cancer, as determined by the investigator. Participants who experience relapse or progression of their underlying malignancy (for which HSCT or SOT was performed), as determined by the investigator, are not to be enrolled.
* Be undergoing treatment for acute or chronic hepatitis B or hepatitis C.
* Requiring ongoing treatment with or an anticipated need for treatment with a strong cytochrome P450 3A (CYP3A) inducer.
* Have a low body weight where total blood volume (TBV) required during study participation will exceed 1 percent (%) TBV per study visit or 3% TBV over a 4-week period.
Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Takeda Development Center Americas, Inc.

INDUSTRY

Sponsor Role collaborator

Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Nebraska Medical Center -985400 Nebraska Medical Center

Omaha, Nebraska, United States

Site Status RECRUITING

Cincinnati Children's Hospital Medical Center - PIN

Cincinnati, Ohio, United States

Site Status RECRUITING

Cook Children's Health Care System

Fort Worth, Texas, United States

Site Status RECRUITING

University of Texas MD Anderson Cancer Center - 1515 Holcombe Blvd

Houston, Texas, United States

Site Status RECRUITING

Sydney Children's Hospital

Randwick, New South Wales, Australia

Site Status RECRUITING

Queensland Children's Hospital

South Brisbane, Queensland, Australia

Site Status RECRUITING

Royal Children's Hospital Melbourne - PIN

Parkville, Victoria, Australia

Site Status RECRUITING

Perth Children's Hospital

Nedlands, Western Australia, Australia

Site Status RECRUITING

Hôpital Universitaire des Enfants Reine Fabiola (HUDERF)

Brussels, Brussels Capital, Belgium

Site Status RECRUITING

Cliniques Universitaires Saint-Luc

Woluwe-Saint-Lambert, Brussels Capital, Belgium

Site Status RECRUITING

UZ Gent

Ghent, Oost-Vlaanderen, Belgium

Site Status RECRUITING

Irmandade Da Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status RECRUITING

Hospital de Clinicas de Porto Alegre (HCPA) - PPDS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status RECRUITING

Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo

Porto Alegre, Rio Grande do Sul, Brazil

Site Status RECRUITING

Hospital Do Rim E Hipertensão

São Paulo, , Brazil

Site Status RECRUITING

Children's Hospital Capital Institute of Pediatrics

Beijing, Beijing Municipality, China

Site Status RECRUITING

Beijing Children's Hospital, Capital Medical University - PIN

Beijing, Beijing Municipality, China

Site Status RECRUITING

Shanghai Children's Medical Center

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Institute of Hematology and Blood Diseases Hospital Chinese Academy of Medical Sciences - PPDS

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

CHU de Rennes - Hôpital Pontchaillou

Rennes, Ille-et-Vilaine, France

Site Status RECRUITING

CHU de Grenoble Alpes - Hôpital Michallon

La Tronche, Isère, France

Site Status RECRUITING

CHRU Nantes

Nantes, Loire-Atlantique, France

Site Status RECRUITING

Hopital Necker

Paris, , France

Site Status RECRUITING

Universitätsklinikum Würzburg

Würzburg, Bavaria, Germany

Site Status RECRUITING

Universitätsklinikum Münster

Münster, North Rhine-Westphalia, Germany

Site Status RECRUITING

Universitatsklinikum Jena - Am Klinikum 1-Erlanger Allee 101

Jena, Thuringia, Germany

Site Status RECRUITING

Universitätsklinikum Hamburg Eppendorf

Hamburg, , Germany

Site Status RECRUITING

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status RECRUITING

The Chaim Sheba Medical Center - PPDS

Ramat Gan, Tel Aviv, Israel

Site Status RECRUITING

Tel Aviv Sourasky Medical Center Ichilov - PPDS

Tel Aviv, Tel Aviv, Israel

Site Status RECRUITING

Rambam Health Care Campus - PPDS

Haifa, , Israel

Site Status RECRUITING

Hadassah Medical Center- Ein Kerem - PPDS

Petah Tikva, , Israel

Site Status RECRUITING

National Center for Child Health and Development

Nagoya, Aiti, Japan

Site Status RECRUITING

Saitama Children's Medical Center

Isehara-Shi, Kanagawa, Japan

Site Status RECRUITING

Shizuoka Children's Hospital

Aoi-ku, Shizuoka, Japan

Site Status RECRUITING

Hyogo Prefectural Kobe Children's Hospital

Chiba, , Japan

Site Status RECRUITING

Osaka Women's and Children's Hospital

Izumi-Shi, Ôsaka, Japan

Site Status RECRUITING

Hospital Sant Joan de Deu - PIN

Espluges de Llobregat, Barcelona, Spain

Site Status RECRUITING

Hospital Universitario La Paz - PPDS

Horcajo de la Sierra, Madrid, Spain

Site Status RECRUITING

Hospital Regional Universitario de Malaga - Hospital Materno-Infantil

Málaga, Málaga, Spain

Site Status RECRUITING

Hospital Universitario Vall d´Hebron- PPDS

Barcelona, , Spain

Site Status RECRUITING

Hospital Infantil Universitario Niño Jesus - PIN

Madrid, , Spain

Site Status RECRUITING

King's College Hospital

London, Lambeth, United Kingdom

Site Status RECRUITING

Royal Manchester Children's Hospital - PIN

Manchester, Lancashire, United Kingdom

Site Status RECRUITING

Nottingham University Hospitals NHS Trust

Nottingham, Nottinghamshire, United Kingdom

Site Status RECRUITING

Birmingham Women's and Children's NHS Foundation Trust

Birmingham, West Midlands, United Kingdom

Site Status RECRUITING

Great Ormond Street Hospital

London, , United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Belgium Brazil China France Germany Israel Japan Spain United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Takeda Contact

Role: CONTACT

+1-877-825-3327

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Site Contact

Role: primary

402-559-6463

Site Contact

Role: primary

513-636-9101

Site Contact

Role: primary

682-885-8084

Site Contact

Role: primary

713-792-3497

Site Contact

Role: primary

+61293821690

Site Contact

Role: primary

+61393455522

Site Contact

Role: primary

+61393455522

Site Contact

Role: primary

+61893408222

Site Contact

Role: primary

+3224773100

Site Contact

Role: primary

+3227641387

Site Contact

Role: primary

+3293325860

Site Contact

Role: primary

+555132148640

Site Contact

Role: primary

+555133598317

Site Contact

Role: primary

+555132178555

Site Contact

Role: primary

+551150878000

Site Contact

Role: primary

+8613601123876

Site Contact

Role: primary

+8613601203966

Site Contact

Role: primary

+8618930830632

Site Contact

Role: primary

+8613752090418

Site Contact

Role: primary

+33299265835

Site Contact

Role: primary

+33476765911

Site Contact

Role: primary

+33240083610

Site Contact

Role: primary

+33144494622

Site Contact

Role: primary

+4993120127999

Site Contact

Role: primary

+492518343415

Site Contact

Role: primary

+493641328134

Site Contact

Role: primary

+4940741052720

Site Contact

Role: primary

+495115326747

Site Contact

Role: primary

+97235303030

Site Contact

Role: primary

+972524266464

Site Contact

Role: primary

+97247774798

Site Contact

Role: primary

+97226417095

Site Contact

Role: primary

+81524815111

Site Contact

Role: primary

+81463931121

Site Contact

Role: primary

+81542476251

Site Contact

Role: primary

+81789457300

Site Contact

Role: primary

+81725561220

Site Contact

Role: primary

+34 932532100

Site Contact

Role: primary

+34917277223

Site Contact

Role: primary

+34686595189

Site Contact

Role: primary

+34 934893000

Site Contact

Role: primary

+34 630667275

Site Contact

Role: primary

441132432799

Site Contact

Role: primary

+441612761234

Site Contact

Role: primary

+448888888888

Site Contact

Role: primary

+441213338252

Site Contact

Role: primary

442074059200

References

Explore related publications, articles, or registry entries linked to this study.

Fisher JE, Mulieri K, Finch E, Ericson JE. Use of Maribavir for Multidrug Resistant Cytomegaloviremia in a Pediatric Oncology Patient. J Pediatr Hematol Oncol. 2024 Apr 1;46(3):e244-e247. doi: 10.1097/MPH.0000000000002841. Epub 2024 Mar 1.

Reference Type DERIVED
PMID: 38447094 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2021-004279-15

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

jRCT2031230753

Identifier Type: REGISTRY

Identifier Source: secondary_id

2023-508988-73-00

Identifier Type: CTIS

Identifier Source: secondary_id

TAK-620-2004

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.