Prophylactic Use of Maribavir for the Prevention of Cytomegalovirus (CMV) Disease in Stem Cell Transplant Recipients

NCT ID: NCT00411645

Last Updated: 2021-06-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

681 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-12-13

Study Completion Date

2009-05-23

Brief Summary

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The purpose of this research study is to investigate whether or not maribavir is safe and effective for preventing CMV disease when taken by mouth for up to 12 weeks in patients who have had a stem cell transplant.

Detailed Description

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Cytomegalovirus (CMV) infections remain a significant problem following various types of transplants that are associated with strong immunosuppressive therapy. Maribavir is a new oral anti-CMV drug with a novel mechanism of action compared to currently available anti-CMV drugs. This study will test the safety and efficacy of maribavir for the prevention of CMV disease when given as prophylaxis for up to 12 weeks following allogeneic stem cell transplant.

Conditions

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Cytomegalovirus Infections

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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A

Group Type EXPERIMENTAL

maribavir

Intervention Type DRUG

100 mg twice daily for up to 12 weeks

B

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type OTHER

twice daily for up to 12 weeks

Interventions

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maribavir

100 mg twice daily for up to 12 weeks

Intervention Type DRUG

placebo

twice daily for up to 12 weeks

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Allogeneic stem cell transplant recipient
* Recipient or donor CMV seropositive
* Have transplant engraftment
* Able to swallow tablets

Exclusion Criteria

* CMV organ disease
* HIV infection
* Use of other anti-CMV therapy post-transplant
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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University of Arkansas Myeloma Institute

Little Rock, Arkansas, United States

Site Status

City of Hope Medical Center

Duarte, California, United States

Site Status

Scripps Green Hospital

La Jolla, California, United States

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UCSD Moores Center

La Jolla, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

Rocky Mountain Cancer Center

Denver, Colorado, United States

Site Status

Shands Hospital

Gainesville, Florida, United States

Site Status

H. Lee Moffitt Cancer Center

Tampa, Florida, United States

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Emory University

Atlanta, Georgia, United States

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Northwestern University Medical Center

Chicago, Illinois, United States

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University of Chicago

Chicago, Illinois, United States

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Loyola University

Maywood, Illinois, United States

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St Francis Hospital

Beech Grove, Indiana, United States

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University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

University of Kentucky Chandler Medical Center

Lexington, Kentucky, United States

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University Medical Center University of Louisville Hospital

Louisville, Kentucky, United States

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Greenbaum Cancer Center

Baltimore, Maryland, United States

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Massachusettes General

Boston, Massachusetts, United States

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Brigham and Women's Hospital

Boston, Massachusetts, United States

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Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

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University of Michigan

Ann Arbor, Michigan, United States

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Wayne State Medical Center

Detroit, Michigan, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic College of Medicine

Rochester, Minnesota, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Memorial Sloan-Kettering Cancer Center

New York, New York, United States

Site Status

New York Presbyterian Hospital,Weill Cornell Medical Center

New York, New York, United States

Site Status

Mount Sinai Hospital

New York, New York, United States

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University of Rochester Medical Center

Rochester, New York, United States

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University of North Carolina Hospital

Chapel Hill, North Carolina, United States

Site Status

Duke Medical Center

Durham, North Carolina, United States

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Wake Forest Medical Center

Winston-Salem, North Carolina, United States

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The Jewish Hospital

Cincinnati, Ohio, United States

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Ireland Cancer Center Case Western Reserve University

Cleveland, Ohio, United States

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University of Oklahoma

Oklahoma City, Oklahoma, United States

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Oregon Health and Sciences University

Portland, Oregon, United States

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Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

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Thomas Jefferson

Philadelphia, Pennsylvania, United States

Site Status

Jeanes Hospital - Temple

Philadelphia, Pennsylvania, United States

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Western Pennsylvania Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

Vanderbilt Medical Center

Nashville, Tennessee, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

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MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Methodist Hospital

Houston, Texas, United States

Site Status

Texas Transplant Institute

San Antonio, Texas, United States

Site Status

Latter Day Saints Hospital

Salt Lake City, Utah, United States

Site Status

Medical College of Virginia

Richmond, Virginia, United States

Site Status

VA Puget Sound Health Center

Seattle, Washington, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

West Virginia University Hospital

Morgantown, West Virginia, United States

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ZNA Stuivenberg

Antwerp, , Belgium

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AZ Sint Jan, Department of Hematology

Bruges, , Belgium

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Cliniques Universitaires St,Luc Dept Hematology

Brussels, , Belgium

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UZ Gasthuisberg

Leuven, , Belgium

Site Status

CHU Sart -Tilman Department of Medicine, Hematology

Liège, , Belgium

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QEII Health Sciences Center

Halifax, Nova Scotia, Canada

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McMaster University Medical Center

Hamilton, Ontario, Canada

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London Health Sciences Centre

London, Ontario, Canada

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Ottawa General Campus

Ottawa, Ontario, Canada

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Hopital l'Enfant Jesus

Québec, Quebec, Canada

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Hopital Henri Mondor

Créteil, , France

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Edouard Herriot Hopital

Lyon, , France

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Institut Paoli Calmettes

Marseille, , France

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Hopital Hotel Dieu

Nantes, , France

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Hopital St. Louis

Paris, , France

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Hopital Haut-Leveque

Pessac, , France

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Universitaetsklinikum Koeln, Clinic I for internal Medicine

Cologne, , Germany

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Univ. Clinic Dresden

Dresden, , Germany

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University Clinic of Dresden

Dresden, , Germany

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University of Essen

Essen, , Germany

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University of Freiburg

Freiburg im Breisgau, , Germany

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University of Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Hannover, Medizinische Hochschule

Hanover, , Germany

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University of Heidelberg

Heidelberg, , Germany

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Johannes-Gutenberg University

Mainz, , Germany

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University Clinic of Ulm

Ulm, , Germany

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Careggi University Hospital

Florence, , Italy

Site Status

University of San Martino Hospital

Genova, , Italy

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San Raffaele del Monte Tabor

Milan, , Italy

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Pescara Hospital

Pescara, , Italy

Site Status

Bianchi-Melacrino-Morelli Hospital

Reggio Calabria, , Italy

Site Status

Barcelona Hospital

Barcelona, , Spain

Site Status

Duran i Reynals Hospital

Barcelona, , Spain

Site Status

University of Salamanca

Salamanca, , Spain

Site Status

Karolinska University Hospital

Huddinge, Stockholm County, Sweden

Site Status

Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status

Karolinska University Hospital,Huddinge

Stockholm, , Sweden

Site Status

Akademiska Sjukhuset, Dept Hematology

Uppsala, , Sweden

Site Status

University College Hospital

London, , United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Hammersmith Hospital

London, , United Kingdom

Site Status

Countries

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United States Belgium Canada France Germany Italy Spain Sweden United Kingdom

References

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Marty FM, Ljungman P, Papanicolaou GA, Winston DJ, Chemaly RF, Strasfeld L, Young JA, Rodriguez T, Maertens J, Schmitt M, Einsele H, Ferrant A, Lipton JH, Villano SA, Chen H, Boeckh M; Maribavir 1263-300 Clinical Study Group. Maribavir prophylaxis for prevention of cytomegalovirus disease in recipients of allogeneic stem-cell transplants: a phase 3, double-blind, placebo-controlled, randomised trial. Lancet Infect Dis. 2011 Apr;11(4):284-92. doi: 10.1016/S1473-3099(11)70024-X. Epub 2011 Mar 21.

Reference Type DERIVED
PMID: 21414843 (View on PubMed)

Other Identifiers

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2006-005692-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

SHP620-300

Identifier Type: OTHER

Identifier Source: secondary_id

1263-300

Identifier Type: -

Identifier Source: org_study_id

NCT00430339

Identifier Type: -

Identifier Source: nct_alias

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