Effects of Low-level Mechanical Vibration on Bone Density in Ambulant Children Affected by Duchenne Muscular Dystrophy

NCT ID: NCT05281120

Last Updated: 2022-03-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-11-30

Study Completion Date

2007-11-30

Brief Summary

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Duchenne muscular dystrophy (DMD) is a X-linked recessive disorder due to a mutation of the dystrophin gene (Xp21). Dystrophin is a sarcolemmal protein of skeletal and cardiac muscle, and its absence causes progressive muscle degeneration and substitution with fat and connective tissue. The progressive muscle degeneration leads to loss of autonomous walking before the age of 15 years and death for cardiac and/or respiratory failure. There are no specific treatment for DMD, and the standard of care is now based on long-term corticosteroid (CS) use. The studies on bone mass in DMD are very few, but they agree in reporting the presence of a reduced bone mass and an increased rate of fractures probably due to long-term steroid therapy and disuse-osteopenia. The aim of this study, involving 20 ambulant DMD boys (age 7-10 years) has been the evaluation of the effects of low-level mechanical vibrations on bone in a group of ambulant DMD children for 1 year, with RDA-adjusted dietary calcium intake and 25OH vitamin D supplementation.

Detailed Description

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All children were instructed to have a daily intake of calcium equal to the 100% of the RDA and were supplemented with calcifediol (0.7 mcg/kg/die).

The 20 boys were randomly assigned to two groups:

group 1 (mechanical intervention group) = a mechanical device (a small platform designed to induce vertical, sinusoidal acceleration) was installed in the home of each boy of group 1.

group 2 (placebo control group) = a placebo device was installed in the home of each boy of group 2

All boys were instructed to stand on the platform for 10 minutes each day for 12 months.

Compliance was followed and stimulated through weekly telephone contacts with parents and children.

Conditions

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Osteoporosis Duchenne Muscular Dystrophy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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mechanical intervention group

20 subjects participated to the study (1 year double-blind, randomized, placebo controlled, parallel group study) and 10 subjects were randomized to this arm.

Intervention: to stand on the active platform (inducing vertical, sinusoidal acceleration) for 10 minutes each day for 12 months.

Group Type ACTIVE_COMPARATOR

Low-level mechanical vibrations WITH vertical sinusoidal acceleration

Intervention Type DEVICE

Small platform designed to induce vertical, sinusoidal acceleration.

mechanical placebo group

20 subjects participated to the study (1 year double-blind, randomized, placebo controlled, parallel group study) and 10 subjects were randomized to this arm.

Intervention: to stand on the placebo platform (not inducing vertical, sinusoidal acceleration) for 10 minutes each day for 12 months.

Group Type PLACEBO_COMPARATOR

Low-level mechanical vibrations WITHOUT vertical sinusoidal acceleration

Intervention Type DEVICE

Small platform designed to NOT induce vertical, sinusoidal acceleration

Interventions

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Low-level mechanical vibrations WITH vertical sinusoidal acceleration

Small platform designed to induce vertical, sinusoidal acceleration.

Intervention Type DEVICE

Low-level mechanical vibrations WITHOUT vertical sinusoidal acceleration

Small platform designed to NOT induce vertical, sinusoidal acceleration

Intervention Type DEVICE

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of DMD
* Ability to stand up and walk (some balance assistance allowed, but full weight-bearing necessary)
* All the children must already be on glucocorticoid therapy for at least 6 months before the start of the study.

Exclusion Criteria

* Presence of other diseases interfering with bone density and bone turnover
* The inability to regularly use the vibratory platform.
Minimum Eligible Age

7 Years

Maximum Eligible Age

10 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Istituto Auxologico Italiano

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Maria Luisa Bianchi

Role: PRINCIPAL_INVESTIGATOR

Istituto Auxologico Italiano

References

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Other Identifiers

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02C701

Identifier Type: -

Identifier Source: org_study_id

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