A Study of Itolizumab in Combination With Corticosteroids for the First-Line Treatment of Acute Graft Versus Host Disease (EQUATOR)

NCT ID: NCT05263999

Last Updated: 2025-06-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

158 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-04-29

Study Completion Date

2025-05-12

Brief Summary

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This is a multi-center study to compare the efficacy and safety of itolizumab versus placebo as first-line therapy for subjects with Grade III-IV aGVHD or Grade II with LGI involvement, in combination with corticosteroids

Detailed Description

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This study will enroll 200 subjects at approximately 125 sites globally. Subjects will be randomized in a 1:1 ratio to active or placebo and will receive a total of 7 doses administered intravenously approximately every 2 weeks. The study follows the patients for a total of approximately 365 days.

Conditions

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Graft Versus Host Disease GVHD Acute-graft-versus-host Disease Acute GVHD aGVHD

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Itolizumab (EQ001)

Itolizumab (EQ001) administered in a blinded fashion by intravenous infusion every 2 weeks for a total of 7 doses.

Group Type EXPERIMENTAL

Itolizumab

Intervention Type BIOLOGICAL

Itolizumab \[Bmab600\]

EQ001 Placebo

EQ001 Placebo administered in a blinded fashion by intravenous infusion every 2 weeks for a total of 7 doses

Group Type PLACEBO_COMPARATOR

EQ001 Placebo

Intervention Type DRUG

EQ001 Placebo

Interventions

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Itolizumab

Itolizumab \[Bmab600\]

Intervention Type BIOLOGICAL

EQ001 Placebo

EQ001 Placebo

Intervention Type DRUG

Other Intervention Names

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EQ001 Bmab600

Eligibility Criteria

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Inclusion Criteria

1. Is willing and able to provide written informed consent/assent and to comply with all protocol procedures and assessments required for the study.
2. Is age ≥12 years and \>40kg at informed consent/assent.
3. Has had an initial allogeneic HSCT for any indication using any graft source, donor source, conditioning regimen intensity or prophylaxis.
4. Has evidence of myeloid engraftment
5. Has a clinical diagnosis of aGVHD Grades III-IV or Grade II with LGI involvement based on Mount Sinai Acute GVHD International Consortium (MAGIC) grading criteria.
6. Began systemic corticosteroid treatment for aGVHD ≤72 hours prior to the start of study drug dosing AND must receive 2 mg/kg/day methylprednisolone or equivalent on Day 1.

Exclusion Criteria

1. Evidence of morphological relapsed, progressive, persistent, or untreated malignancy, with the exception of nonmelanoma skin cancer and in situ ductal carcinoma of the breast.
2. An unplanned donor lymphocyte infusion for persistent or recurrent malignancy after HSCT.
3. Evidence of persistent molecular disease requiring treatment that was not specified prior to HSCT.
4. Evidence of cGVHD or overlap syndrome
5. Use of immunosuppressants other than corticosteroids for the treatment of aGVHD.
6. Use of any systemic corticosteroids of \>0.5 mg/kg/day methylprednisolone or equivalent for any indication other than aGVHD within 7 days before the onset of aGVHD.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biocon Limited

INDUSTRY

Sponsor Role collaborator

Equillium

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chief Development Officer

Role: STUDY_DIRECTOR

Equillium, Inc.

Locations

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Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

Institut Paoli Calmettes - Hematology

Marseille, , France

Site Status

CHU Nice, Hospital l'Archet

Nice, , France

Site Status

AP-HP Hopital Saint-Louis

Paris, , France

Site Status

McGill University Health Center - Research Institute

Montreal, Quebec, Canada

Site Status

CHU de Québec - Université Laval

Québec, Quebec, Canada

Site Status

University of Saskatchewan

Saskatoon, Saskatchewan, Canada

Site Status

CHU Amiens Picardie - Hopital Sud

Amiens, , France

Site Status

CHU de Caen - Hopital Femme-Enfant-Hematologie (FEH)

Caen, , France

Site Status

CHU de Grenoble Hôpital Michallon

Grenoble, , France

Site Status

CHU de Lille - Hopital Claude Huriez

Lille, , France

Site Status

CHU de Nantes - Hôtel-Dieu

Lyon, , France

Site Status

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

City of Hope

Duarte, California, United States

Site Status

University of California, San Diego (UCSD) - Moores Cancer Center

La Jolla, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

University of California, Los Angeles (UCLA) - Medical Center

Los Angeles, California, United States

Site Status

Stanford Cancer Center

Stanford, California, United States

Site Status

AdventHealth Orlando

Orlando, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status

The University of Chicago Medical Center (UCMC)

Chicago, Illinois, United States

Site Status

Loyola University Chicago, performing research at Loyola University Medical Center

Maywood, Illinois, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

Tulane University Medical Center

New Orleans, Louisiana, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Spectrum Health

Grand Rapids, Michigan, United States

Site Status

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status

John Theurer Cancer Center At Hackensack UMC

Hackensack, New Jersey, United States

Site Status

Rutgers Cancer Institute of NJ

New Brunswick, New Jersey, United States

Site Status

Northwell Health

Lake Success, New York, United States

Site Status

David H. Koch Center for Cancer Care at Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Stony Brook University Medical Center

Stony Brook, New York, United States

Site Status

University of North Carolina (UNC)

Chapel Hill, North Carolina, United States

Site Status

Wake Forest

Winston-Salem, North Carolina, United States

Site Status

Oncology Hematology in Cincinnati

Cincinnati, Ohio, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

The Ohio State University (OSU)

Columbus, Ohio, United States

Site Status

Oregon Health & Science University (OHSU)

Portland, Oregon, United States

Site Status

University of Pennsylvania Abramson Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center (UPMC) - Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status

Sarah Cannon Research Institute, LLC (SCRI)

Nashville, Tennessee, United States

Site Status

Baylor Scott & White Research Institute

Dallas, Texas, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

Royal Adelaide Hospital

Adelaide, , Australia

Site Status

Royal Melbourne Hospital

East Melbourne, , Australia

Site Status

Austin Health

Heidelberg, , Australia

Site Status

Westmead Hospital

Westmead, , Australia

Site Status

ULB - Institut Jules Bordet; department of Hematology

Anderlecht, , Belgium

Site Status

ZNA Stuivenberg

Antwerp, , Belgium

Site Status

AZ Sint-Jan Brugge-Oostende AV

Bruges, , Belgium

Site Status

Cliniques Universitaires Saint-Luc; Hematology Department

Brussels, , Belgium

Site Status

UZ Leuven - Campus Gasthuisberg - Department of Hematology

Leuven, , Belgium

Site Status

CHU de Liege - Hematology Department

Liège, , Belgium

Site Status

AZ Delta

Roeselare, , Belgium

Site Status

Vancouver Coastal Health Authority

Vancouver, British Columbia, Canada

Site Status

CHU Bordeaux - Hopital Haut-Leveque - Centre François Magendie

Pessac, , France

Site Status

HCL Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

CHU de Rennes Hôpital Pontchaillou

Rennes, , France

Site Status

CHU Toulouse, Hematology

Toulouse, , France

Site Status

Institut Gustave Roussy - Hematology

Villejuif, , France

Site Status

Charité Universitätsmedizin Berlin, Tumorimmunologie Campus Virchow-Klinikum

Berlin, , Germany

Site Status

Universitaetsklinikum Koeln (AoeR)

Cologne, , Germany

Site Status

Universitaetsklinikum Duesseldorf

Düsseldorf, , Germany

Site Status

Martin Luther Universitat Halle-Wittenberg

Halle, , Germany

Site Status

Universitätsklinikum Jena

Jena, , Germany

Site Status

Universitaetsklinikum Leipzig

Leipzig, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

Site Status

Universitaetsklinikum Ulm

Ulm, , Germany

Site Status

Universitätsklinikum Würzburg, Medizinische Klinik II

Würzburg, , Germany

Site Status

Rambam Health Care Campus

Haifa, , Israel

Site Status

Hadassah Medical Center Ein Karem

Jerusalem, , Israel

Site Status

Bone Marrow Transplantation Unit Rabin MC

Petah Tikva, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Chaim Sheba Medical Center

Tel Litwinsky, , Israel

Site Status

Dipartimento Malattie oncologiche ed ematologiche - U.O. Ematologia - Programma dipartimentale Terapie cellulari avanzate

Bologna, BO, Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico G. Rodolico-San Marco- Presidio Ospedaliero Ferrarotto Alessi

Catania, , Italy

Site Status

Azienda Ospedaliero-Universitaria Careggi

Florence, , Italy

Site Status

Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII

Milan, , Italy

Site Status

IRCCS Ospedale San Raffaele

Milan, , Italy

Site Status

Fondazione IRCCS San Gerardo dei Tintori

Monza, , Italy

Site Status

Grande Ospedale Metropolitano "Bianchi Melacrino Morelli"

Reggio Calabria, , Italy

Site Status

Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore

Rome, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

AOU Citta della Salute e della Scienza di Torino - Ospedale Regina Margherita

Torino, , Italy

Site Status

Azienda Ospedaliera - Universitaria Integrata di Verona - Ospedale Borgo Roma

Verona, , Italy

Site Status

Starship Children's Hospital

Auckland, , New Zealand

Site Status

Instituto Português de Oncologia de Lisboa Francisco Gentil, E.P.E.

Lisbon, , Portugal

Site Status

Instituto Português de Oncologia do Porto Francisco Gentil, E.P.E.

Porto, , Portugal

Site Status

Chonnam National University Hwasun Hospital

Hwasun, Jeollanam-do, South Korea

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Kyungpook National University Hospital

Daegu, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Donostia

Donostia / San Sebastian, Gipuzkoa, Spain

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Institut Catala d'Oncologia - L'Hospitalet

Barcelona, , Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Virgen de las Nieves

Granada, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Clinica Universidad de Navarra - Pamplona

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Marques de Valdecilla

Madrid, , Spain

Site Status

Hospital Universitario Regional de Málaga

Málaga, , Spain

Site Status

Hospital Clinico Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Hospital Clínico Universitario de Valencia

Valencia, , Spain

Site Status

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status

Countries

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United States Australia Belgium Canada France Germany Israel Italy New Zealand Portugal South Korea Spain

Related Links

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Other Identifiers

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EQ-100-02

Identifier Type: -

Identifier Source: org_study_id

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