A Study to Evaluate Axatilimab and Corticosteroids as Initial Treatment for Chronic Graft-Versus-Host Disease

NCT ID: NCT06585774

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

240 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-01-21

Study Completion Date

2030-03-31

Brief Summary

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This study will be conducted to compare the efficacy of axatilimab versus placebo in combination with corticosteroids as initial treatment for moderate or severe chronic graft-versus-host disease (cGVHD).

Detailed Description

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Conditions

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Chronic Graft-versus-host-disease

Keywords

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cGVHD

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Axatilimab + Corticosteroids

Axatilimab and Corticosteroids at the protocol-defined dose.

Group Type EXPERIMENTAL

INCA034176

Intervention Type DRUG

IV infusion

Corticosteroids

Intervention Type DRUG

Oral/IV Infusion

Placebo + Corticosteroids

Matching placebo and Corticosteroids at the protocol-defined dose.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

IV infusion

Corticosteroids

Intervention Type DRUG

Oral/IV Infusion

Interventions

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INCA034176

IV infusion

Intervention Type DRUG

Placebo

IV infusion

Intervention Type DRUG

Corticosteroids

Oral/IV Infusion

Intervention Type DRUG

Other Intervention Names

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Axatilimab prednisone, methylprednisolone, prednisolone

Eligibility Criteria

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Inclusion Criteria

* ≥ 12 years of age at the time of informed consent.
* New-onset moderate or severe cGVHD, as defined by the 2014 NIH Consensus Development Project Criteria for Clinical Trials in cGVHD, requiring systemic therapy.
* History of allo-HCT from any donor HLA type (related or unrelated donor with any degree of HLA matching) using any graft source (bone marrow, peripheral blood stem cells, or cord blood). Recipients of myeloablative, nonmyeloablative, or reduced-intensity conditioning are eligible.
* Adequate hematologic function with ANC ≥ 0.5 × 109/L independent of growth factors for at least 7 days prior to study entry.
* Willingness to avoid pregnancy or fathering children.

Exclusion Criteria

* Received more than 1 prior allo-HCT. Prior autologous HCT is allowed.
* Has overlap cGVHD, defined as simultaneous presence of features or characteristics of aGVHD in a patient with cGVHD.
* Received more than 7 days of systemic corticosteroid treatment for cGVHD or unable to begin a prednisone dose ≥ 1.0 mg/kg per day (or methylprednisolone equivalent) for cGVHD.
* Received previous systemic treatment for cGVHD, including extracorporeal photopheresis.
* Systemic treatment with CNIs or mTOR inhibitors started within 2 weeks prior to C1D1.
* Prior treatment with CSF-1R targeted therapies.
* Active, uncontrolled bacterial, fungal, parasitic, or viral infection.
* Evidence of relapse of the primary hematologic disease or treatment for relapse after the allo-HCT was performed, including DLIs for the treatment of molecular relapse.
* History of acute or chronic pancreatitis.
* Active symptomatic myositis.
* History or current diagnosis of cardiac disease indicating significant risk of safety for participation in the study, such as uncontrolled or significant cardiac disease.
* Severe renal impairment, that is, estimated CrCl \< 30 mL/min measured or calculated by Cockcroft-Gault equation in adults and Schwartz formula in pediatric participants, or endstage renal disease on dialysis.
* Impaired liver function, defined as total bilirubin \> 1.5 × ULN and/or ALT and AST \> 3 × ULN in participants with no evidence of liver cGVHD.
* Pregnant or breastfeeding.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Albert Assad, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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University of California San Diego Medical Center, Moores Cancer Center

La Jolla, California, United States

Site Status RECRUITING

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status RECRUITING

Childrens National Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Orlando Health Cancer Institute Downtown Orlando

Orlando, Florida, United States

Site Status RECRUITING

Memorial Cancer Institute

Pembroke Pines, Florida, United States

Site Status RECRUITING

Emory University-Winship Cancer Institute

Atlanta, Georgia, United States

Site Status RECRUITING

University of Illinois

Chicago, Illinois, United States

Site Status RECRUITING

The University of Kansas Cancer Center

Kansas City, Kansas, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Henry Ford Hospital

Detroit, Michigan, United States

Site Status RECRUITING

Corewell Health Hematology Oncology

Grand Rapids, Michigan, United States

Site Status RECRUITING

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status RECRUITING

Rutgers Cancer Institute of Nj

New Brunswick, New Jersey, United States

Site Status RECRUITING

Stony Brook University Medical Center

Stony Brook, New York, United States

Site Status RECRUITING

Oregon Health and Science University

Portland, Oregon, United States

Site Status RECRUITING

Jefferson University Hospitals

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

Prisma Health Upstate

Greenville, South Carolina, United States

Site Status RECRUITING

Baptist Cancer Center

Memphis, Tennessee, United States

Site Status RECRUITING

Texas Transplant Institute

San Antonio, Texas, United States

Site Status RECRUITING

Intermountain Blood and Marrow Transplant

Salt Lake City, Utah, United States

Site Status RECRUITING

West Virginia University Cancer Institute

Morgantown, West Virginia, United States

Site Status RECRUITING

Royal Prince Alfred Hospital

Sydney, New South Wales, Australia

Site Status RECRUITING

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status RECRUITING

Austin Health Medical Oncology and Clinical Haematology

Heidelberg, Victoria, Australia

Site Status RECRUITING

Landeskrankenhaus Universitatsklinikum Graz

Graz, , Austria

Site Status RECRUITING

Innsbruck University Hospital

Innsbruck, , Austria

Site Status RECRUITING

Ordensklinikum Linz Gmbh Elisabethinen

LINZ CET, , Austria

Site Status RECRUITING

St. Anna Childrens Hospital

Vienna, , Austria

Site Status RECRUITING

Alberta'S Children Hospital

Calgary, Alberta, Canada

Site Status RECRUITING

Juravinski Cancer Centre

Hamilton, Ontario, Canada

Site Status RECRUITING

Princess Margaret Cancer Center

Toronto, Ontario, Canada

Site Status RECRUITING

Hospital Maisonneuve Rosemont

Montreal, Quebec, Canada

Site Status RECRUITING

Vancouver General Hospital

Vancouver, , Canada

Site Status RECRUITING

Rigshospitalet

Copenhagen, , Denmark

Site Status RECRUITING

Chu Amiens Picardie - Hopital Sud

Amiens, , France

Site Status RECRUITING

Hopitaux de Brabois

Nancy, , France

Site Status RECRUITING

Centre Hospitalier Universitaire de Nantes (Chu de Nantes) - Hotel-Dieu

Nantes, , France

Site Status RECRUITING

Chu de Nice - Hospital L Archet

Nice, , France

Site Status RECRUITING

Hospital Saint Louis

Paris, , France

Site Status RECRUITING

Hospices Civils de Lyon Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status RECRUITING

Universitaire Du Cancer de Toulouse Institut Claudius Regaud Iuct-Oncopole

Toulouse, , France

Site Status RECRUITING

University Medical Center Rwth Aachen

Aachen, , Germany

Site Status RECRUITING

Charite Universitatsmedizin Berlin

Berlin, , Germany

Site Status RECRUITING

Universitaetsklinikum Bonn, University Hospital Bonn

Bonn, , Germany

Site Status RECRUITING

University Clinic Carl Gustav Carus Technical University Dresden

Dresden, , Germany

Site Status RECRUITING

University Hospital Duesseldorf

Düsseldorf, , Germany

Site Status RECRUITING

Universitaetsklinikum Erlangen

Erlangen, , Germany

Site Status RECRUITING

Universitatsklinikum Essen

Essen, , Germany

Site Status RECRUITING

Universitatsklinikum Halle (Saale)

Halle, , Germany

Site Status RECRUITING

University Hospital Schleswig-Holstein Campus Kiel

Kiel, , Germany

Site Status RECRUITING

Universitatsklinikum Leipzig

Leipzig, , Germany

Site Status RECRUITING

Universitatsmedizin Der Johannes Gutenberg-Universitat Mainz Iii

Mainz, , Germany

Site Status RECRUITING

Klinikum Der Philipps-Universitaet Marburg

Marburg, , Germany

Site Status RECRUITING

Universitatsklinikum Munster

Münster, , Germany

Site Status RECRUITING

St. James Hospital

Dublin, , Ireland

Site Status RECRUITING

Azienda Ospedaliero-Universitaria Di Alessandria Ss.Antonio E Biagio E Cesare Arrigo

Alessandria, , Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria Delle Marche

Ancona, , Italy

Site Status RECRUITING

Asst Degli Spedali Civili Di Brescia

Brescia, , Italy

Site Status RECRUITING

Irccs Azienda Ospedaliera Universitaria San Martino

Genova, , Italy

Site Status RECRUITING

Ospedale San Raffaele - Milano

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliera Di Rilievo Nazionale Antonio Cardarelli

Napoli, , Italy

Site Status RECRUITING

Azienda Ospedaliera Ospedali Riuniti Villa Sofia - Cervello

Palermo, , Italy

Site Status RECRUITING

Irccs Fondazione Policlinico San Matteo

Pavia, , Italy

Site Status RECRUITING

Grande Ospedale Metropolitano Bianchi-Melacrino-Morelli

Reggio Calabria, , Italy

Site Status RECRUITING

Azienda Policlinico Umberto 1 Universita Sapienza Di Roma

Rome, , Italy

Site Status RECRUITING

Ospedale Pediatrico Bambino Gesu Irccs

Rome, , Italy

Site Status RECRUITING

I.R.C.C.S. Casa Sollievo Della Sofferenza

San Giovanni Rotondo, , Italy

Site Status RECRUITING

Azienda Ospedaliera Card. G. Panico

Tricase, , Italy

Site Status RECRUITING

Centro Ricerche Cliniche Di Verona

Verona, , Italy

Site Status RECRUITING

Fujita Health University Hospital

Aichi, , Japan

Site Status RECRUITING

Anjo Kosei Hospital

Aichi-ken, , Japan

Site Status RECRUITING

Kyushu University Hospital

Fukuoka, , Japan

Site Status RECRUITING

Hiroshima University Hospital

Hiroshima, , Japan

Site Status RECRUITING

Kobe City Medical Center General Hospital

Hyōgo, , Japan

Site Status RECRUITING

Tokai University Hospital

Isehara Kanagawa, , Japan

Site Status RECRUITING

National Hospital Organization Kumamoto Medical Center

Kumamoto Kumamoto, , Japan

Site Status RECRUITING

Gunma Saiseikai Maebashi Hospital

Maebashi, , Japan

Site Status RECRUITING

Tohoku University Hospital

Miyagi, , Japan

Site Status RECRUITING

Okayama University Hospital

Okayama-ken, , Japan

Site Status RECRUITING

Osaka Metropolitan University Hospital

Osaka, , Japan

Site Status RECRUITING

Hokkaido University Hospital

Sapporo Hokkaido, , Japan

Site Status RECRUITING

Tokyo Metropolitan Cancer and Infectious Diseases Center Komagome Hospital

Tokyo, , Japan

Site Status RECRUITING

Amsterdam University Medical Centre

Amsterdam, , Netherlands

Site Status RECRUITING

Hospital General Universitario Vall D Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital de La Santa Creu I Sant Pau

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Donostia

Donostia / San Sebastian, , Spain

Site Status RECRUITING

Hospital Universitario de Gran Canaria Doctor Negrin

Las Palmas de Gran Canaria, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status RECRUITING

Hospital Puerta de Hierro

Majadahonda, , Spain

Site Status RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Universitari I Politecnic La Fe

Valencia, , Spain

Site Status RECRUITING

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status RECRUITING

Bristol Haematology and Oncology Centre

Bristol, , United Kingdom

Site Status RECRUITING

Royal Marsden Hospital

London, , United Kingdom

Site Status RECRUITING

University College London Hospitals (Uclh)

London, , United Kingdom

Site Status RECRUITING

Manchester University Nhs Foundation Trust

Manchester, , United Kingdom

Site Status RECRUITING

Nottingham University Hospitals

Nottingham, , United Kingdom

Site Status RECRUITING

Plymouth Hospitals Nhs Trust

Plymouth, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Austria Canada Denmark France Germany Ireland Italy Japan Netherlands Spain United Kingdom

Central Contacts

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Incyte Corporation Call Center (US)

Role: CONTACT

Phone: 1.855.463.3463

Email: [email protected]

Incyte Corporation Call Center (ex-US)

Role: CONTACT

Phone: +800 00027423

Email: [email protected]

Related Links

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Other Identifiers

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2023-510292-65-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

INCA34176-357

Identifier Type: -

Identifier Source: org_study_id