Ibrutinib in Combination With Corticosteroids vs Placebo in Combination With Corticosteroids in Participants With New Onset Chronic Graft Versus Host Disease (cGVHD)

NCT ID: NCT02959944

Last Updated: 2023-03-30

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

193 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-05-11

Study Completion Date

2021-07-12

Brief Summary

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To evaluate the safety and efficacy of ibrutinib in combination with prednisone in subjects with newly diagnosed moderate to severe cGVHD.

Detailed Description

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Conditions

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Chronic Graft Versus Host Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ibrutinib + Prednisone

Ibrutinib (420 mg) given orally once daily continuously starting on Week 1 Day 1 until cGVHD progression, progression of underlying malignancy, participant begins another systemic treatment for cGVHD or unacceptable toxicity. The 420 mg dose was adjusted for cytochrome P450 \[CYP\] inhibitors or hepatic dysfunction as applicable.

Prednisone 1 mg/kg/d given orally once daily continuously starting on Week 1 Day 1 until unacceptable toxicity or until participant is successfully tapered from the prednisone. Starting prednisone dose may be as low as 0.5 mg/kg/d if a participant cannot tolerate higher doses.

Group Type EXPERIMENTAL

ibrutinib

Intervention Type DRUG

Ibrutinib capsules administered orally daily

Prednisone

Intervention Type DRUG

Prednisone administered daily

Placebo + Prednisone

Placebo given orally once daily continuously starting on Week 1 Day 1 until cGVHD progression, progression of underlying malignancy, participant begins another systemic treatment for cGVHD or unacceptable toxicity.

Prednisone 1 mg/kg/d given orally once daily continuously starting on Week 1 Day 1 until unacceptable toxicity or until participant is successfully tapered from the prednisone. Starting prednisone dose may be as low as 0.5 mg/kg/d if a participant cannot tolerate higher doses.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo capsules administered orally daily

Prednisone

Intervention Type DRUG

Prednisone administered daily

Interventions

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ibrutinib

Ibrutinib capsules administered orally daily

Intervention Type DRUG

Placebo

Placebo capsules administered orally daily

Intervention Type DRUG

Prednisone

Prednisone administered daily

Intervention Type DRUG

Other Intervention Names

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IMBRUVICA® PCI-32765

Eligibility Criteria

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Inclusion Criteria

* New onset moderate or severe cGVHD as defined by the 2014 National Institutes of Health (NIH) Consensus Development Project Criteria
* Need for systemic treatment with corticosteroids for cGVHD
* No previous systemic treatment for cGVHD (including extracorporeal photopheresis \[ECP\])
* Participants may be receiving other immunosuppressants for the prophylaxis or treatment of acute GVHD but if the subject is receiving prednisone for prophylaxis or treatment of acute GVHD it must be at or below 0.5 mg/kg/d
* Age ≥12 years old
* Karnofsky or Lansky (subjects \<16 years) performance status ≥60

Exclusion Criteria

* Received any previous systemic treatment for cGVHD with the exception of corticosteroids administered for cGVHD within the 72 hours prior to signing the informed consent form.
* Inability to begin a prednisone dose ≥0.5 mg/kg/d for the treatment of cGVHD
* Any uncontrolled infection or active infection requiring ongoing systemic treatment
* Progressive underlying malignant disease or any post-transplant lymphoproliferative disease
* Known bleeding disorders
* Active hepatitis C virus (HCV) or hepatitis B virus (HBV)
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role collaborator

Pharmacyclics LLC.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Justin Wahlstrom, MD

Role: STUDY_DIRECTOR

Pharmacyclics LLC.

Locations

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Arizona Oncology - Scottsdale - Cancer Transplant Institute Location /ID# 1140-1120

Scottsdale, Arizona, United States

Site Status

LPCH Stanford /ID# 1140-1128

Palo Alto, California, United States

Site Status

Ucsf /Id# 1140-0003

San Francisco, California, United States

Site Status

Stanford University/Stanford Cancer Center, Pasteur Drive /ID# 1140-0400

Stanford, California, United States

Site Status

UCHSC Anschultz Cancer Pavilion /ID# 1140-0068

Aurora, Colorado, United States

Site Status

Children's National Medical Center /ID# 1140-1122

Washington D.C., District of Columbia, United States

Site Status

Jackson Memorial Hospital, University of Miami /ID# 1140-0647

Miami, Florida, United States

Site Status

Florida Hospital Cancer Institute/Adventist Health System/Sunbelt, Inc /ID# 1140-1121

Orlando, Florida, United States

Site Status

Emory University, Winship Cancer Institute /ID# 1140-0033

Atlanta, Georgia, United States

Site Status

Emory University/Winship Cancer Institute /ID# 1140-1179

Atlanta, Georgia, United States

Site Status

University of Chicago /ID# 1140-0126

Chicago, Illinois, United States

Site Status

Loyola University /ID# 1140-0713

Maywood, Illinois, United States

Site Status

Indiana University Melvin and Bren Simon Cancer Center /ID# 1140-0010

Indianapolis, Indiana, United States

Site Status

University of Kentucky /ID# 1140-1140

Lexington, Kentucky, United States

Site Status

University of Louisville Hospital /ID# 1140-1131

Louisville, Kentucky, United States

Site Status

University of Maryland /ID# 1140-0205

Baltimore, Maryland, United States

Site Status

Massachusetts General Hospital Cancer Center /ID# 1140-0020

Boston, Massachusetts, United States

Site Status

Boston Childrens Hospital /ID# 1140-1615

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute /ID# 1140-0349

Boston, Massachusetts, United States

Site Status

Barbara Ann Karmanos Cancer In /ID# 1140-0130

Detroit, Michigan, United States

Site Status

University of Minnesota /ID# 1140-0807

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic, Rochester, MN /ID# 1140-0240

Rochester, Minnesota, United States

Site Status

Hackensack University Medical Center/ John Theurer Cancer Center /ID# 1140-0343

Hackensack, New Jersey, United States

Site Status

Rutgers Cancer Institute of NJ /ID# 1140-0803

New Brunswick, New Jersey, United States

Site Status

New York Presbyterian Hospital/Weill Cornell Med College /ID# 1140-0200

New York, New York, United States

Site Status

Stony Brook University Medical Center /ID# 1140-0719

New York, New York, United States

Site Status

Columbia University Medical Center, MS-CHONY /ID# 1140-1124

New York, New York, United States

Site Status

Weill Cornell Physicians - Hematologic Malignancies & Bone Marrow Transplant /ID# 1140-0019

New York, New York, United States

Site Status

University of Rochester Cancer Center /ID# 1140-0127

Rochester, New York, United States

Site Status

Montefiore Medical Center - Moses Campus /ID# 1140-0120

The Bronx, New York, United States

Site Status

University of North Carolina - Lineberger Comprehensive Cancer Center /ID# 1140-1133

Chapel Hill, North Carolina, United States

Site Status

Univ Hosp Cleveland /ID# 1140-0941

Cleveland, Ohio, United States

Site Status

University of Pittsburgh - UPMC (Hillman Cancer Center) /ID# 1140-0050

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina, MUSC /ID# 1140-0738

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center Vanderbilt Ingram Cancer Center /ID# 1140-0024

Nashville, Tennessee, United States

Site Status

Methodist San Antonio /ID# 1140-1118

San Antonio, Texas, United States

Site Status

Fred Hutchinson Cancer Research Center /ID# 1140-0404

Seattle, Washington, United States

Site Status

West Virginia University /ID# 1140-1090

Morgantown, West Virginia, United States

Site Status

The Kinghorn Cancer Centre /ID# 1140-1165

Darlinghurst, New South Wales, Australia

Site Status

Westmead Hospital /ID# 1140-0848

Westmead, New South Wales, Australia

Site Status

Royal Brisbane and Women's Hospital /ID# 1140-0190

Herston, Queensland, Australia

Site Status

Royal Children's Hospital/ID# 1140-1154

Parkville, Victoria, Australia

Site Status

Royal Melbourne Hospital (RMH) /ID# 1140-0633

Parkville, Victoria, Australia

Site Status

Fiona Stanley Hospital /ID# 1140-0880

Perth, Western Australia, Australia

Site Status

Univ. Klinik for Innere Medizin, Klinische Abteilung for Hematologie, Graz /ID# 1140-0373

Graz, , Austria

Site Status

Krankenhaus der Elisabethinen Linz /ID# 1140-0849

Linz, , Austria

Site Status

University of British Columbia (UBC) - Vancouver General Hospital (VGH) /ID# 1140-1166

Vancouver, British Columbia, Canada

Site Status

The Ottawa Hospital Regional Cancer Center /ID# 1140-0159

Ottawa, Ontario, Canada

Site Status

Princess Margaret Cancer Centre /ID# 1140-0043

Toronto, Ontario, Canada

Site Status

CHU Sainte-Justine /ID# 1140-1143

Montreal, Quebec, Canada

Site Status

The First Affiliated Hospital of Soochow University /ID# 1140-1208

Suzhou, Jiangsu, China

Site Status

Chinese PLA General Hospital /ID# 1140-1198

Beijing, , China

Site Status

Nanfang Hospital /ID# 1140-1379

Guangzhou, , China

Site Status

UHC Zagreb /ID# 1140-1169

Zagreb, , Croatia

Site Status

Hopital de Brabois /ID# 1140-0775

Vandœuvre-lès-Nancy, Meurthe-et-Moselle, France

Site Status

CHU Amiens Groupe hospitalier Sud /ID# 1140-1205

Amiens, , France

Site Status

CHU de GRENOBLE Alpes /ID# 1140-1058

Grenoble, , France

Site Status

Centre Hospitalier Regional Universitaire de Lille /ID# 1140-0750

Lille, , France

Site Status

CHU de Nantes /ID# 1140-0520

Nantes, , France

Site Status

Groupe Hospitalier Pitie-Salpetriere /ID# 1140-0918

Paris, , France

Site Status

Hopital Saint-Louis - Institut Hematologie Centre Hayem CHU /ID# 1140-0735

Paris, Île-de-France Region, France

Site Status

Robert Bosch Hospital /ID# 1140-1160

Stuttgart, Baden-Wurttemberg, Germany

Site Status

Universitatsklinikum Munster /ID# 1140-1195

Munster, Lower Saxony, Germany

Site Status

Universitaetsklinikum Dresden /ID# 1140-1367

Dresden, , Germany

Site Status

Hannover Medical School /ID# 1140-1141

Hanover, , Germany

Site Status

Dr. Haunerschen Kinderspital /ID# 1140-1142

Munich, , Germany

Site Status

University Hospital of Regensburg /ID# 1140-1446

Regensburg, , Germany

Site Status

St. Laszlo Hospital /ID# 1140-1164

Budapest, , Hungary

Site Status

IRCCS Ospedale Pediatrico Bambino Gesu /ID# 1140-1150

Rome, Lazio, Italy

Site Status

A.O. Univ. Ospedali Riuniti /ID# 1140-0932

Ancona, The Marches, Italy

Site Status

ASST Papa Giovanni XXIII /ID# 1140-1231

Bergamo, , Italy

Site Status

Ospedale San Raffaele IRCCS /ID# 1140-0523

Milan, , Italy

Site Status

University of Torino /ID# 1140-1268

Torino, , Italy

Site Status

Centro Trapianti Cellule Staminali, Ospedale Infantile Regina Margherita /ID# 1140-1156

Turin, , Italy

Site Status

Anjou Kousei Hospital /ID# 1140-1435

Anjo, Aichi-ken, Japan

Site Status

Hiroshima Red Cross Hospital and Atomic-bomb Survivors Hospital /ID# 1140-1437

Hiroshima, Hiroshima, Japan

Site Status

Kobe City Medical Center General Hospital /ID# 1140-1438

Kobe, Hyōgo, Japan

Site Status

Hyogo College of Medicine College Hospital /Id# 1140-1434

Nishinomiya-shi, Hyōgo, Japan

Site Status

Duplicate_University of Tsukuba Hospital /ID# 1140-1445

Tsukuba, Ibaraki, Japan

Site Status

Tokai University Hospital /ID# 1140-1444

Isehara-shi, Kanagawa, Japan

Site Status

Duplicate_Kurashiki Central Hospital /ID# 1140-1442

Kurishiki-shi, Okayama-ken, Japan

Site Status

Okayama University Hospital /ID# 1140-1430

Okayama, Okayama-ken, Japan

Site Status

Osaka Women's and Children's Hospital /ID# 1140-1440

Izumi-Shi, Osaka, Japan

Site Status

Osaka City University Hospital /ID# 1140-1157

Osaka, Osaka, Japan

Site Status

Dup_Tokyo Metropolitan Cancer and Infectious Diseases Center Komagome Hospital /ID# 1140-1439

Bunkyo-ku, Tokyo, Japan

Site Status

National Center for Child Health and Development /ID# 1140-1443

Setagaya-ku, Tokyo, Japan

Site Status

Kumamoto Medical Center /ID# 1140-1431

Kumamoto, , Japan

Site Status

Hokkaido University Hospital /ID# 1140-1436

Sapporo, , Japan

Site Status

National University Cancer Institute - National University Health System /ID# 1140-1155

Singapore, , Singapore

Site Status

Singapore General Hospital /ID# 1140-1162

Singapore, , Singapore

Site Status

Kyungpook National Univ Hosp /ID# 1140-1153

Daegu, Daegu Gwang Yeogsi, South Korea

Site Status

Yonsei University Health System, Severance Hospital /ID# 1140-0927

Seodaemun-gu, Seoul Teugbyeolsi, South Korea

Site Status

Samsung Medical Center /ID# 1140-0925

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

Cath Univ Seoul St Mary's Hosp /ID# 1140-0928

Seoul, Seoul Teugbyeolsi, South Korea

Site Status

SoonChunHyang University Seoul /ID# 1140-1163

Seoul, , South Korea

Site Status

Asan Medical Center /ID# 1140-0963

Seoul, , South Korea

Site Status

Hospital Clinic /ID# 1140-0533

Barcelona, , Spain

Site Status

Hospital Santa Creu i Sant Pau /ID# 1140-0535

Barcelona, , Spain

Site Status

Hospital Universitario Virgen del Rocio /ID# 1140-0863

Seville, , Spain

Site Status

Hospital Clinico Universitario de Valencia /ID# 1140-1145

Valencia, , Spain

Site Status

China Medical University Hosp /ID# 1140-1199

Taichung, Taichung, Taiwan

Site Status

National Taiwan Univ Hosp /ID# 1140-1184

Taipei City, Taipei, Taiwan

Site Status

Countries

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United States Australia Austria Canada China Croatia France Germany Hungary Italy Japan Singapore South Korea Spain Taiwan

References

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Miklos DB, Abu Zaid M, Cooney JP, Albring JC, Flowers M, Skarbnik AP, Yakoub-Agha I, Ko BS, Bruno B, Waller EK, Yared J, Sohn SK, Bulabois CE, Teshima T, Jacobsohn D, Greinix H, Mokatrin A, Lee Y, Wahlstrom JT, Styles L, Socie G. Ibrutinib for First-Line Treatment of Chronic Graft-Versus-Host Disease: Results From the Randomized Phase III iNTEGRATE Study. J Clin Oncol. 2023 Apr 1;41(10):1876-1887. doi: 10.1200/JCO.22.00509. Epub 2023 Jan 6.

Reference Type DERIVED
PMID: 36608310 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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PCYC-1140-IM

Identifier Type: -

Identifier Source: org_study_id

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