A Phase 3 Study to Assess Efficacy Safety and Tolerability of Remibrutinib in Adult and Adolescent Patients With Moderate to Severe Hidradenitis Suppurativa

NCT ID: NCT06840392

Last Updated: 2026-01-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

555 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-20

Study Completion Date

2028-03-17

Brief Summary

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The purpose of this study is to establish the efficacy, safety, and tolerability of remibrutinib (LOU064) Dose A and Dose B compared to placebo in participants with moderate to severe hidradenitis suppurativa (HS).

Detailed Description

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The total duration of the study is 76 weeks and consists of: Screening (up to 4 weeks), Treatment Period 1 (16 weeks, double-blind treatment with remibrutinib (Dose A or Dose B) or placebo, Treatment Period 2 (52 weeks, treatment with remibrutinib (Dose A or Dose B) and Safety Follow-Up (treatment-free follow-up for 4 weeks).

Participants who prematurely discontinue study treatment (either during Treatment Period 1 or Treatment Period 2) are encouraged to remain in the study. Participants who do not wish to remain in the study will enter a 4-week Safety Follow-Up period.

Conditions

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Hidradenitis Suppurativa

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Remibrutinib Dose A (Treatment Period 1 and 2)

articipants randomized to receive remibrutinib Dose A during Treatment Period 1 and 2

Group Type EXPERIMENTAL

Remibrutinib Dose A

Intervention Type DRUG

Remibrutinib Dose A (oral)

Remibrutinib Dose B (Treatment Period 1 and 2)

Participants randomized to receive remibrutinib Dose B during Treatment Period 1 and 2

Group Type EXPERIMENTAL

Remibrutinib Dose B

Intervention Type DRUG

Remibrutinib Dose B (oral)

Placebo (Treatment Period 1) + remibrutinib Dose B (Treatment Period 2)

Participants randomized to receive placebo during Treatment Period 1 followed by remibrutinib dose B during Treatment Period 2

Group Type PLACEBO_COMPARATOR

Remibrutinib Dose B

Intervention Type DRUG

Remibrutinib Dose B (oral)

Placebo 1

Intervention Type DRUG

Placebo matching to remibrutinib Dose A (oral)

Placebo 2

Intervention Type DRUG

Placebo matching to remibrutinib Dose B (oral)

Interventions

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Remibrutinib Dose A

Remibrutinib Dose A (oral)

Intervention Type DRUG

Remibrutinib Dose B

Remibrutinib Dose B (oral)

Intervention Type DRUG

Placebo 1

Placebo matching to remibrutinib Dose A (oral)

Intervention Type DRUG

Placebo 2

Placebo matching to remibrutinib Dose B (oral)

Intervention Type DRUG

Other Intervention Names

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LOU064 LOU064

Eligibility Criteria

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Inclusion Criteria

1. Male and female participants ≥ 12 years of age at the time of signing of the informed consent.
2. Diagnosis of HS based on clinical history and physical examination for at least 6 months prior to the Baseline visit.
3. Participants with moderate to severe HS defined as:

* A total of at least 5 AN count (abscesses and/or inflammatory nodules) AND
* Inflammatory lesions should affect at least 2 distinct anatomic areas (e.g., left and right axillae)

Exclusion Criteria

1. Presence of more than 20 fistulae/tunnels (both draining and non-draining) in total at baseline.
2. Any active skin disease or conditions that may interfere with the assessment of HS.
3. Previous exposure to remibrutinib or other BTK inhibitors.
4. Use of other investigational drugs within 5 half-lives of enrollment, or within 30 days (for small molecules) prior to randomization, or until the pharmacodynamic effect has returned to baseline (for biologics), whichever is longer.
5. Significant bleeding risk or coagulation disorders.
6. History of gastrointestinal bleeding.
7. Requirement for anti-platelet (except for acetylsalicylic acid up to 100 mg/d or clopidogrel up to 75 mg/d) or anti-coagulant medication.
8. History or current hepatic disease.
9. Evidence of clinically significant cardiovascular, neurological, psychiatric, pulmonary, renal, hepatic, endocrine, metabolic, hematological disorders, gastrointestinal disease or immunodeficiency that, in the Investigator's opinion, would compromise the safety of the participant, interfere with the interpretation of the study results or otherwise preclude participation or protocol adherence of the participant.
10. History of hypersensitivity to any of the study drug constituents.
11. Known or suspected infectious disease that is active, chronic or recurrent which precludes the participant from participating in the trial as per investigator's assessment. These infectious diseases include and are not limited to opportunistic infections (e.g., tuberculosis, atypical mycobacterioses, listeriosis or aspergillosis) and/or known or suspected Human Immunodeficiency Virus (HIV) infection. Should it be required by local regulations and/or considered appropriate by the investigator, an HIV test can be performed to confirm eligibility.
12. History of live attenuated vaccine administration within 6 weeks prior to randomization or requirement to receive these vaccinations at any time while on study treatment.
13. Major surgery within 8 weeks prior to screening or planned surgery for the duration of the study.
Minimum Eligible Age

12 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Total Skin and Beauty Dermatology Center PC

Birmingham, Alabama, United States

Site Status RECRUITING

CTT Research

Gilbert, Arizona, United States

Site Status RECRUITING

Ctr Dermatology and Plastic Surgery

Scottsdale, Arizona, United States

Site Status RECRUITING

Ctr for Dermatology Clinical Res

Fremont, California, United States

Site Status RECRUITING

USC Keck School of Medicine

Los Angeles, California, United States

Site Status RECRUITING

MedDerm Associates

San Diego, California, United States

Site Status RECRUITING

Driven Research

Coral Gables, Florida, United States

Site Status RECRUITING

Floridian Research Institute

Miami, Florida, United States

Site Status RECRUITING

Sarasota Arthritis Res Ctr

Sarasota, Florida, United States

Site Status RECRUITING

University Of South Florida

Tampa, Florida, United States

Site Status RECRUITING

Emory School of Med Dermatology

Atlanta, Georgia, United States

Site Status RECRUITING

Atlanta Biomedical Clin Res LLC

Atlanta, Georgia, United States

Site Status RECRUITING

Northwestern University

Chicago, Illinois, United States

Site Status RECRUITING

Endeavor Health

Glenview, Illinois, United States

Site Status RECRUITING

Dundee Dermatology

West Dundee, Illinois, United States

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Southern IN Clinical Trials

New Albany, Indiana, United States

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Beth Israel Deaconess Med Center

Boston, Massachusetts, United States

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Metro Boston Clinical Partners

Brighton, Massachusetts, United States

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Clinical Research Inst of MI

Chesterfield, Michigan, United States

Site Status RECRUITING

Deluxe Dermatology

St Louis, Missouri, United States

Site Status RECRUITING

Skin Specialists PC

Omaha, Nebraska, United States

Site Status RECRUITING

Vivida Dermatology

Las Vegas, Nevada, United States

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North Shore University Hospital

New Hyde Park, New York, United States

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Cameron Dermatology

New York, New York, United States

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Optima Research Boardman

Boardman, Ohio, United States

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Ohio State University

Columbus, Ohio, United States

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Wright State University

Fairborn, Ohio, United States

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Apex Clinical Research Center LLC

Mayfield Heights, Ohio, United States

Site Status RECRUITING

Clinical Research Ctr of Carolinas

Charleston, South Carolina, United States

Site Status RECRUITING

Goodlettsville Dermatology Research

Goodlettsville, Tennessee, United States

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Accurate Clinical Research

Humble, Texas, United States

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Austin Inst for Clinical Research

Pflugerville, Texas, United States

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Center for Clinical Studies-Lee

Webster, Texas, United States

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Care Access Alexandria

Arlington, Virginia, United States

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Complexions Dermatology

Danville, Virginia, United States

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Forefront Dermatology

Vienna, Virginia, United States

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Novartis Investigative Site

Berazategui, Buenos Aires, Argentina

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CABA, , Argentina

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Caba, , Argentina

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Córdoba, , Argentina

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Linz, , Austria

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Brussels, Brussels Capital, Belgium

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Woluwe-Saint-Lambert, Brussels Capital, Belgium

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Leuven, Vlaams Brabant, Belgium

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Liège, , Belgium

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Edmonton, Alberta, Canada

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London, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Medellín, Antioquia, Colombia

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Bogota, Cundinamarca, Colombia

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Bogota, Cundinamarca, Colombia

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Medellín, , Colombia

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Karlovy Vary, , Czechia

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Plzen Bolevec, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Brest, , France

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La Rochelle, , France

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Lyon, , France

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Nice, , France

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Reims, , France

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Rouen, , France

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Toulouse, , France

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Freiburg im Breisgau, Baden-Wurttemberg, Germany

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Würzburg, Bavaria, Germany

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Frankfurt am Main, Hesse, Germany

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Düsseldorf, North Rhine-Westphalia, Germany

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Merzig, Saarland, Germany

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Leipzig, Saxony, Germany

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Bad Bentheim, , Germany

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Berlin, , Germany

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Dessau, , Germany

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Dortmund, , Germany

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Essen, , Germany

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Hamburg, , Germany

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Lübeck, , Germany

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Minden, , Germany

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München, , Germany

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Tübingen, , Germany

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Athens, , Greece

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Chaïdári, , Greece

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Thessaloniki, , Greece

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Pécs, Baranya, Hungary

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Debrecen, Hajdu Bihar Megye, Hungary

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Debrecen, Hajdú-Bihar, Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Kecskemét, , Hungary

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Szeged, , Hungary

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Kuala Lumpur, Kuala Lumpur, Malaysia

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Ipoh, Perak, Malaysia

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Kota Kinabalu, Sabah, Malaysia

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Johor Bahru, , Malaysia

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Selangor Darul Ehsan, , Malaysia

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Wilayah Persekutuan, , Malaysia

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Durango, , Mexico

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Warsaw, Masovian Voivodeship, Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Alma Cruz-Santana Private Practice

Carolina, , Puerto Rico

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Bucharest, District 2, Romania

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Bucharest, District 2, Romania

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Bucharest, , Romania

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Timișoara, , Romania

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Granada, Andalusia, Spain

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Palma, Balearic Islands, Spain

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Barcelona, , Spain

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Granollers, , Spain

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Las Palmas GC, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Pontevedra, , Spain

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Seville, , Spain

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Valencia, , Spain

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Izmir, Balcova, Turkey (Türkiye)

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Ankara, Bilkent-Cankaya, Turkey (Türkiye)

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Izmir, Buca, Turkey (Türkiye)

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Aydin, Efeler, Turkey (Türkiye)

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Denizli, Kinikli, Turkey (Türkiye)

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Ankara, Sihhiye-Altindag, Turkey (Türkiye)

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Ankara, Yenimahalle, Turkey (Türkiye)

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Mersin, Yenisehir, Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Kecioren Ankara, , Turkey (Türkiye)

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Leeds, West Yorkshire, United Kingdom

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Cardiff, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Southampton, , United Kingdom

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Countries

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United States Argentina Austria Belgium Canada Colombia Czechia France Germany Greece Hungary Malaysia Mexico Poland Puerto Rico Romania Spain Turkey (Türkiye) United Kingdom

Central Contacts

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Novartis Pharmaceuticals

Role: CONTACT

1-888-669-6682

Novartis Pharmaceuticals

Role: CONTACT

+41613241111

Facility Contacts

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Brittany Powell

Role: primary

Ranvitha Davalagar

Role: primary

+1 801 528 9503

Lindsey Arcuri

Role: primary

Evguenia Vals

Role: primary

510-797-0140

Kenan Kherallah

Role: primary

Kristian Cadag

Role: primary

619-542-0013

Haymara Gonzalez

Role: primary

Yusmara Villa

Role: primary

Nancy Alvarado

Role: primary

941-366-1244

Lucy Lam

Role: primary

813-974-6378

Julie Bonds

Role: primary

Leah Morse

Role: primary

Itzel Lara

Role: primary

Megan Calderon

Role: primary

JoAnn Hawkinson

Role: primary

Skyler Carl

Role: primary

Nazrin Ashina

Role: primary

617-667-7000

Stella Schandorf

Role: primary

617-783-7100

Joachina Jenuwine

Role: primary

Stephanie Kirkpatrick

Role: primary

Kayleigh Koziol

Role: primary

402-334-7546

Tracey Jablonka

Role: primary

Alicia Premdas

Role: primary

516-719-3376

Grace Ulerio

Role: primary

Robert Mackovick

Role: primary

Elizabeth Begle

Role: primary

614-293-4434

Jessica Hong

Role: primary

937-245-7500

Brooke Glivar

Role: primary

Gina Gregory

Role: primary

843-556-8886

David Laneve

Role: primary

615-859-0900

Valerie Blanco

Role: primary

Alivia Hernandez

Role: primary

512-259-2545

Karina Gonzalez

Role: primary

281-333-2288

Ernest Evans

Role: primary

Janaya Patron

Role: primary

Gianna Riley

Role: primary

Veronica Duque Osorno

Role: primary

+1 787 769 1954

Other Identifiers

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2024-513266-19-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CLOU064J12302

Identifier Type: -

Identifier Source: org_study_id

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