A Study to Evaluate the Safety, Tolerability, PK, PD, and Clinical Activity of EQ001 in Subjects With aGVHD

NCT ID: NCT03763318

Last Updated: 2025-04-18

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

30 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-07-15

Study Completion Date

2022-11-21

Brief Summary

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This is a multi-center study to evaluate the safety, tolerability, PK, PD, and clinical activity of EQ001 in subjects with Acute Graft Versus Host Disease (aGVHD).

Detailed Description

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The study will enroll approximately 100 subjects in two (2) parts:

Part A is an open label study and will enroll approximately 40 evaluable subjects with aGVHD across 4 cohorts. The total number of patients will depend on the number of dose escalations necessary to enable a decision to be made on the recommended dose to take forward into Part B of the study. The planned dose escalation will start with cohort 1, where subjects will receive EQ001 administered intravenously every two weeks for a total of 5 doses.

Part B is a randomized, double-blind, placebo-controlled study and will enroll approximately 60 additional subjects, randomized in a 2:1 ratio to either active treatment EQ001 (40) or placebo (20). Subjects will receive either EQ001 or placebo administered intravenously every two weeks for a total of 5 doses.

Conditions

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Acute-graft-versus-host Disease aGVHD GVHD GVHD, Acute

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Part A is an open label 3+3 dose escalation Part B is blinded and randomized 2:1
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Part B will be blinded to all study staff that has direct access to the subjects and the sponsor. The site's pharmacist or designee will be unblinded to prepare the study drug.

Study Groups

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EQ001 Dose Escalation (Part A)

Open label EQ001 administered by intravenous infusion every two weeks for a total of 5 doses.

Group Type EXPERIMENTAL

EQ001

Intervention Type BIOLOGICAL

Itolizumab \[Bmab 600\])

EQ001 (Part B)

EQ001 administered in a blinded fashion using the optimal dose selected from Part A by intravenous infusion every two weeks for a total of 5 doses.

Group Type EXPERIMENTAL

EQ001

Intervention Type BIOLOGICAL

Itolizumab \[Bmab 600\])

EQ001 Placebo (Part B)

Placebo administered in a blinded fashion by intravenous infusion every two weeks for a total of 5 doses.

Group Type PLACEBO_COMPARATOR

EQ001 Placebo

Intervention Type BIOLOGICAL

EQ001 Placebo

Interventions

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EQ001

Itolizumab \[Bmab 600\])

Intervention Type BIOLOGICAL

EQ001 Placebo

EQ001 Placebo

Intervention Type BIOLOGICAL

Other Intervention Names

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Bmab600 Itolizumab

Eligibility Criteria

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Inclusion Criteria

1. Male or female subject at least 18 years of age for Part A, and at least 12 years of age for Part B.
2. Recipients of allogeneic hematopoietic stem cell transplantation (alloHSCT) using myeloablative or non myeloablative conditioning regimens.
3. Have a clinical diagnosis of acute GVHD requiring systemic immune suppressive therapy.
4. Deemed by the investigator to be likely to comply with the planned procedure as required by the protocol for the duration of the study

Exclusion Criteria

1. Presence of morphologic relapsed primary malignancy, treatment for relapse after alloHSCT was performed, or requirement for rapid immunosuppressive treatment withdrawal for early malignancy relapse.
2. Evidence of graft failure based on cytopenia(s), and as determined by the investigator.
3. Evidence of post-transplant lymphoproliferative disease.
4. Any prior therapy for acute GVHD, except for alloHSCT prophylaxis regimens or systemically administered corticosteroids.
5. As determined by the investigator, any medical, psychiatric, or other condition or circumstance that is likely to negatively affect: the subject's participation in this clinical study, the subject's safety, or the reliability of the study data.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biocon Limited

INDUSTRY

Sponsor Role collaborator

Equillium

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Joel Rothman

Role: STUDY_DIRECTOR

Equillium

Locations

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City of Hope Comprehensive Cancer Center

Duarte, California, United States

Site Status

University of Florida Health Shands Hospital

Gainesville, Florida, United States

Site Status

University of Miami - Miller School of Medicine

Miami, Florida, United States

Site Status

H. Lee Moffitt Cancer Center & Research Institute

Tampa, Florida, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan - C.S. Mott Children's Hospital

Ann Arbor, Michigan, United States

Site Status

Washington University and Barnes Jewish Heart & Vascular Center

St Louis, Missouri, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

University of North Carolina Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

University of Pennsylvania, Abramson Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

TriStar Centennial Medical Center (SCRI)

Nashville, Tennessee, United States

Site Status

Intermountain Healthcare

Salt Lake City, Utah, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

Countries

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United States

References

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Rambaldi B, Kim HT, Arihara Y, Asano T, Reynolds C, Manter M, Halpern M, Weber A, Koreth J, Cutler C, Gooptu M, Nikiforow S, Ho VT, Antin JH, Romee R, Ampudia J, Ng C, Connelly S, Soiffer RJ, Ritz J. Phenotypic and functional characterization of the CD6-ALCAM T-cell co-stimulatory pathway after allogeneic cell transplantation. Haematologica. 2022 Nov 1;107(11):2617-2629. doi: 10.3324/haematol.2021.280444.

Reference Type DERIVED
PMID: 35484649 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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EQ001-aGVHD-001

Identifier Type: -

Identifier Source: org_study_id

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