Study to Evaluate the Efficacy, Safety and Tolerability of IMU-838 in Patients With Relapsing Multiple Sclerosis

NCT ID: NCT05201638

Last Updated: 2024-04-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1050 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-01-12

Study Completion Date

2032-10-31

Brief Summary

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Multi-Center, Randomized, Double-Blinded Phase 3 Study to Evaluate the Efficacy, Safety, and Tolerability of IMU-838 versus Placebo in Adults with Relapsing Multiple Sclerosis (ENSURE-2)

Detailed Description

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This study will be a multicenter, randomized, double-blind, placebo-controlled study with a blinded Main Treatment Period (MT) and an Open Label Period (OLE) to evaluate the efficacy, safety, and tolerability of IMU-838 in adult patients with RMS.

The study will consist of the following periods:

Screening Period: Approximately 28 days Main Treatment Period: 72 weeks (approximately 15 months) Open Label Extension Period: Up to approximately 8 years

Conditions

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Multiple Sclerosis, Relapsing-Remitting

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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IMU-838

IMU-838 (vidofludimus calcium), a small molecule inhibitor of DHODH.

Formulation:

Tablets with 15 or 30 mg IMU-838 for once daily oral intake in the morning.

Group Type EXPERIMENTAL

IMU-838 tablets

Intervention Type DRUG

Patients are randomized to IMU-838 or placebo in ratio 1:1

Placebo

Matching placebo, as described for the test product, identical number of tablets as given for IMU-838.

Group Type PLACEBO_COMPARATOR

Placebo matching IMU-838 tablets

Intervention Type DRUG

Patients are randomized to IMU-838 or placebo in ratio 1:1

Interventions

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IMU-838 tablets

Patients are randomized to IMU-838 or placebo in ratio 1:1

Intervention Type DRUG

Placebo matching IMU-838 tablets

Patients are randomized to IMU-838 or placebo in ratio 1:1

Intervention Type DRUG

Other Intervention Names

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Vidofludimus calcium Placebo matching vidofludimus calcium

Eligibility Criteria

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Inclusion Criteria

* Male or female patient (age ≥18 to ≤55 years).
* Patients with an established diagnosis of MS according to 2017 McDonald Criteria.
* Patients with RMS comprising of relapsing remitting MS (RRMS) and active secondary progressive MS, both defined according to Lublin criteria 1996 and 2014.
* Active disease as defined by Lublin 2014 evidenced prior to Screening by:

1. At least 2 relapses in the last 24 months before randomization, or
2. At least 1 relapse in the last 12 months before randomization, or
3. A positive Gd+ MRI scan (brain and/or spine) in the last 12 months prior to randomization.
* Willingness and ability to comply with the protocol.
* Written informed consent given prior to any study-related procedure.

Exclusion Criteria

* Patients with non-active secondary progressive MS and primary progressive MS.
* Any disease other than MS that may better explain the signs and symptoms, including history of complete transverse myelitis.
* Clinical signs or presence of laboratory findings suggestive for neuromyelitis optica (NMO) spectrum disorders or myelin oligodendrocyte glycoprotein (MOG)-IgG-associated encephalomyelitis
* Any active and uncontrolled coexisting autoimmune disease, other than MS (except for type 1 diabetes mellitus and inflammatory bowel disease)
* Use of experimental/investigational drug (with the exception of COVID-19 vaccines approved by emergency use authorization) and/or participation in drug clinical studies within 6 months prior to Screening
* Previous or current use of MS treatments lifelong, or within a pre-specified time period.
* Use of the pre-specified concomitant medications.
* Clinically significantly abnormal and pre-specified lab values.
* History of chronic systemic infections within 6 months before the date of informed consent.
* Diagnosis or suspected liver function impairment, which may cause fluctuating liver function tests during this study.
* Known history of nephrolithiasis or underlying condition with a strong association of nephrolithiasis.
* History or clinical diagnosis of gout.
* History or presence of any major medical or psychiatric illness
* Substantial medical condition that could create undue risk to the patient, could affect adherence with the study protocol or could undesirably affect study outcomes
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Immunic AG

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert J. Fox, MD

Role: PRINCIPAL_INVESTIGATOR

Mellen Center for MS, Neurological Institute, Cleveland Clinic, Ohio

Locations

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HonorHealth Research Institute - Bob Bove Neuroscience Institute

Scottsdale, Arizona, United States

Site Status RECRUITING

Neuro of Central Florida

Altamonte Springs, Florida, United States

Site Status RECRUITING

Healthcare Innovations

Coral Springs, Florida, United States

Site Status RECRUITING

Homestead Associates

Miami, Florida, United States

Site Status RECRUITING

Premier Clinical Research

Miami, Florida, United States

Site Status RECRUITING

Baptist Health Lexington

Nicholasville, Kentucky, United States

Site Status RECRUITING

Boston Clinical Trials

Boston, Massachusetts, United States

Site Status RECRUITING

Heratsi Hospital Complex 1

Yerevan, , Armenia

Site Status RECRUITING

Erebouni Medical Center

Yerevan, , Armenia

Site Status RECRUITING

UCC of Rep of Srpska

Banja Luka, , Bosnia and Herzegovina

Site Status RECRUITING

Cantonal Hospital Bihac Dr. Irfan Ljubijankic

Bihać, , Bosnia and Herzegovina

Site Status RECRUITING

University Clinical Center of Sarajevo

Sarajevo, , Bosnia and Herzegovina

Site Status RECRUITING

University Clinical Center Sarajevo

Sarajevo, , Bosnia and Herzegovina

Site Status RECRUITING

University Clinical Center Tuzla

Tuzla, , Bosnia and Herzegovina

Site Status RECRUITING

Astra Clinic

Tallinn, , Estonia

Site Status RECRUITING

Post-Graduation Institute of Medical Education and Research (PGIMER)

Chandigarh, , India

Site Status RECRUITING

Fortis Memorial Research Institute

Gurugramam, , India

Site Status RECRUITING

Dr Ram Manohar Lohia Institute of Medical Sciences

Lucknow, , India

Site Status RECRUITING

All India Institute of Medical Sciences

New Delhi, , India

Site Status RECRUITING

GB Pant Institute of Postgraduate Medical Education and Research

New Delhi, , India

Site Status RECRUITING

SRI Guru Ram Das Institute of Medical Sciences and Research

Punjābi Bāgh, , India

Site Status RECRUITING

DKS PGI

Raipur, , India

Site Status RECRUITING

Centro de Investig. Médicas

Lima, , Peru

Site Status RECRUITING

NZOZ Wielospecjalistyczna Poradnia Lekarska "Synapsis"

Katowice, , Poland

Site Status RECRUITING

Neuro-Medic Janusz Zbrojkiewicz

Katowice, , Poland

Site Status RECRUITING

NZOZ Neuromed

Lublin, , Poland

Site Status RECRUITING

Indywidualna Praktyka Lekarska prof. Konrad Rejdak

Lublin, , Poland

Site Status RECRUITING

Instytut Zdrowia Boczarska

Oświęcim, , Poland

Site Status RECRUITING

NZOZ Hertmanowskiej

Plewiska, , Poland

Site Status RECRUITING

NZOZ Neuro-Kard

Poznan, , Poland

Site Status RECRUITING

Centrum Medyczne NeuroProtect

Warsaw, , Poland

Site Status RECRUITING

FutureMeds Warszawa Centrum

Warsaw, , Poland

Site Status RECRUITING

Centrum Med. Ibismed

Zabrze, , Poland

Site Status RECRUITING

SC Sana Monitoring SRL

Bucharest, , Romania

Site Status RECRUITING

Elias University Emergency Hospital

Bucharest, , Romania

Site Status RECRUITING

Clubul Sanatatii SRL

Campulung Muscel, , Romania

Site Status RECRUITING

Spitalul clinic CF Constanta

Constanța, , Romania

Site Status RECRUITING

Asociatia Comunitatea Oamenilor

Craiova, , Romania

Site Status RECRUITING

Aria Clinic SRL

Sibiu, , Romania

Site Status RECRUITING

Neuro Therapy

Timișoara, , Romania

Site Status WITHDRAWN

Spit Jud Branzeu TIM Neuro

Timișoara, , Romania

Site Status RECRUITING

Klinicko bolnicki centar Dr Dragisa Misovic - Dedinje

Belgrade, , Serbia

Site Status RECRUITING

Klinicko bolnicki centar Zvezdara

Belgrade, , Serbia

Site Status RECRUITING

Opsta bolnica Medicinski sistem Beograd

Belgrade, , Serbia

Site Status RECRUITING

Vojnomedicinska akademija

Belgrade, , Serbia

Site Status RECRUITING

Univerzitetski Klinicki centar Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

Univerzitetski Klinicki centar Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

Univerzitetski Klinicki centar Nis

Niš, , Serbia

Site Status RECRUITING

Hsptl Sveti Vracevi

Novi Kneževac, , Serbia

Site Status RECRUITING

General Hospital Uzice

Užice, , Serbia

Site Status RECRUITING

Klinicko Bolnicki centar Zemun

Zemun, , Serbia

Site Status RECRUITING

Opsta bolnica Djordje Jovanovic Zrenjanin

Zrenjanin, , Serbia

Site Status RECRUITING

Acibadem Adana Hospital

Adana, , Turkey (Türkiye)

Site Status RECRUITING

Adana Baskent Hospital

Adana, , Turkey (Türkiye)

Site Status RECRUITING

Baskent University Ankara Hospital

Ankara, , Turkey (Türkiye)

Site Status RECRUITING

Bezmialem Vakif University Hospital

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

T.C. Ministry of Health Istanbul Haseki Training and Research Hospital

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Sancaktepe Sehit Prof.Dr. Ilhan Varank Training and Research Hospital

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Marmara University Pendik Training and Research Hospital

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Haydar Pasa Num. EAH

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Kocaeli University Research and Application Hospital

Kocaeli, , Turkey (Türkiye)

Site Status RECRUITING

T.C. Ministry of Health Kutahya Provincial Directorate of Health Kutahya University of Health Sciences Evliya Celebi Training and Research Hospital

Kütahya, , Turkey (Türkiye)

Site Status RECRUITING

Manisa Celal Bayar University Hafsa Sultan Hospital

Manisa, , Turkey (Türkiye)

Site Status RECRUITING

19 Mayis University Medical Faculty Hospital Health Application and Research Center

Samsun, , Turkey (Türkiye)

Site Status RECRUITING

Namik Kemal Uni Hospital

Tekirdağ, , Turkey (Türkiye)

Site Status RECRUITING

Zonguldak Bulent Ecevit University Health Practice and Research Hospital

Zonguldak, , Turkey (Türkiye)

Site Status RECRUITING

Communal noncommercial enterprise "First Cherkasy City Hospital"

Cherkasy, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

MS Diagnosis Treatment Center

Cherkasy, , Ukraine

Site Status RECRUITING

Chernihiv City Hospital 4

Chernihiv, , Ukraine

Site Status RECRUITING

Municipal Institution "Dnipropetrovsk Regional Rehabilitation Hospital" of Dnipropetrovsk Regional Council"

Dnipro, , Ukraine

Site Status RECRUITING

Ukrainian State Research Institute of Medico-Social Problems of Disability

Dnipro, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

"University Clinic" of Dnipro State Medical University, Department of Neurology

Dnipro, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Dnipro City Hospital 6

Dnipro, , Ukraine

Site Status RECRUITING

Communal Non-Commercial Medical Enterprise "O.T.Bohayevskyi Kremenchuk City Hospital #1

Kremenchuk, , Ukraine

Site Status RECRUITING

State Institution "National Research Center for Radiation Medicine of the National Academy of Medical Sciences of Ukraine

Kyiv, , Ukraine

Site Status RECRUITING

1 Private Clinic Medical Center

Kyiv, , Ukraine

Site Status RECRUITING

Dopomoga Plus medical center

Kyiv, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Volyn Reg Clin Hospital

Lutsk, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Lviv Regional Central Hospital

Lviv, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

5 City Clin Hospital

Lviv, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Communal institution "City Clinical Hospital №3" of Poltava City Council

Poltava, , Ukraine

Site Status RECRUITING

City Clinical Hospital 2

Rivne, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Sumy Reg Clinical Hospital

Sumy, , Ukraine

Site Status RECRUITING

Salutem

Vinnytsia, , Ukraine

Site Status RECRUITING

LCC Medical center INET-09

Zaporizhzhya, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Zaporizhia Med

Zaporizhzhya, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Zaporizhia Regional Clinic Hospital

Zaporizhzhya, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Zaporizhzhya City Hospital 6

Zaporizhzhya, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Zaporizhzhya Hospital 9

Zaporizhzhya, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Royal Devon Uni NHS

Exeter, , United Kingdom

Site Status RECRUITING

Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status RECRUITING

Countries

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United States Armenia Bosnia and Herzegovina Estonia India Peru Poland Romania Serbia Turkey (Türkiye) Ukraine United Kingdom

Central Contacts

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Andreas Muehler, MD

Role: CONTACT

+49 89 2080 477 00

Facility Contacts

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Todd Levine, Dr.

Role: primary

Alicia Cabrera, Dr.

Role: primary

Sonia Kalirao, Dr.

Role: primary

Angel Carrasco, Dr.

Role: primary

Diego Rielo, Dr.

Role: primary

James Winkley, Dr.

Role: primary

Deborah Green-LaRoche, Dr.

Role: primary

Yekaterina Hovhannisyan, Dr.

Role: primary

Nune Yeghiazaryan, Dr.

Role: primary

Sanja Grgic, Prof.

Role: primary

Muhamed Lepuzanovic, Dr.

Role: primary

Admir Mehicevic, Dr.

Role: primary

Enra Suljic, Dr.

Role: primary

Aida Sehanovic, Dr.

Role: primary

Katrin Gross-Paju, Dr.

Role: primary

Dheeraj Khurana, Dr.

Role: primary

Praveen Gupta, Dr.

Role: primary

Abdul Qavi, Dr.

Role: primary

Manjari Triphathi, Dr.

Role: primary

Debashish Chowdhury, Dr.

Role: primary

Dinesh Kumar, Dr.

Role: primary

Abhijeet Kohat, Dr.

Role: primary

Wenzel Duenas Pacheco, Dr.

Role: primary

Marek Smilowski, Dr.

Role: primary

Janusz Zbrojkiewicz, Dr.

Role: primary

Marcin Nastaj, Dr.

Role: primary

Konrad Rejdak, Prof

Role: primary

Magdalena Boczarska-Jedynak, Dr.

Role: primary

Adriana Chelminiak, Dr.

Role: primary

Jan Ilkowski, Dr.

Role: primary

Maciej Czarnecki, Dr.

Role: primary

Bartosz Otak, Dr.

Role: primary

Monika Adamczyk-Sowa, Prof.

Role: primary

Mirela Chiru, Dr.

Role: primary

Christina Panea, Dr.

Role: primary

Emilian S. Manescu, Dr.

Role: primary

Ana-Maria Ionescu, Dr.

Role: primary

Iuliu Trifan, Dr.

Role: primary

Catalin C. Mutu, Dr.

Role: primary

Mihaela Simu, Prof.

Role: primary

Dragana Kuljic Obradovic, Dr.

Role: primary

Vera Cvijanovic, Dr.

Role: primary

Miodrag Vujcic, Dr.

Role: primary

Evica Dincic, Dr.

Role: primary

Tatjana Boskovic Matic, Prof.

Role: primary

Svetlana Miletic Drakulic, Dr.

Role: primary

Slobodan Vojinovic, Prof.

Role: primary

Jovana Stijovic, Dr.

Role: primary

Mira Gavric Kezic, Dr.

Role: primary

Dusica Smiljanic-Miljkovic, Dr.

Role: primary

Julijana Filipov, Dr.

Role: primary

Cem Ortacbayram, Dr.

Role: primary

Basak Karakurum Goksel, Prof.

Role: primary

Munire Kilinc Toprak, Prof.

Role: primary

Gulsen Akman-Demir, Prof.

Role: primary

Belgin Balci, Prof.

Role: primary

Serkan Demir, Prof.

Role: primary

Gulin Sunter, Prof

Role: primary

Recai Türkoğlu, Prof.

Role: primary

Husnu Efendi, Prof.

Role: primary

Sibel Canbaz Kabay, Prof.

Role: primary

Hikmet Yilmaz, Prof.

Role: primary

Murat Terzi, Prof.

Role: primary

Aysun Ünal, Prof.

Role: primary

Bilge Piri Cinar, Prof.

Role: primary

Valentyna Drobotenko, Dr.

Role: primary

Larysa Kadina, Dr.

Role: primary

Roman Khaitov, Dr.

Role: primary

Larysa Zakharova, Dr.

Role: primary

Iryna Piskunova, Dr.

Role: primary

Olena Kolosynska, Prof.

Role: primary

Iryna Ihnatenko, Dr.

Role: primary

Svetlana Ivashchenko, Dr.

Role: primary

Oleksii Kmyta, Dr.

Role: primary

Sergii Moskovko, Dr.

Role: primary

Timothy Harrower, Dr.

Role: primary

Azza Ismail, Dr.

Role: primary

Other Identifiers

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P3-IMU-838-RMS-02

Identifier Type: -

Identifier Source: org_study_id

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