Study to Evaluate the Efficacy, Safety, and Tolerability of IMU-838 in Patients With Relapsing Multiple Sclerosis

NCT ID: NCT05134441

Last Updated: 2024-04-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1050 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-11-18

Study Completion Date

2032-09-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Multi-Center, Randomized, Double-Blinded Phase 3 Study to Evaluate the Efficacy, Safety, and Tolerability of IMU-838 versus Placebo in Adults with Relapsing Multiple Sclerosis (ENSURE-1)

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study will be a multicenter, randomized, double-blind, placebo-controlled study with a blinded Main Treatment Period (MT) and an Open Label Period (OLE) to evaluate the efficacy, safety, and tolerability of IMU-838 in adult patients with RMS. The study will consist of the following periods:

Screening Period: Approximately 28 days Main Treatment Period: Up to 72 weeks (approximately 15 months) Open Label Extension Period: Up to approximately 8 years

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Multiple Sclerosis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

IMU-838

IMU-838 (vidofludimus calcium), a small molecule inhibitor of DHODH.

Formulation:

Tablets with 15 or 30 mg IMU-838 for once daily oral intake in the morning.

Group Type EXPERIMENTAL

IMU-838 tablets

Intervention Type DRUG

Patients are randomized to IMU-838 or placebo in ratio 1:1

Placebo

Matching placebo, as described for the test product, identical number of tablets as given for IMU-838.

Group Type PLACEBO_COMPARATOR

Placebo matching IMU-838 tablets

Intervention Type DRUG

Patients are randomized to IMU-838 or placebo in ratio 1:1

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

IMU-838 tablets

Patients are randomized to IMU-838 or placebo in ratio 1:1

Intervention Type DRUG

Placebo matching IMU-838 tablets

Patients are randomized to IMU-838 or placebo in ratio 1:1

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

vidofludimus calcium Placebo matching vidofludimus calcium

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Male or female patient (age ≥18 to ≤55 years).
* Patients with an established diagnosis of MS according to 2017 McDonald Criteria.
* Patients with RMS comprising of relapsing remitting MS (RRMS) and active secondary progressive MS, both defined according to Lublin criteria 1996 and 2014.
* Active disease as defined by Lublin 2014 evidenced prior to Screening by:

1. At least 2 relapses in the last 24 months before randomization, or
2. At least 1 relapse in the last 12 months before randomization, or
3. A positive Gd+ MRI scan (brain and/or spine) in the last 12 months prior to randomization.
* Willingness and ability to comply with the protocol.
* Written informed consent given prior to any study-related procedure.

Exclusion Criteria

* Patients with non-active secondary progressive MS and primary progressive MS.
* Any disease other than MS that may better explain the signs and symptoms, including history of complete transverse myelitis.
* Clinical signs or presence of laboratory findings suggestive for neuromyelitis optica (NMO) spectrum disorders or myelin oligodendrocyte glycoprotein (MOG)-IgG-associated encephalomyelitis
* Any active and uncontrolled coexisting autoimmune disease, other than MS (except for type 1 diabetes mellitus and inflammatory bowel disease)
* Use of experimental/investigational drug (with the exception ofCOVID-19 vaccines approved by emergency use authorization) and/or participation in drug clinical studies within 6 months prior to Screening
* Previous or current use of MS treatments lifelong, or within a pre-specified time period.
* Use of the pre-specified concomitant medications.
* Clinically significantly abnormal and pre-specified lab values.
* History of chronic systemic infections within 6 months before the date of informed consent.
* Diagnosis or suspected liver function impairment, which may cause fluctuating liver function tests during this study.
* Known history of nephrolithiasis or underlying condition with a strong association of nephrolithiasis.
* History or clinical diagnosis of gout.
* History or presence of any major medical or psychiatric illness
* Substantial medical condition that could create undue risk to the patient, could affect adherence with the study protocol or could undesirably affect study outcomes
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Immunic AG

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Robert J. Fox, MD

Role: PRINCIPAL_INVESTIGATOR

Mellen Center for MS, Neurological Institute, Cleveland Clinic, Ohio

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Xenoscience, Inc., 21st Century Neurology

Phoenix, Arizona, United States

Site Status RECRUITING

Bradenton Research Center

Bradenton, Florida, United States

Site Status RECRUITING

Reliant Medical Research, LLC

Miami, Florida, United States

Site Status WITHDRAWN

Collier Neurologic Specialists

Naples, Florida, United States

Site Status RECRUITING

Neurology Associates of Ormond Beach

Ormond Beach, Florida, United States

Site Status RECRUITING

Consultants in Neurology, Ltd

Northbrook, Illinois, United States

Site Status RECRUITING

Klinika Mjekesore Nuova, Neurology Clinic

Tirana, , Albania

Site Status RECRUITING

Hygeia Hospital Tirana

Tirana, , Albania

Site Status RECRUITING

MHAT Puls AD

Blagoevgrad, , Bulgaria

Site Status RECRUITING

MHAT "Heart and Brain", EAD

Burgas, , Bulgaria

Site Status RECRUITING

MC Exacta Medica OOD

Pleven, , Bulgaria

Site Status RECRUITING

MHAT Avis Medica

Pleven, , Bulgaria

Site Status RECRUITING

UMHAT Dr.Georgi Stranski EAD

Pleven, , Bulgaria

Site Status RECRUITING

Heart and Brain University Hospital

Pleven, , Bulgaria

Site Status RECRUITING

MC Vita 1

Pleven, , Bulgaria

Site Status RECRUITING

UMHAT Sveti Georgi

Plovdiv, , Bulgaria

Site Status RECRUITING

UMHAT "Medica Ruse"

Rousse, , Bulgaria

Site Status RECRUITING

CCB Medical Institute Ministry of Interior

Sofia, , Bulgaria

Site Status RECRUITING

Diagnostic and Consultative Center Neoclinic

Sofia, , Bulgaria

Site Status RECRUITING

UMHAT "Sveti Ivan Rilski" EAD

Sofia, , Bulgaria

Site Status RECRUITING

MHATNP "Sveti Naum", EAD

Sofia, , Bulgaria

Site Status RECRUITING

MHATNPsy Sveti Naum EAD

Sofia, , Bulgaria

Site Status RECRUITING

UMHAT "Alexandrovska" EAD

Sofia, , Bulgaria

Site Status RECRUITING

UMHAT "Alexandrovska"

Sofia, , Bulgaria

Site Status RECRUITING

Military Medical Academy MHAT

Sofia, , Bulgaria

Site Status RECRUITING

MHAT "Sveta Sofia" EOOD

Sofia, , Bulgaria

Site Status RECRUITING

Military Medical Academy

Sofia, , Bulgaria

Site Status RECRUITING

UMHAT"Tsaritsa Yoanna -ISUL

Sofia, , Bulgaria

Site Status RECRUITING

UMHATEM N.Pirogov

Sofia, , Bulgaria

Site Status RECRUITING

UMHAT "Sveta Marina" EAD, First Clinic of Neurological Diseases

Varna, , Bulgaria

Site Status RECRUITING

Clínica Colsanitas S.A. Sede Clínica Universitaria Colombia

Bogotá, , Colombia

Site Status RECRUITING

Neurocountry Portoazul S.A.S.

Puerto Colombia, , Colombia

Site Status RECRUITING

1st Uni Clinic of Tbilisi LEPL

Tbilisi, , Georgia

Site Status RECRUITING

Eristavi Experimental Center

Tbilisi, , Georgia

Site Status RECRUITING

J.S.C. Curatio Clinic

Tbilisi, , Georgia

Site Status RECRUITING

Katsiashvili Emergency Center

Tbilisi, , Georgia

Site Status RECRUITING

Khechinashvili University Hospital

Tbilisi, , Georgia

Site Status RECRUITING

LTD Aversi Clinic

Tbilisi, , Georgia

Site Status RECRUITING

LTD New Hospitals

Tbilisi, , Georgia

Site Status RECRUITING

MediClub Georgia LLC

Tbilisi, , Georgia

Site Status RECRUITING

Pineo Medical Ecosystem LTD

Tbilisi, , Georgia

Site Status RECRUITING

Sarajishvili Neurology Institute

Tbilisi, , Georgia

Site Status RECRUITING

Athens Medical Center

Athens, , Greece

Site Status RECRUITING

Thessaloniki Hosptl

Thessaloniki, , Greece

Site Status RECRUITING

Kanoria Hospital & Research Centre

Gandhinagar, , India

Site Status RECRUITING

Mallikatte, Kadri

Mangalore, , India

Site Status RECRUITING

Jasleen Hospital

Nagpur, , India

Site Status RECRUITING

Sir Ganga Ram Hospital

New Delhi, , India

Site Status RECRUITING

Ruby Hospital

Pune, , India

Site Status RECRUITING

Indira Gandhi Medical College & Hospital

Shimla, , India

Site Status RECRUITING

Institute of Medical Sciences Banaras Hindu University,IMS BHU Varanasi

Varanasi, , India

Site Status RECRUITING

TSH Advanced Clinical Center

Amman, , Jordan

Site Status RECRUITING

Irbid Speciality Hospital

Irbid, , Jordan

Site Status RECRUITING

Hotel Dieu de France Hospital

Beirut, , Lebanon

Site Status RECRUITING

AUB Medical Center

Hamra, , Lebanon

Site Status RECRUITING

Lietuvos Sveikatos Mokslu Universitetas - Kauno Klinikos

Kaunas, , Lithuania

Site Status RECRUITING

Klaipedos Universitetine Ligonine - Klaipedos Issetines Sklerozes Centra

Klaipėda, , Lithuania

Site Status RECRUITING

Neurociencias Estudios Clínicos S.C

Culiacán, , Mexico

Site Status RECRUITING

Instituto Jalisciense de Metabolismo, SC

Guadalajara, , Mexico

Site Status RECRUITING

Grupo medico camino SC

Mexico City, , Mexico

Site Status RECRUITING

Cliditer S.A de C.V

Mexico City, , Mexico

Site Status RECRUITING

Unidad de Investigación en Salud de Chihuahua S.C.

Mexico City, , Mexico

Site Status RECRUITING

Clinstile SA de CV

Mexico City, , Mexico

Site Status RECRUITING

Centro de Morelia

Morelia, , Mexico

Site Status RECRUITING

Faicic de RL de CV

Veracruz, , Mexico

Site Status RECRUITING

Sociedad de Metabolismo y Corazon, S.C.

Veracruz, , Mexico

Site Status RECRUITING

Instititute of Emergency Medicine

Chisinau, , Moldova

Site Status RECRUITING

Medico-Sanitary Public Institution, Institute of Neurology and Neurosurgery "Diomid Gherman"

Chisinau, , Moldova

Site Status RECRUITING

The Diomid Gherman Institute of Neurology and Neurosurgery

Chisinau, , Moldova

Site Status RECRUITING

General Hospital Niksic

Nikšić, , Montenegro

Site Status RECRUITING

Clinical Center of Montenegro

Podgorica, , Montenegro

Site Status RECRUITING

Hospital "8 mi Septemvri"

Skopje, , North Macedonia

Site Status RECRUITING

University Clinic of Neurology

Skopje, , North Macedonia

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Chernihiv Regional Hospital

Chernivtsi, , Ukraine

Site Status RECRUITING

Regional Clinical Hospital

Ivano-Frankivsk, , Ukraine

Site Status RECRUITING

Neuro Global, LLC

Ivano-Frankivsk, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Khmelnytsky regional hospital of war veterans

Khmelnytskyi, , Ukraine

Site Status RECRUITING

Clinical Hospital #15 of the Podilskyi District of the Kyiv City

Kiev, , Ukraine

Site Status RECRUITING

"Medbud"

Kyiv, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

SMART medical center

Kyiv, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

Kyiv City Hospital 4

Kyiv, , Ukraine

Site Status RECRUITING

Odesa Regional Clinical Hospital, Department of Neurosurgery

Odesa, , Ukraine

Site Status RECRUITING

Medical and diagnostic center of a LLC "Medcontinent", neurology and rehabilitation center

Poltava, , Ukraine

Site Status RECRUITING

Ternopil Psycho-Neuro Hospital

Ternopil, , Ukraine

Site Status RECRUITING

Regional Clinical Center for Neurosurgery and Neurology

Uzhhorod, , Ukraine

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Albania Bulgaria Colombia Georgia Greece India Jordan Lebanon Lithuania Mexico Moldova Montenegro North Macedonia Spain Ukraine

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Andreas Muehler, MD

Role: CONTACT

+49 89 2080 477 00

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Stephen Flitman, Dr.

Role: primary

Eric Martin Folkens, Dr.

Role: primary

Matthew Baker, Dr.

Role: primary

James Scott, Dr.

Role: primary

Daniel Wynn, Dr.

Role: primary

Hajri Gerbi, Dr.

Role: primary

Erion Dushi, Dr.

Role: primary

Sasho Kastrev, Dr.

Role: primary

Ivan Dimitrov, Prof.

Role: primary

Albena Antimova, Dr.

Role: primary

Hristo Lilovski, Dr.

Role: primary

Maya Danovska, Dr.

Role: primary

Plamen Bozhinov, Dr.

Role: primary

Plamen Petkov, Dr.

Role: primary

Georgi Slavov, Prof.

Role: primary

Rositsa Krasteva, Dr.

Role: primary

Kosta Kostov, Dr.

Role: primary

Rosen Ikonomov, Dr.

Role: primary

Penko Shotekov, Prof.

Role: primary

Ivan Milanov, Prof.

Role: primary

Paraskeva Stamenova, Prof.

Role: primary

Ivaylo Tarnev, Prof.

Role: primary

Latchezar Traykov, Prof.

Role: primary

Radostina Dimova, Dr.

Role: primary

Emil Olevski, Dr.

Role: primary

Stratieva Stratina, Dr.

Role: primary

Evgenia Vasileva-Ruscheva, MD

Role: primary

Maria Dimitrova, Dr.

Role: primary

Ara Kaprelyan, MD

Role: primary

Carlos Navas, MD

Role: primary

Laureano Caparroso Diaz, MD

Role: primary

Maia Beridze, Prof.

Role: primary

Natia Zarkua, Dr.

Role: primary

Anna Gauarashvili, Dr.

Role: primary

Darejan Gugutsidze, Dr.

Role: primary

Marina Janelidze, Dr.

Role: primary

Maka Mania, Dr.

Role: primary

Temur Marghania, Dr.

Role: primary

Nana Guldedava, Dr.

Role: primary

Alexander Tsiskaridze, Dr.

Role: primary

Roman Shakarishvili, Dr.

Role: primary

Klimentini Karageorgiou, Prof.

Role: primary

Dimitrios Kazis, Prof.

Role: primary

Devasi Visana, Dr.

Role: primary

Shankara Nellikunja, Dr.

Role: primary

Sanjay Ramteke, Dr.

Role: primary

Laxmikant R. Singh Tomar, Dr.

Role: primary

Santosh Sontakke, Dr.

Role: primary

Sudhir Sharma, Dr.

Role: primary

Abhishek Phatakh, Dr.

Role: primary

Murad Rasheed, Dr.

Role: primary

Eyad Awad, Dr.

Role: primary

Halim Abboud, Dr.

Role: primary

Samia Khoury, Dr.

Role: primary

Renata Balnyte, Dr.

Role: primary

Lina Malciene, Dr.

Role: primary

Elmer G. Lopez Meza, Dr.

Role: primary

Jose L. Ruiz Sandoval, Dr.

Role: primary

Freddy Castro Farfan, Dr.

Role: primary

Minerva Lopez Ruiz

Role: primary

Alma Vigueras, Dr.

Role: primary

Sandra Quiñones Aguilar, Dr.

Role: primary

Guillermo Punzo-Bravo, Dr.

Role: primary

David Reyes Barrios, Dr.

Role: primary

Marco Santos Diaz, Dr.

Role: primary

Stanislav Groppa, Dr.

Role: primary

Olesea Odainic, Dr.

Role: primary

Mihail Gavriliuc, Dr.

Role: primary

Zlatana Perovic, MD

Role: primary

Ljijana Radulovic, MD

Role: primary

Tatjana Stoshevska Deleva, Dr.

Role: primary

Ivan Barbov, Dr.

Role: primary

Antonio Tallon, Dr.

Role: primary

Valeriy Pashkovskyy, MD

Role: primary

Galyna Chmyr, Dr.

Role: primary

Inna Kovalchuk, MD

Role: primary

Olga Kovalenko, MD

Role: primary

Tetiana Kobys, MD

Role: primary

Alla Goloborodko, MD

Role: primary

Nataliya Lytvynenko, MD

Role: primary

Svitlana Skhrobot, Dr.

Role: primary

Volodymyr Smolanka, MD

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

P3-IMU-838-RMS-01

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Extension Study of MT-1303
NCT01890655 COMPLETED PHASE2
Dose-finding Study of MT-1303
NCT01742052 COMPLETED PHASE2