Phase Ib Study to Evaluate MOR103 in Multiple Sclerosis

NCT ID: NCT01517282

Last Updated: 2014-11-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

32 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-01-31

Study Completion Date

2014-02-28

Brief Summary

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Multiple sclerosis (MS) is a chronic inflammatory disease associated with central nervous system (CNS) demyelination and subsequent axonal degeneration. Multiple sclerosis exhibits an unpredictable and variable clinical course.

Multiple sclerosis plaques contain numerous types of cells and infiltrating macrophages have been identified to contribute significantly to demyelination in both clinical MS and animal models of MS. Granulocyte-macrophage colony-stimulating factor (GM CSF) stimulates proliferation and activation of macrophages, monocytes, neutrophils, eosinophils, dendritic cells and microglia with subsequent induction of proinflammatory biomolecules.

Therefore blocking GM CSF activity might be a therapeutic approach for the treatment of MS.

Detailed Description

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Recent clinical studies demonstrated a possible dysregulation of the balance of pro and anti inflammatory lymphocytes, which may contribute to the pathogenesis of MS.

It was shown in animal models of EAE that during the disease effect or phase GM CSF sustained neuroinflammation via myeloid cells that infiltrate the CNS proving an essential role of GM CSF in encephalitogenicity.

Conditions

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Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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MOR103 0.5 mg/kg

6 doses of MOR103 0.5 mg/kg administered on Days 1 (Baseline), 15 (Visit 2), 29 (Visit 3), 43 (Visit 4), 57 (Visit 5), and 71 (Visit 6).

Group Type EXPERIMENTAL

MOR103

Intervention Type BIOLOGICAL

Anti-GM-CSF monoclonal antibody

MOR103 1.0 mg/kg

6 doses of MOR103 1.0 mg/kg administered on Days 1 (Baseline), 15 (Visit 2), 29 (Visit 3), 43 (Visit 4), 57 (Visit 5), and 71 (Visit 6).

Group Type EXPERIMENTAL

MOR103

Intervention Type BIOLOGICAL

Anti-GM-CSF monoclonal antibody

MOR103 2.0 mg/kg

6 doses of MOR103 2.0 mg/kg administered on Days 1 (Baseline), 15 (Visit 2), 29 (Visit 3), 43 (Visit 4), 57 (Visit 5), and 71 (Visit 6).

Group Type EXPERIMENTAL

MOR103

Intervention Type BIOLOGICAL

Anti-GM-CSF monoclonal antibody

Placebo

6 doses of placebo administered on Days 1 (Baseline), 15 (Visit 2), 29 (Visit 3), 43 (Visit 4), 57 (Visit 5), and 71 (Visit 6).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo to anti-GM-CSF monoclonal antibody

Interventions

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MOR103

Anti-GM-CSF monoclonal antibody

Intervention Type BIOLOGICAL

Placebo

Placebo to anti-GM-CSF monoclonal antibody

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

Outpatients with a diagnosis of RRMS or SPMS, who are currently not being treated and who have at least 1 of the following:

* At least 1 documented relapse within 1 year before Screening, or
* Two documented relapses within the past 2 years before Screening, or
* A new gadolinium (Gd)-enhancing lesion on magnetic resonance imaging (MRI) T1-weighted imaging within 1 year before Screening, or
* A new T2 lesion on MRI within 1 year before Screening. The patient must have 10 or less, Gd-enhancing lesions per T1-weighted MRI at Screening as assessed by a central reader.

The patient must be able and willing to ambulate, with an Expanded Disability Status Scale (EDSS) score of ≥ 2.0 and ≤ 6.5 at both the Screening Visit and the Baseline Visit

Exclusion Criteria

1. A patient with primary progressive MS (PPMS)
2. A patient who has previously received at any time any of the following

* B-cell or T-cell depleting therapies
* Cytotoxic agents, any immunosuppressive/immunomodulating agents
3. A patient who has not stabilized, in the opinion of the investigator
4. A patient with any medical condition or uncontrolled disease states other than MS requiring or likely to require systemic treatment with corticosteroids or other immune compromising agents
5. A patient with current or a history of major chronic inflammatory autoimmune diseases other than MS
6. A patient with any type of infection
7. Patients on chronic prophylactic or suppressive antibiotic, antifungal,or antiviral agents
8. A patient with a history of tuberculosis.
9. A patient with any signs of excretory hepatic or kidney dysfunction
10. A patient with a positive test for Hepatitis B or Hepatitis C
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MorphoSys AG

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Roman P Korolkiewicz, MD, PhD

Role: STUDY_DIRECTOR

MorphoSys AG

Locations

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Morphosys Investigative Site

Berlin, , Germany

Site Status

Morphosys Investigative Site

Gdansk, , Poland

Site Status

Morphosys Investigative Site

Poznan, , Poland

Site Status

Morhosys Investigative Site

Manchester, , United Kingdom

Site Status

MorphoSys Investigative Site

Nottingham, , United Kingdom

Site Status

Countries

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Germany Poland United Kingdom

Other Identifiers

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2011-001064-22

Identifier Type: -

Identifier Source: org_study_id