A Study to Evaluate Ocrelizumab Treatment in Participants With Progressive Multiple Sclerosis

NCT ID: NCT03523858

Last Updated: 2026-01-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

927 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-05-28

Study Completion Date

2026-11-12

Brief Summary

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This study is a prospective, multicenter, open-label, single-arm effectiveness and safety study in participants with progressive multiple sclerosis (PMS).

Detailed Description

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Conditions

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Progressive Multiple Sclerosis (PMS)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Ocrelizumab

Ocrelizumab will be administered via intravenous (IV) infusion.

Group Type EXPERIMENTAL

Ocrelizumab

Intervention Type DRUG

Ocrelizumab will be administered via intravenous (IV) infusion at an initial dose of two 300-mg infusions separated by 14 days (on Days 1 and 15), and then 600 mg at every subsequent dose every 24 weeks for the remainder of the study treatment period (approximately 192 weeks)

Interventions

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Ocrelizumab

Ocrelizumab will be administered via intravenous (IV) infusion at an initial dose of two 300-mg infusions separated by 14 days (on Days 1 and 15), and then 600 mg at every subsequent dose every 24 weeks for the remainder of the study treatment period (approximately 192 weeks)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Have a definite diagnosis of PMS (as per the revised McDonald 2010 criteria for PPMS or Lublin et al. 2014 criteria for PMS)
* EDSS (Expanded Disability Status Scale) \</ =6.5 at screening
* Have a documented evidence of disability progression independent of relapse at any point over the 2 years prior to the screening visit. In case relapse(s) have occurred in the last 2 years, disability progression will have to be considered as independent of relapse activity as per treating physician's judgment
* Fulfill at least one of the 21 criteria assessing the evidence of disability progression independent of relapse activity in the last 2 years using the pre-baseline disability progression rating system checklist
* Have experience of having used a smartphone and connecting a smartphone to Wi-Fi network providers
* For women of childbearing potential: agreement to remain abstinent or use acceptable contraceptive methods during the treatment period and for at least 6 months, or longer if the local label is more stringent after the last dose of study drug

Exclusion Criteria

* Relapsing-remitting multiple sclerosis (RRMS) at screening
* Inability to complete an MRI
* Gadolinium (Gd) intolerance
* Known presence of other neurological disorders

Exclusions Related to General Health:

* Pregnancy confirmed by positive serum β human chorionic gonadotropin (hCG) measured at screening
* Lactation
* Any concomitant disease that may require chronic treatment of systemic corticosteroids or immunosuppressants during the course of the study
* History or currently active primary or secondary immunodeficiency
* Lack of peripheral venous access
* Significant or uncontrolled somatic disease or any other significant disease that may preclude participant from participating in the study.
* Active infections must be treated and resolved prior to the first infusion of ocrelizumab
* Participants in a severely immunocompromised state until the condition resolves
* Participants with known active malignancies or being actively monitored for recurrence of malignancy
* Participants who have or have had confirmed progressive multifocal leukoencephalopathy (PML)

Exclusions Related to Laboratory Findings:

* Positive screening tests for hepatitis B
* CD4 count \<250/μL
* ANC \<1.0 × 103/μL
* AST/SGOT or ALT/SGPT ≥3.0 × ULN in combination with either an elevated total bilirubin (\>2 X ULN) or clinical jaundice

Exclusions Related to Medications:

* Hypersensitivity to ocrelizumab or to any of its excipients
* Previous treatment with ocrelizumab
* Previous treatment with B-cell targeted therapies (i.e., atacicept, tabalumab, belimumab, ofatumumab, or obinutuzumab). Note: previous treatment with rituximab is allowed as long as the last dose was administered more than 6 months before the ocrelizumab infusion AND if discontinuation was due to adverse events or immunogenicity AND if Bcell levels are above the lower limit of normal (LLN) prior to screening.
* Any previous treatment with alemtuzumab (Campath/Mabcampath/Lemtrada), total body irradiation, or bone marrow transplantation
* Previous treatment with natalizumab where PML has not been excluded according to specific algorithm
* Contraindications to or intolerance of oral or intravenous (IV) corticosteroids, including methylprednisolone administered IV, according to the country label
* Systemic corticosteroid therapy within 4 weeks prior to screening
* All vaccines should be given at least 6 weeks before the first infusion of ocrelizumab, unless the local regulations allow for a shorter interval. Live/live attenuated vaccines should be avoided during treatment and safety follow-up period until B cells are peripherally repleted
* Previous treatment with daclizumab, ozanimod or figolimod in the last 8 weeks
* Previous treatment with siponimod in the last 2 weeks
* Treatment with fampridine/dalfampridine (Fampyra)/Ampyra) or other symptomatic MS treatment unless on stable dose for ≥30 days prior to screening
* Previous treatment with natalizumab in the last 12 weeks.
* Previous treatment with teriflunomide in the last 12 weeks. This washout period can be shortened if an accelerated elimination procedure is implemented before screening visit. One of the following elimination procedures can be used:
* Cholestyramine 8 g administered 3 times daily for a period of at least 7 days (cholestyramine 4 g three times a day can be used, if cholestyramine 8 g three times a day is not well tolerated)
* Alternatively, 50 g of activated powdered charcoal is administered every 12 hours for a period of at least 7 days.
* Previous treatment with azathioprine, cyclophosphamide, mycophenolate mofetil or methotrexate in the last 12 weeks
* Treatment with any investigational agent within 24 weeks of screening (Visit 1) or five half-lives of the investigational drug (whichever is longer) or treatment with any experimental procedures for MS
* Previous treatment with mitoxantrone, cyclosporine or cladribine in the last 96 weeks
* Participants previously treated with teriflunomide within the last two years, unless measured plasma concentrations are less than 0.02 mg/l. If above or not known, an accelerated elimination procedure should be implemented before screening visit
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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MS Center of California

Laguna Hills, California, United States

Site Status

SC3 Research Group, Inc

Pasadena, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Yale University

North Haven, Connecticut, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dragonfly Research, LLC

Wellesley, Massachusetts, United States

Site Status

Wayne State University School of Medicine

Detroit, Michigan, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

The MS Center of Northeastern New York

Latham, New York, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic Mellen Center

Cleveland, Ohio, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Neurology Clinic PC

Cordova, Tennessee, United States

Site Status

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status

Lone Star Neurology of San Antonio

San Antonio, Texas, United States

Site Status

Swedish Multiple Sclerosis Center

Seattle, Washington, United States

Site Status

University Clinical Center of the Republic of Srpska

Banja Luka, , Bosnia and Herzegovina

Site Status

University Hospital Mostar

Mostar, , Bosnia and Herzegovina

Site Status

Clinical Center University of Sarajevo

Sarajevo, , Bosnia and Herzegovina

Site Status

University Clinical Center Tuzla

Tuzla, , Bosnia and Herzegovina

Site Status

Instituto de Neurologia de Curitiba

Curitiba, Paraná, Brazil

Site Status

Hospital Sao Lucas - PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital das Clínicas Faculdades Médicas de Ribeirão Preto

Ribeirão Preto, São Paulo, Brazil

Site Status

Hospital das Clinicas - FMUSP_X

São Paulo, São Paulo, Brazil

Site Status

Fraser Health Authority - Fraser Health Multiple Sclerosis

Burnaby, British Columbia, Canada

Site Status

University of British Columbia Hospital

Vancouver, British Columbia, Canada

Site Status

London Health Sciences Centre Uni Campus

London, Ontario, Canada

Site Status

St. Michael'S Hospital

Toronto, Ontario, Canada

Site Status

Recherche Sepmus Inc.

Greenfield Park, Quebec, Canada

Site Status

Hospital Notre-Dame du Centre Hospitalier de l'Universite de Montreal

Montreal, Quebec, Canada

Site Status

Saskatoon City Hospital

Saskatoon, Saskatchewan, Canada

Site Status

Organizacion Sanitas Internacional

Bogotá, , Colombia

Site Status

Fundacion Clinica Valle del Lili

Cali, , Colombia

Site Status

Hospital Clínica Biblica

San José, , Costa Rica

Site Status

Nemocnice Jihlava

Jihlava, , Czechia

Site Status

Fakultní Nemocnice Olomouc

Olomouc, , Czechia

Site Status

Fakultni nemocnice Ostrava

Ostrava-Poruba, , Czechia

Site Status

Vseobecna fakultni nemocnice v Praze

Prague, , Czechia

Site Status

Aarhus Universitetshospital

Aarhus N, , Denmark

Site Status

Rigshospitalet

Glostrup Municipality, , Denmark

Site Status

Hjerne- og nervesygdomme, Ambulatorium, Skleroseklinikken

Sønderborg, , Denmark

Site Status

Clinical Research Center-Alex university

Alexandria, , Egypt

Site Status

Neurology Department, Ain Shams University Hospitals

Cairo, , Egypt

Site Status

CHIC Cote Basque Bayonne

Bayonne, , France

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Groupe Hospitalier Pellegrin

Bordeaux, , France

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Hopital neurologique Pierre Wertheimer - CHU Lyon

Bron, , France

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CHU De Caen

Caen, , France

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Hopital Gabriel Montpied CHU de Clermont-Ferrand

Clermont-Ferrand, , France

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Hopital B Roger Salengro

Lille, , France

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CHU de la Timone - Hopital d Adultes

Marseille, , France

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Hopital Gui de Chauliac

Montpellier, , France

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CHRU Nancy

Nancy, , France

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Hopital Nord Laennec

Nantes, , France

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Hôpital Pasteur

Nice, , France

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GroupeHospitalo-Universitaire Caremeau

Nîmes, , France

Site Status

Centre Hospitalier Universitaire de Rennes

Rennes, , France

Site Status

CHU Amiens Hopital Sud

Salouël, , France

Site Status

Hopitaux Universitaires de Strasbourg

Strasbourg, , France

Site Status

Universitätsklinikum "Carl Gustav Carus", Zentrum für Klinische Neurowissenschaften

Dresden, , Germany

Site Status

Universitätsmedizin Greifswald

Greifswald, , Germany

Site Status

NeuroConcept AG C/O mind mvz GmbH

Stuttgart, , Germany

Site Status

NeuroPoint Gesellschaft fur vorbeugende Gesundheitspflege mbH

Ulm, , Germany

Site Status

Studienzentrum Nordwest Dr med Joachim Springub Herr Wolfgang Schwarz

Westerstede, , Germany

Site Status

Deutsche Klinik für Diagnostik

Wiesbaden, , Germany

Site Status

Nucare

Guatemala City, , Guatemala

Site Status

Semmelweis Egyetem AOK

Budapest, , Hungary

Site Status

VALEOMED Diagnosztikai Központ

Esztergom, , Hungary

Site Status

Jósa András Oktatókórház

Nyíregyháza, , Hungary

Site Status

Pécsi Tudományegyetem, Klinikai Központ Neurológiai Klinika

Pécs, , Hungary

Site Status

Cork University Hospital

Cork, , Ireland

Site Status

Beaumont Hospital

Dublin, , Ireland

Site Status

St Vincents University Hospital

Dublin, , Ireland

Site Status

Azienda Ospedaliero Universitaria Consorziale Policlinico di

Bari, Apulia, Italy

Site Status

A. O. U. Federico II

Napoli, Campania, Italy

Site Status

Università degli Studi della Campania Luigi Vanvitelli

Napoli, Campania, Italy

Site Status

Università degli studi della Campania Luigi Vanvitelli

Napoli, Campania, Italy

Site Status

Ospedale Cattinara

Trieste, Friuli Venezia Giulia, Italy

Site Status

Policlinico Tor Vergata Dip. Neuroscienze-Clinica Neurologica-UOSD Sclerosi Multipla

Rome, Lazio, Italy

Site Status

Policlinico Universitario A. Gemelli

Rome, Lazio, Italy

Site Status

A.O. Sant'Andrea

Rome, Lazio, Italy

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Azienda Ospedaliera Sant'Andrea

Rome, Lazio, Italy

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Irccs A.O.U.San Martino Ist

Genoa, Liguria, Italy

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IRCCS Ospedale San Raffaele

Milan, Lombardy, Italy

Site Status

Fond. Istituto Neurologico C.Besta

Milan, Lombardy, Italy

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IRCCS Istituto Neurologico C. Mondino?Dip. Neurologia Neuroriabilitazione S.S. Sclerosi Multipla

Pavia, Lombardy, Italy

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IRCCS Istituto Neurologico Neuromed

Pozzilli, Molise, Italy

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Azienda Sanitaria Ospedaliera S. Luigi Gonzaga

Orbassano, Piedmont, Italy

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AOU Città della Salute e della Scienza

Turin, Piedmont, Italy

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Ospedale Binaghi

Cagliari, Sardinia, Italy

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AOU Policlinico V. Emanuele - P.O G. Rodolico

Catania, Sicily, Italy

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AOUC Azienda Ospedaliero-Universitaria Careggi

Florence, Tuscany, Italy

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Policlinico G.B. Rossi

Verona, Veneto, Italy

Site Status

American University of Beirut - Medical Center

Beirut, , Lebanon

Site Status

Lebanese American University Medical Center- Rizk Hospial

Beirut, , Lebanon

Site Status

Grupo Medico de Investigacion Clinica Multidisciplinaria

Mexico City, Mexico CITY (federal District), Mexico

Site Status

Clinstile S.A de C.V.

Mexico City, Mexico CITY (federal District), Mexico

Site Status

Hospital General de Mexico

Mexico, Tlaxcala, Mexico

Site Status

Unidad de investigacion en salud (UIS)

Mexico City, , Mexico

Site Status

Centre Hospitalier Universitaire Hassan II

Fes, , Morocco

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Hopital Cheikh Zaid

Rabat, , Morocco

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Hopital Militaire d'Instruction Mohamed V

Rabat, , Morocco

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Amphia Ziekenhuis

Breda, , Netherlands

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Catharina ziekenhuis

Eindhoven, , Netherlands

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Maasstadziekenhuis

NL -rotterdam, , Netherlands

Site Status

Zuyderland Medisch Centrum - Sittard Geleen

Sittard-Geleen, , Netherlands

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Consultorios Médicos PaItilla

Panama City, , Panama

Site Status

Uniwersytecki Szpital Kliniczny w Bialymstoku

Bialystok, , Poland

Site Status

Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status

Centrum Neurologii Krzysztof Selmaj

Lodz, , Poland

Site Status

SP Swiecickiego UM Marcinkowskiego

Późna, , Poland

Site Status

Centrum Medyczne "MEDYK"

Rzeszów, , Poland

Site Status

Wojskowy Instytut Medyczny - Pa?Stwowy Instytut Badawczy

Warsaw, , Poland

Site Status

SPSK nr 1

Zabrze, , Poland

Site Status

Jusupovskaya Hospital

Moscow, Moscow Oblast, Russia

Site Status

Vladimirskiy Regional Scientific Research Inst.

Moscow, Moscow Oblast, Russia

Site Status

City Clinical Hospital #24

Moskva, Moscow Oblast, Russia

Site Status

National Center of Social Significant Disease

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Hospital Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Virgen de Arrixaca

Murcia, , Spain

Site Status

Hospital Universitario la Fe

Valencia, , Spain

Site Status

Cleveland Clinic Abu Dhabi

Abu Dhabi, , United Arab Emirates

Site Status

Rashid hospital

Dubai, , United Arab Emirates

Site Status

Countries

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United States Bosnia and Herzegovina Brazil Canada Colombia Costa Rica Czechia Denmark Egypt France Germany Guatemala Hungary Ireland Italy Lebanon Mexico Morocco Netherlands Panama Poland Russia Spain United Arab Emirates

References

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Kappos L, Yiu S, Dahlke F, Coetzee T, Cutter GR, Yuen S, Bonati U, Lublin FD. Composite Confirmed Disability Worsening/Progression Is a Useful Clinical Endpoint for Multiple Sclerosis Clinical Trials. Neurology. 2025 May 27;104(10):e213558. doi: 10.1212/WNL.0000000000213558. Epub 2025 Apr 21.

Reference Type DERIVED
PMID: 40258203 (View on PubMed)

Other Identifiers

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2017-001313-93

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-506429-13-00

Identifier Type: CTIS

Identifier Source: secondary_id

MN39159

Identifier Type: -

Identifier Source: org_study_id

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