A Study of the Efficacy and Safety of Ocrelizumab in Patients With Relapsing-Remitting Multiple Sclerosis

NCT ID: NCT00676715

Last Updated: 2024-12-31

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

220 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-07-17

Study Completion Date

2023-11-08

Brief Summary

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This is a phase II, multicenter, randomized, parallel-group, partially blinded, placebo and Avonex (interferon beta-1a) controlled dose finding study to evaluate the efficacy as measured by brain MRI lesions, and safety of 2 dose regimens of ocrelizumab in participants with Relapsing Remitting Multiple Sclerosis (RRMS).

Detailed Description

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Conditions

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Multiple Sclerosis, Relapsing-Remitting

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Placebo

Participants received two intravenous (IV) infusions of matching placebo separated by 14 days in Cycle 1, followed by two infusions of ocrelizumab 300 mg separated by 14 days in cycle 2. A single infusion of ocrelizumab 600 mg was administered on Day 1 of cycles 3 and 4. Each cycle was of 168 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo matching to ocrelizumab administered as IV infision in Cycle 1 Day 1.

Ocrelizumab 600 mg

Participants two IV infusions of ocrelizumab 300 mg separated by 14 days in Cycle 1, followed by an infusion of ocrelizumab 600 mg on Day 1 and an infusion of placebo on Day 15 of Cycle 2. A single infusion of ocrelizumab 600 mg was administered on Day 1 of Cycles 3 and 4. Each cycle was of 168 days.

Group Type EXPERIMENTAL

Ocrelizumab

Intervention Type DRUG

Ocrelizumab 300 mg was administered in cycle 1 followed by an infusion of ocrelizumab 600 mg on Day 1. A single infusion of ocrelizumab 600 mg was administered on Day 1 of cycles 3 and 4.

Ocrelizumab 1000 mg

Participants received two IV infusions of ocrelizumab 1000 mg separated by 14 days in Cycle 1, followed by an infusion of ocrelizumab 1000 mg on Day 1 and an infusion of placebo on Day 15 of Cycle 2. A single infusion of ocrelizumab 1000 mg was administered on Day 1 of Cycle 3 and a single infusion of ocrelizumab 600 mg was administered on Day 1 of Cycle 4. Each cycle was of 168 days.

Group Type EXPERIMENTAL

Ocrelizumab

Intervention Type DRUG

Ocrelizumab 300 mg was administered in cycle 1 followed by an infusion of ocrelizumab 600 mg on Day 1. A single infusion of ocrelizumab 600 mg was administered on Day 1 of cycles 3 and 4.

Avonex

Participants received weekly intramuscular injections of Avonex 30 microgram (mcg) in Cycle 1, followed by two infusions of OCR 300 mg separated by 14 days in Cycle 2. A single infusion of ocrelizumab 600 mg was administered on Day 1 of Cycles 3 and 4. Each cycle was of 168 days.

Group Type ACTIVE_COMPARATOR

Avonex

Intervention Type DRUG

Avonex was administered weekly intramuscular injections of 30 mcg in cycle 1 Day 1.

Interventions

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Placebo

Placebo matching to ocrelizumab administered as IV infision in Cycle 1 Day 1.

Intervention Type DRUG

Ocrelizumab

Ocrelizumab 300 mg was administered in cycle 1 followed by an infusion of ocrelizumab 600 mg on Day 1. A single infusion of ocrelizumab 600 mg was administered on Day 1 of cycles 3 and 4.

Intervention Type DRUG

Avonex

Avonex was administered weekly intramuscular injections of 30 mcg in cycle 1 Day 1.

Intervention Type DRUG

Other Intervention Names

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RO4964913 Interferon-beta-alpha1

Eligibility Criteria

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Inclusion Criteria

* Ability to provide written informed consent and to be compliant with the schedule of protocol assessments
* Relapsing-remitting multiple sclerosis (MS)
* Ages 18-55 years inclusive
* For sexually active female and male participants of reproductive potential, use of reliable means of contraception

Exclusion Criteria

* Secondary or primary progressive multiple sclerosis at screening
* Incompatibility with MRI
* Contra-indications to or intolerance of oral or IV corticosteroids
* Known presence of other neurologic disorders
* Pregnancy or lactation
* Lack of peripheral venous access
* History of severe allergic or anaphylactic reactions to humanized or murine monoclonal antibodies
* Significant, uncontrolled disease, such as cardiovascular, pulmonary, renal, hepatic, endocrine or gastrointestinal
* Congestive heart failure
* Known active bacterial, viral, fungal, mycobacterial infection or other infection or any major episode of infection requiring hospitalization or treatment with IV antibiotics within 4 weeks prior to screening or oral antibiotics within 2 weeks prior to screening
* History or known presence of recurrent or chronic infection
* History of cancer, including solid tumors and hematological malignancies (except basal cell, in situ squamous cell carcinomas of the skin, and in situ carcinoma of the cervix of the uterus that have been excised and resolved)
* History of alcohol or drug abuse within 24 weeks prior to randomization
* History of or currently active primary or secondary immunodeficiency
* History of coagulation disorders
* Treatment with any investigational agent within 4 weeks of screening
* Receipt of a live vaccine within 6 weeks prior to randomization
* Incompatibility with Avonex use
* Previous treatment with rituximab
* Previous treatment with lymphocyte-depleting therapies except mitoxantrone
* Treatment with lymphocyte trafficking blockers within 24 weeks prior to randomization
* Treatment with beta interferons, glatiramer acetate, IV immunoglobulin, plasmapheresis, or immunosuppressive therapies within 12 weeks prior to randomization
* Systemic corticosteroid therapy within 4 weeks prior to randomization
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Roche Pharma AG

INDUSTRY

Sponsor Role collaborator

Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Genentech, Inc.

Locations

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Phoenix Neurological Associates Ltd

Phoenix, Arizona, United States

Site Status

Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

East Bay Physicians Med Group;Sutter East Bay Med Foundation

Berkeley, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Advanced Neurology of Colorado, LLC

Fort Collins, Colorado, United States

Site Status

Bradenton Research Center

Bradenton, Florida, United States

Site Status

MS Center of Vero Beach

Vero Beach, Florida, United States

Site Status

Shepherd Center; Multiple Sclerosis Center

Atlanta, Georgia, United States

Site Status

University of Chicago; Neurology

Chicago, Illinois, United States

Site Status

Kansas University Medical Center

Kansas City, Kansas, United States

Site Status

John Hopkins University

Baltimore, Maryland, United States

Site Status

Michigan Institute for Neurological Disorders

Farmington Hills, Michigan, United States

Site Status

Dartmouth-Hitchcock Medical Center; Dept of Neurology

Lebanon, New Hampshire, United States

Site Status

Columbia University Medical Center; The Neurological Institute of New York

New York, New York, United States

Site Status

Island Neurological Associates, P.C.

Plainview, New York, United States

Site Status

Suny At Stony Brook; Department Of Neurology

Stony Brook, New York, United States

Site Status

The Neurological Institute PA

Charlotte, North Carolina, United States

Site Status

Clinical Research of Winston Salem

Winston-Salem, North Carolina, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Ohio State University Med Ctr; MS Center

Columbus, Ohio, United States

Site Status

Legacy Health System; Clinical Research & Tech Ctr

Tualatin, Oregon, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Integra Clinical Research, Llc

San Antonio, Texas, United States

Site Status

Fletcher Allen Health Care/University of Vermont

Burlington, Vermont, United States

Site Status

University of Virginia - Fontain Research Park

Charlottesville, Virginia, United States

Site Status

UZ Antwerpen

Edegem, , Belgium

Site Status

First MHAT; Clinic of Neurology

Sofia, , Bulgaria

Site Status

Shat of Cardiovascular Diseases; Clinic of Neurology

Sofia, , Bulgaria

Site Status

ACIBADEM CITY CLINIC TOKUDA HOSPITAL EAD; Clinic of Neurology and Sleep Medicine

Sofia, , Bulgaria

Site Status

UMHAT Tzaritza Yoanna Sofia; CLINIC OF NEUROLOGY

Sofia, , Bulgaria

Site Status

CCB Medical institute, Ministry of Interior Sofia; CLINIC OF NEUROLOGY

Sofia, , Bulgaria

Site Status

Military Medical Academy; Neurology

Sofia, , Bulgaria

Site Status

Uni of British Columbia Hospital; Ms Clinical Research Group

Vancouver, British Columbia, Canada

Site Status

St. Michael'S Hospital

Toronto, Ontario, Canada

Site Status

McGill University; Montreal Neurological Institute; Neurological and Psychiatric

Montreal, Quebec, Canada

Site Status

Fakultni Nemocnice Ostrava; Klinika hematoonkologie FNO a LF OU

Ostrava, , Czechia

Site Status

Krajska Nemocnice Pardubice Neurologicka Klinika

Pardubice, , Czechia

Site Status

Fakultni nemocnice Motol; Neurologicka klinika

Prague, , Czechia

Site Status

Nemocnice Teplice; Neurologicke Oddeleni - Ms Centrum

Teplice, , Czechia

Site Status

Aarhus Universitetshospital; Neurologisk Afd. F, Skleroseklinikken

Aarhus N, , Denmark

Site Status

Hopital Pellegrin-CHU de Bordeaux; Service de Neurologie

Bordeaux, , France

Site Status

CHU De Caen; Service De Neurologie Dejerine

Caen, , France

Site Status

Hopital Gabriel Montpied CHU de Clermont-Ferrand; Service de Neurologie B

Clermont-Ferrand, , France

Site Status

CHU De Nimes, Hopital Caremeau; Service De Neurologie Du Prof. Pierre Labauge

Nîmes, , France

Site Status

St. Joseph-Krankenhaus

Berlin, , Germany

Site Status

Jüdisches Krankenhaus Berlin; Abteilung fur Neurologie

Berlin, , Germany

Site Status

Asklepios Klinik Nord-Heidberg; Neurologie

Hamburg, , Germany

Site Status

Universitatsklinikum Marburg; Zentrum für Nervenheilkunde, Klinik für Psychiatrie+Psychotherapie

Marburg, , Germany

Site Status

Ospedale S.Andrea-Universita di Roma; Centro Sclerosi Multipla

Rome, Lazio, Italy

Site Status

Hospital CIMA, Sta. Engracia

Monterrey, Nuevo León, Mexico

Site Status

Instituto Biomedico De Investigacion A.C.

Aguascalientes, , Mexico

Site Status

Unidad de Investigacion CIMA SC

Chihuahua City, , Mexico

Site Status

Hospital Cima Chihauhau

Chihuahua City, , Mexico

Site Status

Spitalul Clinic Colentina; Clinica de Neurologie

Bucharest, , Romania

Site Status

Spitalul Clinic Judetean de Urgenta Targu Mures; Clinica Neurologie

Târgu Mureş, , Romania

Site Status

Central Clinical Hospital #2 N.A. Semashko OAO RJHD

Moskva, Moscow Oblast, Russia

Site Status

Municipal City Hospital #33; Neurology

Nizhny Novgorod, Niznij Novgorod, Russia

Site Status

SHI Sverdlovsk Regional Clinical Hospital #1;Neurology

Yekaterinburg, Sverdlovsk Oblast, Russia

Site Status

LLC Research Medical Complex Vashe Zdorovie

Kazan', Tatarstan Republic, Russia

Site Status

Regional Multiple Sclerosis Centre b/o CC ECM Neftyanik; Neurology

Tyumen, Tyumen Oblast, Russia

Site Status

MRC for Oncology and Neurology; Neurology

Novosibirsk, , Russia

Site Status

Clinical Center of Serbia; Institute of Neurology

Belgrade, , Serbia

Site Status

Clinical Center Nis; Clinic for Mental Health

Niš, , Serbia

Site Status

Clinic of Neurology

Nova Sad, , Serbia

Site Status

Fakultna Nemocnica F. D. Roosevelta; Ii. Neurologicka Klinika Szu

Banská Bystrica, , Slovakia

Site Status

Fakultna Nemocnica, Pracovisko Stare Mesto; Neurology

Bratislava, , Slovakia

Site Status

Fakultna Nemocnica Paterua, Pracovisko Trieda Snp1 Kosice; Neurologicka Klinika

Košice, , Slovakia

Site Status

Fakultna Nemocnica Nitra; Neurologicka Klinika

Nitra, , Slovakia

Site Status

Nemocnica s Poliklinikou Spisska Nova Ves, a.s.

Spišská Nová Ves, , Slovakia

Site Status

Hospital Universitari Vall d'Hebron; Servicio de Neumo-Inmunologia

Barcelona, , Spain

Site Status

Hospital Clinic i Provincial; Servicio de Neurologia

Barcelona, , Spain

Site Status

Hospital Ramon y Cajal; Servicio de Neurologia

Madrid, , Spain

Site Status

Hospital Regional Universitario Carlos Haya; Servicio de Neurologia

Málaga, , Spain

Site Status

Hospital Universitario Virgen Macarena; Servicio de Neurologia

Seville, , Spain

Site Status

Hospital Universitario La Fe; Unidad de Esclerosis Multiple

Valencia, , Spain

Site Status

Universitätsspital Basel; Neurologie

Basel, , Switzerland

Site Status

Ams of Ukraine; Inst. of Neurology, Psychiatry & Narcology

Kharkiv, , Ukraine

Site Status

City Clin.Hosp #4; Dept. of Neurology

Kyiv, , Ukraine

Site Status

Ukr.State Inst. of Med and Social Probl. Disab; Dept of Neur and Border states

Propetrovsk, , Ukraine

Site Status

Vin.Reg.Psych.Hosp.N.A Yuschenko O.I., Vnmu N.A. Pyrogov; Department of Nervous Diseases

Vinnytsia, , Ukraine

Site Status

Walton Centre NHS Foundation Trust, Neuroscience Research Centre; CLINICAL TRIALS UNIT

Liverpool, , United Kingdom

Site Status

Uni Hospital Queens Medical Centre; Neurology

Nottingham, , United Kingdom

Site Status

Royal Hallamshire Hospital; Neurology

Sheffield, , United Kingdom

Site Status

Countries

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Finland Netherlands United States Belgium Bulgaria Canada Czechia Denmark France Germany Italy Mexico Romania Russia Serbia Slovakia Spain Switzerland Ukraine United Kingdom

References

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Kappos L, Li D, Calabresi PA, O'Connor P, Bar-Or A, Barkhof F, Yin M, Leppert D, Glanzman R, Tinbergen J, Hauser SL. Ocrelizumab in relapsing-remitting multiple sclerosis: a phase 2, randomised, placebo-controlled, multicentre trial. Lancet. 2011 Nov 19;378(9805):1779-87. doi: 10.1016/S0140-6736(11)61649-8. Epub 2011 Oct 31.

Reference Type DERIVED
PMID: 22047971 (View on PubMed)

Other Identifiers

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2007-006338-32

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

WA21493

Identifier Type: OTHER

Identifier Source: secondary_id

ACT4422g

Identifier Type: -

Identifier Source: org_study_id