Nebulized Bacteriophage Therapy in Cystic Fibrosis Patients With Chronic Pseudomonas Aeruginosa Pulmonary Infection

NCT ID: NCT05010577

Last Updated: 2025-07-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

43 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-06-21

Study Completion Date

2024-03-10

Brief Summary

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This is a Phase 1b/2a study with the primary objective to determine if BX004-A is safe and tolerable. Exploratory objectives include whether BX004-A reduces sputum Pseudomonas aeruginosa (PsA) bacterial load in CF subjects with chronic PsA pulmonary infection.

Detailed Description

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This is a randomized, double-blind, placebo-controlled, multicenter study to evaluate the safety and tolerability of BX004-A in CF subjects with chronic PsA pulmonary infection. The study is divided into two parts, a single-ascending and multiple-dose phase (Part 1) and a multiple dose phase (Part 2). Subjects in both parts will be included in a 6-month safety follow-up. A Data Safety Monitoring Board will monitor safety in both parts. The purpose of the study is to evaluate safety and tolerability of BX004-A, and whether BX004-A reduces the PsA burden in the sputum of CF subjects with chronic PsA pulmonary infection. Clinically stable CF subjects with a confirmed diagnosis of CF and chronic PsA pulmonary infection will be enrolled.

Conditions

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Chronic Pseudomonas Aeruginosa Infection Cystic Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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BX004-A

Participants will be randomized to receive standard dose of nebulized bacteriophage

Group Type EXPERIMENTAL

BX004-A

Intervention Type DRUG

Combination of nebulized bacteriophages targeting Pseudomonas aeruginosa

Placebo

Participants will be randomized to receive nebulized placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Nebulized placebo

Interventions

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BX004-A

Combination of nebulized bacteriophages targeting Pseudomonas aeruginosa

Intervention Type DRUG

Placebo

Nebulized placebo

Intervention Type DRUG

Other Intervention Names

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Bacteriophage Vehicle buffer

Eligibility Criteria

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Inclusion Criteria

* Cystic fibrosis patients with chronic Pseudomonas aeruginosa pulmonary infection receiving standard of care CF medications
* Age ≥ 18 years
* FEV1 ≥ 40% predicted
* Clinically stable lung disease
* Willing and able to provide adequate sputum samples, using any method (spontaneously expectorated, induced, from home or clinic) at designated study visits.

Exclusion Criteria

* Known hypersensitivity to bacteriophages or excipients in the formulation.
* Receipt of prior bacteriophage therapy within the 6 months prior to Screening
* Recovery of Burkholderia species from respiratory tract within 1 year prior to screening
* Currently receiving treatment for allergic bronchopulmonary aspergillosis
* Currently receiving treatment for active infection with non-tuberculous mycobacteria
* History of severe neutropenia
* History of lung transplant
* History of solid organ transplant
* Acquired or primary immunodeficiency syndrome
* Initiation or change in CF modulator therapy less than 3 months prior to screening
* Pregnant or breastfeeding female
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BiomX, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Urania Rappo, MD

Role: STUDY_DIRECTOR

BiomX, Inc.

Locations

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The University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Providence Alaska Medical Center

Anchorage, Alaska, United States

Site Status

University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

Site Status

Yale University

New Haven, Connecticut, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Joe DiMaggio Children's Hospital

Hollywood, Florida, United States

Site Status

Central Florida Pulmonary Group

Orlando, Florida, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

New York Medical College

Valhalla, New York, United States

Site Status

Cincinnati Children's Hospital

Cincinnati, Ohio, United States

Site Status

University Hospitals Rainbow Babies and Children's Hospital

Cleveland, Ohio, United States

Site Status

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

Penn State Health Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Baylor College of Medicine, Texas Children Clinic

Houston, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

University Hospital in Motol

Prague, , Czechia

Site Status

Rambam Health Care Campus (RHCC) - Ruth Rappaport Children's Hospital

Haifa, , Israel

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Hadassah University Medical Center

Jerusalem, , Israel

Site Status

Schneider Children's Medical Center of Israel

Petach Tikvah, , Israel

Site Status

The Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Amsterdam Medical Center

Amsterdam, , Netherlands

Site Status

University Medical Center Utrecht

Utrecht, , Netherlands

Site Status

Hospital Clinico Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

Site Status

Vall d'Hebron Barcelona Hospital Campus

Barcelona, , Spain

Site Status

Countries

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United States Czechia Israel Netherlands Spain

Other Identifiers

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BMX-04-001

Identifier Type: -

Identifier Source: org_study_id

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