MP-376 (Aeroquin™, Levofloxacin for Inhalation) in Patients With Cystic Fibrosis

NCT ID: NCT01180634

Last Updated: 2024-12-18

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

330 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-11-04

Study Completion Date

2012-05-07

Brief Summary

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Patients with cystic fibrosis (CF) suffer from chronic infections of the lower respiratory tract that can be caused by one or multiple bacteria, including Pseudomonas aeruginosa, which has been particularly problematic to eradicate and been implicated as the major cause of morbidity and mortality in CF patients. Aerosol delivery of antibiotics directly to the lung increases the local concentrations of antibiotic at the site of infection resulting in improved antimicrobial effects compared to systemic administration. Decreased efficacy, intolerance and high treatment burden with currently available therapies indicate a need for additional therapies. MP-376 (Aeroquin™) is a novel formulation of the fluoroquinolone levofloxacin that has been optimized for aerosol delivery. Preclinical and clinical studies conducted to date show that aerosol doses of MP-376 are safe and well tolerated, exert an antimicrobial effect, improve lung function and reduce the need for other anti-pseudomonal antibiotics. High concentrations of levofloxacin in the lung delivered as MP-376 are active against CF pathogens including those with high minimum inhibitory concentration (MIC) levels to aminoglycosides such as tobramycin (TOBI®) and other inhaled antimicrobial agents. Inhaled MP-376 can be delivered rapidly and efficiently using a customized PARI investigational configuration of the eFlow® nebulizer system.

Detailed Description

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This trial will be a double-blind, placebo-controlled study to evaluate the efficacy and safety of levofloxacin administered as MP-376 given for 28 days by the aerosol route to CF patients.

Study with completed results acquired from Horizon in 2024.

Conditions

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Cystic Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Aeroquin 240 mg

Participants received 240 milligrams (mg) of Aeroquin by inhalation route twice daily (BID) for a period of 28 days.

Group Type EXPERIMENTAL

Aeroquin

Intervention Type DRUG

Inhalation Solution

Placebo

Participants placebo matching Aeroquin by inhalation route, BID for a period of 28 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Inhalation Solution

Interventions

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Aeroquin

Inhalation Solution

Intervention Type DRUG

Placebo

Inhalation Solution

Intervention Type DRUG

Other Intervention Names

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MP-376, Levofloxacin Inhalation solution 240 mg

Eligibility Criteria

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Inclusion Criteria

* \>/= 12 years of age
* Confirmed Diagnosis of Cystic Fibrosis
* Positive sputum culture for P. aeruginosa at screening and within the past 12 months
* Patients are able to elicit an FEV1 \>/= 25% but \</= 85% of predicted value at screening
* Have received at least 3 courses of inhaled antimicrobials over the preceding 12 months
* Clinically stable with no changes in health status within the last 28 days
* Able to reproducibly produce sputum and perform spirometry

Exclusion Criteria

* Use of any nebulized or systemic antibiotics within 28 days prior to baseline
* History of hypersensitivity to fluoroquinolones or intolerance with aerosol medication
* Evidence of respiratory infections within 14 days prior to dosing
* CrCl \< 20ml/min or \< 20ml/min/1.73 m2 at Screening
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Forest Laboratories

INDUSTRY

Sponsor Role collaborator

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Mobile, Alabama, United States

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Anchorage, Alaska, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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La Jolla, California, United States

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Long Beach, California, United States

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Childrens Hospital

Los Angeles, California, United States

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Los Angeles, California, United States

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Oakland, California, United States

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Orange, California, United States

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Palo Alto, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Hartford, Connecticut, United States

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Wilmington, Delaware, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Boise, Idaho, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Glenview, Illinois, United States

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Niles, Illinois, United States

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Indianapolis, Indiana, United States

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Wichita, Kansas, United States

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Lexington, Kentucky, United States

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Louisville, Kentucky, United States

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New Orleans, Louisiana, United States

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Portland, Maine, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Worcester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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Grand Rapids, Michigan, United States

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Minneapolis, Minnesota, United States

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Jackson, Mississippi, United States

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Columbia, Missouri, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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Manchester, New Hampshire, United States

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Livingston, New Jersey, United States

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Long Branch, New Jersey, United States

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Morristown, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albany, New York, United States

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New York, New York, United States

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New York, New York, United States

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New York, New York, United States

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Syracuse, New York, United States

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Valhalla, New York, United States

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Chapel Hill, North Carolina, United States

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Akron, Ohio, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Toledo, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Hershey, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Sioux Falls, South Dakota, United States

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Memphis, Tennessee, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Tyler, Texas, United States

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Salt Lake City, Utah, United States

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Colchester, Vermont, United States

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Charlottesville, Virginia, United States

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Norfolk, Virginia, United States

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Portsmouth, Virginia, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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Seattle, Washington, United States

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Morgantown, West Virginia, United States

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Milwaukee, Wisconsin, United States

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John Hunter Hospital

New South Wales, New South Wales, Australia

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Westmead Chilren's Hospital

Westmead, New South Wales, Australia

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Westmead Hospital

Westmead, New South Wales, Australia

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Mater Miscericordiae Hospital

Brisbane, Queensland, Australia

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Brisbane, Queensland, Australia

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Royal Adelaide Hospital

Adelaide, South Australia, Australia

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Royal Children's Hospital

Melbourne, Victoria, Australia

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The Alfred Hospital

Melbourne, Victoria, Australia

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Monash Medical Center

Melbourne, , Australia

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Hamilton, Ontario, Canada

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Kingston, Ontario, Canada

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Ottawa, Ontario, Canada

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Rambam Medical Center

Haifa, , Israel

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Hadassah Medical Center Mount Scopus

Jerusalem, , Israel

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Schneider Childrens Medical Center of Israel

Petah Tikva, , Israel

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Sheba Medical Center

Ramat Gan, , Israel

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Auckland Hospital

Auckland, , New Zealand

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Countries

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United States Australia Canada Israel New Zealand

Other Identifiers

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2010-019515-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

Mpex-207

Identifier Type: -

Identifier Source: org_study_id