Ciprofloxacin Dry Powder for Inhalation (DPI) in Non-cystic Fibrosis Bronchiectasis (Non-CF BE)

NCT ID: NCT02106832

Last Updated: 2017-10-02

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

521 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-04-30

Study Completion Date

2016-10-19

Brief Summary

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The purpose of this study is to evaluate if the time to first pulmonary exacerbation of bronchiectasis or its frequency can be prolonged by inhalation of ciprofloxacin for 28 days every other 28 days or for 14 days every other 14 days over 48 weeks.

Detailed Description

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Number of participants with Adverse events will be covered in Adverse Events section.

Conditions

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Bronchiectasis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ciprofloxacin DPI 28 Days on/off (Cipro 28)

Subjects received ciprofloxacin (BAYQ3939) 32.5 milligram (mg) corresponding to 50 mg dry powder for inhalation (DPI) administered twice daily (BID) (every 12 hours); a treatment cycle consisted of a 28-day on-treatment phase followed by a 28-day off-treatment phase (48 weeks treatment phase = 6 active cycles).

Group Type EXPERIMENTAL

Ciprofloxacin (BAYQ3939) dry powder for inhalation

Intervention Type DRUG

Ciprofloxacin dry powder for inhalation (DPI) 32.5 mg inhaled twice daily in cycles of 28 days on-treatment and 28 days off-treatment.

Ciprofloxacin DPI 14 Days on/off (Cipro 14)

Subjects received ciprofloxacin 32.5 mg corresponding to 50 mg DPI administered BID (every 12 hours); a treatment cycle consisted of a 14-day on-treatment phase followed by a 14-day off-treatment phase (48 weeks treatment phase = 12 active cycles).

Group Type EXPERIMENTAL

Ciprofloxacin (BAYQ3939) dry powder for inhalation

Intervention Type DRUG

Ciprofloxacin DPI 32.5 mg inhaled twice daily in cycles of 14 days on-treatment and 14 days off-treatment.

Placebo 28 Days on/off (Placebo 28)

Subjects received placebo matched to ciprofloxacin 32.5 mg powder (containing 40 mg dry powder) administered BID (every 12 hours); a treatment cycle consisted of a 28-day on-treatment phase followed by a 28-day off-treatment phase (48 weeks treatment phase = 6 cycles).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo inhaled twice daily intermittently for 28 days on / 28 days off

Placebo 14 Days on/off (Placebo 14)

Subjects received placebo matched to ciprofloxacin 32.5 mg powder (containing 40 mg dry powder) administered BID (every 12 hours); a treatment cycle consisted of a 14-day on-treatment phase followed by a 14-day off-treatment phase (48 weeks treatment phase = 12 cycles).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo inhaled twice daily intermittently for 14 days on / 14 days off

Interventions

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Ciprofloxacin (BAYQ3939) dry powder for inhalation

Ciprofloxacin dry powder for inhalation (DPI) 32.5 mg inhaled twice daily in cycles of 28 days on-treatment and 28 days off-treatment.

Intervention Type DRUG

Ciprofloxacin (BAYQ3939) dry powder for inhalation

Ciprofloxacin DPI 32.5 mg inhaled twice daily in cycles of 14 days on-treatment and 14 days off-treatment.

Intervention Type DRUG

Placebo

Matching placebo inhaled twice daily intermittently for 28 days on / 28 days off

Intervention Type DRUG

Placebo

Matching placebo inhaled twice daily intermittently for 14 days on / 14 days off

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients with a proven and documented diagnosis of non CF idiopathic or post infectious bronchiectasis
* Stable pulmonary status and stable regimen of standard treatment at least for the past 4 weeks

Exclusion Criteria

* Forced expiratory volume in 1 second (FEV1) \<30% or \>90% predicted
* Active allergic bronchopulmonary aspergillosis
* Active and actively treated non tuberculosis mycobacterial (NTM) infection or tuberculosis
* Primary diagnosis of Chronic obstructive pulmonary disease (COPD)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis

INDUSTRY

Sponsor Role collaborator

Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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Peoria, Arizona, United States

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Fountain Valley, California, United States

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La Jolla, California, United States

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Long Beach, California, United States

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Newport Beach, California, United States

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San Diego, California, United States

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Kissimmee, Florida, United States

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Miami, Florida, United States

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Sarasota, Florida, United States

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Tampa, Florida, United States

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Decatur, Georgia, United States

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Skokie, Illinois, United States

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Olathe, Kansas, United States

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Rochester, Minnesota, United States

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Brooklyn, New York, United States

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Mineola, New York, United States

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Asheville, North Carolina, United States

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Portland, Oregon, United States

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Doylestown, Pennsylvania, United States

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Greenville, South Carolina, United States

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Edinburg, Texas, United States

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Tyler, Texas, United States

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Buenos Aires, Ciudad Auton. de Buenos Aires, Argentina

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Capital Federal, Ciudad Auton. de Buenos Aires, Argentina

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Godoy Cruz, Mendoza Province, Argentina

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Córdoba, , Argentina

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Vicente López, , Argentina

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Kogarah, New South Wales, Australia

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New Lambton Heights, New South Wales, Australia

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Adelaide, South Australia, Australia

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Adelaide, South Australia, Australia

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Parkville, Victoria, Australia

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Murdoch, Western Australia, Australia

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Perth, Western Australia, Australia

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Graz, , Austria

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Salzburg, , Austria

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Belo Horizonte, Minas Gerais, Brazil

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Recife, Pernambuco, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, São Paulo, Brazil

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Porto Alegre, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Gabrovo, , Bulgaria

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Kozloduy, , Bulgaria

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Lovech, , Bulgaria

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Razgrad, , Bulgaria

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Rousse, , Bulgaria

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Sevlievo, , Bulgaria

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Sliven, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Stara Zagora, , Bulgaria

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Fuzhou, Fujian, China

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Guangzhou, Guangdong, China

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Hohehot, Inner Mongolia, China

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Suzhou, Jiangsu, China

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Wuxi, Jiangsu, China

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Nanchang, Jiangxi, China

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Shenyang, Liaoning, China

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Yinchuan, Ningxia, China

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Chengdu, Sichuan, China

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Beijing, , China

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Beijing, , China

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Chongqing, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Brno, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Treuenbrietzen, Brandenburg, Germany

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Frankfurt am Main, Hesse, Germany

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Neu-Isenburg, Hesse, Germany

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Hanover, Lower Saxony, Germany

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Hanover, Lower Saxony, Germany

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Gelsenkirchen, North Rhine-Westphalia, Germany

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Leipzig, Saxony, Germany

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Bad Berka, Thuringia, Germany

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Jena, Thuringia, Germany

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Berlin, , Germany

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Berlin, , Germany

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Hamburg, , Germany

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Hong Kong, , Hong Kong

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Kowloon, , Hong Kong

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New Territories, , Hong Kong

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Shatin, , Hong Kong

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Daugavpils, , Latvia

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Daugavpils, , Latvia

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Jūrmala, , Latvia

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Krāslava, , Latvia

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Riga, , Latvia

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Riga, , Latvia

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Riga, , Latvia

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Riga, , Latvia

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Talsi, , Latvia

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Klaipėda, , Lithuania

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Vilnius, , Lithuania

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Alkmaar, , Netherlands

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Assen, , Netherlands

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Groningen, , Netherlands

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Helmond, , Netherlands

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Maastricht, , Netherlands

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Sittard-Geleen, , Netherlands

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Veldhoven, , Netherlands

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City of San Fernando, , Philippines

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Manila, , Philippines

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Manila, , Philippines

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Quezon City, , Philippines

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Quezon City, , Philippines

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Bielsko-Biala, , Poland

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Częstochowa, , Poland

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Gorzów Wielkopolski, , Poland

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Grudziądz, , Poland

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Katowice, , Poland

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Kielce, , Poland

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Kielce, , Poland

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Kielce, , Poland

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Krakow, , Poland

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Ksawerów, , Poland

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Mrozy, , Poland

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Ostrowiec Świętokrzyski, , Poland

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Rzeszów, , Poland

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Warsaw, , Poland

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Angra do Heroísmo, Azores, Portugal

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Vila Nova de Gaia, Porto District, Portugal

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Faro, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Bragadiru, , Romania

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Brasov, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Codlea, , Romania

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Constanța, , Romania

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Iași, , Romania

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Ploieşti, , Romania

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Timișoara, , Romania

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Arkhangelsk, , Russia

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Chelyabinsk, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Tomsk, , Russia

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Ufa, , Russia

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Voronezh, , Russia

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Yaroslavl, , Russia

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Belgrade, , Serbia

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Belgrade, , Serbia

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Čačak, , Serbia

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Kamenitz, , Serbia

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Knez-Selo, , Serbia

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Kragujevac, , Serbia

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Sombor, , Serbia

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Valjevo, , Serbia

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Bratislava, , Slovakia

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Prešov, , Slovakia

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Johannesburg, Gauteng, South Africa

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eManzimtoti, KwaZulu-Natal, South Africa

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Cape Town, Western Cape, South Africa

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Cape Town, Western Cape, South Africa

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Daejeon, Daejeon Gwang''yeogsi, South Korea

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Bucheon-si, Gyeonggido, South Korea

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Incheon Gwangyeogsi,, Incheon Gwang''yeogsi, South Korea

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Seoul, Seoul Teugbyeolsi, South Korea

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Daegu, , South Korea

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Incheon, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Chiayi City, , Taiwan

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Kaohsiung City, , Taiwan

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New Taipei City, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Khon Kaen, , Thailand

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NakhonRatchasima, , Thailand

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Phitsanulok, , Thailand

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Udon Thani, , Thailand

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Ankara, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Balcalı, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Kampus, , Turkey (Türkiye)

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Konya, , Turkey (Türkiye)

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Maltepe, , Turkey (Türkiye)

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Mersin, , Turkey (Türkiye)

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Pendik, , Turkey (Türkiye)

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Samsun, , Turkey (Türkiye)

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Şehitkamil, , Turkey (Türkiye)

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Countries

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United States Argentina Australia Austria Brazil Bulgaria China Czechia Germany Hong Kong Latvia Lithuania Netherlands Philippines Poland Portugal Romania Russia Serbia Slovakia South Africa South Korea Taiwan Thailand Turkey (Türkiye)

References

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Aksamit T, De Soyza A, Bandel TJ, Criollo M, Elborn JS, Operschall E, Polverino E, Roth K, Winthrop KL, Wilson R. RESPIRE 2: a phase III placebo-controlled randomised trial of ciprofloxacin dry powder for inhalation in non-cystic fibrosis bronchiectasis. Eur Respir J. 2018 Jan 25;51(1):1702053. doi: 10.1183/13993003.02053-2017. Print 2018 Jan.

Reference Type DERIVED
PMID: 29371384 (View on PubMed)

Aksamit T, Bandel TJ, Criollo M, De Soyza A, Elborn JS, Operschall E, Polverino E, Roth K, Winthrop KL, Wilson R. The RESPIRE trials: Two phase III, randomized, multicentre, placebo-controlled trials of Ciprofloxacin Dry Powder for Inhalation (Ciprofloxacin DPI) in non-cystic fibrosis bronchiectasis. Contemp Clin Trials. 2017 Jul;58:78-85. doi: 10.1016/j.cct.2017.05.007. Epub 2017 May 8.

Reference Type DERIVED
PMID: 28495619 (View on PubMed)

Related Links

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http://www.clinicaltrialsregister.eu/

Click here to find information about studies related to Bayer Healthcare products conducted in Europe.

Other Identifiers

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2013-004659-19

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

15626

Identifier Type: -

Identifier Source: org_study_id